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CK syndrome is a rare, genetic, X-linked syndromic intellectual disability disorder characterized by mild to severe intellectual disability, infancy-onset seizures, post-natal microcephaly, cerebral cortical malformations, dysmorphic facial features (including long, narrow face, almond-shaped palpebral fissures, epic...
CK syndrome
c3151781
1,500
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=251383
2021-01-23T17:39:36
{"omim": ["300831"], "synonyms": ["X-linked intellectual disability-microcephaly-cortical malformation-thin habitus syndrome"]}
Nisan et al. (1988) described agenesis of 5 cervical vertebrae in a 7-year-old son of first-cousin parents. The patient had a webbed neck, and a diagnosis of Klippel-Feil syndrome was made before x-rays were taken. Spine \- Cervical vertebrae agenesis Neck \- Webbed Inheritance \- Autosomal recessive ▲ Close *...
CERVICAL VERTEBRAE, AGENESIS OF
c0432160
1,501
omim
https://www.omim.org/entry/214290
2019-09-22T16:29:47
{"mesh": ["C562952"], "omim": ["214290"]}
Ectodermal dysplasia-blindness syndrome is characterized by intellectual deficit, blindness caused by ocular malformations (microphthalmia, microcornea and sclerocornea), short stature, dysmorphic facial features (narrow nasal bridge and prominent ears), hypotrichosis, and malaligned teeth. It has been described in t...
Ectodermal dysplasia-blindness syndrome
c1849332
1,502
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1806
2021-01-23T18:57:44
{"gard": ["2045"], "mesh": ["C535865"], "omim": ["268320"], "umls": ["C1849332"], "icd-10": ["Q87.8"]}
The 1951 Pont-Saint-Esprit mass poisoning, also known as Le Pain Maudit, was a mass poisoning on 15 August 1951, in the small town of Pont-Saint-Esprit in southern France. More than 250 people were involved, including 50 people interned in asylums and 7 deaths. A foodborne illness was suspected, and among these it wa...
1951 Pont-Saint-Esprit mass poisoning
None
1,503
wikipedia
https://en.wikipedia.org/wiki/1951_Pont-Saint-Esprit_mass_poisoning
2021-01-18T19:10:29
{"wikidata": ["Q13420313"]}
Sexually transmitted disease caused by the invasive serovars L1, L2, L2a or L3 of Chlamydia trachomatis This article is about the sexually transmitted disease caused by certain types of chlamydia. For the ulcerative disease caused by Klebsiella granulomatis, see Granuloma inguinale. Lymphogranuloma venereum L...
Lymphogranuloma venereum
c0024286
1,504
wikipedia
https://en.wikipedia.org/wiki/Lymphogranuloma_venereum
2021-01-18T18:59:46
{"gard": ["9545"], "mesh": ["D008219"], "umls": ["C0024286"], "icd-10": ["A55"], "wikidata": ["Q694552"]}
Davies et al. (1994) and Cordell et al. (1995) observed linkage between the X chromosome and type I diabetes. Cucca et al. (1998) examined the male-female bias in type I diabetes. Contrary to assumption, the male:female (M:F) ratio in patients with IDDM is not 1. Karvonen et al. (1997) found that high-incidence c...
DIABETES MELLITUS, INSULIN-DEPENDENT, X-LINKED, SUSCEPTIBILITY TO
c1848042
1,505
omim
https://www.omim.org/entry/300136
2019-09-22T16:20:50
{"omim": ["300136"], "synonyms": ["Alternative titles", "IDDMX", "INSULIN-DEPENDENT DIABETES MELLITUS, X-LINKED, SUSCEPTIBILITY TO"]}
Meromelia is a birth defect characterized by the lacking of a part, but not all, of one or more limbs with the presence of a hand or foot. It results in a shrunken and deformed extremity. [1] ## Contents * 1 Cause * 2 Diagnosis * 3 Treatment * 4 Etymology * 5 See also * 6 References ## Cause[edit] Suc...
