patient_id string | genotype string | sex string | race_ethnicity string | geographic_region string | socioeconomic_status string | age_at_dx_years float64 | age_at_cohort_entry_years float64 | follow_up_years float64 | alpha_thal_coinheritance string | coinherited_g6pd_deficiency_flag int64 | hemoglobin_g_dl_baseline float64 | hbf_pct_baseline float64 | hbs_pct_baseline float64 | reticulocyte_pct float64 | wbc_k_ul_baseline float64 | platelet_k_ul_baseline int64 | ldh_u_l_baseline int64 | bilirubin_total_mg_dl float64 | ast_u_l_baseline int64 | creatinine_mg_dl_baseline float64 | uric_acid_mg_dl float64 | epo_mu_ml int64 | nt_probnp_pg_ml int64 | soluble_vcam1_ng_ml int64 | hscrp_mg_l float64 | disease_severity_score float64 | voc_episodes_yr int64 | voc_hospitalization_flag int64 | voc_location_primary string | voc_trigger_primary string | voc_duration_days_median float64 | voc_severity_nrs_mean float64 | acs_flag int64 | acs_icu_flag int64 | acs_mechanical_ventilation_flag int64 | acs_trigger_primary string | chronic_pain_flag int64 | pain_nrs_baseline float64 | pain_interference_promis_t float64 | opioid_prescription_flag int64 | opioid_type_primary string | opioid_mme_per_day float64 | ed_visits_yr int64 | hospitalization_days_voc_yr int64 | sickle_nephropathy_stage string | egfr_ml_min float64 | upcr_mg_g_cr int64 | esrd_flag int64 | pulmonary_hypertension_flag int64 | trv_m_s float64 | bnp_pg_ml int64 | lv_diastolic_dysfunction_flag int64 | lvh_flag int64 | tcd_velocity_cm_s int64 | stroke_overt_flag int64 | silent_cerebral_infarct_flag int64 | moyamoya_flag int64 | cognitive_score_iq_analog float64 | avascular_necrosis_hip_flag int64 | avascular_necrosis_shoulder_flag int64 | avn_stage_ficat_arlet string | joint_replacement_flag int64 | proliferative_retinopathy_flag int64 | retinopathy_stage string | laser_photocoagulation_flag int64 | sickle_hepatopathy_flag int64 | cholelithiasis_flag int64 | cholecystectomy_flag int64 | priapism_flag int64 | priapism_max_duration_hrs float64 | spleen_status string | functional_asplenia_flag int64 | leg_ulcer_flag int64 | bacterial_pathogen_primary string | sepsis_episode_flag int64 | transfusion_program_type string | transfusion_indication_primary string | hbs_target_pct float64 | units_prbc_lifetime int64 | alloimmunization_flag int64 | alloantibody_count int64 | dhtr_flag int64 | autoantibody_flag int64 | serum_ferritin_ng_ml int64 | liver_iron_concentration_mg_g_dry float64 | myocardial_iron_flag int64 | chelation_agent string | chelation_adherence_pct float64 | chelation_renal_toxicity_flag int64 | exchange_transfusion_hct_pre float64 | exchange_fraction_cells_replaced float64 | hydroxyurea_use_flag int64 | hu_dose_mg_kg_day float64 | hu_max_tolerated_dose_mg_kg float64 | hu_hbf_response_pct float64 | hu_wbc_nadir_k_ul float64 | hu_voc_reduction_fraction float64 | hu_adherence_pct float64 | hu_toxicity_flag int64 | l_glutamine_use_flag int64 | l_glutamine_voc_reduction_fraction float64 | crizanlizumab_use_flag int64 | crizanlizumab_voc_reduction_fraction float64 | voxelotor_use_flag int64 | voxelotor_hgb_rise_g_dl float64 | voxelotor_ldh_normalization_flag int64 | hsct_enrollment_flag int64 | hsct_donor_type string | hsct_conditioning_regimen string | hsct_engraftment_flag int64 | hsct_gvhd_flag int64 | hsct_tma_flag int64 | hsct_overall_survival_estimate float64 | gene_therapy_enrollment_flag int64 | gene_therapy_product string | gt_cd34_cells_per_kg int64 | gt_hbf_or_hbat_rise_pct float64 | gt_voc_free_months float64 | gt_tdf_flag int64 | gt_engraftment_pct float64 | gt_hematologic_response string | mortality_flag int64 | mortality_cause string | time_to_mortality_months float64 | hospitalization_any_flag int64 | hospitalization_days_yr int64 | qol_sf36_pcs float64 | promis_fatigue_t_score float64 | promis_pain_interference_t_score float64 | depression_phq9_score int64 | anxiety_gad7_score int64 | school_days_missed_yr int64 | employment_status string | penicillin_prophylaxis_flag int64 | vaccine_pneumococcal_flag int64 | vaccine_meningococcal_flag int64 | vaccine_influenza_flag int64 | palliative_care_referral_flag int64 | goals_of_care_documented_flag int64 | sku string |
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HC002-000001 | HbSC | Female | Black_non_Hispanic | Europe | Middle | 0.95 | 8.3 | 8.9 | No_deletion | 0 | 7.58 | 6.25 | 79.8 | 15 | 6.7 | 375 | 564 | 6.65 | 22 | 0.49 | 6.7 | 388 | 110 | 3,896 | 2.11 | 4.08 | 2 | 1 | Bilateral_legs | Dehydration | 4.6 | 8.7 | 0 | 0 | 0 | Infection | 1 | 4.8 | 72.8 | 0 | Hydromorphone | 0 | 3 | 25 | Macroalbuminuria | 120.4 | 159 | 0 | 1 | 1.93 | 23 | 0 | 0 | 133 | 0 | 1 | 0 | 94.1 | 0 | 0 | III | 0 | 0 | null | 0 | 0 | 1 | 1 | 0 | 0 | Surgical_splenectomy | 0 | 0 | Streptococcus_pneumoniae | 0 | Chronic_simple | Stroke_prevention | 33.5 | 54 | 0 | 0 | 0 | 0 | 2,946 | 40 | 0 | Deferasirox | 0.81 | 0 | 0.247 | 0.86 | 1 | 31.4 | 31.4 | 21.8 | 2.51 | 0.321 | 0.65 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 14 | 38.1 | 68.7 | 53.6 | 9 | 9 | 15 | Employed_full | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000002 | HbSS | Female | Black_non_Hispanic | Other | Middle | 2 | 40.9 | 15.7 | 2_gene_del | 0 | 8.3 | 8.94 | 66.9 | 14.3 | 10.8 | 577 | 424 | 9.97 | 41 | 1.28 | 4.3 | 187 | 119 | 4,939 | 3.58 | 4.32 | 8 | 1 | Lumbar_back | Infection | 7.5 | 7.3 | 0 | 0 | 0 | Hypoventilation | 1 | 2.3 | 75.9 | 0 | Morphine | 0 | 6 | 12 | null | 99.8 | 238 | 0 | 0 | 2.92 | 63 | 1 | 1 | 207 | 0 | 0 | 0 | 98.2 | 0 | 0 | II | 0 | 0 | NPSR | 0 | 0 | 1 | 1 | 0 | 0 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | ACS | 43.7 | 60 | 0 | 0 | 0 | 0 | 1,184 | 12.91 | 0 | Deferiprone | 0.64 | 0 | 0.206 | 0.78 | 0 | 0 | 0 | 0 | 11.12 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Partial | 1 | Cardiac | 438.8 | 1 | 17 | 34.7 | 64.3 | 83.3 | 19 | 11 | 15 | Employed_full | 1 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000003 | HbSC | Female | Black_non_Hispanic | US_Northeast | High | 2 | 41.9 | 17.2 | No_deletion | 0 | 10.54 | 2.44 | 77.3 | 6.4 | 14.7 | 437 | 191 | 2.23 | 24 | 0.77 | 5.2 | 58 | 149 | 5,000 | 8.18 | 3.38 | 2 | 0 | Chest | Dehydration | 2.2 | 7.5 | 1 | 0 | 0 | Hypoventilation | 0 | 1.7 | 69.3 | 1 | Oxycodone | 34.1 | 4 | 36 | null | 74.3 | 16 | 0 | 0 | 2.19 | 55 | 0 | 0 | 122 | 0 | 0 | 0 | 90.3 | 0 | 0 | III | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | E_coli | 1 | Chronic_exchange | ACS | 34.2 | 43 | 1 | 3 | 0 | 0 | 27,000 | 5.88 | 0 | Deferasirox | 0.73 | 1 | 0.207 | 0.53 | 1 | 14.9 | 14.9 | 14.2 | 1.5 | 0.383 | 0.81 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 1 | 10 | 36.4 | 61.4 | 56 | 10 | 16 | 4 | Employed_part | 0 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000004 | HbSC | Female | Black_non_Hispanic | US_Northeast | Middle | 0.83 | 15.4 | 14.9 | No_deletion | 0 | 10.76 | 3.05 | 59.8 | 7.5 | 7.3 | 544 | 635 | 4.71 | 82 | 0.68 | 8.4 | 202 | 61 | 2,555 | 5.8 | 3.69 | 4 | 1 | Lumbar_back | Infection | 4.8 | 9 | 0 | 0 | 0 | Fat_embolism | 1 | 4.9 | 54.2 | 1 | Oxycodone | 336 | 5 | 30 | null | 110.2 | 255 | 0 | 1 | 2.01 | 49 | 0 | 0 | 94 | 0 | 0 | 0 | 82.9 | 0 | 0 | II | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Surgical_splenectomy | 0 | 0 | Salmonella_sp | 0 | Episodic | Stroke_prevention | 58.7 | 43 | 1 | 2 | 0 | 0 | 976 | 6.26 | 0 | Deferiprone | 0.86 | 0 | 0.272 | 0.76 | 1 | 27.3 | 27.3 | 4.7 | 4.36 | 0.702 | 0.49 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | NMA | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 0 | 45 | 46.5 | 70.9 | 66.2 | 15 | 12 | 14 | Employed_full | 0 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000005 | HbSS | Female | Black_non_Hispanic | Africa | Low | 0.58 | 19.4 | 11.6 | No_deletion | 0 | 11.15 | 7.77 | 83.9 | 3 | 10.3 | 456 | 388 | 2.37 | 24 | 0.4 | 6.9 | 199 | 101 | 2,305 | 11.68 | 3.77 | 5 | 0 | Abdomen | Infection | 9.6 | 5.8 | 1 | 0 | 0 | Unknown | 1 | 4.1 | 58.2 | 1 | Oxycodone | 29.2 | 6 | 12 | null | 106.7 | 55 | 0 | 0 | 2.11 | 20 | 0 | 0 | 150 | 0 | 1 | 0 | 96.4 | 0 | 0 | IV | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | Stroke_prevention | 46.9 | 57 | 0 | 0 | 0 | 0 | 1,313 | 10.25 | 0 | Deferoxamine | 0.69 | 0 | 0.168 | 0.67 | 1 | 29.6 | 29.6 | 10.3 | 4.66 | 0.697 | 0.79 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 1 | Lovotibeglogene_autotemcel | 10,000,000 | 41.4 | 10.1 | 0 | 0.996 | Complete | 0 | null | 0 | 0 | 7 | 37.7 | 61.5 | 52.9 | 13 | 3 | 8 | Unemployed | 1 | 0 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000006 | HbSB+_thal | Female | Black_non_Hispanic | US_Midwest | High | 0.45 | 9.6 | 14.8 | 2_gene_del | 0 | 11.54 | 8.8 | 88.5 | 14.4 | 9.8 | 356 | 576 | 8.94 | 30 | 0.61 | 4.3 | 68 | 397 | 2,173 | 13.09 | 3.29 | 1 | 0 | Bilateral_legs | Dehydration | 9 | 6.3 | 0 | 0 | 0 | Infection | 0 | 4.1 | 83.2 | 1 | Other | 65.8 | 3 | 25 | null | 139.4 | 168 | 0 | 0 | 1.75 | 28 | 0 | 0 | 192 | 1 | 0 | 0 | 87.3 | 1 | 0 | III | 0 | 0 | null | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 0 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 26 | 37 | 0 | 0 | 0 | 0 | 3,255 | 33.93 | 0 | Deferasirox | 0.54 | 0 | 0.33 | 0.76 | 1 | 24.5 | 24.5 | 10.5 | 4.63 | 0.429 | 0.8 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 29 | 49.3 | 55.5 | 68.9 | 14 | 1 | 6 | Employed_full | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000007 | HbSC | Male | Middle_Eastern | Europe | Middle | 2 | 33.4 | 13.9 | 2_gene_del | 0 | 11.6 | 8.95 | 74.7 | 11 | 8.9 | 436 | 550 | 2.79 | 53 | 0.89 | 7.3 | 231 | 60 | 3,218 | 4.94 | 3.04 | 1 | 1 | Bilateral_legs | Stress | 4.4 | 6 | 0 | 0 | 0 | Hypoventilation | 1 | 1.2 | 65.5 | 1 | Oxycodone | 13.5 | 4 | 44 | Macroalbuminuria | 111.6 | 307 | 0 | 0 | 1.64 | 83 | 0 | 0 | 106 | 0 | 0 | 0 | 87.2 | 0 | 0 | III | 0 | 1 | NPSR | 1 | 1 | 0 | 0 | 1 | 2.3 | Normal | 0 | 0 | Staphylococcus_aureus | 0 | Chronic_exchange | ACS | 31.1 | 91 | 1 | 3 | 0 | 0 | 4,639 | 40 | 0 | Deferoxamine | 0.67 | 0 | 0.208 | 0.8 | 1 | 21.9 | 21.9 | 14.5 | 7.84 | 0.1 | 0.75 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | UCB | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 28 | 30.1 | 68.7 | 59.1 | 14 | 12 | 13 | Unemployed | 0 | 0 | 0 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000008 | HbSC | Female | Black_non_Hispanic | US_Northeast | Low | 2 | 23.9 | 5.5 | No_deletion | 0 | 9.15 | 12.07 | 78.2 | 11.4 | 11.7 | 508 | 285 | 3.19 | 35 | 1.77 | 6 | 47 | 43 | 5,000 | 1.37 | 3.11 | 0 | 1 | Abdomen | Stress | 9.9 | 6.6 | 0 | 0 | 0 | Hypoventilation | 0 | 4.9 | 64 | 1 | Other | 49.7 | 6 | 7 | Microalbuminuria | 43.3 | 309 | 0 | 0 | 1.92 | 45 | 0 | 0 | 80 | 0 | 0 | 0 | 79 | 1 | 0 | II | 0 | 1 | null | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 0 | 0 | Staphylococcus_aureus | 0 | Episodic | Stroke_treatment | 45.1 | 32 | 0 | 0 | 0 | 0 | 1,422 | 4.94 | 0 | Deferoxamine | 0.39 | 0 | 0.212 | 0.95 | 1 | 18.2 | 18.2 | 13.9 | 2.51 | 0.579 | 0.77 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 6 | 34.1 | 70 | 70.7 | 0 | 7 | 5 | Unemployed | 0 | 0 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000009 | HbSS | Male | Hispanic | US_South | Low | 1.88 | 29.8 | 11.5 | No_deletion | 0 | 7.48 | 3.43 | 89.4 | 5.2 | 12.3 | 563 | 267 | 7.82 | 24 | 0.98 | 5.5 | 185 | 114 | 2,719 | 3.3 | 4.72 | 2 | 1 | Chest | Cold_exposure | 4.7 | 9.6 | 1 | 0 | 0 | Infection | 1 | 2.6 | 52.5 | 1 | Morphine | 35.5 | 2 | 22 | Macroalbuminuria | 123.5 | 105 | 0 | 0 | 1.95 | 34 | 0 | 1 | 142 | 0 | 1 | 0 | 65.1 | 0 | 0 | III | 0 | 1 | PSR_Sea_Fan | 0 | 0 | 1 | 0 | 1 | 20 | Autoinfarction | 1 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_prevention | 43.7 | 66 | 0 | 0 | 0 | 0 | 286 | 7.39 | 1 | Deferoxamine | 0.47 | 0 | 0.235 | 0.79 | 1 | 25.6 | 25.6 | 26.3 | 3.35 | 0.655 | 0.69 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 26 | 19.4 | 59.8 | 58.4 | 6 | 4 | 9 | Employed_full | 0 | 0 | 0 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000010 | HbSS | Male | Black_non_Hispanic | Europe | Middle | 2 | 28 | 15.6 | 2_gene_del | 0 | 8.07 | 3.6 | 68 | 7.6 | 12.3 | 404 | 542 | 10.29 | 101 | 1.3 | 5.1 | 297 | 39 | 4,934 | 5.59 | 4.84 | 1 | 1 | Bilateral_legs | Unknown | 1.5 | 4.1 | 0 | 0 | 0 | Unknown | 1 | 6.7 | 61 | 0 | Hydromorphone | 0 | 1 | 21 | Microalbuminuria | 165.4 | 112 | 0 | 0 | 1.78 | 209 | 1 | 0 | 171 | 0 | 1 | 0 | 84.3 | 0 | 0 | IV | 0 | 0 | NPSR | 0 | 0 | 0 | 0 | 1 | 2.6 | Normal | 1 | 0 | Staphylococcus_aureus | 0 | Episodic | Stroke_treatment | 41.3 | 41 | 0 | 0 | 0 | 0 | 3,373 | 5.67 | 0 | Deferoxamine | 0.38 | 0 | 0.241 | 0.8 | 0 | 0 | 0 | 0 | 7.96 | 0 | 0 | 0 | 0 | 0 | 1 | 0.567 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 0 | 18 | 24.9 | 66.6 | 56.9 | 7 | 14 | 16 | Employed_part | 1 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000011 | HbSS | Male | Hispanic | US_South | Low | 0.59 | 31 | 7 | 2_gene_del | 0 | 7.11 | 4.61 | 71.4 | 10.1 | 8.1 | 222 | 352 | 5.59 | 30 | 0.4 | 8.3 | 264 | 30 | 1,114 | 3.25 | 4.8 | 2 | 0 | Bilateral_legs | Infection | 6.6 | 5.1 | 0 | 0 | 0 | Fat_embolism | 0 | 3 | 69.9 | 0 | Morphine | 0 | 2 | 20 | null | 111 | 263 | 0 | 0 | 2.6 | 445 | 1 | 1 | 80 | 0 | 0 | 0 | 89 | 1 | 0 | I | 0 | 0 | null | 0 | 1 | 1 | 0 | 0 | 0 | Normal | 1 | 0 | Staphylococcus_aureus | 0 | Episodic | Stroke_treatment | 48.3 | 51 | 0 | 0 | 0 | 0 | 1,030 | 12.36 | 0 | Deferasirox | 0.58 | 0 | 0.194 | 0.53 | 1 | 23.7 | 23.7 | 3.6 | 5.74 | 0.561 | 0.5 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | NMA | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 34 | 30.8 | 65 | 60.3 | 10 | 6 | 18 | Employed_part | 0 | 0 | 1 | 1 | 1 | 1 | HC-GEN-002 |
HC002-000012 | HbSB0_thal | Female | Black_non_Hispanic | US_South | Low | 1.01 | 22.3 | 13.4 | No_deletion | 0 | 8.2 | 13 | 80.2 | 9.3 | 6.1 | 214 | 615 | 8.05 | 41 | 0.7 | 3.9 | 176 | 86 | 3,003 | 2.6 | 4.05 | 13 | 1 | Bilateral_legs | Infection | 11 | 4.7 | 0 | 0 | 0 | Infection | 1 | 2.2 | 62.2 | 1 | Hydromorphone | 138.9 | 0 | 35 | null | 144.5 | 15 | 0 | 0 | 1.79 | 64 | 1 | 0 | 179 | 0 | 0 | 0 | 106.2 | 0 | 1 | II | 0 | 0 | NPSR | 0 | 1 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | E_coli | 0 | null | Stroke_prevention | 54.3 | 69 | 1 | 4 | 0 | 0 | 2,193 | 40 | 0 | Deferoxamine | 0.65 | 0 | 0.234 | 0.87 | 1 | 15.4 | 15.4 | 23.1 | 5.54 | 0.541 | 0.71 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 1 | Infection | 269.6 | 1 | 25 | 39.5 | 60.9 | 62 | 5 | 7 | 4 | Employed_full | 1 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000013 | HbSS | Male | Black_non_Hispanic | US_Midwest | Low | 0.69 | 16.4 | 10.1 | 2_gene_del | 0 | 8.7 | 10.13 | 76 | 12.5 | 11.8 | 381 | 372 | 7.92 | 41 | 1.36 | 5.5 | 229 | 517 | 5,000 | 6.4 | 4.11 | 2 | 0 | Lumbar_back | Dehydration | 8.1 | 9.7 | 1 | 0 | 0 | Infection | 1 | 6.4 | 56.3 | 0 | Hydromorphone | 0 | 2 | 44 | Hyperfiltration | 92.3 | 29 | 0 | 0 | 1.73 | 20 | 1 | 1 | 85 | 0 | 0 | 0 | 103.9 | 1 | 0 | III | 0 | 0 | null | 0 | 0 | 1 | 0 | 1 | 4.1 | Autoinfarction | 1 | 1 | Haemophilus_influenzae | 0 | Episodic | Stroke_treatment | 50.1 | 81 | 0 | 0 | 0 | 0 | 1,335 | 19.52 | 0 | Deferoxamine | 0.53 | 0 | 0.183 | 0.85 | 0 | 0 | 0 | 0 | 14.06 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 24 | 29.8 | 45.4 | 64.5 | 8 | 4 | 9 | Employed_part | 1 | 1 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000014 | HbSC | Male | Middle_Eastern | Europe | Middle | 2 | 21.7 | 10.6 | No_deletion | 1 | 8.98 | 13.09 | 79.6 | 14.3 | 9.5 | 139 | 639 | 5.43 | 59 | 0.48 | 7 | 131 | 117 | 3,343 | 42.28 | 3.4 | 0 | 0 | Abdomen | Cold_exposure | 3.4 | 6.1 | 0 | 0 | 0 | Infection | 1 | 1.4 | 58.8 | 0 | Hydromorphone | 0 | 3 | 19 | null | 129.8 | 64 | 0 | 0 | 1.63 | 92 | 0 | 1 | 169 | 0 | 1 | 0 | 84.5 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Haemophilus_influenzae | 1 | null | Stroke_treatment | 48.1 | 50 | 1 | 3 | 0 | 0 | 988 | 28.51 | 0 | Deferiprone | 0.63 | 0 | 0.196 | 0.52 | 1 | 21.4 | 21.4 | 16.5 | 6.8 | 0.386 | 0.83 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | NMA | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 38 | 24.1 | 48.7 | 54.4 | 3 | 0 | 14 | Unemployed | 1 | 1 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000015 | HbSS | Male | Black_non_Hispanic | Africa | Middle | 1.45 | 13.3 | 2.7 | No_deletion | 0 | 9.88 | 1.59 | 71.9 | 21.1 | 16.5 | 635 | 488 | 3.5 | 54 | 1.2 | 9.2 | 247 | 145 | 2,405 | 4.09 | 4.54 | 1 | 1 | Lumbar_back | Dehydration | 8.5 | 6.6 | 0 | 0 | 0 | Unknown | 1 | 2.3 | 75.1 | 1 | Morphine | 21 | 0 | 11 | Hyperfiltration | 83.9 | 18 | 0 | 0 | 1.59 | 20 | 1 | 0 | 80 | 0 | 1 | 0 | 83 | 0 | 1 | II | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | E_coli | 0 | Episodic | Stroke_treatment | 44.1 | 110 | 1 | 3 | 0 | 1 | 2,428 | 34.71 | 0 | Deferoxamine | 0.73 | 0 | 0.156 | 0.88 | 0 | 0 | 0 | 0 | 11.72 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 1 | 22 | 38.1 | 56.6 | 52.1 | 0 | 3 | 12 | Unemployed | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000016 | HbSS | Male | Black_non_Hispanic | US_South | Middle | 2 | 50.1 | 13.7 | 1_gene_del | 0 | 8.34 | 9.12 | 83.7 | 11.9 | 16.7 | 492 | 459 | 8.02 | 32 | 1.07 | 7.6 | 256 | 30 | 2,622 | 6.04 | 4.34 | 5 | 0 | Bilateral_legs | Unknown | 8.7 | 4.3 | 0 | 0 | 0 | Infection | 1 | 7.8 | 69.3 | 1 | Oxycodone | 23.1 | 7 | 40 | null | 101.4 | 65 | 0 | 1 | 2.66 | 23 | 0 | 0 | 81 | 0 | 0 | 0 | 78.2 | 0 | 0 | III | 0 | 0 | null | 0 | 1 | 1 | 0 | 1 | 2.8 | Normal | 1 | 0 | Salmonella_sp | 1 | null | Stroke_prevention | 53.7 | 40 | 1 | 4 | 0 | 0 | 1,624 | 9.15 | 0 | Deferiprone | 0.85 | 0 | 0.226 | 0.9 | 1 | 27.5 | 27.5 | 24.4 | 5.74 | 0.464 | 0.43 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 26 | 18 | 60.6 | 46.5 | 22 | 4 | 18 | Disability | 1 | 1 | 0 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000017 | HbSS | Male | Hispanic | US_South | Low | 0.23 | 21.2 | 17.4 | No_deletion | 0 | 5.78 | 2.6 | 80.8 | 16.5 | 17 | 344 | 341 | 8.22 | 39 | 0.85 | 5.5 | 119 | 188 | 801 | 2.12 | 5.2 | 3 | 0 | Chest | Infection | 2.4 | 6.7 | 0 | 0 | 0 | Unknown | 1 | 3.7 | 67.9 | 1 | Morphine | 57 | 5 | 18 | Microalbuminuria | 101.6 | 61 | 0 | 0 | 2.2 | 93 | 0 | 1 | 165 | 0 | 0 | 0 | 104.7 | 1 | 0 | III | 0 | 1 | null | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 1 | 1 | Salmonella_sp | 0 | null | ACS | 45.1 | 79 | 0 | 0 | 0 | 0 | 1,292 | 4.57 | 0 | Deferasirox | 0.74 | 0 | 0.213 | 0.63 | 1 | 19.6 | 19.6 | 12.6 | 5.63 | 0.602 | 0.62 | 0 | 1 | 0.276 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 47 | 18.1 | 48.8 | 55.5 | 7 | 0 | 5 | Unemployed | 0 | 1 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000018 | HbSS | Female | African_born | Other | Low | 0.61 | 17.1 | 3.7 | 2_gene_del | 0 | 8.13 | 7 | 86.4 | 8.7 | 8.2 | 287 | 448 | 9.46 | 41 | 0.63 | 9.1 | 303 | 133 | 2,195 | 16.36 | 4.51 | 3 | 0 | Bilateral_legs | Cold_exposure | 6.8 | 8.8 | 1 | 0 | 0 | Infection | 1 | 6.3 | 66.8 | 1 | Hydromorphone | 50.7 | 10 | 29 | null | 126.7 | 100 | 0 | 0 | 2.38 | 22 | 0 | 0 | 189 | 0 | 0 | 0 | 91.3 | 0 | 0 | I | 0 | 0 | VH_RD | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 0 | 0 | Staphylococcus_aureus | 0 | Chronic_exchange | Stroke_prevention | 28.4 | 37 | 0 | 0 | 0 | 0 | 9,414 | 9.14 | 0 | Deferasirox | 0.71 | 0 | 0.139 | 0.68 | 1 | 11 | 11 | 7.5 | 4.92 | 0.371 | 0.77 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 33 | 26.5 | 39.3 | 43.4 | 15 | 7 | 6 | Unemployed | 0 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000019 | HbSC | Male | Black_non_Hispanic | US_South | Middle | 1.92 | 19.4 | 8 | 1_gene_del | 0 | 10.89 | 6.49 | 83.6 | 5.3 | 12.7 | 543 | 690 | 7.07 | 60 | 0.45 | 4.8 | 302 | 62 | 5,000 | 12.18 | 3.48 | 1 | 1 | Abdomen | Cold_exposure | 5.8 | 7.7 | 0 | 0 | 0 | Unknown | 1 | 1.4 | 49 | 1 | Other | 54.9 | 6 | 26 | Hyperfiltration | 81.2 | 84 | 0 | 0 | 2.51 | 53 | 1 | 0 | 140 | 0 | 0 | 0 | 99.3 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 0 | 0 | 0 | Surgical_splenectomy | 1 | 1 | E_coli | 0 | Episodic | Stroke_prevention | 59.3 | 59 | 0 | 0 | 0 | 0 | 1,089 | 37.39 | 0 | Deferasirox | 0.91 | 0 | 0.193 | 0.93 | 1 | 30 | 30 | 20 | 3.61 | 0.433 | 0.88 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 46 | 38.9 | 58.7 | 47.9 | 13 | 8 | 11 | Employed_full | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000020 | HbSS | Female | Black_non_Hispanic | US_South | Low | 1.26 | 19.9 | 1.9 | No_deletion | 0 | 9.56 | 2.71 | 83.7 | 10.6 | 13.6 | 286 | 394 | 3.37 | 28 | 1.8 | 7.2 | 214 | 145 | 2,721 | 11.53 | 4.45 | 8 | 1 | Lumbar_back | Infection | 4.9 | 7 | 0 | 0 | 0 | Unknown | 0 | 2.8 | 65 | 1 | Morphine | 29.1 | 3 | 35 | CKD3+ | 58.7 | 325 | 0 | 0 | 1.97 | 20 | 1 | 1 | 236 | 0 | 0 | 0 | 106.1 | 1 | 0 | II | 1 | 0 | PSR_Sea_Fan | 0 | 1 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Salmonella_sp | 1 | Chronic_simple | Pre_op | 33.4 | 48 | 0 | 0 | 0 | 0 | 2,465 | 30.05 | 0 | Deferasirox | 0.49 | 0 | 0.219 | 0.95 | 0 | 0 | 0 | 0 | 13.15 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 50 | 26 | 60.3 | 59.3 | 7 | 11 | 18 | Employed_part | 0 | 1 | 0 | 1 | 1 | 1 | HC-GEN-002 |
