patient_id
string
genotype
string
sex
string
race_ethnicity
string
geographic_region
string
socioeconomic_status
string
age_at_dx_years
float64
age_at_cohort_entry_years
float64
follow_up_years
float64
alpha_thal_coinheritance
string
coinherited_g6pd_deficiency_flag
int64
hemoglobin_g_dl_baseline
float64
hbf_pct_baseline
float64
hbs_pct_baseline
float64
reticulocyte_pct
float64
wbc_k_ul_baseline
float64
platelet_k_ul_baseline
int64
ldh_u_l_baseline
int64
bilirubin_total_mg_dl
float64
ast_u_l_baseline
int64
creatinine_mg_dl_baseline
float64
uric_acid_mg_dl
float64
epo_mu_ml
int64
nt_probnp_pg_ml
int64
soluble_vcam1_ng_ml
int64
hscrp_mg_l
float64
disease_severity_score
float64
voc_episodes_yr
int64
voc_hospitalization_flag
int64
voc_location_primary
string
voc_trigger_primary
string
voc_duration_days_median
float64
voc_severity_nrs_mean
float64
acs_flag
int64
acs_icu_flag
int64
acs_mechanical_ventilation_flag
int64
acs_trigger_primary
string
chronic_pain_flag
int64
pain_nrs_baseline
float64
pain_interference_promis_t
float64
opioid_prescription_flag
int64
opioid_type_primary
string
opioid_mme_per_day
float64
ed_visits_yr
int64
hospitalization_days_voc_yr
int64
sickle_nephropathy_stage
string
egfr_ml_min
float64
upcr_mg_g_cr
int64
esrd_flag
int64
pulmonary_hypertension_flag
int64
trv_m_s
float64
bnp_pg_ml
int64
lv_diastolic_dysfunction_flag
int64
lvh_flag
int64
tcd_velocity_cm_s
int64
stroke_overt_flag
int64
silent_cerebral_infarct_flag
int64
moyamoya_flag
int64
cognitive_score_iq_analog
float64
avascular_necrosis_hip_flag
int64
avascular_necrosis_shoulder_flag
int64
avn_stage_ficat_arlet
string
joint_replacement_flag
int64
proliferative_retinopathy_flag
int64
retinopathy_stage
string
laser_photocoagulation_flag
int64
sickle_hepatopathy_flag
int64
cholelithiasis_flag
int64
cholecystectomy_flag
int64
priapism_flag
int64
priapism_max_duration_hrs
float64
spleen_status
string
functional_asplenia_flag
int64
leg_ulcer_flag
int64
bacterial_pathogen_primary
string
sepsis_episode_flag
int64
transfusion_program_type
string
transfusion_indication_primary
string
hbs_target_pct
float64
units_prbc_lifetime
int64
alloimmunization_flag
int64
alloantibody_count
int64
dhtr_flag
int64
autoantibody_flag
int64
serum_ferritin_ng_ml
int64
liver_iron_concentration_mg_g_dry
float64
myocardial_iron_flag
int64
chelation_agent
string
chelation_adherence_pct
float64
chelation_renal_toxicity_flag
int64
exchange_transfusion_hct_pre
float64
exchange_fraction_cells_replaced
float64
hydroxyurea_use_flag
int64
hu_dose_mg_kg_day
float64
hu_max_tolerated_dose_mg_kg
float64
hu_hbf_response_pct
float64
hu_wbc_nadir_k_ul
float64
hu_voc_reduction_fraction
float64
hu_adherence_pct
float64
hu_toxicity_flag
int64
l_glutamine_use_flag
int64
l_glutamine_voc_reduction_fraction
float64
crizanlizumab_use_flag
int64
crizanlizumab_voc_reduction_fraction
float64
voxelotor_use_flag
int64
voxelotor_hgb_rise_g_dl
float64
voxelotor_ldh_normalization_flag
int64
hsct_enrollment_flag
int64
hsct_donor_type
string
hsct_conditioning_regimen
string
hsct_engraftment_flag
int64
hsct_gvhd_flag
int64
hsct_tma_flag
int64
hsct_overall_survival_estimate
float64
gene_therapy_enrollment_flag
int64
gene_therapy_product
string
gt_cd34_cells_per_kg
int64
gt_hbf_or_hbat_rise_pct
float64
gt_voc_free_months
float64
gt_tdf_flag
int64
gt_engraftment_pct
float64
gt_hematologic_response
string
mortality_flag
int64
mortality_cause
string
time_to_mortality_months
float64
hospitalization_any_flag
int64
hospitalization_days_yr
int64
qol_sf36_pcs
float64
promis_fatigue_t_score
float64
promis_pain_interference_t_score
float64
depression_phq9_score
int64
anxiety_gad7_score
int64
school_days_missed_yr
int64
employment_status
string
penicillin_prophylaxis_flag
int64
vaccine_pneumococcal_flag
int64
vaccine_meningococcal_flag
int64
vaccine_influenza_flag
int64
palliative_care_referral_flag
int64
goals_of_care_documented_flag
int64
sku
string
HC002-000001
HbSC
Female
Black_non_Hispanic
Europe
Middle
0.95
8.3
8.9
No_deletion
0
7.58
6.25
79.8
15
6.7
375
564
6.65
22
0.49
6.7
388
110
3,896
2.11
4.08
2
1
Bilateral_legs
Dehydration
4.6
8.7
0
0
0
Infection
1
4.8
72.8
0
Hydromorphone
0
3
25
Macroalbuminuria
120.4
159
0
1
1.93
23
0
0
133
0
1
0
94.1
0
0
III
0
0
null
0
0
1
1
0
0
Surgical_splenectomy
0
0
Streptococcus_pneumoniae
0
Chronic_simple
Stroke_prevention
33.5
54
0
0
0
0
2,946
40
0
Deferasirox
0.81
0
0.247
0.86
1
31.4
31.4
21.8
2.51
0.321
0.65
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
1
14
38.1
68.7
53.6
9
9
15
Employed_full
1
1
1
1
0
0
HC-GEN-002
HC002-000002
HbSS
Female
Black_non_Hispanic
Other
Middle
2
40.9
15.7
2_gene_del
0
8.3
8.94
66.9
14.3
10.8
577
424
9.97
41
1.28
4.3
187
119
4,939
3.58
4.32
8
1
Lumbar_back
Infection
7.5
7.3
0
0
0
Hypoventilation
1
2.3
75.9
0
Morphine
0
6
12
null
99.8
238
0
0
2.92
63
1
1
207
0
0
0
98.2
0
0
II
0
0
NPSR
0
0
1
1
0
0
Autoinfarction
1
0
Streptococcus_pneumoniae
0
Episodic
ACS
43.7
60
0
0
0
0
1,184
12.91
0
Deferiprone
0.64
0
0.206
0.78
0
0
0
0
11.12
0
0
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Partial
1
Cardiac
438.8
1
17
34.7
64.3
83.3
19
11
15
Employed_full
1
1
1
1
0
1
HC-GEN-002
HC002-000003
HbSC
Female
Black_non_Hispanic
US_Northeast
High
2
41.9
17.2
No_deletion
0
10.54
2.44
77.3
6.4
14.7
437
191
2.23
24
0.77
5.2
58
149
5,000
8.18
3.38
2
0
Chest
Dehydration
2.2
7.5
1
0
0
Hypoventilation
0
1.7
69.3
1
Oxycodone
34.1
4
36
null
74.3
16
0
0
2.19
55
0
0
122
0
0
0
90.3
0
0
III
0
0
null
0
0
0
0
0
0
Normal
1
0
E_coli
1
Chronic_exchange
ACS
34.2
43
1
3
0
0
27,000
5.88
0
Deferasirox
0.73
1
0.207
0.53
1
14.9
14.9
14.2
1.5
0.383
0.81
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Minimal
0
null
0
1
10
36.4
61.4
56
10
16
4
Employed_part
0
0
0
1
0
0
HC-GEN-002
HC002-000004
HbSC
Female
Black_non_Hispanic
US_Northeast
Middle
0.83
15.4
14.9
No_deletion
0
10.76
3.05
59.8
7.5
7.3
544
635
4.71
82
0.68
8.4
202
61
2,555
5.8
3.69
4
1
Lumbar_back
Infection
4.8
9
0
0
0
Fat_embolism
1
4.9
54.2
1
Oxycodone
336
5
30
null
110.2
255
0
1
2.01
49
0
0
94
0
0
0
82.9
0
0
II
0
0
PSR_Sea_Fan
0
0
1
1
0
0
Surgical_splenectomy
0
0
Salmonella_sp
0
Episodic
Stroke_prevention
58.7
43
1
2
0
0
976
6.26
0
Deferiprone
0.86
0
0.272
0.76
1
27.3
27.3
4.7
4.36
0.702
0.49
0
0
0
0
0
0
0
0
0
Haplo
NMA
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Minimal
0
null
0
0
45
46.5
70.9
66.2
15
12
14
Employed_full
0
1
0
1
0
0
HC-GEN-002
HC002-000005
HbSS
Female
Black_non_Hispanic
Africa
Low
0.58
19.4
11.6
No_deletion
0
11.15
7.77
83.9
3
10.3
456
388
2.37
24
0.4
6.9
199
101
2,305
11.68
3.77
5
0
Abdomen
Infection
9.6
5.8
1
0
0
Unknown
1
4.1
58.2
1
Oxycodone
29.2
6
12
null
106.7
55
0
0
2.11
20
0
0
150
0
1
0
96.4
0
0
IV
0
0
PSR_Sea_Fan
0
0
1
1
0
0
Autoinfarction
1
0
Streptococcus_pneumoniae
0
Episodic
Stroke_prevention
46.9
57
0
0
0
0
1,313
10.25
0
Deferoxamine
0.69
0
0.168
0.67
1
29.6
29.6
10.3
4.66
0.697
0.79
0
0
0
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
1
Lovotibeglogene_autotemcel
10,000,000
41.4
10.1
0
0.996
Complete
0
null
0
0
7
37.7
61.5
52.9
13
3
8
Unemployed
1
0
1
1
0
0
HC-GEN-002
HC002-000006
HbSB+_thal
Female
Black_non_Hispanic
US_Midwest
High
0.45
9.6
14.8
2_gene_del
0
11.54
8.8
88.5
14.4
9.8
356
576
8.94
30
0.61
4.3
68
397
2,173
13.09
3.29
1
0
Bilateral_legs
Dehydration
9
6.3
0
0
0
Infection
0
4.1
83.2
1
Other
65.8
3
25
null
139.4
168
0
0
1.75
28
0
0
192
1
0
0
87.3
1
0
III
0
0
null
0
0
1
1
0
0
Normal
0
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
26
37
0
0
0
0
3,255
33.93
0
Deferasirox
0.54
0
0.33
0.76
1
24.5
24.5
10.5
4.63
0.429
0.8
0
0
0
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
0
Other
0
0
0
0
0
Partial
0
null
0
0
29
49.3
55.5
68.9
14
1
6
Employed_full
1
1
1
1
0
0
HC-GEN-002
HC002-000007
HbSC
Male
Middle_Eastern
Europe
Middle
2
33.4
13.9
2_gene_del
0
11.6
8.95
74.7
11
8.9
436
550
2.79
53
0.89
7.3
231
60
3,218
4.94
3.04
1
1
Bilateral_legs
Stress
4.4
6
0
0
0
Hypoventilation
1
1.2
65.5
1
Oxycodone
13.5
4
44
Macroalbuminuria
111.6
307
0
0
1.64
83
0
0
106
0
0
0
87.2
0
0
III
0
1
NPSR
1
1
0
0
1
2.3
Normal
0
0
Staphylococcus_aureus
0
Chronic_exchange
ACS
31.1
91
1
3