Meromelia
c0265549
1,506
wikipedia
https://en.wikipedia.org/wiki/Meromelia
2021-01-18T18:33:35
{"wikidata": ["Q6819940"]}
Gastrointestinal perforation Other namesRuptured bowel,[1] gastrointestinal rupture Free air under the right diaphragm from a perforated bowel. SpecialtyGastroenterology, emergency medicine SymptomsAbdominal pain, tenderness[2] ComplicationsSepsis, abscess[2] Usual onsetSudden or more gradual[2] Cau...
Gastrointestinal perforation
c0151664
1,507
wikipedia
https://en.wikipedia.org/wiki/Gastrointestinal_perforation
2021-01-18T19:06:47
{"icd-9": ["863.9", "569.83"], "icd-10": ["K63.1"], "wikidata": ["Q279324"]}
Livedoid vasculopathy is a blood vessel disorder that causes painful ulcers and scarring (atrophie blanche) on the feet and lower legs. These symptoms can persist for months to years and the ulcers often recur. Livedoid vasculopathy lesions appear as painful red or purple marks and spots that may progress to smal...
Livedoid vasculopathy
c0857794
1,508
gard
https://rarediseases.info.nih.gov/diseases/12784/livedoid-vasculopathy
2021-01-18T17:59:21
{"icd-9": ["709.1"], "synonyms": ["Segmental hyalinizing vasculopathy", "Livedo vasculitis", "Livedoid vasculitis", "Livedo reticularis with summer ulcerations", "Livedo reticularis with winter ulcerations"]}
A number sign (#) is used with this entry because of evidence that early-onset neurodegeneration with choreoathetoid movements and microcytic anemia (NDCAMA) is caused by compound heterozygous mutation in the iron responsive element-binding protein-2 gene (IREB2; 147582) on chromosome 15q25. One such patient has been...
NEURODEGENERATION, EARLY-ONSET, WITH CHOREOATHETOID MOVEMENTS AND MICROCYTIC ANEMIA
None
1,509
omim
https://www.omim.org/entry/618451
2019-09-22T15:41:53
{"omim": ["618451"]}
A rare genetic eye disease characterized by congenital profound excavation of the optic nerve head with diminished visual field, in the absence of elevated intraocular pressure. Many patients lack a well-formed retinal artery and have multiple radial cilioretinal arteries instead. The condition is mostly bilateral, m...
Familial cavitary optic disc anomaly
c1969063
1,510
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=464760
2021-01-23T18:59:36
{"mesh": ["C566924"], "omim": ["611543"], "synonyms": ["Familial CODA"]}
A number sign (#) is used with this entry because non-Hodgkin lymphoma is associated with somatic mutations in a number of genes, including CASP10 (601762), ATM (607585), RAD54L (603615), BRAF (164757), CARD11 (607210), and RAD54B (604289). Inheritance Wiernik et al. (2000) analyzed 11 published reports of multigen...
LYMPHOMA, NON-HODGKIN, FAMILIAL
c0024305
1,511
omim
https://www.omim.org/entry/605027
2019-09-22T16:11:38
{"doid": ["0060060"], "mesh": ["D008228"], "omim": ["605027"], "orphanet": ["547"], "synonyms": ["Alternative titles", "NON-HODGKIN LYMPHOMA"]}
Alopecia totalis A woman with alopecia totalis SpecialtyDermatology Alopecia totalis is the loss of all skull and facial hair. Its causes are unclear, but believed to be autoimmune. Research suggests there may be a genetic component linked to developing alopecia totalis; the presence of DRB1*0401 and DQB1*03...
Alopecia totalis
c0263504
1,512
wikipedia
https://en.wikipedia.org/wiki/Alopecia_totalis
2021-01-18T19:06:41
{"gard": ["613"], "umls": ["C0263504"], "icd-10": ["L63.0"], "orphanet": ["700"], "wikidata": ["Q4734614"]}
A number sign (#) is used with this entry because of evidence that keratoconus-9 (KCTN9) is caused by heterozygous mutation in the TUBA3D gene (617878) on chromosome 2q21. Description Keratoconus-9, a degenerative corneal disease with onset during adolescence, is characterized by corneal ectasia, thinning, and ...