HC002-000021 | HbSC | Female | African_born | US_South | Middle | 2 | 23.4 | 1.6 | No_deletion | 0 | 10.03 | 7.51 | 70.4 | 5.6 | 13.3 | 298 | 512 | 8.54 | 100 | 1.02 | 7.5 | 1,697 | 144 | 2,886 | 17.95 | 3.44 | 0 | 0 | Lumbar_back | Stress | 6.8 | 4.4 | 0 | 0 | 0 | Infection | 1 | 3.2 | 73.7 | 0 | Hydromorphone | 0 | 6 | 12 | null | 126.5 | 179 | 0 | 0 | 2.69 | 70 | 1 | 1 | 99 | 0 | 1 | 0 | 77.2 | 0 | 0 | I | 0 | 1 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Haemophilus_influenzae | 0 | null | Splenic_sequestration | 44.3 | 40 | 0 | 0 | 0 | 0 | 3,123 | 17.8 | 0 | Deferiprone | 0.6 | 0 | 0.254 | 0.52 | 1 | 22.7 | 22.7 | 17.9 | 5.07 | 0.383 | 0.79 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 65 | 35.9 | 68.4 | 68.4 | 17 | 4 | 11 | Disability | 1 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000022 | HbSS | Male | Hispanic | US_Midwest | Low | 2 | 23.4 | 19.8 | No_deletion | 1 | 9.36 | 5.45 | 85.9 | 12.1 | 9.9 | 328 | 412 | 6.05 | 33 | 0.88 | 5.5 | 219 | 42 | 1,135 | 4.3 | 4.32 | 2 | 0 | Bilateral_legs | Stress | 1.2 | 6.6 | 0 | 0 | 0 | Infection | 0 | 3.4 | 59.1 | 0 | Hydromorphone | 0 | 3 | 22 | null | 125.1 | 83 | 0 | 0 | 1.85 | 164 | 0 | 0 | 99 | 0 | 0 | 0 | 82.1 | 0 | 0 | I | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 1 | 12.1 | Normal | 1 | 0 | Staphylococcus_aureus | 1 | Chronic_exchange | Splenic_sequestration | 31.7 | 82 | 0 | 0 | 0 | 0 | 507 | 40 | 0 | Deferasirox | 0.73 | 0 | 0.169 | 0.5 | 1 | 19.4 | 19.4 | 8.7 | 5.15 | 0.287 | 0.58 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 30 | 42.2 | 79.5 | 58.3 | 5 | 0 | 12 | Disability | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000023 | HbSB+_thal | Male | Other | Africa | Low | 1.28 | 17.7 | 10.4 | 1_gene_del | 0 | 10.06 | 3.16 | 79.4 | 8.9 | 14.8 | 434 | 427 | 4.75 | 45 | 0.6 | 7.8 | 196 | 169 | 1,611 | 4.75 | 3.84 | 1 | 1 | Bilateral_legs | Stress | 4.7 | 7.5 | 1 | 1 | 1 | Unknown | 1 | 4.1 | 72.8 | 1 | Hydromorphone | 27.9 | 6 | 29 | null | 113.9 | 60 | 0 | 0 | 1.66 | 41 | 1 | 0 | 128 | 0 | 0 | 0 | 121.6 | 0 | 1 | III | 0 | 1 | NPSR | 0 | 1 | 1 | 0 | 1 | 3.6 | Normal | 0 | 0 | Salmonella_sp | 0 | Episodic | ACS | 51.6 | 71 | 0 | 0 | 0 | 0 | 952 | 19.02 | 0 | Deferasirox | 0.55 | 0 | 0.208 | 0.64 | 1 | 20.2 | 20.2 | 22.8 | 5.48 | 0.592 | 0.62 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | UCB | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 26 | 39.6 | 46.3 | 83.9 | 9 | 6 | 16 | Unemployed | 0 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000024 | HbSC | Female | Black_non_Hispanic | Europe | Low | 2 | 23.6 | 7.8 | 1_gene_del | 0 | 8.66 | 4.09 | 80.7 | 4.2 | 11 | 494 | 876 | 5.22 | 28 | 0.75 | 6 | 175 | 402 | 5,000 | 23.76 | 4.28 | 2 | 1 | Abdomen | Cold_exposure | 8.5 | 5.4 | 1 | 1 | 0 | Infection | 1 | 6.4 | 68 | 0 | Other | 0 | 7 | 7 | null | 142.7 | 85 | 0 | 0 | 2.25 | 66 | 1 | 0 | 126 | 0 | 0 | 0 | 99.1 | 1 | 0 | III | 0 | 0 | NPSR | 0 | 1 | 0 | 0 | 0 | 0 | Autoinfarction | 0 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 28.8 | 75 | 0 | 0 | 0 | 0 | 3,116 | 11.8 | 0 | Deferasirox | 0.54 | 1 | 0.176 | 0.62 | 1 | 27.6 | 27.6 | 10.7 | 5.48 | 0.3 | 0.71 | 0 | 0 | 0 | 1 | 0.343 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 17 | 52 | 63.6 | 65.3 | 12 | 2 | 2 | Employed_full | 0 | 0 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000025 | HbSC | Male | Hispanic | Europe | Middle | 2 | 49.4 | 6.2 | No_deletion | 0 | 8.52 | 3.3 | 90.4 | 18.9 | 11.4 | 563 | 693 | 4.28 | 27 | 0.8 | 7.8 | 113 | 97 | 4,957 | 10.04 | 4.2 | 2 | 0 | Bilateral_legs | Infection | 2.8 | 8.4 | 1 | 1 | 0 | Infection | 0 | 1.2 | 71.1 | 0 | Hydromorphone | 0 | 8 | 22 | Hyperfiltration | 102.9 | 87 | 0 | 1 | 2.31 | 35 | 1 | 1 | 151 | 0 | 0 | 0 | 88.7 | 0 | 0 | IV | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 1 | Streptococcus_pneumoniae | 0 | null | Pre_op | 57.8 | 28 | 0 | 0 | 0 | 0 | 2,990 | 3.43 | 0 | Deferiprone | 0.4 | 0 | 0.249 | 0.71 | 0 | 0 | 0 | 0 | 9.28 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 42 | 36.4 | 83.9 | 64.2 | 9 | 7 | 22 | Employed_full | 1 | 0 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000026 | HbSS | Male | Black_non_Hispanic | US_South | Low | 0.89 | 11.9 | 19.6 | No_deletion | 0 | 9.77 | 5.28 | 76.2 | 9.8 | 6.4 | 545 | 418 | 9.43 | 32 | 0.9 | 4 | 424 | 51 | 1,903 | 1.02 | 4.25 | 1 | 0 | Lumbar_back | Infection | 4.3 | 8.8 | 0 | 0 | 0 | Unknown | 0 | 1.1 | 62.6 | 1 | Other | 121.2 | 8 | 25 | CKD3+ | 119.8 | 1,849 | 0 | 0 | 2.16 | 37 | 0 | 1 | 110 | 0 | 0 | 0 | 106.9 | 0 | 0 | IV | 0 | 0 | null | 0 | 0 | 0 | 0 | 1 | 11.2 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | null | ACS | 48.5 | 35 | 1 | 3 | 0 | 0 | 1,368 | 40 | 0 | Deferasirox | 0.36 | 0 | 0.193 | 0.71 | 1 | 19.4 | 13.6 | 14.1 | 6.74 | 0.575 | 0.7 | 1 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 11 | 49 | 46.9 | 49.5 | 8 | 10 | 9 | Disability | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000027 | HbSS | Female | Middle_Eastern | US_Northeast | Middle | 1.44 | 14.4 | 5.8 | No_deletion | 0 | 9.87 | 6.34 | 92.8 | 5.4 | 12.9 | 420 | 444 | 2.98 | 30 | 1.07 | 7.3 | 141 | 102 | 2,656 | 8.7 | 4.19 | 0 | 0 | Lumbar_back | Stress | 6 | 6.2 | 1 | 0 | 0 | Unknown | 1 | 3.2 | 71.8 | 1 | Hydromorphone | 35.5 | 9 | 20 | Macroalbuminuria | 97.8 | 16 | 0 | 0 | 2.51 | 34 | 0 | 0 | 163 | 0 | 0 | 0 | 88.3 | 1 | 0 | IV | 0 | 0 | NPSR | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | Splenic_sequestration | 42.7 | 26 | 0 | 0 | 0 | 0 | 3,163 | 14.94 | 0 | Combination | 0.71 | 0 | 0.241 | 0.95 | 0 | 0 | 0 | 0 | 7.85 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 37 | 41 | 50.3 | 68.4 | 0 | 5 | 2 | Disability | 1 | 0 | 0 | 1 | 1 | 1 | HC-GEN-002 |
HC002-000028 | HbSS | Female | Black_non_Hispanic | US_Northeast | Low | 2 | 46.7 | 14.8 | 2_gene_del | 0 | 8.65 | 5.42 | 93.6 | 15.6 | 10.2 | 542 | 294 | 3.68 | 38 | 0.5 | 6.2 | 155 | 286 | 3,588 | 3.8 | 4.37 | 8 | 1 | Bilateral_legs | Infection | 7.1 | 8.5 | 1 | 1 | 0 | Hypoventilation | 1 | 3.4 | 45.9 | 0 | Oxycodone | 0 | 1 | 33 | Microalbuminuria | 100.9 | 30 | 0 | 1 | 2.29 | 125 | 0 | 0 | 162 | 1 | 1 | 0 | 75.9 | 0 | 0 | I | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 0 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 29.7 | 35 | 0 | 0 | 0 | 0 | 4,369 | 10.47 | 0 | Deferasirox | 0.58 | 0 | 0.206 | 0.62 | 1 | 12.8 | 12.8 | 23.6 | 4.28 | 0.75 | 0.41 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 21 | 30.8 | 69.9 | 68.3 | 13 | 7 | 26 | Employed_part | 0 | 0 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000029 | HbSS | Female | Hispanic | US_South | Middle | 1.53 | 34 | 6.4 | No_deletion | 0 | 10.29 | 2.24 | 88 | 9.1 | 12.4 | 339 | 373 | 5.13 | 30 | 0.4 | 8.5 | 159 | 36 | 2,002 | 12.41 | 4.31 | 7 | 1 | Bilateral_legs | Infection | 4.8 | 7 | 1 | 1 | 1 | Unknown | 0 | 8.3 | 62.4 | 0 | Hydromorphone | 0 | 0 | 27 | Microalbuminuria | 121.9 | 25 | 0 | 0 | 2.23 | 22 | 1 | 0 | 205 | 0 | 0 | 0 | 85.2 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 0 | 0 | Staphylococcus_aureus | 0 | Episodic | ACS | 42.3 | 64 | 0 | 0 | 0 | 0 | 6,206 | 14.84 | 0 | Deferasirox | 0.64 | 0 | 0.152 | 0.57 | 1 | 18.4 | 18.4 | 25 | 3.2 | 0.693 | 0.63 | 0 | 0 | 0 | 1 | 0.25 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 40 | 25.1 | 62 | 51.6 | 14 | 0 | 10 | Employed_part | 1 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000030 | HbSC | Male | Black_non_Hispanic | US_South | Middle | 2 | 45.6 | 2.3 | No_deletion | 0 | 11.98 | 4.73 | 74.2 | 16.4 | 11.7 | 201 | 464 | 13.56 | 59 | 0.77 | 6.7 | 111 | 217 | 1,337 | 8.39 | 3.17 | 0 | 0 | Lumbar_back | Dehydration | 11.9 | 9.3 | 1 | 0 | 0 | Fat_embolism | 1 | 8.1 | 69.8 | 0 | Morphine | 0 | 2 | 22 | null | 180 | 124 | 0 | 1 | 2.79 | 51 | 1 | 1 | 120 | 0 | 0 | 0 | 91.8 | 0 | 0 | I | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Streptococcus_pneumoniae | 0 | Chronic_exchange | Stroke_prevention | 25.8 | 61 | 1 | 2 | 0 | 0 | 6,774 | 40 | 0 | Deferasirox | 0.77 | 0 | 0.217 | 0.9 | 1 | 18.5 | 18.5 | 15 | 8.6 | 0.389 | 0.83 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 33 | 36.7 | 62.3 | 62.4 | 7 | 5 | 16 | Employed_full | 1 | 0 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000031 | HbSC | Female | Black_non_Hispanic | US_Northeast | Low | 0.7 | 29.6 | 14 | No_deletion | 0 | 11.46 | 9.05 | 64.5 | 9.1 | 11.5 | 339 | 592 | 10.25 | 33 | 0.4 | 8.7 | 60 | 62 | 3,362 | 1.5 | 3.1 | 0 | 0 | Bilateral_legs | Stress | 3 | 10 | 0 | 0 | 0 | Hypoventilation | 1 | 2.7 | 65.3 | 1 | Morphine | 60.7 | 7 | 24 | Macroalbuminuria | 136 | 119 | 0 | 0 | 2.21 | 93 | 0 | 0 | 153 | 0 | 1 | 0 | 80.7 | 0 | 1 | III | 0 | 1 | VH_RD | 0 | 1 | 1 | 0 | 0 | 0 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | null | Stroke_prevention | 51.5 | 79 | 0 | 0 | 0 | 0 | 12,305 | 40 | 1 | Deferiprone | 0.47 | 0 | 0.173 | 0.89 | 1 | 22.6 | 22.6 | 10.7 | 5.58 | 0.451 | 0.52 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 31 | 22.1 | 65.8 | 78.8 | 14 | 13 | 9 | Unemployed | 1 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000032 | HbSB+_thal | Female | Hispanic | US_South | Middle | 2 | 36.9 | 1 | 1_gene_del | 0 | 8.52 | 4.49 | 90.6 | 9.8 | 10.9 | 323 | 565 | 2.66 | 31 | 0.63 | 7.6 | 169 | 155 | 4,848 | 7.5 | 4.2 | 3 | 1 | Abdomen | Dehydration | 2.4 | 5.2 | 0 | 0 | 0 | Infection | 1 | 0.9 | 74.1 | 0 | Hydromorphone | 0 | 4 | 14 | Hyperfiltration | 129.2 | 45 | 0 | 0 | 2.3 | 138 | 1 | 0 | 164 | 0 | 1 | 0 | 75 | 1 | 1 | IV | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Haemophilus_influenzae | 0 | Chronic_exchange | ACS | 32.1 | 54 | 0 | 0 | 0 | 0 | 3,664 | 11.47 | 0 | Deferasirox | 0.65 | 0 | 0.265 | 0.6 | 0 | 0 | 0 | 0 | 8.94 | 0 | 0 | 0 | 0 | 0 | 1 | 0.05 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 17 | 32.6 | 67.5 | 64.9 | 10 | 9 | 13 | Unemployed | 0 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000033 | HbSS | Male | Black_non_Hispanic | US_Midwest | Low | 1.24 | 10.4 | 13.8 | No_deletion | 0 | 10.62 | 5.64 | 82.9 | 13.4 | 13.4 | 344 | 245 | 11.89 | 38 | 0.57 | 6.6 | 492 | 69 | 4,895 | 7.16 | 3.89 | 2 | 0 | Bilateral_legs | Unknown | 3.3 | 8.6 | 0 | 0 | 0 | Unknown | 0 | 3.8 | 60.3 | 1 | Other | 18.1 | 2 | 20 | null | 137.1 | 264 | 0 | 1 | 1.68 | 95 | 1 | 0 | 140 | 0 | 1 | 0 | 86.9 | 0 | 0 | I | 0 | 1 | null | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | Splenic_sequestration | 45.9 | 41 | 0 | 0 | 0 | 1 | 706 | 26.3 | 0 | Deferasirox | 0.61 | 0 | 0.293 | 0.93 | 1 | 27 | 27 | 12.5 | 5 | 0.486 | 0.77 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | NMA | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Minimal | 1 | Other | 227.1 | 1 | 16 | 33.4 | 64.2 | 71.3 | 15 | 4 | 10 | Employed_full | 0 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000034 | HbSS | Female | African_born | Europe | Middle | 2 | 36.2 | 5.8 | 1_gene_del | 0 | 8.95 | 4.89 | 76 | 14.4 | 10.4 | 305 | 626 | 11.88 | 66 | 0.95 | 8 | 286 | 69 | 5,000 | 8.09 | 4.64 | 9 | 1 | Chest | Dehydration | 9 | 9.5 | 0 | 0 | 0 | Hypoventilation | 0 | 0.8 | 56 | 1 | Oxycodone | 30.8 | 5 | 22 | CKD3+ | 27.8 | 140 | 0 | 0 | 3.59 | 63 | 0 | 0 | 132 | 0 | 0 | 0 | 84.3 | 0 | 0 | II | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | E_coli | 0 | Chronic_simple | Stroke_treatment | 32.1 | 44 | 1 | 2 | 0 | 0 | 2,351 | 40 | 0 | Deferasirox | 0.57 | 0 | 0.246 | 0.93 | 1 | 22.8 | 22.8 | 15.8 | 4.1 | 0.518 | 0.77 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 5 | 46.4 | 65.8 | 58.3 | 13 | 3 | 9 | Employed_part | 1 | 1 | 1 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000035 | HbSS | Male | Black_non_Hispanic | US_South | Low | 1.98 | 25 | 15.2 | No_deletion | 0 | 7.66 | 2.85 | 91.4 | 15.1 | 6.6 | 365 | 388 | 3.36 | 49 | 2 | 8 | 853 | 557 | 1,674 | 9.59 | 4.83 | 2 | 0 | Lumbar_back | Infection | 4.1 | 5.5 | 0 | 0 | 0 | Hypoventilation | 1 | 2.1 | 44 | 1 | Hydromorphone | 59.4 | 6 | 14 | Hyperfiltration | 121.2 | 277 | 0 | 0 | 1.5 | 42 | 0 | 0 | 80 | 0 | 0 | 0 | 98.9 | 0 | 0 | II | 0 | 0 | PSR_Sea_Fan | 0 | 1 | 0 | 0 | 0 | 0 | Normal | 0 | 1 | Streptococcus_pneumoniae | 0 | null | Stroke_prevention | 40 | 66 | 0 | 0 | 0 | 0 | 806 | 23.28 | 0 | Deferasirox | 0.63 | 0 | 0.194 | 0.86 | 1 | 14 | 14 | 13.8 | 9.01 | 0.682 | 0.84 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 11 | 27.5 | 48.4 | 42.7 | 8 | 7 | 15 | Employed_part | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000036 | HbSS | Male | Black_non_Hispanic | US_Northeast | Middle | 2 | 37.6 | 15.6 | No_deletion | 0 | 7.26 | 5.1 | 75.1 | 11.6 | 12.7 | 494 | 259 | 1.71 | 43 | 0.4 | 7.5 | 446 | 30 | 3,748 | 20.02 | 4.65 | 5 | 1 | Chest | Dehydration | 4.5 | 6.2 | 0 | 0 | 0 | Unknown | 0 | 3.8 | 59 | 0 | Oxycodone | 0 | 1 | 21 | null | 141.9 | 382 | 0 | 0 | 1.88 | 140 | 0 | 1 | 143 | 0 | 1 | 0 | 80.3 | 1 | 0 | I | 0 | 0 | null | 0 | 0 | 1 | 1 | 1 | 2.3 | Autoinfarction | 0 | 1 | Staphylococcus_aureus | 0 | Episodic | Stroke_treatment | 57.4 | 82 | 1 | 2 | 0 | 0 | 8,245 | 18.55 | 0 | Deferasirox | 0.83 | 1 | 0.221 | 0.87 | 1 | 27.7 | 27.7 | 9.6 | 6.39 | 0.514 | 0.81 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 40 | 39 | 70.1 | 67.3 | 19 | 9 | 6 | Disability | 1 | 1 | 1 | 1 | 1 | 1 | HC-GEN-002 |