0
0
4,639
40
0
Deferoxamine
0.67
0
0.208
0.8
1
21.9
21.9
14.5
7.84
0.1
0.75
0
0
0
0
0
0
0
0
0
UCB
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
28
30.1
68.7
59.1
14
12
13
Unemployed
0
0
0
0
0
1
HC-GEN-002
HC002-000008
HbSC
Female
Black_non_Hispanic
US_Northeast
Low
2
23.9
5.5
No_deletion
0
9.15
12.07
78.2
11.4
11.7
508
285
3.19
35
1.77
6
47
43
5,000
1.37
3.11
0
1
Abdomen
Stress
9.9
6.6
0
0
0
Hypoventilation
0
4.9
64
1
Other
49.7
6
7
Microalbuminuria
43.3
309
0
0
1.92
45
0
0
80
0
0
0
79
1
0
II
0
1
null
0
0
1
0
0
0
Autoinfarction
0
0
Staphylococcus_aureus
0
Episodic
Stroke_treatment
45.1
32
0
0
0
0
1,422
4.94
0
Deferoxamine
0.39
0
0.212
0.95
1
18.2
18.2
13.9
2.51
0.579
0.77
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
6
34.1
70
70.7
0
7
5
Unemployed
0
0
1
1
0
1
HC-GEN-002
HC002-000009
HbSS
Male
Hispanic
US_South
Low
1.88
29.8
11.5
No_deletion
0
7.48
3.43
89.4
5.2
12.3
563
267
7.82
24
0.98
5.5
185
114
2,719
3.3
4.72
2
1
Chest
Cold_exposure
4.7
9.6
1
0
0
Infection
1
2.6
52.5
1
Morphine
35.5
2
22
Macroalbuminuria
123.5
105
0
0
1.95
34
0
1
142
0
1
0
65.1
0
0
III
0
1
PSR_Sea_Fan
0
0
1
0
1
20
Autoinfarction
1
0
Haemophilus_influenzae
0
Episodic
Stroke_prevention
43.7
66
0
0
0
0
286
7.39
1
Deferoxamine
0.47
0
0.235
0.79
1
25.6
25.6
26.3
3.35
0.655
0.69
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
0
26
19.4
59.8
58.4
6
4
9
Employed_full
0
0
0
1
1
0
HC-GEN-002
HC002-000010
HbSS
Male
Black_non_Hispanic
Europe
Middle
2
28
15.6
2_gene_del
0
8.07
3.6
68
7.6
12.3
404
542
10.29
101
1.3
5.1
297
39
4,934
5.59
4.84
1
1
Bilateral_legs
Unknown
1.5
4.1
0
0
0
Unknown
1
6.7
61
0
Hydromorphone
0
1
21
Microalbuminuria
165.4
112
0
0
1.78
209
1
0
171
0
1
0
84.3
0
0
IV
0
0
NPSR
0
0
0
0
1
2.6
Normal
1
0
Staphylococcus_aureus
0
Episodic
Stroke_treatment
41.3
41
0
0
0
0
3,373
5.67
0
Deferoxamine
0.38
0
0.241
0.8
0
0
0
0
7.96
0
0
0
0
0
1
0.567
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Minimal
0
null
0
0
18
24.9
66.6
56.9
7
14
16
Employed_part
1
0
0
1
0
0
HC-GEN-002
HC002-000011
HbSS
Male
Hispanic
US_South
Low
0.59
31
7
2_gene_del
0
7.11
4.61
71.4
10.1
8.1
222
352
5.59
30
0.4
8.3
264
30
1,114
3.25
4.8
2
0
Bilateral_legs
Infection
6.6
5.1
0
0
0
Fat_embolism
0
3
69.9
0
Morphine
0
2
20
null
111
263
0
0
2.6
445
1
1
80
0
0
0
89
1
0
I
0
0
null
0
1
1
0
0
0
Normal
1
0
Staphylococcus_aureus
0
Episodic
Stroke_treatment
48.3
51
0
0
0
0
1,030
12.36
0
Deferasirox
0.58
0
0.194
0.53
1
23.7
23.7
3.6
5.74
0.561
0.5
0
0
0
0
0
0
0
0
0
MSD
NMA
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
1
34
30.8
65
60.3
10
6
18
Employed_part
0
0
1
1
1
1
HC-GEN-002
HC002-000012
HbSB0_thal
Female
Black_non_Hispanic
US_South
Low
1.01
22.3
13.4
No_deletion
0
8.2
13
80.2
9.3
6.1
214
615
8.05
41
0.7
3.9
176
86
3,003
2.6
4.05
13
1
Bilateral_legs
Infection
11
4.7
0
0
0
Infection
1
2.2
62.2
1
Hydromorphone
138.9
0
35
null
144.5
15
0
0
1.79
64
1
0
179
0
0
0
106.2
0
1
II
0
0
NPSR
0
1
0
0
0
0
Normal
1
0
E_coli
0
null
Stroke_prevention
54.3
69
1
4
0
0
2,193
40
0
Deferoxamine
0.65
0
0.234
0.87
1
15.4
15.4
23.1
5.54
0.541
0.71
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
1
Infection
269.6
1
25
39.5
60.9
62
5
7
4
Employed_full
1
1
1
0
0
0
HC-GEN-002
HC002-000013
HbSS
Male
Black_non_Hispanic
US_Midwest
Low
0.69
16.4
10.1
2_gene_del
0
8.7
10.13
76
12.5
11.8
381
372
7.92
41
1.36
5.5
229
517
5,000
6.4
4.11
2
0
Lumbar_back
Dehydration
8.1
9.7
1
0
0
Infection
1
6.4
56.3
0
Hydromorphone
0
2
44
Hyperfiltration
92.3
29
0
0
1.73
20
1
1
85
0
0
0
103.9
1
0
III
0
0
null
0
0
1
0
1
4.1
Autoinfarction
1
1
Haemophilus_influenzae
0
Episodic
Stroke_treatment
50.1
81
0
0
0
0
1,335
19.52
0
Deferoxamine
0.53
0
0.183
0.85
0
0
0
0
14.06
0
0
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
24
29.8
45.4
64.5
8
4
9
Employed_part
1
1
0
1
0
1
HC-GEN-002
HC002-000014
HbSC
Male
Middle_Eastern
Europe
Middle
2
21.7
10.6
No_deletion
1
8.98
13.09
79.6
14.3
9.5
139
639
5.43
59
0.48
7
131
117
3,343
42.28
3.4
0
0
Abdomen
Cold_exposure
3.4
6.1
0
0
0
Infection
1
1.4
58.8
0
Hydromorphone
0
3
19
null
129.8
64
0
0
1.63
92
0
1
169
0
1
0
84.5
0
0
II
0
0
null
0
0
1
0
0
0
Autoinfarction
1
0
Haemophilus_influenzae
1
null
Stroke_treatment
48.1
50
1
3
0
0
988
28.51
0
Deferiprone
0.63
0
0.196
0.52
1
21.4
21.4
16.5
6.8
0.386
0.83
0
0
0
0
0
0
0
0
0
Haplo
NMA
0
0
0
0
0
Other
0
0
0
0
0
Partial
0
null
0
1
38
24.1
48.7
54.4
3
0
14
Unemployed
1
1
0
0
0
0
HC-GEN-002
HC002-000015
HbSS
Male
Black_non_Hispanic
Africa
Middle
1.45
13.3
2.7
No_deletion
0
9.88
1.59
71.9
21.1
16.5
635
488
3.5
54
1.2
9.2
247
145
2,405
4.09
4.54
1
1
Lumbar_back
Dehydration
8.5
6.6
0
0
0
Unknown
1
2.3
75.1
1
Morphine
21
0
11
Hyperfiltration
83.9
18
0
0
1.59
20
1
0
80
0
1
0
83
0
1
II
0
0
null
0
0
0
0
0
0
Autoinfarction
1
0
E_coli
0
Episodic
Stroke_treatment
44.1
110
1
3
0
1
2,428
34.71
0
Deferoxamine
0.73
0
0.156
0.88
0
0
0
0
11.72
0
0
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Minimal
0
null
0
1
22
38.1
56.6
52.1
0
3
12
Unemployed
0
1
1
1
0
0
HC-GEN-002
HC002-000016
HbSS
Male
Black_non_Hispanic
US_South
Middle
2
50.1
13.7
1_gene_del
0
8.34
9.12
83.7
11.9
16.7
492
459
8.02
32
1.07
7.6
256
30
2,622
6.04
4.34
5
0
Bilateral_legs
Unknown
8.7
4.3
0
0
0
Infection
1
7.8
69.3
1
Oxycodone
23.1
7
40
null
101.4
65
0
1
2.66
23
0
0
81
0
0
0
78.2
0
0
III
0
0
null
0
1
1
0
1
2.8
Normal
1
0
Salmonella_sp
1
null
Stroke_prevention
53.7
40
1
4
0
0
1,624
9.15
0
Deferiprone
0.85
0
0.226
0.9
1
27.5
27.5
24.4
5.74
0.464
0.43
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
bb2121
0
0
0
0
0
Partial
0
null
0
0
26
18
60.6
46.5
22
4
18
Disability
1
1
0
0
0
1
HC-GEN-002
HC002-000017
HbSS
Male
Hispanic
US_South
Low
0.23
21.2
17.4
No_deletion
0
5.78
2.6
80.8
16.5
17
344
341
8.22
39
0.85
5.5
119
188
801
2.12
5.2
3
0
Chest
Infection
2.4
6.7
0
0
0
Unknown
1
3.7
67.9
1
Morphine
57
5
18
Microalbuminuria
101.6
61
0
0
2.2
93
0
1
165
0
0
0
104.7
1
0
III
0
1
null
0
0
1
0
0
0
Normal
1
1
Salmonella_sp
0
null
ACS
45.1
79
0
0
0
0
1,292
4.57
0
Deferasirox
0.74
0
0.213
0.63
1
19.6
19.6
12.6
5.63
0.602
0.62
0
1
0.276
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
47
18.1
48.8
55.5
7
0
5
Unemployed
0
1
0
0
0
0
HC-GEN-002
HC002-000018
HbSS
Female
African_born
Other
Low
0.61
17.1
3.7
2_gene_del
0
8.13
7
86.4
8.7
8.2
287
448
9.46
41
0.63
9.1
303
133
2,195
16.36
4.51
3
0
Bilateral_legs
Cold_exposure
6.8
8.8
1
0
0
Infection
1
6.3
66.8
1
Hydromorphone
50.7
10
29
null
126.7
100
0
0
2.38
22
0
0
189
0
0
0
91.3
0
0
I
0
0
VH_RD
0
0
1
1
0
0
Normal
0
0
Staphylococcus_aureus
0
Chronic_exchange
Stroke_prevention
28.4
37
0
0
0
0
9,414
9.14
0
Deferasirox
0.71
0
0.139
0.68
1
11
11
7.5
4.92
0.371
0.77
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
33
26.5
39.3
43.4
15
7
6
Unemployed
0
1
1
1
0
1
HC-GEN-002
HC002-000019
HbSC
Male
Black_non_Hispanic
US_South
Middle
1.92
19.4
8
1_gene_del
0
10.89
6.49
83.6
5.3
12.7
543
690
7.07
60
0.45
4.8
302
62
5,000
12.18
3.48
1
1
Abdomen
Cold_exposure
5.8
7.7
0
0
0
Unknown
1
1.4
49
1
Other
54.9
6
26
Hyperfiltration
81.2
84
0
0
2.51
53
1
0
140
0
0
0
99.3
0
0
II
0
0
null
0
0
1
0
0
0
Surgical_splenectomy
1
1
E_coli
0
Episodic
Stroke_prevention
59.3
59
0
0
0
0
1,089
37.39
0
Deferasirox
0.91
0
0.193
0.93
1
30
30
20
3.61
0.433
0.88
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
0
46
38.9
58.7
47.9
13
8
11
Employed_full
0
1
1
1
0
0
HC-GEN-002
HC002-000020
HbSS
Female
Black_non_Hispanic
US_South
Low
1.26
19.9
1.9
No_deletion
0
9.56
2.71
83.7
10.6
13.6
286
394
3.37
28
1.8
7.2
214
145
2,721
11.53
4.45
8
1
Lumbar_back
Infection
4.9
7
0
0
0
Unknown
0
2.8
65
1
Morphine
29.1
3
35
CKD3+
58.7
325
0
0
1.97
20
1
1
236
0
0
0
106.1
1
0
II
1
0
PSR_Sea_Fan
0
1
0
0
0
0
Autoinfarction
1
0
Salmonella_sp
1
Chronic_simple
Pre_op
33.4
48
0
0
0
0
2,465
30.05
0
Deferasirox
0.49
0
0.219
0.95
0
0
0
0
13.15
0
0
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Other
0
0
0
0
0
Partial
0
null
0
1
50
26
60.3
59.3
7
11
18
Employed_part
0
1
0
1
1
1
HC-GEN-002
HC002-000021
HbSC
Female
African_born
US_South
Middle
2
23.4
1.6
No_deletion
0
10.03
7.51
70.4
5.6
13.3
298
512
8.54
100
1.02
7.5
1,697
144
2,886
17.95
3.44
0
0
Lumbar_back
Stress
6.8
4.4
0
0
0
Infection
1