KERATOCONUS 9
c4693660
1,513
omim
https://www.omim.org/entry/617928
2019-09-22T15:44:22
{"omim": ["617928"]}
Skeletal fluorosis Fluorosis victim of the industrial city of Raigarh, Chhattisgarh SpecialtyRheumatology Skeletal fluorosis is a bone disease caused by excessive accumulation of fluoride leading to weakened bones.[1] In advanced cases, skeletal fluorosis causes painful damage to bones and joints. ## Conten...
Skeletal fluorosis
c0410447
1,514
wikipedia
https://en.wikipedia.org/wiki/Skeletal_fluorosis
2021-01-18T19:00:02
{"icd-9": ["733.9"], "icd-10": ["M85.1"], "wikidata": ["Q3266880"]}
A number sign (#) is used with this entry because of evidence that 3-methylglutaconic aciduria with cataracts, neurologic involvement, and neutropenia (MEGCANN), also referred to as 3-methylglutaconic aciduria type VII (MGCA7), is caused by homozygous or compound heterozygous mutation in the CLPB gene (616254) on...
3-METHYLGLUTACONIC ACIDURIA WITH CATARACTS, NEUROLOGIC INVOLVEMENT, AND NEUTROPENIA
c4225393
1,515
omim
https://www.omim.org/entry/616271
2019-09-22T15:49:25
{"doid": ["0110003"], "omim": ["616271"], "orphanet": ["445038"], "synonyms": ["Alternative titles", "3-METHYLGLUTACONIC ACIDURIA, TYPE VII", "MGA7", "3-methylglutaconic aciduria-cataract-neurologic involvement-neutropenia syndrome"], "genereviews": ["NBK396257"]}
A rare vascular anomaly characterized by congenital narrowing of the inferior vena cava mostly at the diaphragmatic level or hepatic segment, with or without web formation. Patients may present with deep vein thrombosis below the obstructed segment, lower extremity swellings, pain, and varices, abdominal pain/varices...
Congenital stenosis of the inferior vena cava
c0265934
1,516
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=99122
2021-01-23T16:59:52
{"umls": ["C0265934", "C0340757"], "icd-10": ["Q26.0"], "synonyms": ["Congenital stenosis of the IVC", "Congenital stenosis of the inferior caval vein"]}
A rare vascular tumor characterized by a solitary lesion in the superficial or deep soft tissue of the extremities, most often originating from a small vein as a fusiform intravascular mass also infiltrating surrounding tissues. It is composed of epithelioid endothelial cells arranged in short cords and nests in a my...
Epithelioid hemangioendothelioma
c0206732
1,517
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=157791
2021-01-23T18:40:53
{"mesh": ["D018323"], "umls": ["C0206732"], "icd-10": ["D18.0"]}
A number sign (#) is used with this entry because of evidence that X-linked hypoparathyroidism (HYPX) is caused by an interstitial deletion/insertion on chromosome Xq27.1, which may have a position effect on expression of SOX3 (313430). Clinical Features Peden (1960) reported a family in which multiple males had ne...
HYPOPARATHYROIDISM, X-LINKED
c1832648
1,518
omim
https://www.omim.org/entry/307700
2019-09-22T16:18:10
{"doid": ["11199"], "mesh": ["C537156"], "omim": ["307700"], "orphanet": ["2238", "2239"], "synonyms": ["Alternative titles", "PARATHYROID GLANDS, AGENESIS OF"]}
Wilson et al. (1989) described the single case of a 2-year-old girl with virtual absence of body and scalp hair, rounded nails, thin dental enamel, preaxial polydactyly of the feet, and an unusual facial appearance consisting of dystopia canthorum, thickened frenulum giving an appearance of slight median cleft of the...