HC002-000037 | HbSS | Female | Black_non_Hispanic | Europe | High | 0.82 | 26.4 | 14.8 | No_deletion | 0 | 8.56 | 3.7 | 78.6 | 14.1 | 8.6 | 626 | 736 | 5.84 | 25 | 2.31 | 3.4 | 372 | 197 | 3,184 | 8.42 | 4.9 | 1 | 0 | Lumbar_back | Infection | 3 | 6.1 | 0 | 0 | 0 | Fat_embolism | 1 | 7.8 | 67.7 | 1 | Hydromorphone | 124.6 | 0 | 17 | Microalbuminuria | 113 | 10 | 0 | 0 | 1.87 | 33 | 0 | 0 | 164 | 1 | 1 | 0 | 55 | 0 | 0 | III | 0 | 0 | null | 0 | 1 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 31.3 | 58 | 1 | 4 | 0 | 0 | 14,738 | 2.03 | 0 | Deferasirox | 0.47 | 0 | 0.232 | 0.95 | 1 | 15.2 | 15.2 | 23.9 | 3.62 | 0.632 | 0.93 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 17 | 24.8 | 76.1 | 60.3 | 5 | 4 | 20 | Unemployed | 1 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000038 | HbSS | Male | Black_non_Hispanic | Europe | Low | 0.19 | 4.8 | 1.5 | No_deletion | 0 | 5.86 | 5.52 | 86.2 | 15 | 7 | 213 | 779 | 10.6 | 28 | 0.66 | 5.3 | 1,103 | 686 | 3,486 | 6.16 | 5.39 | 1 | 0 | Bilateral_legs | Infection | 5.3 | 7 | 1 | 1 | 0 | Hypoventilation | 0 | 5.3 | 70.4 | 1 | Other | 239 | 4 | 39 | null | 108.5 | 205 | 0 | 0 | 2.94 | 34 | 1 | 0 | 138 | 0 | 0 | 0 | 99.5 | 0 | 1 | II | 0 | 0 | null | 0 | 1 | 1 | 0 | 1 | 10.5 | Autoinfarction | 1 | 0 | E_coli | 0 | Chronic_exchange | Splenic_sequestration | 26.8 | 79 | 0 | 0 | 0 | 0 | 3,233 | 40 | 0 | Deferasirox | 0.68 | 0 | 0.263 | 0.85 | 1 | 19.6 | 19.6 | 14.5 | 3.71 | 0.325 | 0.73 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 1 | Exagamglogene_autotemcel_CRISPR | 10,000,000 | 51.6 | 34.4 | 0 | 0.93 | Partial | 0 | null | 0 | 1 | 38 | 43.1 | 71.8 | 64.7 | 0 | 6 | 30 | Disability | 1 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000039 | HbSS | Male | Black_non_Hispanic | Africa | Middle | 0.87 | 18.2 | 14.4 | No_deletion | 0 | 9.18 | 7.44 | 73.1 | 12.8 | 7.9 | 265 | 454 | 13.41 | 27 | 0.88 | 8.9 | 226 | 241 | 3,275 | 15.16 | 4.27 | 4 | 1 | Lumbar_back | Stress | 17.5 | 6.6 | 0 | 0 | 0 | Fat_embolism | 1 | 4.2 | 46.6 | 0 | Morphine | 0 | 0 | 20 | null | 77.1 | 19 | 0 | 0 | 1.86 | 197 | 1 | 1 | 109 | 0 | 0 | 0 | 99.7 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Salmonella_sp | 0 | Episodic | Stroke_prevention | 42.1 | 44 | 1 | 1 | 0 | 0 | 11,688 | 5.88 | 0 | Deferoxamine | 0.59 | 0 | 0.212 | 0.68 | 1 | 21.5 | 21.5 | 29.5 | 4.6 | 0.567 | 0.95 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 36 | 49.9 | 65.1 | 62.5 | 0 | 0 | 16 | Employed_part | 1 | 1 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000040 | HbSC | Female | Black_non_Hispanic | US_Northeast | Middle | 1.39 | 14.9 | 19.8 | No_deletion | 0 | 9.17 | 7.03 | 81.1 | 11.4 | 11.8 | 325 | 555 | 3.91 | 75 | 0.4 | 4.9 | 257 | 32 | 2,617 | 36.39 | 3.69 | 2 | 1 | Lumbar_back | Dehydration | 4.7 | 6.8 | 0 | 0 | 0 | Infection | 0 | 5.6 | 74.9 | 1 | Hydromorphone | 32.1 | 9 | 14 | null | 94.8 | 121 | 0 | 0 | 2.28 | 89 | 1 | 0 | 80 | 0 | 1 | 0 | 111 | 0 | 0 | IV | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 1 | E_coli | 0 | Chronic_simple | Stroke_prevention | 28.3 | 62 | 0 | 0 | 0 | 1 | 10,842 | 2.53 | 0 | Deferasirox | 0.89 | 0 | 0.236 | 0.73 | 0 | 0 | 0 | 0 | 13.59 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 24 | 26.6 | 78.7 | 53.4 | 11 | 10 | 9 | Employed_full | 1 | 1 | 1 | 0 | 1 | 0 | HC-GEN-002 |
HC002-000041 | HbSS | Female | Black_non_Hispanic | Africa | Low | 2 | 31 | 5.6 | No_deletion | 0 | 8.72 | 10 | 90.7 | 6.2 | 10.7 | 512 | 570 | 14.53 | 55 | 1.22 | 8.1 | 242 | 34 | 805 | 12.58 | 4.3 | 3 | 1 | Lumbar_back | Infection | 2.1 | 8.7 | 0 | 0 | 0 | Infection | 1 | 3.7 | 51.3 | 0 | Hydromorphone | 0 | 2 | 13 | Hyperfiltration | 80.8 | 82 | 0 | 0 | 1.87 | 92 | 1 | 0 | 158 | 0 | 0 | 0 | 92.2 | 1 | 0 | I | 0 | 0 | VH_RD | 0 | 0 | 0 | 0 | 0 | 0 | Surgical_splenectomy | 1 | 0 | Salmonella_sp | 0 | null | Stroke_treatment | 41.1 | 40 | 0 | 0 | 0 | 0 | 4,545 | 2.71 | 0 | Deferoxamine | 0.45 | 0 | 0.153 | 0.63 | 1 | 17 | 17 | 13.2 | 3.57 | 0.662 | 0.7 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 1 | ACS | 600 | 1 | 14 | 36.1 | 62 | 62.7 | 0 | 4 | 2 | Disability | 0 | 1 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000042 | HbSC | Female | Hispanic | US_South | Middle | 1.25 | 28.2 | 6.2 | No_deletion | 0 | 9.77 | 2.67 | 83.7 | 14.4 | 4.6 | 395 | 756 | 1.99 | 32 | 0.76 | 7.9 | 841 | 57 | 5,000 | 7.13 | 4.03 | 3 | 1 | Lumbar_back | Dehydration | 7.7 | 3.8 | 0 | 0 | 0 | Unknown | 1 | 6.3 | 60.7 | 1 | Hydromorphone | 40.8 | 3 | 16 | null | 145 | 87 | 0 | 0 | 1.68 | 108 | 0 | 1 | 141 | 0 | 1 | 0 | 86.2 | 0 | 0 | II | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Haemophilus_influenzae | 0 | Chronic_exchange | ACS | 27.5 | 25 | 0 | 0 | 0 | 0 | 5,809 | 6.99 | 0 | Deferiprone | 0.8 | 0 | 0.23 | 0.89 | 1 | 27.3 | 27.3 | 14 | 1.5 | 0.466 | 0.44 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 20 | 60 | 69.9 | 55 | 6 | 10 | 13 | Employed_part | 1 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000043 | HbSC | Female | Hispanic | US_Northeast | Middle | 2 | 17.8 | 16.5 | 2_gene_del | 0 | 10.13 | 4.21 | 92 | 12.2 | 9.8 | 333 | 560 | 5.03 | 36 | 0.72 | 5.7 | 245 | 142 | 4,294 | 8.55 | 3.68 | 0 | 0 | Abdomen | Infection | 16.3 | 5.4 | 1 | 0 | 0 | Fat_embolism | 1 | 1.5 | 55.7 | 1 | Other | 32.3 | 9 | 19 | null | 162.6 | 21 | 0 | 1 | 2.48 | 62 | 0 | 0 | 196 | 0 | 1 | 0 | 89.7 | 0 | 0 | III | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Streptococcus_pneumoniae | 0 | Episodic | ACS | 46.3 | 33 | 1 | 0 | 0 | 0 | 9,241 | 26.73 | 0 | Deferoxamine | 0.71 | 0 | 0.186 | 0.51 | 1 | 30.7 | 30.7 | 13.4 | 1.5 | 0.287 | 0.58 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 1 | MSD | NMA | 1 | 1 | 0 | 0.93 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 1 | Cardiac | 222.1 | 0 | 19 | 27.5 | 76.8 | 50.7 | 15 | 8 | 7 | Unemployed | 1 | 1 | 1 | 0 | 1 | 1 | HC-GEN-002 |
HC002-000044 | HbSS | Female | Hispanic | US_South | High | 1.3 | 20.9 | 4 | No_deletion | 1 | 7.14 | 1.76 | 91.1 | 10.3 | 14.5 | 506 | 222 | 4.91 | 32 | 0.4 | 3.8 | 146 | 152 | 1,733 | 7.42 | 4.86 | 6 | 0 | Lumbar_back | Unknown | 3.2 | 8.4 | 1 | 1 | 0 | Hypoventilation | 0 | 5 | 66.6 | 1 | Hydromorphone | 60.7 | 2 | 26 | null | 177.7 | 310 | 0 | 0 | 1.81 | 21 | 0 | 0 | 82 | 0 | 1 | 0 | 96.2 | 0 | 0 | II | 0 | 0 | NPSR | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Salmonella_sp | 0 | Episodic | Stroke_treatment | 54.2 | 62 | 1 | 3 | 0 | 0 | 701 | 40 | 0 | Deferoxamine | 0.53 | 0 | 0.222 | 0.89 | 1 | 21.6 | 21.6 | 15.3 | 7.76 | 0.452 | 0.78 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 1 | Lovotibeglogene_autotemcel | 10,000,000 | 35.8 | 18.9 | 0 | 0.737 | Minimal | 0 | null | 0 | 1 | 18 | 20 | 56.8 | 70.6 | 0 | 9 | 6 | Unemployed | 1 | 1 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000045 | HbSC | Male | Black_non_Hispanic | US_Northeast | High | 1.11 | 15.3 | 13.6 | No_deletion | 0 | 10.27 | 8.08 | 82.1 | 17.1 | 9.6 | 535 | 997 | 10.76 | 31 | 0.77 | 5.9 | 392 | 34 | 4,613 | 6.14 | 3.78 | 4 | 1 | Arms | Infection | 3.2 | 8.2 | 0 | 0 | 0 | Hypoventilation | 1 | 5.6 | 63 | 0 | Hydromorphone | 0 | 0 | 14 | null | 80.3 | 19 | 0 | 0 | 2.18 | 82 | 0 | 0 | 121 | 0 | 1 | 0 | 95.5 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | Chronic_simple | Pre_op | 28.1 | 33 | 0 | 0 | 0 | 0 | 4,274 | 23.14 | 0 | Deferasirox | 0.81 | 0 | 0.178 | 0.58 | 1 | 11.3 | 11.3 | 17.6 | 3.29 | 0.565 | 0.75 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 7 | 37.1 | 73 | 52.7 | 8 | 6 | 6 | Unemployed | 0 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000046 | HbSC | Male | Black_non_Hispanic | US_Northeast | Low | 0.99 | 14.7 | 15.3 | No_deletion | 0 | 13.15 | 4.84 | 63.3 | 6.3 | 10.5 | 418 | 652 | 11.58 | 54 | 1.13 | 9.9 | 127 | 51 | 2,911 | 34.2 | 3.08 | 0 | 0 | Bilateral_legs | Stress | 1.8 | 5.3 | 0 | 0 | 0 | Unknown | 1 | 3.8 | 69.5 | 0 | Oxycodone | 0 | 5 | 35 | Hyperfiltration | 86.6 | 222 | 0 | 0 | 2.35 | 66 | 0 | 0 | 87 | 0 | 1 | 0 | 87.8 | 0 | 0 | II | 0 | 1 | NPSR | 0 | 1 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Staphylococcus_aureus | 0 | null | ACS | 45.5 | 81 | 1 | 1 | 0 | 0 | 5,987 | 40 | 0 | Deferasirox | 0.5 | 0 | 0.236 | 0.54 | 0 | 0 | 0 | 0 | 16.62 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 7 | 24.4 | 48.2 | 60.4 | 9 | 14 | 15 | Disability | 1 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000047 | HbSS | Male | Black_non_Hispanic | US_South | Middle | 0.39 | 11.1 | 1.7 | No_deletion | 0 | 10.14 | 4.48 | 73.2 | 18.6 | 14.1 | 322 | 321 | 9.75 | 40 | 0.66 | 5.5 | 375 | 54 | 2,953 | 3.32 | 4.14 | 9 | 1 | Lumbar_back | Infection | 5.7 | 8.2 | 1 | 1 | 1 | Hypoventilation | 1 | 4.1 | 82.3 | 1 | Hydromorphone | 106.8 | 8 | 44 | Hyperfiltration | 83.8 | 16 | 0 | 0 | 2.86 | 34 | 0 | 0 | 181 | 0 | 1 | 0 | 83.6 | 0 | 0 | I | 0 | 0 | NPSR | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 1 | Salmonella_sp | 0 | null | Stroke_prevention | 52.4 | 49 | 1 | 3 | 1 | 0 | 672 | 10.99 | 0 | Deferasirox | 0.62 | 0 | 0.246 | 0.82 | 1 | 17.8 | 17.8 | 8.9 | 4.32 | 0.362 | 0.45 | 0 | 1 | 0.287 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 1 | Lovotibeglogene_autotemcel | 10,000,000 | 64.7 | 37 | 0 | 0.914 | Partial | 0 | null | 0 | 1 | 17 | 38.5 | 51.4 | 52.2 | 1 | 4 | 19 | Employed_full | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000048 | HbSS | Male | Hispanic | Europe | Middle | 2 | 23.9 | 11.5 | No_deletion | 0 | 8.7 | 4.81 | 88.1 | 11.9 | 13.4 | 452 | 254 | 3.08 | 103 | 1.33 | 5.6 | 341 | 101 | 2,479 | 15.24 | 4.36 | 1 | 0 | Bilateral_legs | Infection | 7.4 | 9.6 | 1 | 0 | 0 | Infection | 0 | 4.9 | 66.4 | 0 | Hydromorphone | 0 | 0 | 34 | null | 74.4 | 88 | 0 | 0 | 1.6 | 28 | 1 | 0 | 190 | 0 | 1 | 0 | 94.1 | 0 | 1 | I | 0 | 1 | NPSR | 1 | 0 | 1 | 1 | 0 | 0 | Surgical_splenectomy | 0 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_prevention | 47.4 | 48 | 0 | 0 | 0 | 0 | 26,668 | 13.04 | 0 | Deferasirox | 0.36 | 0 | 0.211 | 0.89 | 1 | 24.2 | 24.2 | 21.5 | 5.45 | 0.434 | 0.57 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | UCB | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 7 | 43.4 | 50.3 | 77.9 | 10 | 14 | 16 | Employed_full | 0 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000049 | HbSC | Female | African_born | US_Northeast | Low | 1.22 | 16.8 | 11.9 | 