3.2
73.7
0
Hydromorphone
0
6
12
null
126.5
179
0
0
2.69
70
1
1
99
0
1
0
77.2
0
0
I
0
1
null
0
0
0
0
0
0
Normal
0
0
Haemophilus_influenzae
0
null
Splenic_sequestration
44.3
40
0
0
0
0
3,123
17.8
0
Deferiprone
0.6
0
0.254
0.52
1
22.7
22.7
17.9
5.07
0.383
0.79
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
65
35.9
68.4
68.4
17
4
11
Disability
1
0
0
1
0
0
HC-GEN-002
HC002-000022
HbSS
Male
Hispanic
US_Midwest
Low
2
23.4
19.8
No_deletion
1
9.36
5.45
85.9
12.1
9.9
328
412
6.05
33
0.88
5.5
219
42
1,135
4.3
4.32
2
0
Bilateral_legs
Stress
1.2
6.6
0
0
0
Infection
0
3.4
59.1
0
Hydromorphone
0
3
22
null
125.1
83
0
0
1.85
164
0
0
99
0
0
0
82.1
0
0
I
0
0
PSR_Sea_Fan
0
0
1
1
1
12.1
Normal
1
0
Staphylococcus_aureus
1
Chronic_exchange
Splenic_sequestration
31.7
82
0
0
0
0
507
40
0
Deferasirox
0.73
0
0.169
0.5
1
19.4
19.4
8.7
5.15
0.287
0.58
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
30
42.2
79.5
58.3
5
0
12
Disability
0
1
1
1
0
0
HC-GEN-002
HC002-000023
HbSB+_thal
Male
Other
Africa
Low
1.28
17.7
10.4
1_gene_del
0
10.06
3.16
79.4
8.9
14.8
434
427
4.75
45
0.6
7.8
196
169
1,611
4.75
3.84
1
1
Bilateral_legs
Stress
4.7
7.5
1
1
1
Unknown
1
4.1
72.8
1
Hydromorphone
27.9
6
29
null
113.9
60
0
0
1.66
41
1
0
128
0
0
0
121.6
0
1
III
0
1
NPSR
0
1
1
0
1
3.6
Normal
0
0
Salmonella_sp
0
Episodic
ACS
51.6
71
0
0
0
0
952
19.02
0
Deferasirox
0.55
0
0.208
0.64
1
20.2
20.2
22.8
5.48
0.592
0.62
0
0
0
0
0
0
0
0
0
UCB
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
26
39.6
46.3
83.9
9
6
16
Unemployed
0
1
1
0
0
0
HC-GEN-002
HC002-000024
HbSC
Female
Black_non_Hispanic
Europe
Low
2
23.6
7.8
1_gene_del
0
8.66
4.09
80.7
4.2
11
494
876
5.22
28
0.75
6
175
402
5,000
23.76
4.28
2
1
Abdomen
Cold_exposure
8.5
5.4
1
1
0
Infection
1
6.4
68
0
Other
0
7
7
null
142.7
85
0
0
2.25
66
1
0
126
0
0
0
99.1
1
0
III
0
0
NPSR
0
1
0
0
0
0
Autoinfarction
0
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
28.8
75
0
0
0
0
3,116
11.8
0
Deferasirox
0.54
1
0.176
0.62
1
27.6
27.6
10.7
5.48
0.3
0.71
0
0
0
1
0.343
0
0
0
0
Haplo
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
0
17
52
63.6
65.3
12
2
2
Employed_full
0
0
1
0
0
0
HC-GEN-002
HC002-000025
HbSC
Male
Hispanic
Europe
Middle
2
49.4
6.2
No_deletion
0
8.52
3.3
90.4
18.9
11.4
563
693
4.28
27
0.8
7.8
113
97
4,957
10.04
4.2
2
0
Bilateral_legs
Infection
2.8
8.4
1
1
0
Infection
0
1.2
71.1
0
Hydromorphone
0
8
22
Hyperfiltration
102.9
87
0
1
2.31
35
1
1
151
0
0
0
88.7
0
0
IV
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
0
1
Streptococcus_pneumoniae
0
null
Pre_op
57.8
28
0
0
0
0
2,990
3.43
0
Deferiprone
0.4
0
0.249
0.71
0
0
0
0
9.28
0
0
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
42
36.4
83.9
64.2
9
7
22
Employed_full
1
0
1
1
0
0
HC-GEN-002
HC002-000026
HbSS
Male
Black_non_Hispanic
US_South
Low
0.89
11.9
19.6
No_deletion
0
9.77
5.28
76.2
9.8
6.4
545
418
9.43
32
0.9
4
424
51
1,903
1.02
4.25
1
0
Lumbar_back
Infection
4.3
8.8
0
0
0
Unknown
0
1.1
62.6
1
Other
121.2
8
25
CKD3+
119.8
1,849
0
0
2.16
37
0
1
110
0
0
0
106.9
0
0
IV
0
0
null
0
0
0
0
1
11.2
Autoinfarction
1
0
Streptococcus_pneumoniae
0
null
ACS
48.5
35
1
3
0
0
1,368
40
0
Deferasirox
0.36
0
0.193
0.71
1
19.4
13.6
14.1
6.74
0.575
0.7
1
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
1
11
49
46.9
49.5
8
10
9
Disability
1
1
1
1
0
0
HC-GEN-002
HC002-000027
HbSS
Female
Middle_Eastern
US_Northeast
Middle
1.44
14.4
5.8
No_deletion
0
9.87
6.34
92.8
5.4
12.9
420
444
2.98
30
1.07
7.3
141
102
2,656
8.7
4.19
0
0
Lumbar_back
Stress
6
6.2
1
0
0
Unknown
1
3.2
71.8
1
Hydromorphone
35.5
9
20
Macroalbuminuria
97.8
16
0
0
2.51
34
0
0
163
0
0
0
88.3
1
0
IV
0
0
NPSR
0
0
0
0
0
0
Normal
1
0
Streptococcus_pneumoniae
0
Episodic
Splenic_sequestration
42.7
26
0
0
0
0
3,163
14.94
0
Combination
0.71
0
0.241
0.95
0
0
0
0
7.85
0
0
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Partial
0
null
0
1
37
41
50.3
68.4
0
5
2
Disability
1
0
0
1
1
1
HC-GEN-002
HC002-000028
HbSS
Female
Black_non_Hispanic
US_Northeast
Low
2
46.7
14.8
2_gene_del
0
8.65
5.42
93.6
15.6
10.2
542
294
3.68
38
0.5
6.2
155
286
3,588
3.8
4.37
8
1
Bilateral_legs
Infection
7.1
8.5
1
1
0
Hypoventilation
1
3.4
45.9
0
Oxycodone
0
1
33
Microalbuminuria
100.9
30
0
1
2.29
125
0
0
162
1
1
0
75.9
0
0
I
0
0
PSR_Sea_Fan
0
0
1
0
0
0
Normal
0
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
29.7
35
0
0
0
0
4,369
10.47
0
Deferasirox
0.58
0
0.206
0.62
1
12.8
12.8
23.6
4.28
0.75
0.41
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
21
30.8
69.9
68.3
13
7
26
Employed_part
0
0
1
0
0
0
HC-GEN-002
HC002-000029
HbSS
Female
Hispanic
US_South
Middle
1.53
34
6.4
No_deletion
0
10.29
2.24
88
9.1
12.4
339
373
5.13
30
0.4
8.5
159
36
2,002
12.41
4.31
7
1
Bilateral_legs
Infection
4.8
7
1
1
1
Unknown
0
8.3
62.4
0
Hydromorphone
0
0
27
Microalbuminuria
121.9
25
0
0
2.23
22
1
0
205
0
0
0
85.2
0
0
II
0
0
null
0
0
1
0
0
0
Autoinfarction
0
0
Staphylococcus_aureus
0
Episodic
ACS
42.3
64
0
0
0
0
6,206
14.84
0
Deferasirox
0.64
0
0.152
0.57
1
18.4
18.4
25
3.2
0.693
0.63
0
0
0
1
0.25
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
40
25.1
62
51.6
14
0
10
Employed_part
1
1
1
0
0
0
HC-GEN-002
HC002-000030
HbSC
Male
Black_non_Hispanic
US_South
Middle
2
45.6
2.3
No_deletion
0
11.98
4.73
74.2
16.4
11.7
201
464
13.56
59
0.77
6.7
111
217
1,337
8.39
3.17
0
0
Lumbar_back
Dehydration
11.9
9.3
1
0
0
Fat_embolism
1
8.1
69.8
0
Morphine
0
2
22
null
180
124
0
1
2.79
51
1
1
120
0
0
0
91.8
0
0
I
0
0
null
0
0
0
0
0
0
Normal
0
0
Streptococcus_pneumoniae
0
Chronic_exchange
Stroke_prevention
25.8
61
1
2
0
0
6,774
40
0
Deferasirox
0.77
0
0.217
0.9
1
18.5
18.5
15
8.6
0.389
0.83
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Partial
0
null
0
0
33
36.7
62.3
62.4
7
5
16
Employed_full
1
0
0
0
0
0
HC-GEN-002
HC002-000031
HbSC
Female
Black_non_Hispanic
US_Northeast
Low
0.7
29.6
14
No_deletion
0
11.46
9.05
64.5
9.1
11.5
339
592
10.25
33
0.4
8.7
60
62
3,362
1.5
3.1
0
0
Bilateral_legs
Stress
3
10
0
0
0
Hypoventilation
1
2.7
65.3
1
Morphine
60.7
7
24
Macroalbuminuria
136
119
0
0
2.21
93
0
0
153
0
1
0
80.7
0
1
III
0
1
VH_RD
0
1
1
0
0
0
Normal
1
0
Streptococcus_pneumoniae
0
null
Stroke_prevention
51.5
79
0
0
0
0
12,305
40
1
Deferiprone
0.47
0
0.173
0.89
1
22.6
22.6
10.7
5.58
0.451
0.52
0
0
0
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
0
Other
0
0
0
0
0
Complete
0
null
0
0
31
22.1
65.8
78.8
14
13
9
Unemployed
1
1
1
1
1
0
HC-GEN-002
HC002-000032
HbSB+_thal
Female
Hispanic
US_South
Middle
2
36.9
1
1_gene_del
0
8.52
4.49
90.6
9.8
10.9
323
565
2.66
31
0.63
7.6
169
155
4,848
7.5
4.2
3
1
Abdomen
Dehydration
2.4
5.2
0
0
0
Infection
1
0.9
74.1
0
Hydromorphone
0
4
14
Hyperfiltration
129.2
45
0
0
2.3
138
1
0
164
0
1
0
75
1
1
IV
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
0
0
Haemophilus_influenzae
0
Chronic_exchange
ACS
32.1
54
0
0
0
0
3,664
11.47
0
Deferasirox
0.65
0
0.265
0.6
0
0
0
0
8.94
0
0
0
0
0
1
0.05
0
0
0
0
MSD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
17
32.6
67.5
64.9
10
9
13
Unemployed
0
1
1
1
1
0
HC-GEN-002
HC002-000033
HbSS
Male
Black_non_Hispanic
US_Midwest
Low
1.24
10.4
13.8
No_deletion
0
10.62
5.64
82.9
13.4
13.4
344
245
11.89
38
0.57
6.6
492
69
4,895
7.16
3.89
2
0
Bilateral_legs
Unknown
3.3
8.6
0
0
0
Unknown
0
3.8
60.3
1
Other
18.1
2
20
null
137.1
264
0
1
1.68
95
1
0
140
0
1
0
86.9
0
0
I
0
1
null
0
0
0
0
0
0
Autoinfarction
1
0
Streptococcus_pneumoniae
0
Episodic
Splenic_sequestration
45.9
41
0
0
0
1
706
26.3
0
Deferasirox
0.61
0
0.293
0.93
1
27
27
12.5
5
0.486
0.77
0
0
0
0
0
0
0
0
0
Haplo
NMA
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Minimal
1
Other
227.1
1
16
33.4
64.2
71.3
15
4
10
Employed_full
0
1
1
0
0
0
HC-GEN-002
HC002-000034
HbSS
Female
African_born
Europe
Middle
2
36.2
5.8
1_gene_del
0
8.95
4.89
76
14.4
10.4
305
626
11.88
66
0.95
8
286
69
5,000
8.09
4.64
9
1
Chest
Dehydration
9
9.5
0
0
0
Hypoventilation
0
0.8
56
1
Oxycodone
30.8
5
22
CKD3+
27.8
140
0
0
3.59
63
0
0
132
0
0
0
84.3
0
0
II
0
0
PSR_Sea_Fan
0
0
1
0
0
0
Autoinfarction
1
0
E_coli
0
Chronic_simple
Stroke_treatment
32.1
44
1
2
0
0
2,351
40
0
Deferasirox
0.57
0
0.246
0.93
1
22.8
22.8
15.8
4.1
0.518
0.77
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