ECTODERMAL DYSPLASIA SYNDROME WITH DISTINCTIVE FACIAL APPEARANCE AND PREAXIAL POLYDACTYLY OF FEET
c1851851
1,519
omim
https://www.omim.org/entry/129540
2019-09-22T16:42:01
{"mesh": ["C565067"], "omim": ["129540"]}
Infantile Refsum disease (IRD) is the mildest variant of the peroxisome biogenesis disorders, Zellweger syndrome spectrum (PBD- ZSS; see this term), characterized by hypotonia, retinitis pigmentosa, developmental delay, sensorineural hearing loss and liver dysfunction. Phenotypic overlap is seen between IRD and neona...
Infantile Refsum disease
c0282527
1,520
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=772
2021-01-23T17:49:51
{"gard": ["4648"], "mesh": ["D052919"], "omim": ["202370", "266510", "601539", "614863", "614867", "614871", "614873", "614877", "614885", "614920", "617370"], "umls": ["C0282527"], "icd-10": ["G60.1"], "synonyms": ["IRD"]}
For a phenotypic description and a discussion of genetic heterogeneity of Parkinson disease, see 168600. Mapping Soon after a form of autosomal dominant Parkinson disease was mapped to 4q21-q22 and was shown to be due to mutations in the alpha-synuclein gene (SNCA; 163890), genetic heterogeneity became apparent, as...
PARKINSON DISEASE 3, AUTOSOMAL DOMINANT
c1865581
1,521
omim
https://www.omim.org/entry/602404
2019-09-22T16:13:49
{"doid": ["0111250"], "mesh": ["C566552"], "omim": ["602404"], "orphanet": ["2828"], "synonyms": ["PARKINSON DISEASE 3, AUTOSOMAL DOMINANT LEWY BODY", "Alternative titles", "YOPD", "Early-onset Parkinson disease"]}
Rapid onset of confusion caused by alcohol withdrawal "DTs" redirects here. For other uses, see DTS (disambiguation). For other uses, see Delirium tremens (disambiguation). Delirium tremens An alcoholic man with delirium tremens on his deathbed, surrounded by his terrified family. The text "L'Alcool Tue" means "...
Delirium tremens
c0001957
1,522
wikipedia
https://en.wikipedia.org/wiki/Delirium_tremens
2021-01-18T18:40:10
{"mesh": ["D000430"], "icd-9": ["291.0"], "icd-10": ["F10.4"], "wikidata": ["Q209647"]}
Cernunnos-XLF deficiency is a rare form of combined immunodeficiency characterized by microcephaly, growth retardation, and T and B cell lymphopenia. ## Epidemiology Prevalence is unknown. To date, five cases have been reported. ## Clinical description Patients present in childhood with growth retardation, mi...
Cernunnos-XLF deficiency
c1969799
1,523
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=169079
2021-01-23T18:17:19
{"mesh": ["C566970"], "omim": ["611291"], "icd-10": ["D81.1"], "synonyms": ["Cernunnos XLFD", "Cernunnos deficiency", "Combined immunodeficiency-microcephaly-growth retardation-sensitivity to ionizing radiation syndrome", "NHEJ1 deficiency"]}
A rare congenital malformation characterized by a unilateral, complete or partial, absence of the pectoralis major (and often minor) muscle, ipsilateral breast and nipple anomalies, hypoplasia of the pectoral subcutaneous tissue, absence of pectoral and axillary hair, and possibly accompanied by chest wall and/or upp...
Poland syndrome
c0032357
1,524
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2911
2021-01-23T17:04:55
{"gard": ["7412"], "mesh": ["D011045"], "omim": ["173800"], "umls": ["C0032357"], "icd-10": ["Q79.8"], "synonyms": ["Poland anomaly", "Poland sequence"]}
A number sign (#) is used with this entry because some cases of Rothmund-Thomson syndrome (RTS) are caused by compound heterozygous mutation in the DNA helicase gene RECQL4 (603780) on chromosome 8q24. Description Rothmund-Thomson syndrome is rare autosomal recessive disorder characterized by skin atrophy, telangie...