1_gene_del | 0 | 10.46 | 7.66 | 69.6 | 13.3 | 14.1 | 392 | 506 | 9.31 | 74 | 1.31 | 5.3 | 210 | 884 | 4,762 | 5.47 | 3.33 | 0 | 0 | Lumbar_back | Unknown | 4.3 | 7.1 | 0 | 0 | 0 | Infection | 0 | 1.6 | 55.7 | 0 | Oxycodone | 0 | 4 | 25 | null | 74.9 | 785 | 0 | 0 | 2.04 | 64 | 1 | 0 | 217 | 0 | 0 | 0 | 91.1 | 1 | 1 | III | 0 | 1 | null | 0 | 0 | 1 | 0 | 0 | 0 | Surgical_splenectomy | 1 | 0 | Streptococcus_pneumoniae | 1 | Episodic | Stroke_treatment | 50.2 | 79 | 1 | 3 | 1 | 0 | 10,824 | 2.54 | 0 | Deferasirox | 0.64 | 0 | 0.185 | 0.71 | 1 | 23.8 | 23.8 | 19.6 | 5.6 | 0.619 | 0.63 | 0 | 0 | 0 | 1 | 0.224 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 15 | 24.8 | 38.2 | 67.4 | 8 | 8 | 13 | Employed_part | 0 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000050 | HbSS | Male | Black_non_Hispanic | US_South | Low | 0.27 | 22 | 6.8 | No_deletion | 0 | 9.38 | 4.58 | 79.4 | 10.4 | 4 | 391 | 356 | 7.8 | 75 | 0.54 | 8.6 | 385 | 48 | 2,441 | 1.85 | 4.33 | 5 | 1 | Abdomen | Dehydration | 10.8 | 5.4 | 1 | 0 | 0 | Hypoventilation | 1 | 8 | 67.1 | 1 | Hydromorphone | 112.1 | 3 | 13 | null | 92 | 1,531 | 0 | 1 | 2.21 | 23 | 0 | 1 | 161 | 0 | 0 | 0 | 76.5 | 0 | 1 | I | 0 | 0 | PSR_Sea_Fan | 0 | 1 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | Chronic_simple | Stroke_treatment | 25.9 | 65 | 0 | 0 | 0 | 1 | 10,922 | 9.25 | 0 | Deferasirox | 0.56 | 0 | 0.243 | 0.56 | 1 | 10.7 | 10.7 | 5 | 6.05 | 0.192 | 0.92 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 17 | 20 | 53 | 51.1 | 12 | 7 | 11 | Unemployed | 1 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000051 | HbSS | Male | Hispanic | US_South | High | 2 | 25.3 | 17.7 | 2_gene_del | 0 | 9.78 | 9.87 | 84.7 | 5.3 | 16.2 | 359 | 468 | 2.62 | 58 | 1.64 | 6.4 | 74 | 46 | 2,104 | 5.2 | 3.99 | 1 | 0 | Lumbar_back | Unknown | 6.6 | 8.8 | 0 | 0 | 0 | Infection | 1 | 2.6 | 83.4 | 1 | Oxycodone | 72.7 | 0 | 10 | Hyperfiltration | 140.6 | 13 | 0 | 0 | 2.1 | 59 | 1 | 0 | 172 | 0 | 1 | 0 | 66 | 1 | 0 | IV | 1 | 0 | null | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 1 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_treatment | 44.1 | 80 | 1 | 0 | 1 | 0 | 5,103 | 2.13 | 1 | Deferasirox | 0.54 | 0 | 0.282 | 0.5 | 0 | 0 | 0 | 0 | 9.1 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | Myeloablative | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | null | 0 | null | 0 | 1 | 30 | 45.1 | 60.8 | 62.1 | 9 | 6 | 9 | Disability | 1 | 0 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000052 | HbSS | Male | Black_non_Hispanic | US_Northeast | Low | 2 | 25.7 | 4.1 | 1_gene_del | 0 | 7.04 | 5.42 | 93.8 | 11.4 | 12.9 | 531 | 564 | 2.15 | 38 | 0.76 | 5.9 | 279 | 39 | 5,000 | 3.91 | 4.95 | 4 | 0 | Abdomen | Cold_exposure | 16.8 | 10 | 0 | 0 | 0 | Fat_embolism | 0 | 6.6 | 69.2 | 0 | Morphine | 0 | 1 | 15 | Microalbuminuria | 84.9 | 39 | 0 | 0 | 3.13 | 54 | 1 | 0 | 157 | 1 | 0 | 0 | 76.5 | 0 | 0 | I | 0 | 1 | null | 0 | 1 | 1 | 1 | 1 | 15.2 | Autoinfarction | 1 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 34.9 | 71 | 1 | 0 | 0 | 0 | 1,146 | 4.3 | 0 | Deferoxamine | 0.6 | 0 | 0.297 | 0.53 | 0 | 0 | 0 | 0 | 15.39 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 29 | 51.9 | 57.4 | 62.3 | 7 | 7 | 5 | Disability | 0 | 1 | 0 | 1 | 1 | 1 | HC-GEN-002 |
HC002-000053 | HbSC | Male | Black_non_Hispanic | US_Northeast | Middle | 1.68 | 15.1 | 7.9 | No_deletion | 0 | 10.39 | 5.01 | 77.4 | 13.3 | 18.4 | 450 | 313 | 10.17 | 57 | 0.76 | 8.9 | 169 | 229 | 3,329 | 9.6 | 3.35 | 0 | 1 | Lumbar_back | Infection | 4.2 | 5.6 | 0 | 0 | 0 | Infection | 1 | 5.2 | 72.4 | 1 | Hydromorphone | 216 | 7 | 19 | null | 146.9 | 48 | 0 | 0 | 2.03 | 61 | 0 | 0 | 163 | 0 | 1 | 0 | 85.4 | 0 | 0 | III | 0 | 1 | NPSR | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 25.9 | 130 | 0 | 0 | 0 | 0 | 806 | 30.88 | 0 | Deferasirox | 0.93 | 0 | 0.236 | 0.51 | 1 | 21.4 | 21.4 | 17.8 | 6.48 | 0.654 | 0.64 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 1 | MUD | RIC | 1 | 0 | 0 | 0.899 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 1 | 18 | 31.9 | 46.9 | 63.2 | 11 | 7 | 17 | Unemployed | 1 | 1 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000054 | HbSC | Female | Black_non_Hispanic | US_Northeast | Middle | 2 | 17.7 | 17.1 | 1_gene_del | 1 | 7.95 | 3.12 | 76.9 | 14.7 | 8.7 | 544 | 244 | 5.53 | 39 | 0.78 | 7.7 | 2,416 | 117 | 3,382 | 6.51 | 3.92 | 4 | 0 | Lumbar_back | Unknown | 3.4 | 7.3 | 0 | 0 | 0 | Infection | 1 | 1.3 | 44.5 | 0 | Morphine | 0 | 5 | 11 | null | 157.9 | 1,348 | 0 | 0 | 1.5 | 92 | 1 | 0 | 142 | 0 | 0 | 0 | 121.7 | 0 | 0 | IV | 0 | 0 | VH_RD | 0 | 1 | 1 | 1 | 0 | 0 | Normal | 1 | 0 | E_coli | 0 | null | Stroke_prevention | 40 | 95 | 0 | 0 | 0 | 0 | 2,918 | 3.04 | 0 | Deferasirox | 0.65 | 0 | 0.231 | 0.81 | 1 | 15.4 | 10.8 | 4.4 | 3.88 | 0.554 | 0.8 | 1 | 0 | 0 | 0 | 0 | 1 | 1.35 | 1 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | null | 0 | null | 0 | 1 | 46 | 48.7 | 35.3 | 55.2 | 15 | 14 | 17 | Disability | 1 | 0 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000055 | HbSC | Male | Black_non_Hispanic | US_South | Low | 0.77 | 5.6 | 4.6 | No_deletion | 0 | 12.07 | 5.07 | 81.6 | 11.2 | 5.7 | 580 | 480 | 3.18 | 86 | 0.77 | 5.4 | 277 | 50 | 5,000 | 2.67 | 3.14 | 0 | 1 | Lumbar_back | Infection | 1.9 | 9.2 | 0 | 0 | 0 | Unknown | 1 | 2.3 | 66.3 | 1 | Hydromorphone | 9 | 13 | 10 | null | 120 | 83 | 0 | 0 | 2.02 | 110 | 0 | 0 | 165 | 0 | 1 | 0 | 82.6 | 0 | 1 | I | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Streptococcus_pneumoniae | 0 | Episodic | ACS | 46.4 | 99 | 1 | 1 | 0 | 0 | 7,004 | 3.36 | 1 | Deferasirox | 0.54 | 0 | 0.167 | 0.79 | 1 | 25.9 | 25.9 | 6.6 | 6.06 | 0.697 | 0.61 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 24 | 52.7 | 52.1 | 54.6 | 16 | 2 | 9 | Unemployed | 0 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000056 | HbSC | Male | Hispanic | Europe | Middle | 1.19 | 20.9 | 16.6 | No_deletion | 0 | 13.39 | 12.66 | 84.8 | 3.2 | 11 | 475 | 317 | 5.45 | 53 | 0.4 | 5 | 152 | 85 | 2,608 | 19.63 | 2.21 | 2 | 1 | Chest | Unknown | 7 | 7.4 | 0 | 0 | 0 | Unknown | 1 | 2.4 | 59.1 | 0 | Morphine | 0 | 2 | 50 | Hyperfiltration | 153 | 327 | 0 | 0 | 2.05 | 38 | 1 | 0 | 226 | 0 | 1 | 0 | 84.6 | 0 | 0 | II | 0 | 0 | null | 0 | 1 | 1 | 0 | 0 | 0 | Surgical_splenectomy | 0 | 0 | Haemophilus_influenzae | 0 | Chronic_simple | ACS | 29.3 | 50 | 0 | 0 | 0 | 0 | 5,911 | 2.84 | 0 | Deferasirox | 0.88 | 0 | 0.273 | 0.5 | 1 | 12 | 12 | 15.7 | 1.5 | 0.555 | 0.6 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 5 | 42.5 | 50.6 | 78.3 | 12 | 6 | 4 | Employed_full | 1 | 1 | 1 | 0 | 1 | 1 | HC-GEN-002 |
HC002-000057 | HbSS | Male | Middle_Eastern | Other | High | 2 | 31 | 2.5 | 1_gene_del | 0 | 8.31 | 3.77 | 80.8 | 5.8 | 10.2 | 359 | 431 | 7.26 | 50 | 0.68 | 8.5 | 81 | 55 | 2,881 | 14.47 | 4.67 | 0 | 0 | Bilateral_legs | Unknown | 6.7 | 4.1 | 0 | 0 | 0 | Hypoventilation | 0 | 3.3 | 54.5 | 0 | Morphine | 0 | 3 | 27 | null | 62.4 | 129 | 0 | 0 | 2 | 134 | 0 | 0 | 149 | 1 | 0 | 1 | 75.1 | 0 | 0 | III | 0 | 0 | VH_RD | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | Chronic_simple | Stroke_prevention | 28.6 | 36 | 0 | 0 | 0 | 1 | 21,355 | 35.74 | 0 | Deferasirox | 0.75 | 0 | 0.127 | 0.5 | 1 | 23.4 | 23.4 | 29.2 | 6.54 | 0.312 | 0.82 | 0 | 1 | 0.198 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | null | 0 | null | 0 | 1 | 18 | 36 | 79.3 | 52.1 | 13 | 3 | 20 | Unemployed | 1 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000058 | HbSS | Male | Black_non_Hispanic | US_Northeast | Middle | 0.72 | 7.6 | 10.3 | No_deletion | 0 | 5.22 | 7.46 | 90.4 | 20.2 | 13 | 545 | 220 | 5.8 | 47 | 0.4 | 6.8 | 695 | 163 | 4,242 | 21.52 | 4.89 | 2 | 0 | Abdomen | Infection | 1.9 | 8 | 0 | 0 | 0 | Infection | 0 | 3.4 | 61.8 | 1 | Oxycodone | 23 | 4 | 31 | Microalbuminuria | 90.5 | 21 | 0 | 0 | 1.81 | 56 | 0 | 0 | 141 | 0 | 1 | 0 | 91.4 | 0 | 0 | II | 0 | 0 | VH_RD | 0 | 0 | 0 | 0 | 1 | 16.5 | Normal | 1 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_treatment | 57.1 | 32 | 0 | 0 | 0 | 1 | 2,312 | 40 | 0 | Deferoxamine | 0.65 | 0 | 0.268 | 0.84 | 1 | 18.8 | 13.1 | 12.2 | 2.6 | 0.558 | 0.74 | 1 | 0 | 0 | 1 | 0.433 | 1 | 0.93 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 24 | 41.3 | 60.3 | 50.5 | 6 | 5 | 18 | Unemployed | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000059 | HbSS | Female | Black_non_Hispanic | US_Midwest | Low | 1.65 | 34.8 | 2.4 | 2_gene_del | 0 | 9.05 | 2.61 | 75.6 | 7.6 | 14.2 | 476 | 360 | 2.78 | 90 | 1.67 | 4.5 | 185 | 1,780 | 1,685 | 7.31 | 4.53 | 2 | 1 | Bilateral_legs | Infection | 5.3 | 5.4 | 0 | 0 | 0 | Unknown | 1 | 7.5 | 63.2 | 1 | Morphine | 73.6 | 4 | 22 | Microalbuminuria | 116.6 | 10 | 0 | 0 | 1.57 | 271 | 1 | 0 | 148 | 0 | 1 | 0 | 87.4 | 0 | 1 | III | 0 | 1 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 1 | Salmonella_sp | 0 | null | Splenic_sequestration | 55.1 | 39 | 0 | 0 | 0 | 0 | 2,190 | 15.26 | 0 | Deferoxamine | 0.39 | 0 | 0.221 | 0.82 | 1 | 24.6 | 24.6 | 20.2 | 1.59 | 0.567 | 0.7 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 31 | 43.3 | 77.8 | 41.9 | 8 | 7 | 14 | Unemployed | 1 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000060 | HbSS | Male | Hispanic | Africa | Low | 1.57 | 38.3 | 13.9 | No_deletion | 0 | 6.93 | 4.89 | 83 | 17.7 | 10.7 | 732 | 557 | 15 | 25 | 1.64 | 4.1 | 130 | 211 | 4,067 | 5.88 | 5 | 3 | 1 | Lumbar_back | Unknown | 5.3 | 4.9 | 1 | 1 | 1 | Hypoventilation | 0 | 3.4 | 55.1 | 0 | Oxycodone | 0 | 2 | 32 | null | 117.8 | 43 | 0 | 1 | 3.11 | 42 | 1 | 0 | 134 | 0 | 1 | 0 | 76.3 | 1 | 0 | I | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_prevention | 58.6 | 32 | 0 | 0 | 0 | 0 | 3,282 | 40 | 0 | Deferasirox | 0.67 | 0 | 0.123 | 0.84 | 0 | 0 | 0 | 0 | 9.71 | 0 | 0 | 0 | 0 | 0 | 1 | 0.639 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 1 | Renal_failure | 540.4 | 1 | 18 | 12.1 | 53.3 | 59.2 | 11 | 13 | 14 | Disability | 0 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000061 | HbSC | Male | Middle_Eastern | Other | High | 0.65 | 25.1 | 16 | No_deletion | 0 | 9.57 | 7.16 | 85.6 | 8.3 | 10.3 | 457 | 530 | 10 | 93 | 1.13 | 5.1 | 320 | 111 | 2,495 | 10.62 | 3.57 | 1 | 1 | Chest | Dehydration | 3 | 4.1 | 0 | 0 | 0 | Unknown | 1 | 2.5 | 64.1 | 0 | Hydromorphone | 0 | 4 | 21 | Hyperfiltration | 160 | 1,451 | 0 | 1 | 2.38 | 20 | 0 | 0 | 150 | 0 | 0 | 0 | 79.9 | 0 | 0 | IV | 0 | 1 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Staphylococcus_aureus | 0 | Episodic | Stroke_prevention | 53.2 | 62 | 0 | 0 | 0 | 0 | 912 | 5.13 | 0 | Deferasirox | 0.48 | 0 | 0.233 | 0.78 | 0 | 0 | 0 | 0 | 5.8 | 0 | 0 | 0 | 0 | 0 | 1 | 0.463 | 0 | 0 | 0 | 0 | Haplo | NMA | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 21 | 33.8 | 70.3 | 47.8 | 10 | 9 | 11 | Employed_full | 0 | 1 | 0 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000062 | HbSS | Male | Black_non_Hispanic | US_Midwest | Low | 2 | 34.9 | 17.1 | No_deletion | 0 | 9.08 | 6.01 | 78.8 | 11.3 | 12.6 | 504 | 283 | 5.12 | 41 | 0.66 | 4.9 | 411 | 62 | 5,000 | 3.81 | 4.23 | 1 | 1 | Bilateral_legs | Stress | 3.4 | 9.3 | 0 | 0 | 0 | Infection | 0 | 2.2 | 60.1 | 1 | Other | 17.7 | 1 | 21 | CKD3+ | 75 | 123 | 0 | 0 | 2.02 | 130 | 0 | 0 | 133 | 1 | 1 | 0 | 67.2 | 1 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 0 | 1 | 21.2 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | Chronic_simple | Stroke_prevention | 25.7 | 84 | 0 | 0 | 0 | 0 | 16,981 | 40 | 0 | Deferoxamine | 0.48 | 0 | 0.214 | 0.82 | 1 | 30.2 | 30.2 | 16.3 | 8.31 | 0.131 | 0.61 | 0 | 0 | 0 | 1 | 0.516 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 30 | 21.6 | 62.6 | 85 | 12 | 3 | 13 | Employed_full | 1 | 1 | 0 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000063 | HbSS | Female | Black_non_Hispanic | Africa | Middle | 2 | 22.1 | 19.6 | No_deletion | 0 | 8.56 | 2.92 | 88.7 | 14.5 | 10.2 | 455 | 238 | 5.22 | 25 | 0.45 | 3.7 | 406 | 32 | 4,785 | 6.71 | 4.5 | 1 | 0 | Chest | Dehydration | 3.7 | 5.7 | 0 | 0 | 0 | Infection | 1 | 6.4 | 69.7 | 1 | Hydromorphone | 88.8 | 3 | 32 | null | 91.2 | 319 | 0 | 0 | 2.95 | 94 | 1 | 1 | 186 | 0 | 1 | 0 | 73.9 | 0 | 1 | II | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Autoinfarction | 1 | 0 | Streptococcus_pneumoniae | 0 | Chronic_exchange | Stroke_prevention | 34.3 | 82 | 0 | 0 | 0 | 0 | 2,472 | 8.04 | 1 | Deferasirox | 0.77 | 0 | 0.202 | 0.74 | 1 | 26.2 | 26.2 | 7.5 | 3.85 | 0.602 | 0.7 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 35 | 25.6 | 52.1 | 47 | 16 | 6 | 21 | Unemployed | 1 | 0 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000064 | HbSC | Female | Black_non_Hispanic | Africa | Low | 1.99 | 17.1 | 13.8 | No_deletion | 0 | 9.82 | 5.6 | 83.2 | 8.7 | 10 | 408 | 406 | 7.24 | 33 | 0.53 | 5.2 | 249 | 253 | 4,480 | 5.26 | 3.51 | 1 | 0 | Bilateral_legs | Dehydration | 7 | 7.8 | 1 | 0 | 0 | Hypoventilation | 0 | 1.7 | 64.5 | 0 | Oxycodone | 0 | 3 | 15 | Hyperfiltration | 107 | 16 | 0 | 0 | 1.75 | 174 | 0 | 0 | 182 | 0 | 0 | 0 | 89.2 | 0 | 0 | II | 0 | 1 | null | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | Stroke_prevention | 58.9 | 62 | 0 | 0 | 0 | 0 | 4,300 | 32.06 | 0 | Deferasirox | 0.42 | 0 | 0.209 | 0.77 | 1 | 26.1 | 26.1 | 10.3 | 4 | 0.47 | 0.63 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 1 | MSD | NMA | 1 | 0 | 0 | 0.918 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 0 | 18 | 38.2 | 62.3 | 53.5 | 8 | 12 | 13 | Employed_full | 1 | 0 | 1 | 0 | 1 | 0 | HC-GEN-002 |
HC002-000065 | HbSS | Female | Black_non_Hispanic | Europe | Middle | 0.5 | 9.1 | 15.6 | No_deletion | 0 | 7.29 | 6.42 | 88.3 | 18.4 | 14.1 | 389 | 519 | 3.44 | 23 | 1.96 | 5.4 | 278 | 240 | 1,630 | 1.88 | 4.79 | 6 | 1 | Chest | Cold_exposure | 3.8 | 8.2 | 0 | 0 | 0 | Unknown | 0 | 6.9 | 66.1 | 1 | Morphine | 128.4 | 5 | 32 | Hyperfiltration | 91.8 | 61 | 0 | 0 | 2.34 | 85 | 1 | 0 | 227 | 0 | 1 | 0 | 85.7 | 0 | 0 | II | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 0 | Haemophilus_influenzae | 0 | null | Splenic_sequestration | 40 | 26 | 1 | 0 | 0 | 0 | 7,971 | 16 | 0 | Deferasirox | 0.9 | 0 | 0.219 | 0.68 | 0 | 0 | 0 | 0 | 15.37 | 0 | 0 | 0 | 0 | 0 | 1 | 0.191 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 20 | 33.6 | 58.3 | 85 | 2 | 5 | 22 | Employed_full | 0 | 0 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000066 | HbSS | Female | Other | US_Northeast | High | 0.33 | 8.5 | 10.6 | No_deletion | 0 | 8.38 | 5 | 83.6 | 12.3 | 14.8 | 455 | 484 | 7.11 | 58 | 0.52 | 6.1 | 295 | 76 | 3,458 | 6.7 | 4.63 | 8 | 0 | Lumbar_back | Stress | 4.1 | 7.5 | 0 | 0 | 0 | Infection | 0 | 7.2 | 72.8 | 0 | Hydromorphone | 0 | 2 | 13 | null | 73.5 | 229 | 0 | 0 | 1.6 | 434 | 1 | 0 | 139 | 0 | 1 | 0 | 78 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | Pre_op | 50.3 | 54 | 0 | 0 | 0 | 0 | 1,422 | 2.42 | 0 | Deferiprone | 0.32 | 0 | 0.219 | 0.86 | 1 | 11.7 | 11.7 | 16.8 | 3.16 | 0.34 | 0.67 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 14 | 34.9 | 57.3 | 73.9 | 5 | 8 | 6 | Disability | 0 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000067 | HbSS | Female | Black_non_Hispanic | US_South | Middle | 2 | 34.9 | 18.3 | No_deletion | 0 | 7.63 | 3.79 | 85 | 13.8 | 14.3 | 483 | 320 | 3.11 | 30 | 0.4 | 9.3 | 320 | 409 | 2,021 | 4.25 | 4.72 | 7 | 0 | Arms | Stress | 5.5 | 7.7 | 0 | 0 | 0 | Infection | 1 | 3.2 | 68.1 | 1 | Morphine | 152.2 | 7 | 15 | Microalbuminuria | 93.3 | 24 | 0 | 0 | 2.4 | 57 | 0 | 0 | 152 | 0 | 0 | 0 | 109.5 | 0 | 0 | I | 0 | 0 | NPSR | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | Chronic_exchange | ACS | 26.9 | 81 | 1 | 2 | 0 | 0 | 4,416 | 6.79 | 1 | Deferasirox | 0.75 | 0 | 0.161 | 0.86 | 1 | 22.5 | 22.5 | 11.1 | 3.93 | 0.416 | 0.77 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 18 | 33.3 | 43.8 | 41.9 | 10 | 9 | 12 | Disability | 1 | 1 | 1 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000068 | HbSS | Male | Hispanic | US_South | High | 2 | 41.7 | 13.2 | No_deletion | 1 | 6.65 | 7.4 | 76.9 | 10.9 | 10.5 | 559 | 461 | 5.84 | 48 | 1.24 | 6.4 | 344 | 124 | 3,574 | 4.98 | 4.81 | 1 | 1 | Lumbar_back | Cold_exposure | 8.8 | 7.9 | 0 | 0 | 0 | Hypoventilation | 0 | 5.9 | 61.9 | 0 | Other | 0 | 2 | 11 | null | 101.4 | 83 | 0 | 0 | 1.65 | 154 | 1 | 0 | 150 | 0 | 1 | 0 | 97.9 | 0 | 1 | III | 0 | 0 | PSR_Sea_Fan | 0 | 1 | 0 | 0 | 1 | 4.3 | Surgical_splenectomy | 0 | 0 | Salmonella_sp | 0 | null | Splenic_sequestration | 40.8 | 34 | 1 | 2 | 0 | 0 | 3,227 | 19.51 | 0 | Deferasirox | 0.71 | 0 | 0.236 | 0.76 | 1 | 23.6 | 23.6 | 12.5 | 3.57 | 0.556 | 0.64 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 33 | 32.7 | 80.1 | 62.1 | 7 | 6 | 12 | Employed_part | 1 | 1 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000069 | HbSS | Male | Black_non_Hispanic | US_Northeast | Low | 2 | 24.5 | 17.8 | 1_gene_del | 0 | 7.73 | 3.91 | 77 | 14.6 | 4.6 | 457 | 793 | 3.37 | 70 | 1.57 | 6.5 | 587 | 264 | 1,144 | 8.09 | 5.11 | 4 | 0 | Chest | Infection | 2.6 | 7.4 | 1 | 1 | 0 | Unknown | 0 | 4.4 | 39 | 1 | Oxycodone | 208.5 | 12 | 28 | null | 160.7 | 31 | 0 | 0 | 2.29 | 44 | 0 | 1 | 148 | 1 | 0 | 0 | 77.2 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 0 | 0 | 1 | 15.7 | Autoinfarction | 1 | 0 | Haemophilus_influenzae | 0 | Chronic_simple | Stroke_prevention | 34.9 | 57 | 1 | 3 | 0 | 1 | 9,516 | 2.59 | 1 | Deferoxamine | 0.48 | 0 | 0.205 | 0.87 | 1 | 25.3 | 25.3 | 29.6 | 7.74 | 0.517 | 0.48 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 16 | 34.3 | 66 | 64.6 | 3 | 3 | 13 | Employed_full | 0 | 1 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000070 | HbSS | Female | Black_non_Hispanic | US_Northeast | Middle | 2 | 38 | 5.5 | No_deletion | 1 | 8.68 | 6.74 | 91.8 | 18.3 | 10.6 | 364 | 442 | 3.46 | 34 | 1.7 | 7.6 | 256 | 163 | 1,685 | 16.74 | 4.41 | 3 | 0 | Lumbar_back | Infection | 6.1 | 5.8 | 0 | 0 | 0 | Unknown | 1 | 1.8 | 67.7 | 0 | Oxycodone | 0 | 2 | 21 | Hyperfiltration | 74.3 | 243 | 0 | 0 | 2.88 | 99 | 0 | 0 | 185 | 1 | 1 | 0 | 60.4 | 1 | 0 | II | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 1 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 33.1 | 66 | 0 | 0 | 0 | 0 | 3,285 | 22.12 | 0 | Deferasirox | 0.41 | 0 | 0.283 | 0.5 | 1 | 21.5 | 21.5 | 11.9 | 4.34 | 0.44 | 0.62 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 48 | 50.3 | 49.1 | 51.1 | 9 | 8 | 30 | Disability | 1 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000071 | HbSS | Male | African_born | US_Northeast | High | 2 | 27.3 | 10.4 | 1_gene_del | 0 | 7.95 | 6.9 | 87.1 | 11.5 | 8.7 | 381 | 193 | 13.78 | 40 | 1.25 | 6.4 | 127 | 102 | 5,000 | 3.07 | 4.33 | 6 | 0 | Chest | Dehydration | 2.6 | 5.7 | 1 | 0 | 0 | Unknown | 1 | 4.7 | 52 | 1 | Morphine | 10.6 | 2 | 20 | Macroalbuminuria | 138.5 | 145 | 0 | 1 | 2.29 | 115 | 0 | 1 | 80 | 1 | 1 | 0 | 71.6 | 0 | 0 | IV | 0 | 0 | null | 0 | 1 | 1 | 1 | 0 | 0 | Surgical_splenectomy | 1 | 0 | E_coli | 0 | Chronic_simple | Stroke_prevention | 29.5 | 54 | 0 | 0 | 0 | 0 | 180 | 3.99 | 0 | Deferasirox | 0.66 | 0 | 0.254 | 0.71 | 0 | 0 | 0 | 0 | 6.26 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | NMA | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 0 | 31 | 41.2 | 64.1 | 68.7 | 5 | 16 | 17 | Disability | 1 | 1 | 0 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000072 | HbSS | Female | Black_non_Hispanic | US_Midwest | Middle | 2 | 33.6 | 14.9 | No_deletion | 0 | 6.22 | 5.52 | 73.8 | 18.9 | 10.6 | 261 | 442 | 6.23 | 27 | 1.35 | 7.4 | 218 | 47 | 4,379 | 4.62 | 5.01 | 6 | 0 | Abdomen | Infection | 3.2 | 7 | 0 | 0 | 0 | Hypoventilation | 0 | 5.7 | 61.1 | 0 | Morphine | 0 | 5 | 5 | null | 154.5 | 204 | 0 | 0 | 1.5 | 130 | 1 | 0 | 158 | 0 | 0 | 0 | 90.4 | 0 | 0 | IV | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | E_coli | 0 | Chronic_exchange | ACS | 31.7 | 39 | 0 | 0 | 0 | 0 | 1,164 | 28.24 | 0 | Deferoxamine | 0.69 | 0 | 0.259 | 0.78 | 1 | 16.2 | 16.2 | 14.1 | 2.92 | 0.438 | 0.79 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 33 | 25.1 | 57 | 46.3 | 12 | 5 | 13 | Employed_part | 0 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000073 | HbSC | Male | Black_non_Hispanic | US_Midwest | Low | 2 | 26.4 | 4.9 | 2_gene_del | 0 | 11.88 | 9.4 | 83.4 | 9.6 | 9 | 619 | 1,012 | 6.71 | 38 | 0.76 | 7.2 | 447 | 105 | 3,051 | 3.28 | 3.37 | 0 | 1 | Abdomen | Infection | 8.6 | 7 | 0 | 0 | 0 | Unknown | 0 | 5.5 | 66.1 | 1 | Hydromorphone | 120 | 12 | 25 | Hyperfiltration | 92.1 | 256 | 0 | 0 | 2.11 | 124 | 0 | 1 | 220 | 0 | 0 | 0 | 91.2 | 0 | 0 | III | 0 | 0 | PSR_Sea_Fan | 0 | 1 | 1 | 1 | 0 | 0 | Normal | 0 | 0 | Salmonella_sp | 0 | null | Splenic_sequestration | 42.9 | 39 | 0 | 0 | 0 | 0 | 625 | 4.22 | 0 | Deferiprone | 0.27 | 0 | 0.294 | 0.81 | 1 | 34 | 23.8 | 15.7 | 2.15 | 0.364 | 0.58 | 1 | 1 | 0.328 | 0 | 0 | 0 | 0 | 0 | 1 | Haplo | Myeloablative | 1 | 0 | 0 | 0.874 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 47 | 30.6 | 73.7 | 43.2 | 17 | 5 | 14 | Disability | 0 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000074 | HbSS | Female | Middle_Eastern | Africa | High | 1.94 | 25.9 | 5 | 2_gene_del | 0 | 4.5 | 12.19 | 63 | 15.1 | 10.9 | 355 | 226 | 2.21 | 125 | 0.4 | 7 | 59 | 282 | 2,311 | 3.11 | 4.73 | 5 | 1 | Bilateral_legs | Cold_exposure | 4.5 | 8 | 1 | 0 | 0 | Fat_embolism | 0 | 4.4 | 76.7 | 0 | Morphine | 0 | 3 | 32 | null | 119.1 | 68 | 0 | 0 | 2.29 | 20 | 0 | 1 | 195 | 0 | 0 | 0 | 87.2 | 0 | 0 | I | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Surgical_splenectomy | 1 | 0 | E_coli | 0 | null | Pre_op | 58.9 | 71 | 0 | 0 | 0 | 0 | 27,000 | 25.62 | 0 | Deferasirox | 0.67 | 0 | 0.249 | 0.6 | 0 | 0 | 0 | 0 | 8.12 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 1 | MSD | Myeloablative | 1 | 0 | 0 | 0.974 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 46 | 41.4 | 57.5 | 72.4 | 15 | 10 | 21 | Employed_full | 0 | 0 | 1 | 1 | 1 | 1 | HC-GEN-002 |