5
46.4
65.8
58.3
13
3
9
Employed_part
1
1
1
0
0
1
HC-GEN-002
HC002-000035
HbSS
Male
Black_non_Hispanic
US_South
Low
1.98
25
15.2
No_deletion
0
7.66
2.85
91.4
15.1
6.6
365
388
3.36
49
2
8
853
557
1,674
9.59
4.83
2
0
Lumbar_back
Infection
4.1
5.5
0
0
0
Hypoventilation
1
2.1
44
1
Hydromorphone
59.4
6
14
Hyperfiltration
121.2
277
0
0
1.5
42
0
0
80
0
0
0
98.9
0
0
II
0
0
PSR_Sea_Fan
0
1
0
0
0
0
Normal
0
1
Streptococcus_pneumoniae
0
null
Stroke_prevention
40
66
0
0
0
0
806
23.28
0
Deferasirox
0.63
0
0.194
0.86
1
14
14
13.8
9.01
0.682
0.84
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
11
27.5
48.4
42.7
8
7
15
Employed_part
0
1
1
1
0
0
HC-GEN-002
HC002-000036
HbSS
Male
Black_non_Hispanic
US_Northeast
Middle
2
37.6
15.6
No_deletion
0
7.26
5.1
75.1
11.6
12.7
494
259
1.71
43
0.4
7.5
446
30
3,748
20.02
4.65
5
1
Chest
Dehydration
4.5
6.2
0
0
0
Unknown
0
3.8
59
0
Oxycodone
0
1
21
null
141.9
382
0
0
1.88
140
0
1
143
0
1
0
80.3
1
0
I
0
0
null
0
0
1
1
1
2.3
Autoinfarction
0
1
Staphylococcus_aureus
0
Episodic
Stroke_treatment
57.4
82
1
2
0
0
8,245
18.55
0
Deferasirox
0.83
1
0.221
0.87
1
27.7
27.7
9.6
6.39
0.514
0.81
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
40
39
70.1
67.3
19
9
6
Disability
1
1
1
1
1
1
HC-GEN-002
HC002-000037
HbSS
Female
Black_non_Hispanic
Europe
High
0.82
26.4
14.8
No_deletion
0
8.56
3.7
78.6
14.1
8.6
626
736
5.84
25
2.31
3.4
372
197
3,184
8.42
4.9
1
0
Lumbar_back
Infection
3
6.1
0
0
0
Fat_embolism
1
7.8
67.7
1
Hydromorphone
124.6
0
17
Microalbuminuria
113
10
0
0
1.87
33
0
0
164
1
1
0
55
0
0
III
0
0
null
0
1
0
0
0
0
Normal
1
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
31.3
58
1
4
0
0
14,738
2.03
0
Deferasirox
0.47
0
0.232
0.95
1
15.2
15.2
23.9
3.62
0.632
0.93
0
0
0
0
0
0
0
0
0
MUD
Myeloablative
0
0
0
0
0
Other
0
0
0
0
0
Partial
0
null
0
1
17
24.8
76.1
60.3
5
4
20
Unemployed
1
1
1
1
0
1
HC-GEN-002
HC002-000038
HbSS
Male
Black_non_Hispanic
Europe
Low
0.19
4.8
1.5
No_deletion
0
5.86
5.52
86.2
15
7
213
779
10.6
28
0.66
5.3
1,103
686
3,486
6.16
5.39
1
0
Bilateral_legs
Infection
5.3
7
1
1
0
Hypoventilation
0
5.3
70.4
1
Other
239
4
39
null
108.5
205
0
0
2.94
34
1
0
138
0
0
0
99.5
0
1
II
0
0
null
0
1
1
0
1
10.5
Autoinfarction
1
0
E_coli
0
Chronic_exchange
Splenic_sequestration
26.8
79
0
0
0
0
3,233
40
0
Deferasirox
0.68
0
0.263
0.85
1
19.6
19.6
14.5
3.71
0.325
0.73
0
0
0
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
1
Exagamglogene_autotemcel_CRISPR
10,000,000
51.6
34.4
0
0.93
Partial
0
null
0
1
38
43.1
71.8
64.7
0
6
30
Disability
1
1
1
0
0
0
HC-GEN-002
HC002-000039
HbSS
Male
Black_non_Hispanic
Africa
Middle
0.87
18.2
14.4
No_deletion
0
9.18
7.44
73.1
12.8
7.9
265
454
13.41
27
0.88
8.9
226
241
3,275
15.16
4.27
4
1
Lumbar_back
Stress
17.5
6.6
0
0
0
Fat_embolism
1
4.2
46.6
0
Morphine
0
0
20
null
77.1
19
0
0
1.86
197
1
1
109
0
0
0
99.7
0
0
II
0
0
null
0
0
1
0
0
0
Autoinfarction
1
0
Salmonella_sp
0
Episodic
Stroke_prevention
42.1
44
1
1
0
0
11,688
5.88
0
Deferoxamine
0.59
0
0.212
0.68
1
21.5
21.5
29.5
4.6
0.567
0.95
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Partial
0
null
0
1
36
49.9
65.1
62.5
0
0
16
Employed_part
1
1
0
0
0
0
HC-GEN-002
HC002-000040
HbSC
Female
Black_non_Hispanic
US_Northeast
Middle
1.39
14.9
19.8
No_deletion
0
9.17
7.03
81.1
11.4
11.8
325
555
3.91
75
0.4
4.9
257
32
2,617
36.39
3.69
2
1
Lumbar_back
Dehydration
4.7
6.8
0
0
0
Infection
0
5.6
74.9
1
Hydromorphone
32.1
9
14
null
94.8
121
0
0
2.28
89
1
0
80
0
1
0
111
0
0
IV
0
0
null
0
0
0
0
0
0
Normal
0
1
E_coli
0
Chronic_simple
Stroke_prevention
28.3
62
0
0
0
1
10,842
2.53
0
Deferasirox
0.89
0
0.236
0.73
0
0
0
0
13.59
0
0
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
24
26.6
78.7
53.4
11
10
9
Employed_full
1
1
1
0
1
0
HC-GEN-002
HC002-000041
HbSS
Female
Black_non_Hispanic
Africa
Low
2
31
5.6
No_deletion
0
8.72
10
90.7
6.2
10.7
512
570
14.53
55
1.22
8.1
242
34
805
12.58
4.3
3
1
Lumbar_back
Infection
2.1
8.7
0
0
0
Infection
1
3.7
51.3
0
Hydromorphone
0
2
13
Hyperfiltration
80.8
82
0
0
1.87
92
1
0
158
0
0
0
92.2
1
0
I
0
0
VH_RD
0
0
0
0
0
0
Surgical_splenectomy
1
0
Salmonella_sp
0
null
Stroke_treatment
41.1
40
0
0
0
0
4,545
2.71
0
Deferoxamine
0.45
0
0.153
0.63
1
17
17
13.2
3.57
0.662
0.7
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
1
ACS
600
1
14
36.1
62
62.7
0
4
2
Disability
0
1
0
0
0
0
HC-GEN-002
HC002-000042
HbSC
Female
Hispanic
US_South
Middle
1.25
28.2
6.2
No_deletion
0
9.77
2.67
83.7
14.4
4.6
395
756
1.99
32
0.76
7.9
841
57
5,000
7.13
4.03
3
1
Lumbar_back
Dehydration
7.7
3.8
0
0
0
Unknown
1
6.3
60.7
1
Hydromorphone
40.8
3
16
null
145
87
0
0
1.68
108
0
1
141
0
1
0
86.2
0
0
II
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
0
0
Haemophilus_influenzae
0
Chronic_exchange
ACS
27.5
25
0
0
0
0
5,809
6.99
0
Deferiprone
0.8
0
0.23
0.89
1
27.3
27.3
14
1.5
0.466
0.44
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
20
60
69.9
55
6
10
13
Employed_part
1
0
0
1
0
0
HC-GEN-002
HC002-000043
HbSC
Female
Hispanic
US_Northeast
Middle
2
17.8
16.5
2_gene_del
0
10.13
4.21
92
12.2
9.8
333
560
5.03
36
0.72
5.7
245
142
4,294
8.55
3.68
0
0
Abdomen
Infection
16.3
5.4
1
0
0
Fat_embolism
1
1.5
55.7
1
Other
32.3
9
19
null
162.6
21
0
1
2.48
62
0
0
196
0
1
0
89.7
0
0
III
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
0
0
Streptococcus_pneumoniae
0
Episodic
ACS
46.3
33
1
0
0
0
9,241
26.73
0
Deferoxamine
0.71
0
0.186
0.51
1
30.7
30.7
13.4
1.5
0.287
0.58
0
0
0
0
0
0
0
0
1
MSD
NMA
1
1
0
0.93
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
1
Cardiac
222.1
0
19
27.5
76.8
50.7
15
8
7
Unemployed
1
1
1
0
1
1
HC-GEN-002
HC002-000044
HbSS
Female
Hispanic
US_South
High
1.3
20.9
4
No_deletion
1
7.14
1.76
91.1
10.3
14.5
506
222
4.91
32
0.4
3.8
146
152
1,733
7.42
4.86
6
0
Lumbar_back
Unknown
3.2
8.4
1
1
0
Hypoventilation
0
5
66.6
1
Hydromorphone
60.7
2
26
null
177.7
310
0
0
1.81
21
0
0
82
0
1
0
96.2
0
0
II
0
0
NPSR
0
0
0
0
0
0
Autoinfarction
1
0
Salmonella_sp
0
Episodic
Stroke_treatment
54.2
62
1
3
0
0
701
40
0
Deferoxamine
0.53
0
0.222
0.89
1
21.6
21.6
15.3
7.76
0.452
0.78
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
1
Lovotibeglogene_autotemcel
10,000,000
35.8
18.9
0
0.737
Minimal
0
null
0
1
18
20
56.8
70.6
0
9
6
Unemployed
1
1
0
0
0
0
HC-GEN-002
HC002-000045
HbSC
Male
Black_non_Hispanic
US_Northeast
High
1.11
15.3
13.6
No_deletion
0
10.27
8.08
82.1
17.1
9.6
535
997
10.76
31
0.77
5.9
392
34
4,613
6.14
3.78
4
1
Arms
Infection
3.2
8.2
0
0
0
Hypoventilation
1
5.6
63
0
Hydromorphone
0
0
14
null
80.3
19
0
0
2.18
82
0
0
121
0
1
0
95.5
0
0
II
0
0
null
0
0
0
0
0
0
Autoinfarction
1
0
Streptococcus_pneumoniae
0
Chronic_simple
Pre_op
28.1
33
0
0
0
0
4,274
23.14
0
Deferasirox
0.81
0
0.178
0.58
1
11.3
11.3
17.6
3.29
0.565
0.75
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Other
0
0
0
0
0
Complete
0
null
0
1
7
37.1
73
52.7
8
6
6
Unemployed
0
1
1
1
1
0
HC-GEN-002
HC002-000046
HbSC
Male
Black_non_Hispanic
US_Northeast
Low
0.99
14.7
15.3
No_deletion
0
13.15
4.84
63.3
6.3
10.5
418
652
11.58
54
1.13
9.9
127
51
2,911
34.2
3.08
0
0
Bilateral_legs
Stress
1.8
5.3
0
0
0
Unknown
1
3.8
69.5
0
Oxycodone
0
5
35
Hyperfiltration
86.6
222
0
0
2.35
66
0
0
87
0
1
0
87.8
0
0
II
0
1
NPSR
0
1
0
0
0
0
Normal
0
0
Staphylococcus_aureus
0
null
ACS
45.5
81
1
1
0
0
5,987
40
0
Deferasirox
0.5
0
0.236
0.54
0
0
0
0
16.62
0
0
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
7
24.4
48.2
60.4
9
14
15
Disability
1
1
1
0
0
0
HC-GEN-002
HC002-000047
HbSS
Male
Black_non_Hispanic
US_South
Middle
0.39
11.1
1.7
No_deletion
0
10.14
4.48
73.2
18.6
14.1
322
321
9.75
40
0.66
5.5
375
54
2,953
3.32
4.14
9
1
Lumbar_back
Infection
5.7
8.2
1
1
1
Hypoventilation
1
4.1
82.3
1
Hydromorphone
106.8
8
44
Hyperfiltration
83.8
16
0
0
2.86
34
0
0
181
0
1
0
83.6
0
0
I
0
0
NPSR
0
0
1
1
0
0
Normal
1
1
Salmonella_sp
0
null
Stroke_prevention
52.4
49
1
3
1
0
672
10.99
0
Deferasirox
0.62
0
0.246
0.82
1
17.8
17.8
8.9
4.32
0.362
0.45
0
1
0.287
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
1
Lovotibeglogene_autotemcel
10,000,000
64.7
37
0
0.914
Partial
0
null
0
1
17
38.5
51.4
52.2
1
4
19
Employed_full
1
1
1
1
0
0
HC-GEN-002
HC002-000048
HbSS
Male
Hispanic
Europe