ROTHMUND-THOMSON SYNDROME
c0032339
1,525
omim
https://www.omim.org/entry/268400
2019-09-22T16:22:32
{"doid": ["2732"], "mesh": ["D011038"], "omim": ["268400"], "icd-10": ["Q82.8"], "orphanet": ["221016", "221008", "2909"], "synonyms": ["Poikiloderma of Rothmund-Thomson type 2", "RTS2", "RTS1", "Poikiloderma of Rothmund-Thomson type 1", "Alternative titles", "POIKILODERMA ATROPHICANS AND CATARACT"], "genereviews": ["N...
## Summary ### Clinical characteristics. CSF1R-related adult-onset leukoencephalopathy with axonal spheroids and pigmented glia (ALSP) is characterized by executive dysfunction, memory decline, personality changes, motor impairments, and seizures. A frontal lobe syndrome (e.g., loss of judgment, lack of social inhi...
CSF1R-Related Adult-Onset Leukoencephalopathy with Axonal Spheroids and Pigmented Glia
None
1,526
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK100239/
2021-01-18T21:37:27
{"synonyms": ["CSF1R-Related ALSP"]}
A number sign (#) is used with this entry because of evidence that cataract-18 (CTRCT18) is caused by homozygous mutation in the FYCO1 gene (607182) on chromosome 3p21.3. Description Mutations in the FYCO1 gene have been identified in families with autosomal recessive cataract described as congenital and congenital...
CATARACT 18
c0392557
1,527
omim
https://www.omim.org/entry/610019
2019-09-22T16:05:15
{"doid": ["0110238"], "mesh": ["C535342"], "omim": ["610019"], "icd-10": ["Q12.0"], "orphanet": ["98992", "91492", "98995", "98991"], "synonyms": ["CATARACT, AUTOSOMAL RECESSIVE CONGENITAL 2", "Alternative titles"]}
Charcot-Marie-Tooth disease type 4B2 (CMT4B2) is a disorder that affects the peripheral nerves. Peripheral nerves connect the brain and spinal cord to muscles and to sensory cells that detect sensations such as touch, pain, heat, and sound. Damage to the peripheral nerves can result in loss of sensation and wasting (...
Charcot-Marie-Tooth disease type 4B2
c1858278
1,528
gard
https://rarediseases.info.nih.gov/diseases/9200/charcot-marie-tooth-disease-type-4b2
2021-01-18T18:01:30
{"mesh": ["C535421"], "omim": ["604563"], "umls": ["C1858278"], "orphanet": ["99956"], "synonyms": ["CMT 4B2", "Charcot Marie Tooth disease type 4B2", "CHARCOT-MARIE-TOOTH DISEASE, WITH FOCALLY FOLDED MYELIN SHEATHS, AUTOSOMAL RECESSIVE, TYPE 4B2", "CHARCOT-MARIE-TOOTH NEUROPATHY, TYPE 4B2"]}
A rare, hereditary endocrine tumor characterized by a benign pituitary adenoma that is either secreting (e.g. prolactin, growth hormone, thyroid stimulating hormone) or non-secreting. Symptoms may occur due to either the hormonal hypersecretion and/or the mass effect of the lesion on local structures in the brain. #...
Familial isolated pituitary adenoma
c1863340
1,529
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=314777
2021-01-23T18:48:51
{"gard": ["10959"], "mesh": ["C566321"], "omim": ["102200", "600634"], "umls": ["C1863340"], "icd-10": ["D35.2"], "synonyms": ["FIPA"]}
Semicircular canal dehiscence (SCD) syndrome is a rare otorhinolaryngologic disease characterized by the uni- or bilateral dehiscence of the bone(s) overlying the superior (most common), lateral or posterior semicircular canal(s). Patients present audiological (autophony, aural fullness, conductive hearing loss, puls...