HC002-000075 | HbSS | Female | African_born | US_South | Low | 0.32 | 19 | 19.6 | No_deletion | 0 | 7.58 | 7.1 | 77.4 | 14 | 7.9 | 536 | 409 | 4.49 | 61 | 0.75 | 10.9 | 59 | 73 | 2,117 | 3.76 | 4.59 | 2 | 0 | Bilateral_legs | Dehydration | 4.5 | 9.2 | 0 | 0 | 0 | Infection | 1 | 1.1 | 82.3 | 0 | Hydromorphone | 0 | 1 | 39 | Hyperfiltration | 130.2 | 300 | 0 | 0 | 2.46 | 63 | 1 | 0 | 190 | 0 | 1 | 0 | 71.4 | 0 | 0 | IV | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 0 | Staphylococcus_aureus | 0 | Chronic_exchange | Stroke_treatment | 27.2 | 40 | 1 | 0 | 0 | 0 | 15,426 | 37.21 | 0 | Deferoxamine | 0.61 | 0 | 0.214 | 0.87 | 1 | 16.5 | 16.5 | 0.6 | 4.66 | 0.581 | 0.8 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 19 | 31.9 | 59.8 | 68.2 | 4 | 17 | 22 | Employed_part | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000076 | HbSS | Female | Black_non_Hispanic | US_South | Middle | 0.57 | 26.3 | 9.3 | No_deletion | 0 | 7.33 | 4.04 | 89.7 | 7.7 | 7.2 | 453 | 364 | 7.62 | 40 | 1.01 | 8.2 | 510 | 189 | 4,024 | 5.17 | 4.8 | 9 | 1 | Abdomen | Dehydration | 8.6 | 7.8 | 0 | 0 | 0 | Hypoventilation | 0 | 1.2 | 51.9 | 0 | Oxycodone | 0 | 2 | 43 | Hyperfiltration | 124.4 | 44 | 0 | 0 | 2.69 | 42 | 1 | 0 | 174 | 1 | 0 | 0 | 80.4 | 1 | 0 | I | 0 | 1 | PSR_Sea_Fan | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 1 | 1 | Streptococcus_pneumoniae | 0 | Chronic_simple | Stroke_prevention | 32.2 | 27 | 0 | 0 | 0 | 0 | 306 | 13.9 | 0 | Deferasirox | 0.83 | 0 | 0.12 | 0.95 | 0 | 0 | 0 | 0 | 8.76 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 1 | Haplo | Myeloablative | 1 | 1 | 0 | 0.869 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 23 | 39.7 | 54.1 | 82.2 | 6 | 4 | 11 | Employed_full | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000077 | HbSS | Female | Black_non_Hispanic | Europe | High | 1.06 | 16.5 | 4.5 | No_deletion | 0 | 8.41 | 9.14 | 81 | 12.9 | 14.7 | 456 | 421 | 6.67 | 35 | 0.69 | 5.2 | 826 | 41 | 3,066 | 9.67 | 4.29 | 4 | 0 | Bilateral_legs | Stress | 5.7 | 5.7 | 0 | 0 | 0 | Hypoventilation | 1 | 3.8 | 47.5 | 1 | Oxycodone | 23.2 | 0 | 20 | Hyperfiltration | 112.9 | 191 | 0 | 0 | 2.71 | 49 | 0 | 0 | 116 | 0 | 0 | 0 | 87.8 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | null | ACS | 50.5 | 55 | 0 | 0 | 0 | 0 | 1,071 | 15.18 | 0 | Deferoxamine | 0.65 | 0 | 0.23 | 0.75 | 1 | 15.3 | 15.3 | 13.4 | 2.6 | 0.738 | 0.59 | 0 | 1 | 0.05 | 0 | 0 | 0 | 0 | 0 | 1 | Haplo | NMA | 1 | 0 | 1 | 0.908 | 1 | Lovotibeglogene_autotemcel | 10,000,000 | 46.7 | 30.8 | 0 | 0.653 | Complete | 0 | null | 0 | 1 | 21 | 34.5 | 65 | 60.7 | 1 | 2 | 12 | Disability | 1 | 0 | 1 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000078 | HbSC | Female | Black_non_Hispanic | Africa | Low | 0.41 | 8.8 | 7.3 | No_deletion | 0 | 11.29 | 8.41 | 82.9 | 12 | 8.1 | 406 | 440 | 2.06 | 44 | 0.68 | 7.4 | 89 | 265 | 5,000 | 7.82 | 3.05 | 0 | 0 | Bilateral_legs | Dehydration | 5.2 | 3.3 | 0 | 0 | 0 | Fat_embolism | 1 | 5.7 | 65.6 | 1 | Morphine | 82.5 | 5 | 40 | CKD3+ | 86.2 | 10 | 0 | 0 | 2.05 | 53 | 0 | 1 | 110 | 0 | 0 | 0 | 88.9 | 0 | 0 | IV | 0 | 1 | null | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 0 | 1 | Salmonella_sp | 0 | Episodic | ACS | 54.7 | 60 | 0 | 0 | 0 | 0 | 709 | 40 | 1 | Deferoxamine | 0.69 | 0 | 0.289 | 0.83 | 1 | 22.1 | 22.1 | 17.2 | 4.03 | 0.402 | 0.9 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 27 | 37.2 | 59.4 | 79.1 | 15 | 10 | 17 | Employed_part | 1 | 1 | 0 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000079 | HbSS | Female | Black_non_Hispanic | Other | Low | 0.82 | 24.2 | 8.6 | No_deletion | 0 | 9.78 | 7.57 | 57.9 | 8.6 | 11 | 325 | 674 | 6.71 | 47 | 0.46 | 5.6 | 265 | 166 | 3,320 | 2.6 | 4.33 | 0 | 1 | Lumbar_back | Unknown | 3.9 | 5.8 | 1 | 0 | 0 | Infection | 0 | 2.5 | 64.7 | 1 | Oxycodone | 48.1 | 5 | 8 | Microalbuminuria | 133.2 | 37 | 0 | 0 | 1.84 | 146 | 1 | 0 | 110 | 0 | 0 | 0 | 93.1 | 0 | 0 | I | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Surgical_splenectomy | 1 | 0 | Staphylococcus_aureus | 0 | Chronic_exchange | Stroke_treatment | 33.2 | 35 | 0 | 0 | 0 | 0 | 4,129 | 7.51 | 0 | Deferoxamine | 0.31 | 0 | 0.256 | 0.95 | 1 | 22.7 | 22.7 | 14.6 | 1.88 | 0.23 | 0.85 | 0 | 0 | 0 | 1 | 0.427 | 0 | 0 | 0 | 1 | MSD | Myeloablative | 1 | 0 | 0 | 0.938 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 28 | 47.5 | 72.7 | 55.7 | 10 | 10 | 2 | Employed_full | 1 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000080 | HbSC | Male | Black_non_Hispanic | Africa | Low | 1.54 | 10.7 | 12.8 | 1_gene_del | 0 | 9.5 | 2.14 | 78.9 | 13.4 | 13.9 | 304 | 419 | 7.27 | 38 | 0.45 | 7.5 | 178 | 37 | 3,749 | 17.04 | 3.82 | 2 | 1 | Bilateral_legs | Infection | 4.6 | 4.8 | 0 | 0 | 0 | Unknown | 0 | 4.7 | 48.8 | 1 | Hydromorphone | 25.3 | 8 | 29 | null | 96.9 | 1,449 | 0 | 0 | 1.65 | 78 | 0 | 1 | 94 | 0 | 0 | 0 | 91.2 | 0 | 0 | I | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 1 | 0 | 0 | 0 | Autoinfarction | 0 | 0 | Staphylococcus_aureus | 0 | Chronic_simple | Stroke_prevention | 33.2 | 39 | 0 | 0 | 0 | 0 | 1,137 | 9.64 | 0 | Deferasirox | 0.76 | 0 | 0.2 | 0.7 | 1 | 19.5 | 19.5 | 14.6 | 3.31 | 0.453 | 0.86 | 0 | 0 | 0 | 1 | 0.056 | 0 | 0 | 0 | 0 | UCB | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 11 | 38.9 | 63 | 74.5 | 17 | 3 | 5 | Employed_full | 1 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000081 | HbSC | Male | Black_non_Hispanic | Africa | Low | 0.8 | 21.3 | 18.5 | 2_gene_del | 0 | 11.32 | 8.52 | 84.7 | 12.6 | 13.7 | 627 | 717 | 11.49 | 55 | 1.86 | 4.7 | 199 | 97 | 1,818 | 12.88 | 3.28 | 1 | 0 | Bilateral_legs | Dehydration | 3.8 | 5.9 | 1 | 1 | 0 | Unknown | 0 | 3.3 | 61.8 | 0 | Hydromorphone | 0 | 1 | 9 | CKD3+ | 111 | 187 | 0 | 0 | 1.88 | 44 | 0 | 0 | 178 | 0 | 0 | 0 | 92.9 | 1 | 0 | II | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 0 | 0 | Haemophilus_influenzae | 0 | Chronic_exchange | Stroke_prevention | 32.1 | 82 | 1 | 1 | 0 | 0 | 2,430 | 31.21 | 1 | Deferasirox | 0.43 | 0 | 0.222 | 0.95 | 1 | 21.3 | 21.3 | 18.1 | 1.6 | 0.396 | 0.84 | 0 | 0 | 0 | 1 | 0.367 | 0 | 0 | 0 | 0 | MUD | Myeloablative | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 25 | 54.4 | 84.1 | 82.4 | 12 | 6 | 13 | Employed_full | 0 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000082 | HbSS | Female | Middle_Eastern | US_Northeast | Low | 0.93 | 6.4 | 19.7 | No_deletion | 0 | 8.47 | 5.28 | 85.7 | 11.7 | 13.4 | 434 | 383 | 4.36 | 31 | 1.89 | 5.1 | 312 | 308 | 3,040 | 2.94 | 4.49 | 5 | 1 | Chest | Unknown | 3.1 | 7.6 | 1 | 0 | 0 | Infection | 1 | 3.2 | 68.6 | 0 | Hydromorphone | 0 | 1 | 22 | null | 116.2 | 187 | 0 | 0 | 2.29 | 21 | 1 | 0 | 199 | 0 | 1 | 0 | 79.2 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 1 | 1 | 0 | 0 | Autoinfarction | 1 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_prevention | 52.2 | 47 | 0 | 0 | 0 | 0 | 715 | 25.09 | 0 | Deferoxamine | 0.62 | 0 | 0.198 | 0.62 | 0 | 0 | 0 | 0 | 11.37 | 0 | 0 | 0 | 0 | 0 | 1 | 0.614 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 1 | Infection | 272.6 | 1 | 25 | 28 | 58.8 | 51.8 | 7 | 2 | 12 | Employed_full | 1 | 0 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000083 | HbSC | Male | Middle_Eastern | US_Northeast | Middle | 2 | 26.5 | 13.4 | 1_gene_del | 0 | 8.1 | 1.62 | 89.7 | 11.7 | 11.9 | 555 | 345 | 1.97 | 30 | 0.74 | 7.3 | 87 | 35 | 3,978 | 16.11 | 4.08 | 0 | 0 | Lumbar_back | Cold_exposure | 12.8 | 7.4 | 0 | 0 | 0 | Unknown | 1 | 4.2 | 48.5 | 0 | Hydromorphone | 0 | 0 | 9 | Microalbuminuria | 140 | 33 | 0 | 0 | 1.56 | 227 | 1 | 0 | 157 | 0 | 0 | 0 | 96.3 | 0 | 1 | II | 0 | 1 | NPSR | 1 | 0 | 1 | 1 | 1 | 2.8 | Surgical_splenectomy | 1 | 0 | Haemophilus_influenzae | 1 | null | Stroke_treatment | 57 | 67 | 1 | 5 | 0 | 0 | 5,225 | 12.9 | 0 | Deferasirox | 0.74 | 1 | 0.232 | 0.89 | 1 | 15.6 | 15.6 | 29.8 | 6.55 | 0.417 | 0.65 | 0 | 0 | 0 | 1 | 0.354 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 10 | 25.6 | 52.1 | 42.2 | 0 | 6 | 8 | Employed_part | 0 | 1 | 1 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000084 | HbSS | Male | African_born | US_South | Low | 1.8 | 18.1 | 14.3 | No_deletion | 0 | 10.86 | 1.29 | 80.3 | 11.6 | 13.2 | 586 | 299 | 3.68 | 52 | 0.85 | 8.3 | 101 | 42 | 3,022 | 7.86 | 4.18 | 3 | 0 | Bilateral_legs | Unknown | 13.1 | 10 | 0 | 0 | 0 | Infection | 0 | 5.6 | 51.1 | 1 | Hydromorphone | 29.6 | 8 | 21 | Microalbuminuria | 177.5 | 24 | 0 | 0 | 1.73 | 40 | 1 | 0 | 172 | 0 | 0 | 0 | 83.4 | 0 | 0 | III | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 1 | Episodic | Stroke_prevention | 42.3 | 48 | 0 | 0 | 0 | 0 | 513 | 4.88 | 0 | Deferiprone | 0.68 | 0 | 0.2 | 0.5 | 1 | 23.6 | 16.5 | 9.3 | 2.66 | 0.257 | 0.83 | 1 | 0 | 0 | 1 | 0.239 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 21 | 38.7 | 52.8 | 64.3 | 11 | 6 | 23 | Employed_full | 1 | 1 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000085 | HbSS | Female | Other | US_Midwest | Middle | 1.25 | 12 | 7.1 | 2_gene_del | 1 | 6.19 | 4.07 | 80.7 | 10.5 | 15.1 | 371 | 180 | 3.5 | 28 | 0.45 | 7.6 | 192 | 113 | 2,856 | 5.34 | 4.87 | 5 | 1 | Abdomen | Infection | 6.2 | 8.1 | 0 | 0 | 0 | Infection | 1 | 2.2 | 54.9 | 1 | Oxycodone | 28.5 | 0 | 51 | Microalbuminuria | 84.2 | 66 | 0 | 0 | 2.32 | 60 | 0 | 0 | 152 | 0 | 0 | 0 | 78.9 | 0 | 1 | III | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | Chronic_exchange | Stroke_prevention | 29.5 | 40 | 0 | 0 | 0 | 0 | 27,000 | 40 | 0 | Deferasirox | 0.62 | 0 | 0.278 | 0.66 | 0 | 0 | 0 | 0 | 15.02 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | NMA | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 63 | 32.4 | 53.2 | 64.1 | 20 | 11 | 11 | Disability | 0 | 1 | 1 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000086 | HbSS | Female | Hispanic | Other | Low | 1.17 | 20.8 | 17.3 | 2_gene_del | 0 | 8.79 | 1.63 | 71.3 | 12.6 | 12.3 | 471 | 457 | 8.74 | 60 | 1.02 | 8.1 | 218 | 1,026 | 4,287 | 8.06 | 4.74 | 3 | 1 | Bilateral_legs | Infection | 2.7 | 10 | 0 | 0 | 0 | Infection | 0 | 2.5 | 59.7 | 1 | Oxycodone | 25.6 | 2 | 33 | null | 111.8 | 83 | 0 | 1 | 1.99 | 369 | 0 | 0 | 163 | 0 | 0 | 0 | 81.3 | 0 | 0 | IV | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | null | Splenic_sequestration | 57.6 | 41 | 0 | 0 | 0 | 0 | 17,027 | 4.77 | 0 | Combination | 0.51 | 0 | 0.225 | 0.91 | 0 | 0 | 0 | 0 | 11.96 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 7 | 35.9 | 52.2 | 60.2 | 13 | 12 | 13 | Unemployed | 1 | 0 | 1 | 0 | 0 | 0 | HC-GEN-002 |