Middle
2
23.9
11.5
No_deletion
0
8.7
4.81
88.1
11.9
13.4
452
254
3.08
103
1.33
5.6
341
101
2,479
15.24
4.36
1
0
Bilateral_legs
Infection
7.4
9.6
1
0
0
Infection
0
4.9
66.4
0
Hydromorphone
0
0
34
null
74.4
88
0
0
1.6
28
1
0
190
0
1
0
94.1
0
1
I
0
1
NPSR
1
0
1
1
0
0
Surgical_splenectomy
0
0
Haemophilus_influenzae
0
Episodic
Stroke_prevention
47.4
48
0
0
0
0
26,668
13.04
0
Deferasirox
0.36
0
0.211
0.89
1
24.2
24.2
21.5
5.45
0.434
0.57
0
0
0
0
0
0
0
0
0
UCB
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Partial
0
null
0
0
7
43.4
50.3
77.9
10
14
16
Employed_full
0
0
0
1
0
0
HC-GEN-002
HC002-000049
HbSC
Female
African_born
US_Northeast
Low
1.22
16.8
11.9
1_gene_del
0
10.46
7.66
69.6
13.3
14.1
392
506
9.31
74
1.31
5.3
210
884
4,762
5.47
3.33
0
0
Lumbar_back
Unknown
4.3
7.1
0
0
0
Infection
0
1.6
55.7
0
Oxycodone
0
4
25
null
74.9
785
0
0
2.04
64
1
0
217
0
0
0
91.1
1
1
III
0
1
null
0
0
1
0
0
0
Surgical_splenectomy
1
0
Streptococcus_pneumoniae
1
Episodic
Stroke_treatment
50.2
79
1
3
1
0
10,824
2.54
0
Deferasirox
0.64
0
0.185
0.71
1
23.8
23.8
19.6
5.6
0.619
0.63
0
0
0
1
0.224
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
15
24.8
38.2
67.4
8
8
13
Employed_part
0
1
1
1
1
0
HC-GEN-002
HC002-000050
HbSS
Male
Black_non_Hispanic
US_South
Low
0.27
22
6.8
No_deletion
0
9.38
4.58
79.4
10.4
4
391
356
7.8
75
0.54
8.6
385
48
2,441
1.85
4.33
5
1
Abdomen
Dehydration
10.8
5.4
1
0
0
Hypoventilation
1
8
67.1
1
Hydromorphone
112.1
3
13
null
92
1,531
0
1
2.21
23
0
1
161
0
0
0
76.5
0
1
I
0
0
PSR_Sea_Fan
0
1
0
0
0
0
Autoinfarction
1
0
Streptococcus_pneumoniae
0
Chronic_simple
Stroke_treatment
25.9
65
0
0
0
1
10,922
9.25
0
Deferasirox
0.56
0
0.243
0.56
1
10.7
10.7
5
6.05
0.192
0.92
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
17
20
53
51.1
12
7
11
Unemployed
1
1
1
1
0
1
HC-GEN-002
HC002-000051
HbSS
Male
Hispanic
US_South
High
2
25.3
17.7
2_gene_del
0
9.78
9.87
84.7
5.3
16.2
359
468
2.62
58
1.64
6.4
74
46
2,104
5.2
3.99
1
0
Lumbar_back
Unknown
6.6
8.8
0
0
0
Infection
1
2.6
83.4
1
Oxycodone
72.7
0
10
Hyperfiltration
140.6
13
0
0
2.1
59
1
0
172
0
1
0
66
1
0
IV
1
0
null
0
0
1
0
0
0
Normal
1
0
Haemophilus_influenzae
0
Episodic
Stroke_treatment
44.1
80
1
0
1
0
5,103
2.13
1
Deferasirox
0.54
0
0.282
0.5
0
0
0
0
9.1
0
0
0
0
0
0
0
0
0
0
0
MUD
Myeloablative
0
0
0
0
0
bb2121
0
0
0
0
0
null
0
null
0
1
30
45.1
60.8
62.1
9
6
9
Disability
1
0
0
1
0
1
HC-GEN-002
HC002-000052
HbSS
Male
Black_non_Hispanic
US_Northeast
Low
2
25.7
4.1
1_gene_del
0
7.04
5.42
93.8
11.4
12.9
531
564
2.15
38
0.76
5.9
279
39
5,000
3.91
4.95
4
0
Abdomen
Cold_exposure
16.8
10
0
0
0
Fat_embolism
0
6.6
69.2
0
Morphine
0
1
15
Microalbuminuria
84.9
39
0
0
3.13
54
1
0
157
1
0
0
76.5
0
0
I
0
1
null
0
1
1
1
1
15.2
Autoinfarction
1
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
34.9
71
1
0
0
0
1,146
4.3
0
Deferoxamine
0.6
0
0.297
0.53
0
0
0
0
15.39
0
0
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
29
51.9
57.4
62.3
7
7
5
Disability
0
1
0
1
1
1
HC-GEN-002
HC002-000053
HbSC
Male
Black_non_Hispanic
US_Northeast
Middle
1.68
15.1
7.9
No_deletion
0
10.39
5.01
77.4
13.3
18.4
450
313
10.17
57
0.76
8.9
169
229
3,329
9.6
3.35
0
1
Lumbar_back
Infection
4.2
5.6
0
0
0
Infection
1
5.2
72.4
1
Hydromorphone
216
7
19
null
146.9
48
0
0
2.03
61
0
0
163
0
1
0
85.4
0
0
III
0
1
NPSR
0
0
1
0
0
0
Normal
1
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
25.9
130
0
0
0
0
806
30.88
0
Deferasirox
0.93
0
0.236
0.51
1
21.4
21.4
17.8
6.48
0.654
0.64
0
0
0
0
0
0
0
0
1
MUD
RIC
1
0
0
0.899
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Minimal
0
null
0
1
18
31.9
46.9
63.2
11
7
17
Unemployed
1
1
0
1
0
1
HC-GEN-002
HC002-000054
HbSC
Female
Black_non_Hispanic
US_Northeast
Middle
2
17.7
17.1
1_gene_del
1
7.95
3.12
76.9
14.7
8.7
544
244
5.53
39
0.78
7.7
2,416
117
3,382
6.51
3.92
4
0
Lumbar_back
Unknown
3.4
7.3
0
0
0
Infection
1
1.3
44.5
0
Morphine
0
5
11
null
157.9
1,348
0
0
1.5
92
1
0
142
0
0
0
121.7
0
0
IV
0
0
VH_RD
0
1
1
1
0
0
Normal
1
0
E_coli
0
null
Stroke_prevention
40
95
0
0
0
0
2,918
3.04
0
Deferasirox
0.65
0
0.231
0.81
1
15.4
10.8
4.4
3.88
0.554
0.8
1
0
0
0
0
1
1.35
1
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
null
0
null
0
1
46
48.7
35.3
55.2
15
14
17
Disability
1
0
0
0
0
0
HC-GEN-002
HC002-000055
HbSC
Male
Black_non_Hispanic
US_South
Low
0.77
5.6
4.6
No_deletion
0
12.07
5.07
81.6
11.2
5.7
580
480
3.18
86
0.77
5.4
277
50
5,000
2.67
3.14
0
1
Lumbar_back
Infection
1.9
9.2
0
0
0
Unknown
1
2.3
66.3
1
Hydromorphone
9
13
10
null
120
83
0
0
2.02
110
0
0
165
0
1
0
82.6
0
1
I
0
0
null
0
0
0
0
0
0
Normal
0
0
Streptococcus_pneumoniae
0
Episodic
ACS
46.4
99
1
1
0
0
7,004
3.36
1
Deferasirox
0.54
0
0.167
0.79
1
25.9
25.9
6.6
6.06
0.697
0.61
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
24
52.7
52.1
54.6
16
2
9
Unemployed
0
1
1
1
0
1
HC-GEN-002
HC002-000056
HbSC
Male
Hispanic
Europe
Middle
1.19
20.9
16.6
No_deletion
0
13.39
12.66
84.8
3.2
11
475
317
5.45
53
0.4
5
152
85
2,608
19.63
2.21
2
1
Chest
Unknown
7
7.4
0
0
0
Unknown
1
2.4
59.1
0
Morphine
0
2
50
Hyperfiltration
153
327
0
0
2.05
38
1
0
226
0
1
0
84.6
0
0
II
0
0
null
0
1
1
0
0
0
Surgical_splenectomy
0
0
Haemophilus_influenzae
0
Chronic_simple
ACS
29.3
50
0
0
0
0
5,911
2.84
0
Deferasirox
0.88
0
0.273
0.5
1
12
12
15.7
1.5
0.555
0.6
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Other
0
0
0
0
0
Partial
0
null
0
1
5
42.5
50.6
78.3
12
6
4
Employed_full
1
1
1
0
1
1
HC-GEN-002
HC002-000057
HbSS
Male
Middle_Eastern
Other
High
2
31
2.5
1_gene_del
0
8.31
3.77
80.8
5.8
10.2
359
431
7.26
50
0.68
8.5
81
55
2,881
14.47
4.67
0
0
Bilateral_legs
Unknown
6.7
4.1
0
0
0
Hypoventilation
0
3.3
54.5
0
Morphine
0
3
27
null
62.4
129
0
0
2
134
0
0
149
1
0
1
75.1
0
0
III
0
0
VH_RD
0
0
0
0
0
0
Normal
1
0
Streptococcus_pneumoniae
0
Chronic_simple
Stroke_prevention
28.6
36
0
0
0
1
21,355
35.74
0
Deferasirox
0.75
0
0.127
0.5
1
23.4
23.4
29.2
6.54
0.312
0.82
0
1
0.198
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Other
0
0
0
0
0
null
0
null
0
1
18
36
79.3
52.1
13
3
20
Unemployed
1
1
1
0
0
0
HC-GEN-002
HC002-000058
HbSS
Male
Black_non_Hispanic
US_Northeast
Middle
0.72
7.6
10.3
No_deletion
0
5.22
7.46
90.4
20.2
13
545
220
5.8
47
0.4
6.8
695
163
4,242
21.52
4.89
2
0
Abdomen
Infection
1.9
8
0
0
0
Infection
0
3.4
61.8
1
Oxycodone
23
4
31
Microalbuminuria
90.5
21
0
0
1.81
56
0
0
141
0
1
0
91.4
0
0
II
0
0
VH_RD
0
0
0
0
1
16.5
Normal
1
0
Haemophilus_influenzae
0
Episodic
Stroke_treatment
57.1
32
0
0
0
1
2,312
40
0
Deferoxamine
0.65
0
0.268
0.84
1
18.8
13.1
12.2
2.6
0.558
0.74
1
0
0
1
0.433
1
0.93
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
24
41.3
60.3
50.5
6
5
18
Unemployed
1
1
1
1
0
0
HC-GEN-002
HC002-000059
HbSS
Female
Black_non_Hispanic
US_Midwest
Low
1.65
34.8
2.4
2_gene_del
0
9.05
2.61
75.6
7.6
14.2
476
360
2.78
90
1.67
4.5
185
1,780
1,685
7.31
4.53
2
1
Bilateral_legs
Infection
5.3
5.4
0
0
0
Unknown
1
7.5
63.2
1
Morphine
73.6
4
22
Microalbuminuria
116.6
10
0
0
1.57
271
1
0
148
0
1
0
87.4
0
1
III
0
1
null
0
0
0
0
0
0
Normal
1
1
Salmonella_sp
0
null
Splenic_sequestration
55.1
39
0
0
0
0
2,190
15.26
0
Deferoxamine
0.39
0
0.221
0.82
1
24.6
24.6
20.2
1.59
0.567
0.7
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
1
31
43.3
77.8
41.9
8
7
14
Unemployed
1
1
0
1
0
0
HC-GEN-002
HC002-000060
HbSS
Male
Hispanic
Africa
Low
1.57
38.3
13.9
No_deletion
0
6.93
4.89
83
17.7
10.7
732
557
15
25
1.64
4.1
130
211
4,067
5.88
5
3
1
Lumbar_back
Unknown
5.3
4.9
1
1
1
Hypoventilation
0
3.4
55.1
0
Oxycodone
0
2
32
null
117.8
43
0
1
3.11
42
1
0
134
0
1
0
76.3
1
0
I
0
0
PSR_Sea_Fan
0
0
1
0
0
0
Autoinfarction
1
0
Haemophilus_influenzae
0
Episodic
Stroke_prevention
58.6
32
0
0
0
0
3,282
40
0
Deferasirox
0.67
0
0.123
0.84
0
0
0
0
9.71
0
0
0
0
0
1
0.639
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
1
Renal_failure
540.4
1
18
12.1
53.3
59.2
11
13
14
Disability
0
0
0
1
0
0
HC-GEN-002
HC002-000061
HbSC
Male
Middle_Eastern
Other
High
0.65
25.1
16
No_deletion
0
9.57
7.16
85.6
8.3
10.3
457
530
10
93
1.13
5.1
320
111
2,495
10.62
3.57
1
1
Chest
Dehydration
3
4.1
0
0
0
Unknown
1
2.5
64.1
0
Hydromorphone
0
4
21
Hyperfiltration
160
1,451
0
1
2.38
20
0
0
150
0
0
0