Semicircular canal dehiscence syndrome
c4708600
1,530
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=420402
2021-01-23T17:24:32
{"icd-10": ["H83.8"], "synonyms": ["SCD syndrome"]}
Purpura of the nail beds usually result from trauma, with causes of toe involvement including physical pressure on the toes, such as that seen in surfboarding or windsurfing in which one must maintain balance with the toes, or when exogenous pressure is exerted from poorly fitting shoes.[1]:791–2 Purpura beneath the ...
Purpura of the nail bed
None
1,531
wikipedia
https://en.wikipedia.org/wiki/Purpura_of_the_nail_bed
2021-01-18T18:34:04
{"wikidata": ["Q7261509"]}
A rare genetic form of low-renin hypertension characterized by hypertension associated with decreased plasma levels of potassium and aldosterone. ## Epidemiology Liddle syndrome prevalence is unknown. The condition is considered rare with less than 80 families reported worldwide. ## Clinical description The d...
Liddle syndrome
c0221043
1,532
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=526
2021-01-23T17:49:20
{"gard": ["7381"], "mesh": ["D056929"], "omim": ["177200", "618114", "618126"], "umls": ["C0221043"], "icd-10": ["I15.1"], "synonyms": ["Pseudoaldosteronism", "Pseudohyperaldosteronism type 1"]}
This article may be too technical for most readers to understand. Please help improve it to make it understandable to non-experts, without removing the technical details. (July 2015) (Learn how and when to remove this template message) Baggio–Yoshinari syndrome Other namesBYS SpecialtyInfectious disease ...
Baggio–Yoshinari syndrome
None
1,533
wikipedia
https://en.wikipedia.org/wiki/Baggio%E2%80%93Yoshinari_syndrome
2021-01-18T19:06:08
{"wikidata": ["Q20736850"]}
Holt (1975) described hypothenar radial arches in 2 families and concluded that the inheritance is probably recessive. Inheritance \- Autosomal recessive Skin \- Hypothenar radial arches \- Abnormal dermatoglyphics ▲ Close *[v]: View this template *[t]: Discuss this template *[e]: Edit this template ...
DERMATOGLYPHICS--HYPOTHENAR RADIAL ARCH
c1857315
1,534
omim
https://www.omim.org/entry/221780
2019-09-22T16:28:47
{"omim": ["221780"]}
Twin twin transfusion syndrome (TTTS) is a rare condition seen in twin monochorionic pregnancies, typically developing during the 15-26 week gestation period and usually due to unbalanced intertwin placental anastomoses, where an unequal exchange of blood between twins causes oligohydramnios in one sac and polyhydram...
Twin to twin transfusion syndrome
c2909036
1,535
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=95431
2021-01-23T18:26:04
{"gard": ["325"], "mesh": ["D005330"], "icd-10": ["O43.0"], "synonyms": ["Feto-fetal transfusion syndrome"]}
Segmental odontomaxillary dysplasia (SOD) is a rare disorder characterized by unilateral enlargement of the right or left maxillary alveolar bone and gingiva in the region from the back of the canines to the maxillary tuberosity. In the enlarged region, dental abnormalities such as missing teeth, abnormal spacing and...
Segmental odontomaxillary dysplasia
c3698531
1,536
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=67039
2021-01-23T17:14:56
{"icd-10": ["K00.4"]}
Viral meningitis Other namesAseptic meningitis Viral meningitis causes inflammation of the meninges. SpecialtyNeurology Viral meningitis, also known as aseptic meningitis, is a type of meningitis due to a viral infection. It results in inflammation of the meninges (the membranes covering the brain and spin...
Viral meningitis
c0025297
1,537
wikipedia
https://en.wikipedia.org/wiki/Viral_meningitis
2021-01-18T19:06:14
{"mesh": ["D008587"], "umls": ["C0025297"], "wikidata": ["Q3301664"]}
Charcot-Marie-Tooth disease type 4F (CMT4F) is a severe, demyelinating subtype of Charcot-Marie-Tooth disease type 4 characterized by the childhood onset of a slowly-progressing typical CMT phenotype (i.e. distal muscle weakness and atrophy, as well as pes cavus) that presents severe sensory loss (frequently with...