HC002-000087 | HbSC | Male | Hispanic | US_Northeast | Low | 2 | 20.3 | 5.1 | 1_gene_del | 0 | 11.05 | 6.47 | 80.4 | 9.4 | 5.5 | 425 | 1,017 | 1.56 | 44 | 1.79 | 7.4 | 99 | 62 | 5,000 | 5.93 | 3.75 | 2 | 0 | Abdomen | Stress | 2.7 | 8.5 | 0 | 0 | 0 | Fat_embolism | 0 | 6.4 | 69.6 | 1 | Morphine | 203.9 | 5 | 21 | Microalbuminuria | 58 | 895 | 0 | 0 | 2.25 | 41 | 1 | 0 | 80 | 0 | 0 | 0 | 83.9 | 0 | 0 | I | 0 | 1 | null | 1 | 0 | 1 | 1 | 1 | 1 | Normal | 1 | 0 | Staphylococcus_aureus | 0 | Episodic | Stroke_treatment | 57.9 | 86 | 0 | 0 | 0 | 0 | 27,000 | 40 | 0 | Deferasirox | 0.38 | 0 | 0.23 | 0.5 | 0 | 0 | 0 | 0 | 15.17 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 39 | 38.5 | 75.1 | 72.5 | 8 | 7 | 4 | Disability | 0 | 0 | 0 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000088 | HbSS | Male | Hispanic | US_Midwest | Low | 1.15 | 31.8 | 3 | 2_gene_del | 0 | 8.59 | 1.96 | 71.9 | 22.6 | 9.4 | 281 | 496 | 4.83 | 22 | 0.4 | 7.1 | 460 | 199 | 3,915 | 9.36 | 4.79 | 5 | 0 | Lumbar_back | Infection | 5.2 | 9.2 | 0 | 0 | 0 | Infection | 0 | 1.6 | 58.4 | 0 | Other | 0 | 16 | 16 | Hyperfiltration | 161.9 | 306 | 0 | 1 | 1.92 | 53 | 0 | 0 | 153 | 0 | 0 | 0 | 76.5 | 0 | 1 | III | 0 | 0 | null | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 0 | 0 | Haemophilus_influenzae | 0 | Chronic_exchange | Splenic_sequestration | 29.6 | 69 | 0 | 0 | 0 | 0 | 6,341 | 4.98 | 0 | Deferasirox | 0.7 | 0 | 0.187 | 0.69 | 1 | 17.6 | 17.6 | 18.2 | 5.59 | 0.534 | 0.66 | 0 | 1 | 0.197 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | null | 0 | null | 0 | 0 | 20 | 21.7 | 57.8 | 49.5 | 13 | 13 | 12 | Disability | 1 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000089 | HbSS | Male | Black_non_Hispanic | US_South | Middle | 2 | 40.1 | 19.5 | 1_gene_del | 0 | 7.51 | 5.22 | 67.2 | 6.4 | 13.1 | 398 | 550 | 12.34 | 47 | 0.93 | 6 | 175 | 158 | 5,000 | 7.03 | 4.85 | 1 | 0 | Bilateral_legs | Cold_exposure | 2.4 | 6.6 | 1 | 0 | 0 | Hypoventilation | 0 | 5.1 | 62.6 | 1 | Other | 126.1 | 13 | 23 | Hyperfiltration | 111.5 | 103 | 0 | 1 | 2.37 | 80 | 0 | 0 | 123 | 0 | 0 | 0 | 71.7 | 1 | 0 | III | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 1 | Streptococcus_pneumoniae | 0 | null | Stroke_prevention | 58.9 | 96 | 1 | 2 | 1 | 0 | 18,042 | 5.45 | 0 | Deferiprone | 0.79 | 0 | 0.203 | 0.7 | 1 | 21.2 | 21.2 | 9.5 | 1.86 | 0.565 | 0.65 | 0 | 1 | 0.2 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 0 | bb2121 | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 28 | 12.8 | 63.5 | 60.6 | 13 | 11 | 10 | Unemployed | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000090 | HbSS | Male | Black_non_Hispanic | US_South | Middle | 1.63 | 31.2 | 17.4 | No_deletion | 0 | 9.36 | 3.89 | 73.3 | 9.7 | 9.1 | 491 | 335 | 6.07 | 23 | 0.97 | 8 | 175 | 67 | 4,968 | 4.62 | 4.36 | 1 | 1 | Bilateral_legs | Infection | 1.7 | 5.3 | 0 | 0 | 0 | Unknown | 1 | 2.8 | 85 | 1 | Hydromorphone | 19.6 | 4 | 24 | Macroalbuminuria | 99.5 | 97 | 0 | 0 | 1.79 | 20 | 0 | 0 | 138 | 0 | 0 | 0 | 98 | 0 | 1 | I | 0 | 0 | VH_RD | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Streptococcus_pneumoniae | 0 | Episodic | Stroke_treatment | 42.8 | 59 | 1 | 4 | 0 | 0 | 8,689 | 23.14 | 0 | Deferasirox | 0.69 | 0 | 0.174 | 0.53 | 0 | 0 | 0 | 0 | 8.73 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Partial | 0 | null | 0 | 1 | 22 | 41.9 | 47.4 | 53.4 | 15 | 2 | 15 | Employed_full | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000091 | HbSS | Female | Black_non_Hispanic | US_South | Low | 0.54 | 11.8 | 6.8 | 1_gene_del | 0 | 6.02 | 3.97 | 94.1 | 10 | 15.9 | 360 | 361 | 9.47 | 59 | 0.96 | 8.3 | 307 | 143 | 5,000 | 1.2 | 5.08 | 2 | 1 | Bilateral_legs | Infection | 2.7 | 6.4 | 0 | 0 | 0 | Fat_embolism | 1 | 1.8 | 51.5 | 0 | Morphine | 0 | 4 | 12 | null | 111.8 | 224 | 0 | 0 | 1.5 | 20 | 1 | 0 | 149 | 0 | 0 | 0 | 107.3 | 0 | 0 | II | 0 | 0 | null | 0 | 0 | 0 | 0 | 0 | 0 | Autoinfarction | 1 | 1 | Salmonella_sp | 0 | Episodic | ACS | 41.6 | 20 | 0 | 0 | 0 | 0 | 599 | 28.48 | 0 | Deferasirox | 0.38 | 0 | 0.277 | 0.76 | 0 | 0 | 0 | 0 | 11.47 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | null | 0 | null | 0 | 1 | 20 | 20.1 | 60.6 | 79.8 | 5 | 12 | 14 | Employed_part | 0 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000092 | HbSC | Male | Black_non_Hispanic | US_South | High | 1.72 | 15.7 | 13.8 | No_deletion | 0 | 10.41 | 4.14 | 79.8 | 20.2 | 10.8 | 381 | 628 | 2.66 | 40 | 1.68 | 6.7 | 221 | 78 | 2,684 | 9.22 | 3.69 | 2 | 1 | Chest | Dehydration | 1.8 | 7.2 | 0 | 0 | 0 | Unknown | 0 | 4.1 | 54.8 | 1 | Other | 55.1 | 2 | 26 | null | 113.6 | 18 | 0 | 0 | 2.48 | 45 | 1 | 0 | 111 | 0 | 0 | 0 | 98.7 | 0 | 0 | I | 0 | 1 | VH_RD | 0 | 1 | 0 | 0 | 0 | 0 | Normal | 0 | 0 | Haemophilus_influenzae | 0 | null | Splenic_sequestration | 48 | 56 | 0 | 0 | 0 | 0 | 2,161 | 6.21 | 0 | Deferoxamine | 0.72 | 0 | 0.199 | 0.72 | 1 | 27.2 | 27.2 | 22.3 | 7.24 | 0.425 | 0.73 | 0 | 1 | 0.292 | 0 | 0 | 1 | 1.02 | 1 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 41 | 29.8 | 36.5 | 70.4 | 11 | 10 | 6 | Disability | 0 | 0 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000093 | HbSS | Male | Black_non_Hispanic | Other | Middle | 2 | 59.9 | 9.9 | No_deletion | 0 | 7.41 | 4.19 | 83.8 | 6.7 | 11.3 | 399 | 996 | 2.72 | 94 | 2.05 | 6.6 | 478 | 85 | 3,283 | 4.49 | 5.35 | 5 | 1 | Lumbar_back | Stress | 6.3 | 6.1 | 0 | 0 | 0 | Unknown | 1 | 6.4 | 69.5 | 1 | Hydromorphone | 119.9 | 1 | 52 | Hyperfiltration | 84.4 | 10 | 1 | 0 | 1.82 | 47 | 0 | 0 | 97 | 0 | 0 | 0 | 86.2 | 0 | 0 | I | 0 | 0 | null | 0 | 1 | 0 | 0 | 1 | 2.9 | Normal | 0 | 0 | Salmonella_sp | 0 | Chronic_exchange | ACS | 26.5 | 56 | 0 | 0 | 0 | 0 | 5,189 | 40 | 0 | Deferasirox | 0.79 | 0 | 0.226 | 0.79 | 0 | 0 | 0 | 0 | 11.24 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MUD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Other | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 0 | 37 | 32.7 | 64.3 | 54.1 | 2 | 15 | 23 | Disability | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000094 | HbSS | Female | Black_non_Hispanic | US_Northeast | Low | 1.51 | 20.6 | 7.1 | No_deletion | 0 | 7.25 | 9.5 | 77.9 | 13.7 | 14.4 | 673 | 788 | 12.41 | 69 | 0.66 | 9.2 | 116 | 30 | 3,290 | 11.27 | 4.84 | 3 | 1 | Bilateral_legs | Infection | 1.5 | 5.4 | 0 | 0 | 0 | Fat_embolism | 0 | 2.1 | 72.9 | 1 | Morphine | 106.8 | 4 | 35 | null | 151.6 | 220 | 0 | 0 | 2 | 74 | 1 | 0 | 110 | 0 | 0 | 0 | 71.4 | 1 | 0 | I | 0 | 0 | null | 0 | 0 | 1 | 1 | 0 | 0 | Autoinfarction | 1 | 0 | Salmonella_sp | 1 | Episodic | Splenic_sequestration | 59.4 | 56 | 1 | 0 | 0 | 0 | 11,559 | 22.87 | 0 | Combination | 0.49 | 0 | 0.158 | 0.75 | 0 | 0 | 0 | 0 | 16.81 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 1 | MSD | NMA | 1 | 0 | 0 | 0.97 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 36 | 33.7 | 55.2 | 62.4 | 0 | 8 | 10 | Unemployed | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000095 | HbSS | Male | Black_non_Hispanic | Africa | High | 2 | 20.4 | 6.4 | No_deletion | 0 | 8.8 | 13.89 | 67.7 | 13 | 10.5 | 200 | 580 | 6.36 | 29 | 1.04 | 6.8 | 80 | 119 | 4,785 | 8.89 | 4.03 | 3 | 0 | Lumbar_back | Unknown | 3.2 | 8 | 0 | 0 | 0 | Infection | 1 | 5.6 | 66.6 | 1 | Other | 47.7 | 2 | 14 | Microalbuminuria | 132.6 | 98 | 0 | 0 | 1.82 | 30 | 1 | 1 | 82 | 0 | 1 | 0 | 86.3 | 0 | 0 | III | 0 | 0 | PSR_Sea_Fan | 0 | 0 | 0 | 0 | 0 | 0 | Normal | 1 | 0 | Staphylococcus_aureus | 0 | null | Stroke_prevention | 49.9 | 75 | 0 | 0 | 0 | 0 | 3,231 | 12.83 | 0 | Deferoxamine | 0.75 | 0 | 0.171 | 0.7 | 1 | 25.6 | 25.6 | 20 | 4.06 | 0.703 | 0.64 | 0 | 1 | 0.351 | 0 | 0 | 0 | 0 | 0 | 0 | UCB | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 25 | 42.6 | 76.1 | 60 | 13 | 14 | 14 | Unemployed | 1 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000096 | HbSS | Male | Black_non_Hispanic | Europe | Low | 1.09 | 33.7 | 3.6 | No_deletion | 0 | 9.71 | 10.35 | 89.5 | 13.3 | 11.5 | 480 | 410 | 6.37 | 20 | 0.77 | 6.9 | 191 | 299 | 5,000 | 4.58 | 3.92 | 1 | 1 | Bilateral_legs | Infection | 6.8 | 5.4 | 0 | 0 | 0 | Infection | 0 | 2.2 | 81.9 | 1 | Oxycodone | 29.1 | 3 | 26 | null | 137.4 | 19 | 0 | 0 | 2.32 | 94 | 0 | 0 | 94 | 0 | 0 | 0 | 72.7 | 0 | 0 | II | 0 | 1 | null | 0 | 0 | 0 | 0 | 1 | 9.6 | Autoinfarction | 1 | 1 | Staphylococcus_aureus | 0 | Chronic_exchange | Stroke_treatment | 26.4 | 59 | 1 | 3 | 0 | 0 | 5,990 | 24.19 | 0 | Deferoxamine | 0.58 | 0 | 0.21 | 0.81 | 0 | 0 | 0 | 0 | 7.41 | 0 | 0 | 0 | 0 | 0 | 1 | 0.505 | 0 | 0 | 0 | 0 | MUD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 36 | 41.5 | 68.3 | 47.4 | 15 | 0 | 9 | Employed_part | 1 | 1 | 1 | 1 | 1 | 0 | HC-GEN-002 |
HC002-000097 | HbSS | Female | Black_non_Hispanic | US_South | Low | 2 | 33.2 | 11.4 | 2_gene_del | 0 | 7.72 | 2.67 | 64.6 | 16.9 | 13.7 | 390 | 443 | 3.46 | 33 | 0.54 | 7.5 | 257 | 129 | 3,876 | 13.71 | 4.88 | 3 | 0 | Abdomen | Cold_exposure | 2.1 | 4.4 | 0 | 0 | 0 | Hypoventilation | 1 | 5.4 | 65.5 | 1 | Oxycodone | 164 | 14 | 8 | Hyperfiltration | 86.2 | 10 | 0 | 0 | 2.23 | 20 | 0 | 0 | 99 | 1 | 0 | 0 | 79 | 0 | 0 | I | 0 | 0 | null | 0 | 1 | 1 | 1 | 0 | 0 | Autoinfarction | 1 | 0 | Salmonella_sp | 0 | Chronic_simple | Stroke_prevention | 32 | 59 | 0 | 0 | 0 | 0 | 2,257 | 40 | 0 | Deferasirox | 0.71 | 0 | 0.208 | 0.9 | 1 | 19.7 | 19.7 | 0 | 3.67 | 0.326 | 0.75 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Minimal | 0 | null | 0 | 1 | 10 | 36.9 | 68.6 | 79.4 | 9 | 5 | 4 | Disability | 0 | 0 | 0 | 1 | 0 | 1 | HC-GEN-002 |
HC002-000098 | HbSS | Female | Hispanic | US_South | Middle | 0.59 | 12.2 | 9.5 | 1_gene_del | 0 | 9.29 | 8.35 | 77.6 | 16.9 | 6.6 | 343 | 287 | 6.36 | 27 | 0.85 | 6.7 | 91 | 362 | 5,000 | 7.13 | 4.03 | 6 | 0 | Lumbar_back | Infection | 8.4 | 5.2 | 0 | 0 | 0 | Fat_embolism | 0 | 4.6 | 40.3 | 0 | Other | 0 | 7 | 19 | Microalbuminuria | 84.3 | 263 | 0 | 0 | 2.32 | 63 | 0 | 0 | 83 | 0 | 0 | 0 | 82.4 | 0 | 0 | II | 0 | 0 | NPSR | 0 | 0 | 1 | 0 | 0 | 0 | Normal | 0 | 0 | Haemophilus_influenzae | 0 | Chronic_exchange | ACS | 33.3 | 46 | 0 | 0 | 0 | 0 | 2,068 | 40 | 0 | Deferasirox | 0.57 | 0 | 0.23 | 0.5 | 1 | 30.2 | 30.2 | 5.1 | 4.07 | 0.39 | 0.94 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | RIC | 0 | 0 | 0 | 0 | 0 | Exagamglogene_autotemcel_CRISPR | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 1 | 52 | 40.5 | 51.3 | 57.2 | 9 | 0 | 4 | Disability | 1 | 1 | 0 | 0 | 0 | 1 | HC-GEN-002 |
HC002-000099 | HbSS | Female | African_born | Africa | Low | 1.25 | 25.9 | 10.7 | No_deletion | 0 | 8.27 | 10.01 | 81.6 | 10.2 | 10.1 | 387 | 210 | 3.41 | 93 | 1.04 | 5.6 | 81 | 217 | 2,747 | 6.9 | 4.07 | 4 | 0 | Bilateral_legs | Stress | 4.8 | 6.8 | 0 | 0 | 0 | Hypoventilation | 1 | 4 | 63.1 | 1 | Hydromorphone | 7.3 | 4 | 22 | Macroalbuminuria | 106 | 48 | 0 | 0 | 1.88 | 89 | 0 | 0 | 161 | 0 | 1 | 0 | 56.6 | 0 | 1 | I | 0 | 1 | null | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 0 | Salmonella_sp | 0 | null | Stroke_prevention | 53.1 | 57 | 1 | 3 | 0 | 0 | 645 | 19.94 | 0 | Deferoxamine | 0.45 | 0 | 0.3 | 0.94 | 1 | 30.5 | 30.5 | 14.1 | 7.15 | 0.318 | 0.59 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | Haplo | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 48 | 24.5 | 63.7 | 85 | 11 | 6 | 11 | Unemployed | 0 | 1 | 0 | 1 | 0 | 0 | HC-GEN-002 |
HC002-000100 | HbSB+_thal | Female | Black_non_Hispanic | US_South | Low | 0.38 | 11.7 | 5.1 | No_deletion | 0 | 8.55 | 2.07 | 83.8 | 12.8 | 13.5 | 500 | 243 | 10.95 | 45 | 0.83 | 7.4 | 283 | 114 | 5,000 | 5.42 | 4.07 | 2 | 0 | Bilateral_legs | Unknown | 8.9 | 5.4 | 0 | 0 | 0 | Hypoventilation | 0 | 4.7 | 55.7 | 1 | Oxycodone | 10.1 | 11 | 24 | Microalbuminuria | 138 | 146 | 1 | 1 | 2.23 | 87 | 0 | 0 | 104 | 0 | 0 | 0 | 109.8 | 0 | 0 | I | 0 | 1 | PSR_Sea_Fan | 0 | 0 | 1 | 1 | 0 | 0 | Normal | 1 | 0 | Haemophilus_influenzae | 0 | Episodic | Stroke_prevention | 42.9 | 69 | 0 | 0 | 0 | 0 | 5,296 | 4.6 | 1 | Deferasirox | 0.69 | 0 | 0.139 | 0.93 | 1 | 29.8 | 29.8 | 5 | 6.26 | 0.614 | 0.33 | 0 | 1 | 0.183 | 0 | 0 | 0 | 0 | 0 | 0 | MSD | Myeloablative | 0 | 0 | 0 | 0 | 0 | Lovotibeglogene_autotemcel | 0 | 0 | 0 | 0 | 0 | Complete | 0 | null | 0 | 0 | 29 | 27.3 | 79.7 | 62.3 | 15 | 8 | 9 | Disability | 0 | 1 | 1 | 1 | 0 | 0 | HC-GEN-002 |
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