79.9
0
0
IV
0
1
PSR_Sea_Fan
0
0
0
0
0
0
Autoinfarction
1
0
Staphylococcus_aureus
0
Episodic
Stroke_prevention
53.2
62
0
0
0
0
912
5.13
0
Deferasirox
0.48
0
0.233
0.78
0
0
0
0
5.8
0
0
0
0
0
1
0.463
0
0
0
0
Haplo
NMA
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
21
33.8
70.3
47.8
10
9
11
Employed_full
0
1
0
1
1
0
HC-GEN-002
HC002-000062
HbSS
Male
Black_non_Hispanic
US_Midwest
Low
2
34.9
17.1
No_deletion
0
9.08
6.01
78.8
11.3
12.6
504
283
5.12
41
0.66
4.9
411
62
5,000
3.81
4.23
1
1
Bilateral_legs
Stress
3.4
9.3
0
0
0
Infection
0
2.2
60.1
1
Other
17.7
1
21
CKD3+
75
123
0
0
2.02
130
0
0
133
1
1
0
67.2
1
0
II
0
0
null
0
0
1
0
1
21.2
Normal
1
0
Streptococcus_pneumoniae
0
Chronic_simple
Stroke_prevention
25.7
84
0
0
0
0
16,981
40
0
Deferoxamine
0.48
0
0.214
0.82
1
30.2
30.2
16.3
8.31
0.131
0.61
0
0
0
1
0.516
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Partial
0
null
0
0
30
21.6
62.6
85
12
3
13
Employed_full
1
1
0
0
0
0
HC-GEN-002
HC002-000063
HbSS
Female
Black_non_Hispanic
Africa
Middle
2
22.1
19.6
No_deletion
0
8.56
2.92
88.7
14.5
10.2
455
238
5.22
25
0.45
3.7
406
32
4,785
6.71
4.5
1
0
Chest
Dehydration
3.7
5.7
0
0
0
Infection
1
6.4
69.7
1
Hydromorphone
88.8
3
32
null
91.2
319
0
0
2.95
94
1
1
186
0
1
0
73.9
0
1
II
0
0
PSR_Sea_Fan
0
0
1
1
0
0
Autoinfarction
1
0
Streptococcus_pneumoniae
0
Chronic_exchange
Stroke_prevention
34.3
82
0
0
0
0
2,472
8.04
1
Deferasirox
0.77
0
0.202
0.74
1
26.2
26.2
7.5
3.85
0.602
0.7
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
35
25.6
52.1
47
16
6
21
Unemployed
1
0
0
1
0
0
HC-GEN-002
HC002-000064
HbSC
Female
Black_non_Hispanic
Africa
Low
1.99
17.1
13.8
No_deletion
0
9.82
5.6
83.2
8.7
10
408
406
7.24
33
0.53
5.2
249
253
4,480
5.26
3.51
1
0
Bilateral_legs
Dehydration
7
7.8
1
0
0
Hypoventilation
0
1.7
64.5
0
Oxycodone
0
3
15
Hyperfiltration
107
16
0
0
1.75
174
0
0
182
0
0
0
89.2
0
0
II
0
1
null
0
0
1
1
0
0
Normal
1
0
Streptococcus_pneumoniae
0
Episodic
Stroke_prevention
58.9
62
0
0
0
0
4,300
32.06
0
Deferasirox
0.42
0
0.209
0.77
1
26.1
26.1
10.3
4
0.47
0.63
0
0
0
0
0
0
0
0
1
MSD
NMA
1
0
0
0.918
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
0
18
38.2
62.3
53.5
8
12
13
Employed_full
1
0
1
0
1
0
HC-GEN-002
HC002-000065
HbSS
Female
Black_non_Hispanic
Europe
Middle
0.5
9.1
15.6
No_deletion
0
7.29
6.42
88.3
18.4
14.1
389
519
3.44
23
1.96
5.4
278
240
1,630
1.88
4.79
6
1
Chest
Cold_exposure
3.8
8.2
0
0
0
Unknown
0
6.9
66.1
1
Morphine
128.4
5
32
Hyperfiltration
91.8
61
0
0
2.34
85
1
0
227
0
1
0
85.7
0
0
II
0
0
PSR_Sea_Fan
0
0
1
1
0
0
Normal
1
0
Haemophilus_influenzae
0
null
Splenic_sequestration
40
26
1
0
0
0
7,971
16
0
Deferasirox
0.9
0
0.219
0.68
0
0
0
0
15.37
0
0
0
0
0
1
0.191
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
20
33.6
58.3
85
2
5
22
Employed_full
0
0
1
1
0
0
HC-GEN-002
HC002-000066
HbSS
Female
Other
US_Northeast
High
0.33
8.5
10.6
No_deletion
0
8.38
5
83.6
12.3
14.8
455
484
7.11
58
0.52
6.1
295
76
3,458
6.7
4.63
8
0
Lumbar_back
Stress
4.1
7.5
0
0
0
Infection
0
7.2
72.8
0
Hydromorphone
0
2
13
null
73.5
229
0
0
1.6
434
1
0
139
0
1
0
78
0
0
II
0
0
null
0
0
0
0
0
0
Normal
1
0
Streptococcus_pneumoniae
0
Episodic
Pre_op
50.3
54
0
0
0
0
1,422
2.42
0
Deferiprone
0.32
0
0.219
0.86
1
11.7
11.7
16.8
3.16
0.34
0.67
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
14
34.9
57.3
73.9
5
8
6
Disability
0
1
0
1
0
0
HC-GEN-002
HC002-000067
HbSS
Female
Black_non_Hispanic
US_South
Middle
2
34.9
18.3
No_deletion
0
7.63
3.79
85
13.8
14.3
483
320
3.11
30
0.4
9.3
320
409
2,021
4.25
4.72
7
0
Arms
Stress
5.5
7.7
0
0
0
Infection
1
3.2
68.1
1
Morphine
152.2
7
15
Microalbuminuria
93.3
24
0
0
2.4
57
0
0
152
0
0
0
109.5
0
0
I
0
0
NPSR
0
0
1
0
0
0
Normal
1
0
Salmonella_sp
0
Chronic_exchange
ACS
26.9
81
1
2
0
0
4,416
6.79
1
Deferasirox
0.75
0
0.161
0.86
1
22.5
22.5
11.1
3.93
0.416
0.77
0
0
0
0
0
0
0
0
0
MUD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
18
33.3
43.8
41.9
10
9
12
Disability
1
1
1
0
0
1
HC-GEN-002
HC002-000068
HbSS
Male
Hispanic
US_South
High
2
41.7
13.2
No_deletion
1
6.65
7.4
76.9
10.9
10.5
559
461
5.84
48
1.24
6.4
344
124
3,574
4.98
4.81
1
1
Lumbar_back
Cold_exposure
8.8
7.9
0
0
0
Hypoventilation
0
5.9
61.9
0
Other
0
2
11
null
101.4
83
0
0
1.65
154
1
0
150
0
1
0
97.9
0
1
III
0
0
PSR_Sea_Fan
0
1
0
0
1
4.3
Surgical_splenectomy
0
0
Salmonella_sp
0
null
Splenic_sequestration
40.8
34
1
2
0
0
3,227
19.51
0
Deferasirox
0.71
0
0.236
0.76
1
23.6
23.6
12.5
3.57
0.556
0.64
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
0
33
32.7
80.1
62.1
7
6
12
Employed_part
1
1
1
0
0
0
HC-GEN-002
HC002-000069
HbSS
Male
Black_non_Hispanic
US_Northeast
Low
2
24.5
17.8
1_gene_del
0
7.73
3.91
77
14.6
4.6
457
793
3.37
70
1.57
6.5
587
264
1,144
8.09
5.11
4
0
Chest
Infection
2.6
7.4
1
1
0
Unknown
0
4.4
39
1
Oxycodone
208.5
12
28
null
160.7
31
0
0
2.29
44
0
1
148
1
0
0
77.2
0
0
II
0
0
null
0
0
0
0
1
15.7
Autoinfarction
1
0
Haemophilus_influenzae
0
Chronic_simple
Stroke_prevention
34.9
57
1
3
0
1
9,516
2.59
1
Deferoxamine
0.48
0
0.205
0.87
1
25.3
25.3
29.6
7.74
0.517
0.48
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
16
34.3
66
64.6
3
3
13
Employed_full
0
1
0
1
0
1
HC-GEN-002
HC002-000070
HbSS
Female
Black_non_Hispanic
US_Northeast
Middle
2
38
5.5
No_deletion
1
8.68
6.74
91.8
18.3
10.6
364
442
3.46
34
1.7
7.6
256
163
1,685
16.74
4.41
3
0
Lumbar_back
Infection
6.1
5.8
0
0
0
Unknown
1
1.8
67.7
0
Oxycodone
0
2
21
Hyperfiltration
74.3
243
0
0
2.88
99
0
0
185
1
1
0
60.4
1
0
II
0
0
PSR_Sea_Fan
0
0
1
1
0
0
Normal
1
1
Salmonella_sp
0
Chronic_simple
Stroke_prevention
33.1
66
0
0
0
0
3,285
22.12
0
Deferasirox
0.41
0
0.283
0.5
1
21.5
21.5
11.9
4.34
0.44
0.62
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Partial
0
null
0
1
48
50.3
49.1
51.1
9
8
30
Disability
1
1
0
1
0
0
HC-GEN-002
HC002-000071
HbSS
Male
African_born
US_Northeast
High
2
27.3
10.4
1_gene_del
0
7.95
6.9
87.1
11.5
8.7
381
193
13.78
40
1.25
6.4
127
102
5,000
3.07
4.33
6
0
Chest
Dehydration
2.6
5.7
1
0
0
Unknown
1
4.7
52
1
Morphine
10.6
2
20
Macroalbuminuria
138.5
145
0
1
2.29
115
0
1
80
1
1
0
71.6
0
0
IV
0
0
null
0
1
1
1
0
0
Surgical_splenectomy
1
0
E_coli
0
Chronic_simple
Stroke_prevention
29.5
54
0
0
0
0
180
3.99
0
Deferasirox
0.66
0
0.254
0.71
0
0
0
0
6.26
0
0
0
0
0
0
0
0
0
0
0
Haplo
NMA
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Minimal
0
null
0
0
31
41.2
64.1
68.7
5
16
17
Disability
1
1
0
1
1
0
HC-GEN-002
HC002-000072
HbSS
Female
Black_non_Hispanic
US_Midwest
Middle
2
33.6
14.9
No_deletion
0
6.22
5.52
73.8
18.9
10.6
261
442
6.23
27
1.35
7.4
218
47
4,379
4.62
5.01
6
0
Abdomen
Infection
3.2
7
0
0
0
Hypoventilation
0
5.7
61.1
0
Morphine
0
5
5
null
154.5
204
0
0
1.5
130
1
0
158
0
0
0
90.4
0
0
IV
0
0
null
0
0
0
0
0
0
Autoinfarction
1
0
E_coli
0
Chronic_exchange
ACS
31.7
39
0
0
0
0
1,164
28.24
0
Deferoxamine
0.69
0
0.259
0.78
1
16.2
16.2
14.1
2.92
0.438
0.79
0
0
0
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
33
25.1
57
46.3
12
5
13
Employed_part
0
1
1
1
1
0
HC-GEN-002
HC002-000073
HbSC
Male
Black_non_Hispanic
US_Midwest
Low
2
26.4
4.9
2_gene_del
0
11.88
9.4
83.4
9.6
9
619
1,012
6.71
38
0.76
7.2
447
105
3,051
3.28
3.37
0
1
Abdomen
Infection
8.6
7
0
0
0
Unknown
0
5.5
66.1
1
Hydromorphone
120
12
25
Hyperfiltration
92.1
256
0
0
2.11
124
0
1
220
0
0
0
91.2
0
0
III
0
0
PSR_Sea_Fan
0
1
1
1
0
0
Normal
0
0
Salmonella_sp
0
null
Splenic_sequestration
42.9
39
0
0
0
0
625
4.22
0
Deferiprone
0.27
0
0.294
0.81
1
34
23.8
15.7
2.15
0.364
0.58
1
1
0.328
0
0
0
0
0
1
Haplo
Myeloablative
1
0
0
0.874
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
47
30.6
73.7
43.2
17
5
14
Disability
0
1
1
1
0
1
HC-GEN-002
HC002-000074
HbSS
Female
Middle_Eastern
Africa
High
1.94
25.9
5
2_gene_del
0
4.5
12.19
63
15.1
10.9
355
226
2.21
125
0.4
7
59
282
2,311
3.11
4.73
5
1
Bilateral_legs
Cold_exposure
4.5
8
1
0
0
Fat_embolism
0
4.4
76.7
0
Morphine
0
3
32
null
119.1
68
0
0
2.29
20
0
1
195
0
0
0
87.2
0
0
I
0
0
PSR_Sea_Fan
0
0
1
1
0
0
Surgical_splenectomy
1
0
E_coli
0
null
Pre_op
58.9
71
0
0
0
0
27,000
25.62
0
Deferasirox
0.67
0
0.249
0.6
0
0
0
0
8.12
0
0
0
0
0
0
0
0
0
0
1
MSD
Myeloablative
1
0
0
0.974
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