Charcot-Marie-Tooth disease type 4F
c3540453
1,538
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=99952
2021-01-23T18:07:26
{"gard": ["12441"], "omim": ["614895"], "icd-10": ["G60.0"], "synonyms": ["CMT4F"]}
Hall (1965) described 5 families in which 14 cases of myxedema occurred in addition to the 5 probands. In 1 of these families, a case of thyrotoxicosis was also observed, and in each of 2 families a relative had nontoxic goiter. A sixth proband had a daughter with thyrotoxicosis. In the families of 32 other patients ...
MYXEDEMA
c0027145
1,539
omim
https://www.omim.org/entry/255900
2019-09-22T16:24:38
{"doid": ["11634"], "mesh": ["D009230"], "omim": ["255900"], "icd-10": ["E03.9"]}
Abortion in Costa Rica is severely restricted by criminal law. Currently, abortions are allowed in Costa Rica only in order to preserve the life or physical health of the woman. Abortions are illegal in almost all cases, including when the pregnancy is a result of rape or incest and when the fetus suffers from medica...
Abortion in Costa Rica
None
1,540
wikipedia
https://en.wikipedia.org/wiki/Abortion_in_Costa_Rica
2021-01-18T18:34:15
{"wikidata": ["Q4668447"]}
A number sign (#) is used with this entry because type A2 brachydactyly (BDA2) is caused by heterozygous mutation in the BMPR1B gene (603248) on chromosome 4q or in the GDF5 gene (601146) on chromosome 20q11. It can also be caused by heterozygous duplication of a proposed regulatory element on chromosome 20p12 th...
BRACHYDACTYLY, TYPE A2
c1832702
1,541
omim
https://www.omim.org/entry/112600
2019-09-22T16:44:07
{"doid": ["0110965"], "mesh": ["C537089"], "omim": ["112600"], "orphanet": ["93396"], "synonyms": ["Alternative titles", "BRACHYMESOPHALANGY II", "MOHR-WRIEDT TYPE BRACHYDACTYLY"]}
Spinocerebellar ataxia type 15/16 (SCA15/16) is a rare subtype of type I autosomal dominant cerebellar ataxia (ADCA type I; see this term). It is characterized by cerebellar ataxia, tremor and cognitive impairment. ## Epidemiology Prevalence is unknown. Fewer than 80 patients affected by the disease have been ident...
Spinocerebellar ataxia type 15/16
c1847725
1,542
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=98769
2021-01-23T17:31:41
{"gard": ["10477"], "mesh": ["C564685"], "omim": ["606658"], "icd-10": ["G11.2"], "synonyms": ["SCA15/16"]}
Recombinant chromosome 8 syndrome is a condition that involves heart and urinary tract abnormalities, moderate to severe intellectual disability, and a distinctive facial appearance. Many children with recombinant chromosome 8 syndrome do not survive past early childhood, usually due to complications related to their...
Recombinant chromosome 8 syndrome
c0795822
1,543
gard
https://rarediseases.info.nih.gov/diseases/9698/recombinant-chromosome-8-syndrome
2021-01-18T17:58:00
{"mesh": ["C535296"], "omim": ["179613"], "umls": ["C0795822"], "orphanet": ["96167"], "synonyms": ["Rec8 syndrome", "San Luis Valley recombinant chromosome 8 syndrome", "San Luis Valley syndrome"]}
A number sign (#) is used with this entry because karyomegalic interstitial nephritis (KMIN) is caused by homozygous or compound heterozygous mutation in the FAN1 gene (613534) on chromosome 15q. Description Karyomegalic tubulointerstitial nephritis (KTN) is a rare kidney disease characterized clinically by onset i...