46
41.4
57.5
72.4
15
10
21
Employed_full
0
0
1
1
1
1
HC-GEN-002
HC002-000075
HbSS
Female
African_born
US_South
Low
0.32
19
19.6
No_deletion
0
7.58
7.1
77.4
14
7.9
536
409
4.49
61
0.75
10.9
59
73
2,117
3.76
4.59
2
0
Bilateral_legs
Dehydration
4.5
9.2
0
0
0
Infection
1
1.1
82.3
0
Hydromorphone
0
1
39
Hyperfiltration
130.2
300
0
0
2.46
63
1
0
190
0
1
0
71.4
0
0
IV
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Autoinfarction
1
0
Staphylococcus_aureus
0
Chronic_exchange
Stroke_treatment
27.2
40
1
0
0
0
15,426
37.21
0
Deferoxamine
0.61
0
0.214
0.87
1
16.5
16.5
0.6
4.66
0.581
0.8
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
0
19
31.9
59.8
68.2
4
17
22
Employed_part
1
1
1
1
0
0
HC-GEN-002
HC002-000076
HbSS
Female
Black_non_Hispanic
US_South
Middle
0.57
26.3
9.3
No_deletion
0
7.33
4.04
89.7
7.7
7.2
453
364
7.62
40
1.01
8.2
510
189
4,024
5.17
4.8
9
1
Abdomen
Dehydration
8.6
7.8
0
0
0
Hypoventilation
0
1.2
51.9
0
Oxycodone
0
2
43
Hyperfiltration
124.4
44
0
0
2.69
42
1
0
174
1
0
0
80.4
1
0
I
0
1
PSR_Sea_Fan
0
0
1
0
0
0
Autoinfarction
1
1
Streptococcus_pneumoniae
0
Chronic_simple
Stroke_prevention
32.2
27
0
0
0
0
306
13.9
0
Deferasirox
0.83
0
0.12
0.95
0
0
0
0
8.76
0
0
0
0
0
0
0
0
0
0
1
Haplo
Myeloablative
1
1
0
0.869
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
0
23
39.7
54.1
82.2
6
4
11
Employed_full
1
1
1
1
0
0
HC-GEN-002
HC002-000077
HbSS
Female
Black_non_Hispanic
Europe
High
1.06
16.5
4.5
No_deletion
0
8.41
9.14
81
12.9
14.7
456
421
6.67
35
0.69
5.2
826
41
3,066
9.67
4.29
4
0
Bilateral_legs
Stress
5.7
5.7
0
0
0
Hypoventilation
1
3.8
47.5
1
Oxycodone
23.2
0
20
Hyperfiltration
112.9
191
0
0
2.71
49
0
0
116
0
0
0
87.8
0
0
II
0
0
null
0
0
1
1
0
0
Normal
1
0
Salmonella_sp
0
null
ACS
50.5
55
0
0
0
0
1,071
15.18
0
Deferoxamine
0.65
0
0.23
0.75
1
15.3
15.3
13.4
2.6
0.738
0.59
0
1
0.05
0
0
0
0
0
1
Haplo
NMA
1
0
1
0.908
1
Lovotibeglogene_autotemcel
10,000,000
46.7
30.8
0
0.653
Complete
0
null
0
1
21
34.5
65
60.7
1
2
12
Disability
1
0
1
0
0
1
HC-GEN-002
HC002-000078
HbSC
Female
Black_non_Hispanic
Africa
Low
0.41
8.8
7.3
No_deletion
0
11.29
8.41
82.9
12
8.1
406
440
2.06
44
0.68
7.4
89
265
5,000
7.82
3.05
0
0
Bilateral_legs
Dehydration
5.2
3.3
0
0
0
Fat_embolism
1
5.7
65.6
1
Morphine
82.5
5
40
CKD3+
86.2
10
0
0
2.05
53
0
1
110
0
0
0
88.9
0
0
IV
0
1
null
0
0
1
0
0
0
Normal
0
1
Salmonella_sp
0
Episodic
ACS
54.7
60
0
0
0
0
709
40
1
Deferoxamine
0.69
0
0.289
0.83
1
22.1
22.1
17.2
4.03
0.402
0.9
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Other
0
0
0
0
0
Partial
0
null
0
1
27
37.2
59.4
79.1
15
10
17
Employed_part
1
1
0
1
1
0
HC-GEN-002
HC002-000079
HbSS
Female
Black_non_Hispanic
Other
Low
0.82
24.2
8.6
No_deletion
0
9.78
7.57
57.9
8.6
11
325
674
6.71
47
0.46
5.6
265
166
3,320
2.6
4.33
0
1
Lumbar_back
Unknown
3.9
5.8
1
0
0
Infection
0
2.5
64.7
1
Oxycodone
48.1
5
8
Microalbuminuria
133.2
37
0
0
1.84
146
1
0
110
0
0
0
93.1
0
0
I
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Surgical_splenectomy
1
0
Staphylococcus_aureus
0
Chronic_exchange
Stroke_treatment
33.2
35
0
0
0
0
4,129
7.51
0
Deferoxamine
0.31
0
0.256
0.95
1
22.7
22.7
14.6
1.88
0.23
0.85
0
0
0
1
0.427
0
0
0
1
MSD
Myeloablative
1
0
0
0.938
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
28
47.5
72.7
55.7
10
10
2
Employed_full
1
1
0
1
0
0
HC-GEN-002
HC002-000080
HbSC
Male
Black_non_Hispanic
Africa
Low
1.54
10.7
12.8
1_gene_del
0
9.5
2.14
78.9
13.4
13.9
304
419
7.27
38
0.45
7.5
178
37
3,749
17.04
3.82
2
1
Bilateral_legs
Infection
4.6
4.8
0
0
0
Unknown
0
4.7
48.8
1
Hydromorphone
25.3
8
29
null
96.9
1,449
0
0
1.65
78
0
1
94
0
0
0
91.2
0
0
I
0
0
PSR_Sea_Fan
0
0
1
0
0
0
Autoinfarction
0
0
Staphylococcus_aureus
0
Chronic_simple
Stroke_prevention
33.2
39
0
0
0
0
1,137
9.64
0
Deferasirox
0.76
0
0.2
0.7
1
19.5
19.5
14.6
3.31
0.453
0.86
0
0
0
1
0.056
0
0
0
0
UCB
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
11
38.9
63
74.5
17
3
5
Employed_full
1
1
1
1
0
1
HC-GEN-002
HC002-000081
HbSC
Male
Black_non_Hispanic
Africa
Low
0.8
21.3
18.5
2_gene_del
0
11.32
8.52
84.7
12.6
13.7
627
717
11.49
55
1.86
4.7
199
97
1,818
12.88
3.28
1
0
Bilateral_legs
Dehydration
3.8
5.9
1
1
0
Unknown
0
3.3
61.8
0
Hydromorphone
0
1
9
CKD3+
111
187
0
0
1.88
44
0
0
178
0
0
0
92.9
1
0
II
0
0
null
0
0
0
0
0
0
Autoinfarction
0
0
Haemophilus_influenzae
0
Chronic_exchange
Stroke_prevention
32.1
82
1
1
0
0
2,430
31.21
1
Deferasirox
0.43
0
0.222
0.95
1
21.3
21.3
18.1
1.6
0.396
0.84
0
0
0
1
0.367
0
0
0
0
MUD
Myeloablative
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
1
25
54.4
84.1
82.4
12
6
13
Employed_full
0
1
1
1
0
1
HC-GEN-002
HC002-000082
HbSS
Female
Middle_Eastern
US_Northeast
Low
0.93
6.4
19.7
No_deletion
0
8.47
5.28
85.7
11.7
13.4
434
383
4.36
31
1.89
5.1
312
308
3,040
2.94
4.49
5
1
Chest
Unknown
3.1
7.6
1
0
0
Infection
1
3.2
68.6
0
Hydromorphone
0
1
22
null
116.2
187
0
0
2.29
21
1
0
199
0
1
0
79.2
0
0
II
0
0
null
0
0
1
1
0
0
Autoinfarction
1
0
Haemophilus_influenzae
0
Episodic
Stroke_prevention
52.2
47
0
0
0
0
715
25.09
0
Deferoxamine
0.62
0
0.198
0.62
0
0
0
0
11.37
0
0
0
0
0
1
0.614
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
1
Infection
272.6
1
25
28
58.8
51.8
7
2
12
Employed_full
1
0
1
1
1
0
HC-GEN-002
HC002-000083
HbSC
Male
Middle_Eastern
US_Northeast
Middle
2
26.5
13.4
1_gene_del
0
8.1
1.62
89.7
11.7
11.9
555
345
1.97
30
0.74
7.3
87
35
3,978
16.11
4.08
0
0
Lumbar_back
Cold_exposure
12.8
7.4
0
0
0
Unknown
1
4.2
48.5
0
Hydromorphone
0
0
9
Microalbuminuria
140
33
0
0
1.56
227
1
0
157
0
0
0
96.3
0
1
II
0
1
NPSR
1
0
1
1
1
2.8
Surgical_splenectomy
1
0
Haemophilus_influenzae
1
null
Stroke_treatment
57
67
1
5
0
0
5,225
12.9
0
Deferasirox
0.74
1
0.232
0.89
1
15.6
15.6
29.8
6.55
0.417
0.65
0
0
0
1
0.354
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
10
25.6
52.1
42.2
0
6
8
Employed_part
0
1
1
1
0
1
HC-GEN-002
HC002-000084
HbSS
Male
African_born
US_South
Low
1.8
18.1
14.3
No_deletion
0
10.86
1.29
80.3
11.6
13.2
586
299
3.68
52
0.85
8.3
101
42
3,022
7.86
4.18
3
0
Bilateral_legs
Unknown
13.1
10
0
0
0
Infection
0
5.6
51.1
1
Hydromorphone
29.6
8
21
Microalbuminuria
177.5
24
0
0
1.73
40
1
0
172
0
0
0
83.4
0
0
III
0
0
null
0
0
0
0
0
0
Normal
1
0
Salmonella_sp
1
Episodic
Stroke_prevention
42.3
48
0
0
0
0
513
4.88
0
Deferiprone
0.68
0
0.2
0.5
1
23.6
16.5
9.3
2.66
0.257
0.83
1
0
0
1
0.239
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
bb2121
0
0
0
0
0
Complete
0
null
0
0
21
38.7
52.8
64.3
11
6
23
Employed_full
1
1
0
1
0
1
HC-GEN-002
HC002-000085
HbSS
Female
Other
US_Midwest
Middle
1.25
12
7.1
2_gene_del
1
6.19
4.07
80.7
10.5
15.1
371
180
3.5
28
0.45
7.6
192
113
2,856
5.34
4.87
5
1
Abdomen
Infection
6.2
8.1
0
0
0
Infection
1
2.2
54.9
1
Oxycodone
28.5
0
51
Microalbuminuria
84.2
66
0
0
2.32
60
0
0
152
0
0
0
78.9
0
1
III
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
1
0
Salmonella_sp
0
Chronic_exchange
Stroke_prevention
29.5
40
0
0
0
0
27,000
40
0
Deferasirox
0.62
0
0.278
0.66
0
0
0
0
15.02
0
0
0
0
0
0
0
0
0
0
0
MSD
NMA
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
63
32.4
53.2
64.1
20
11
11
Disability
0
1
1
0
0
1
HC-GEN-002
HC002-000086
HbSS
Female
Hispanic
Other
Low
1.17
20.8
17.3
2_gene_del
0
8.79
1.63
71.3
12.6
12.3
471
457
8.74
60
1.02
8.1
218
1,026
4,287
8.06
4.74
3
1
Bilateral_legs
Infection
2.7
10
0
0
0
Infection
0
2.5
59.7
1
Oxycodone
25.6
2
33
null
111.8
83
0
1
1.99
369
0
0
163
0
0
0
81.3
0
0
IV
0
0
null
0
0
0
0
0
0
Normal
1
0
Salmonella_sp
0
null
Splenic_sequestration
57.6
41
0
0
0
0
17,027
4.77
0
Combination
0.51
0
0.225
0.91
0
0
0
0
11.96
0
0
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
7
35.9
52.2
60.2
13
12
13
Unemployed
1
0
1
0
0
0
HC-GEN-002
HC002-000087
HbSC
Male
Hispanic
US_Northeast
Low
2
20.3
5.1
1_gene_del
0
11.05
6.47
80.4
9.4
5.5
425
1,017
1.56
44
1.79
7.4
99
62
5,000
5.93
3.75
2
0
Abdomen
Stress
2.7
8.5
0
0
0
Fat_embolism
0
6.4
69.6
1
Morphine
203.9
5
21
Microalbuminuria
58
895
0
0
2.25
41
1
0
80
0
0
0
83.9
0
0
I
0
1
null
1
0
1
1
1
1
Normal
1
0
Staphylococcus_aureus
0
Episodic
Stroke_treatment
57.9
86
0
0
0
0
27,000
40
0
Deferasirox
0.38
0
0.23
0.5
0
0
0
0
15.17
0
0
0
0
0
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
39
38.5
75.1
72.5
8
7
4
Disability
0
0
0
1
1
0
HC-GEN-002
HC002-000088
HbSS
Male
Hispanic
US_Midwest
Low
1.15
31.8
3
2_gene_del
0
8.59
1.96
71.9
22.6
9.4
281
496
4.83
22
0.4
7.1
460
199
3,915
9.36
4.79
5
0
Lumbar_back
Infection
5.2
9.2
0
0
0
Infection
0
1.6
58.4
0
Other
0
16
16
Hyperfiltration
161.9
306
0
1
1.92
53
0
0
153
0
0
0
76.5
0
1
III
0
0
null
0
0
1
0
0
0
Normal
0
0
Haemophilus_influenzae
0
Chronic_exchange
Splenic_sequestration
29.6
69
0
0
0
0
6,341
4.98
0
Deferasirox
0.7
0
0.187
0.69
1
17.6
17.6
18.2
5.59
0.534
0.66
0
1
0.197
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
null
0
null
0
0
20
21.7
57.8
49.5
13
13
12
Disability
1
1
1
1
1
0
HC-GEN-002
HC002-000089
HbSS
Male
Black_non_Hispanic
US_South
Middle
2
40.1
19.5
1_gene_del
0
7.51
5.22
67.2
6.4
13.1
398
550
12.34
47
0.93
6
175
158
5,000
7.03
4.85
1
0
Bilateral_legs
Cold_exposure
2.4
6.6
1
0
0
Hypoventilation
0
5.1
62.6
1
Other
126.1
13
23
Hyperfiltration
111.5
103
0
1
2.37
80
0
0
123
0
0
0
71.7
1
0
III
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
1
1
Streptococcus_pneumoniae
0
null
Stroke_prevention
58.9
96
1
2
1
0
18,042
5.45
0
Deferiprone
0.79
0
0.203
0.7
1
21.2
21.2
9.5
1.86
0.565
0.65
0
1
0.2
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
0
bb2121
0
0
0
0
0
Partial
0
null
0
1
28
12.8
63.5
60.6
13
11
10
Unemployed
0
1
1
1
0
0
HC-GEN-002
HC002-000090
HbSS
Male
Black_non_Hispanic
US_South
Middle
1.63
31.2
17.4
No_deletion
0
9.36
3.89
73.3
9.7
9.1
491
335
6.07
23
0.97
8
175
67
4,968
4.62
4.36
1
1
Bilateral_legs
Infection
1.7
5.3
0
0
0
Unknown
1
2.8
85
1
Hydromorphone
19.6
4
24
Macroalbuminuria
99.5
97
0
0
1.79
20
0
0
138
0
0
0
98
0
1
I
0
0
VH_RD
0
0
0
0
0
0
Normal
1
0
Streptococcus_pneumoniae
0
Episodic
Stroke_treatment
42.8
59
1
4
0
0
8,689
23.14
0
Deferasirox
0.69
0
0.174
0.53
0
0
0
0
8.73
0
0
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Partial
0
null
0
1
22
41.9
47.4
53.4
15
2
15
Employed_full
1
1
1
1
0
0
HC-GEN-002
HC002-000091
HbSS
Female
Black_non_Hispanic
US_South
Low
0.54
11.8
6.8
1_gene_del
0
6.02
3.97
94.1
10
15.9
360
361
9.47
59
0.96
8.3
307
143
5,000
1.2
5.08
2
1
Bilateral_legs
Infection
2.7
6.4
0
0
0
Fat_embolism
1
1.8
51.5
0
Morphine
0
4
12
null
111.8
224
0
0
1.5
20
1
0
149
0
0
0
107.3
0
0
II
0
0
null
0
0
0
0
0
0
Autoinfarction
1
1
Salmonella_sp
0
Episodic
ACS
41.6
20
0
0
0
0
599
28.48
0
Deferasirox
0.38
0
0.277
0.76
0
0
0
0
11.47
0
0
0
0
0
0
0
0
0
0
0
Haplo
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
null
0
null
0
1
20
20.1
60.6
79.8
5
12
14
Employed_part
0
1
0
1
0
0
HC-GEN-002
HC002-000092
HbSC
Male
Black_non_Hispanic
US_South
High
1.72
15.7
13.8
No_deletion
0
10.41
4.14
79.8
20.2
10.8
381
628
2.66
40
1.68
6.7
221
78
2,684
9.22
3.69
2
1
Chest
Dehydration
1.8
7.2
0
0
0
Unknown
0
4.1
54.8
1
Other
55.1
2
26
null
113.6
18
0
0
2.48
45
1
0
111
0
0
0
98.7
0
0
I
0
1
VH_RD
0
1
0
0
0
0
Normal
0
0
Haemophilus_influenzae
0
null
Splenic_sequestration
48
56
0
0
0
0
2,161
6.21
0
Deferoxamine
0.72
0
0.199
0.72
1
27.2
27.2
22.3
7.24
0.425
0.73
0
1
0.292
0
0
1
1.02
1
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
41
29.8
36.5
70.4
11
10
6
Disability
0
0
0
1
0
1
HC-GEN-002
HC002-000093
HbSS
Male
Black_non_Hispanic
Other
Middle
2
59.9
9.9
No_deletion
0
7.41
4.19
83.8
6.7
11.3
399
996
2.72
94
2.05
6.6
478
85
3,283
4.49
5.35
5
1
Lumbar_back
Stress
6.3
6.1
0
0
0
Unknown
1
6.4
69.5
1
Hydromorphone
119.9
1
52
Hyperfiltration
84.4
10
1
0
1.82
47
0
0
97
0
0
0
86.2
0
0
I
0
0
null
0
1
0
0
1
2.9
Normal
0
0
Salmonella_sp
0
Chronic_exchange
ACS
26.5
56
0
0
0
0
5,189
40
0
Deferasirox
0.79
0
0.226
0.79
0
0
0
0
11.24
0
0
0
0
0
0
0
0
0
0
0
MUD
Myeloablative
0
0
0
0
0
Other
0
0
0
0
0
Minimal
0
null
0
0
37
32.7
64.3
54.1
2
15
23
Disability
1
1
1
1
0
0
HC-GEN-002
HC002-000094
HbSS
Female
Black_non_Hispanic
US_Northeast
Low
1.51
20.6
7.1
No_deletion
0
7.25
9.5
77.9
13.7
14.4
673
788
12.41
69
0.66
9.2
116
30
3,290
11.27
4.84
3
1
Bilateral_legs
Infection
1.5
5.4
0
0
0
Fat_embolism
0
2.1
72.9
1
Morphine
106.8
4
35
null
151.6
220
0
0
2
74
1
0
110
0
0
0
71.4
1
0
I
0
0
null
0
0
1
1
0
0
Autoinfarction
1
0
Salmonella_sp
1
Episodic
Splenic_sequestration
59.4
56
1
0
0
0
11,559
22.87
0
Combination
0.49
0
0.158
0.75
0
0
0
0
16.81
0
0
0
0
0
0
0
0
0
0
1
MSD
NMA
1
0
0
0.97
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
1
36
33.7
55.2
62.4
0
8
10
Unemployed
0
1
1
1
0
0
HC-GEN-002
HC002-000095
HbSS
Male
Black_non_Hispanic
Africa
High
2
20.4
6.4
No_deletion
0
8.8
13.89
67.7
13
10.5
200
580
6.36
29
1.04
6.8
80
119
4,785
8.89
4.03
3
0
Lumbar_back
Unknown
3.2
8
0
0
0
Infection
1
5.6
66.6
1
Other
47.7
2
14
Microalbuminuria
132.6
98
0
0
1.82
30
1
1
82
0
1
0
86.3
0
0
III
0
0
PSR_Sea_Fan
0
0
0
0
0
0
Normal
1
0
Staphylococcus_aureus
0
null
Stroke_prevention
49.9
75
0
0
0
0
3,231
12.83
0
Deferoxamine
0.75
0
0.171
0.7
1
25.6
25.6
20
4.06
0.703
0.64
0
1
0.351
0
0
0
0
0
0
UCB
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
25
42.6
76.1
60
13
14
14
Unemployed
1
1
1
1
0
0
HC-GEN-002
HC002-000096
HbSS
Male
Black_non_Hispanic
Europe
Low
1.09
33.7
3.6
No_deletion
0
9.71
10.35
89.5
13.3
11.5
480
410
6.37
20
0.77
6.9
191
299
5,000
4.58
3.92
1
1
Bilateral_legs
Infection
6.8
5.4
0
0
0
Infection
0
2.2
81.9
1
Oxycodone
29.1
3
26
null
137.4
19
0
0
2.32
94
0
0
94
0
0
0
72.7
0
0
II
0
1
null
0
0
0
0
1
9.6
Autoinfarction
1
1
Staphylococcus_aureus
0
Chronic_exchange
Stroke_treatment
26.4
59
1
3
0
0
5,990
24.19
0
Deferoxamine
0.58
0
0.21
0.81
0
0
0
0
7.41
0
0
0
0
0
1
0.505
0
0
0
0
MUD
Myeloablative
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
0
36
41.5
68.3
47.4
15
0
9
Employed_part
1
1
1
1
1
0
HC-GEN-002
HC002-000097
HbSS
Female
Black_non_Hispanic
US_South
Low
2
33.2
11.4
2_gene_del
0
7.72
2.67
64.6
16.9
13.7
390
443
3.46
33
0.54
7.5
257
129
3,876
13.71
4.88
3
0
Abdomen
Cold_exposure
2.1
4.4
0
0
0
Hypoventilation
1
5.4
65.5
1
Oxycodone
164
14
8
Hyperfiltration
86.2
10
0
0
2.23
20
0
0
99
1
0
0
79
0
0
I
0
0
null
0
1
1
1
0
0
Autoinfarction
1
0
Salmonella_sp
0
Chronic_simple
Stroke_prevention
32
59
0
0
0
0
2,257
40
0
Deferasirox
0.71
0
0.208
0.9
1
19.7
19.7
0
3.67
0.326
0.75
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Minimal
0
null
0
1
10
36.9
68.6
79.4
9
5
4
Disability
0
0
0
1
0
1
HC-GEN-002
HC002-000098
HbSS
Female
Hispanic
US_South
Middle
0.59
12.2
9.5
1_gene_del
0
9.29
8.35
77.6
16.9
6.6
343
287
6.36
27
0.85
6.7
91
362
5,000
7.13
4.03
6
0
Lumbar_back
Infection
8.4
5.2
0
0
0
Fat_embolism
0
4.6
40.3
0
Other
0
7
19
Microalbuminuria
84.3
263
0
0
2.32
63
0
0
83
0
0
0
82.4
0
0
II
0
0
NPSR
0
0
1
0
0
0
Normal
0
0
Haemophilus_influenzae
0
Chronic_exchange
ACS
33.3
46
0
0
0
0
2,068
40
0
Deferasirox
0.57
0
0.23
0.5
1
30.2
30.2
5.1
4.07
0.39
0.94
0
0
0
0
0
0
0
0
0
MSD
RIC
0
0
0
0
0
Exagamglogene_autotemcel_CRISPR
0
0
0
0
0
Complete
0
null
0
1
52
40.5
51.3
57.2
9
0
4
Disability
1
1
0
0
0
1
HC-GEN-002
HC002-000099
HbSS
Female
African_born
Africa
Low
1.25
25.9
10.7
No_deletion
0
8.27
10.01
81.6
10.2
10.1
387
210
3.41
93
1.04
5.6
81
217
2,747
6.9
4.07
4
0
Bilateral_legs
Stress
4.8
6.8
0
0
0
Hypoventilation
1
4
63.1
1
Hydromorphone
7.3
4
22
Macroalbuminuria
106
48
0
0
1.88
89
0
0
161
0
1
0
56.6
0
1
I
0
1
null
0
0
1
1
0
0
Normal
1
0
Salmonella_sp
0
null
Stroke_prevention
53.1
57
1
3
0
0
645
19.94
0
Deferoxamine
0.45
0
0.3
0.94
1
30.5
30.5
14.1
7.15
0.318
0.59
0
0
0
0
0
0
0
0
0
Haplo
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
0
48
24.5
63.7
85
11
6
11
Unemployed
0
1
0
1
0
0
HC-GEN-002
HC002-000100
HbSB+_thal
Female
Black_non_Hispanic
US_South
Low
0.38
11.7
5.1
No_deletion
0
8.55
2.07
83.8
12.8
13.5
500
243
10.95
45
0.83
7.4
283
114
5,000
5.42
4.07
2
0
Bilateral_legs
Unknown
8.9
5.4
0
0
0
Hypoventilation
0
4.7
55.7
1
Oxycodone
10.1
11
24
Microalbuminuria
138
146
1
1
2.23
87
0
0
104
0
0
0
109.8
0
0
I
0
1
PSR_Sea_Fan
0
0
1
1
0
0
Normal
1
0
Haemophilus_influenzae
0
Episodic
Stroke_prevention
42.9
69
0
0
0
0
5,296
4.6
1
Deferasirox
0.69
0
0.139
0.93
1
29.8
29.8
5
6.26
0.614
0.33
0
1
0.183
0
0
0
0
0
0
MSD
Myeloablative
0
0
0
0
0
Lovotibeglogene_autotemcel
0
0
0
0
0
Complete
0
null
0
0
29
27.3
79.7
62.3
15
8
9
Disability
0
1
1
1
0
0
HC-GEN-002