INTERSTITIAL NEPHRITIS, KARYOMEGALIC
c3553774
1,544
omim
https://www.omim.org/entry/614817
2019-09-22T15:54:18
{"doid": ["0060911"], "omim": ["614817"], "orphanet": ["401996"], "synonyms": ["KIN", "Systemic karyomegaly"]}
Distal 7q11.23 microdeletion syndrome is a rare chromosomal anomaly characterized by epilepsy, neurodevelopmental disorder variably including developmental delays and intellectual disabilities of variable severity, learning disability and neurobehavioral abnormalities (autism spectrum disorder, hyperactivity, impulsi...
Distal 7q11.23 microdeletion syndrome
c3150999
1,545
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=254351
2021-01-23T18:19:54
{"omim": ["613729"], "icd-10": ["Q93.5"], "synonyms": ["Distal del(7)(q11.23)", "Distal monosomy 7q11.23"]}
Hereditary hyperferritinemia with congenital cataracts is characterized by the association of early onset (although generally absent at birth) cataract with persistently raised plasma ferritin concentrations in the absence of iron overload. ## Epidemiology Prevalence still needs to be precisely determined but is es...
Hereditary hyperferritinemia-cataract syndrome
c1833213
1,546
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=163
2021-01-23T18:43:45
{"gard": ["2806"], "mesh": ["C538137"], "omim": ["600886"], "umls": ["C1833213"], "icd-10": ["H26.0"], "synonyms": ["Bonneau-Beaumont syndrome", "HHCS", "Hereditary hyperferritinemia with congenital cataracts"]}
A number sign (#) is used with this entry because of evidence that X-linked mental retardation-72 (MRX72) is caused by hemizygous mutation in the RAB39B gene (300774) on chromosome Xq28. Mutation in the RAB39B gene can also cause X-linked recessive mental retardation with early-onset Parkinson disease, known as Wais...
MENTAL RETARDATION, X-LINKED 72
c2931498
1,547
omim
https://www.omim.org/entry/300271
2019-09-22T16:20:35
{"doid": ["0050776"], "mesh": ["C567906"], "omim": ["300271"], "orphanet": ["777"]}
## Description Preeclampsia, which along with chronic hypertension and gestational hypertension comprise the hypertensive disorders of pregnancy, is characterized by new hypertension (blood pressure 140/90 or greater) presenting after 20 weeks' gestation with clinically relevant proteinuria. Preeclampsia is 1 of th...
PREECLAMPSIA/ECLAMPSIA 1
c0032914
1,548
omim
https://www.omim.org/entry/189800
2019-09-22T16:32:28
{"doid": ["10591"], "mesh": ["D011225"], "omim": ["189800"], "icd-10": ["O13", "O14", "O14.2", "O14.90", "O14.9"], "orphanet": ["275555"], "synonyms": ["Alternative titles", "PREG1", "PEE", "TOXEMIA OF PREGNANCY"]}
Bruise on the pelvis from blunt trauma This article needs more medical references for verification or relies too heavily on primary sources. Please review the contents of the article and add the appropriate references if you can. Unsourced or poorly sourced material may be challenged and removed. Find sources: "Hi...
Hip pointer
None
1,549
wikipedia
https://en.wikipedia.org/wiki/Hip_pointer
2021-01-18T18:33:37
{"wikidata": ["Q17143043"]}
Hereditary antithrombin deficiency, also known as antithrombin III deficiency or AT III deficiency, is a disorder in which individuals are at increased risk for developing blood clots. The type of blood clots seen in individuals with this condition are typically clots that form in the deep veins of the leg (deep vein...
Hereditary antithrombin deficiency
c0272375
1,550
gard
https://rarediseases.info.nih.gov/diseases/6148/hereditary-antithrombin-deficiency
2021-01-18T18:00:04
{"mesh": ["D020152"], "omim": ["613118"], "orphanet": ["82"], "synonyms": ["Hereditary thrombophilia due to congenital antithrombin deficiency", "Inherited antithrombin deficiency", "Congenital Antithrombin III Deficiency", "Antithrombin III Deficiency", "Hereditary thrombophilia due to congenital antithrombin 3 defici...
For a general phenotypic description and a discussion of genetic heterogeneity of glioma, see GLM1 (137800). Mapping Working from the hypothesis that coinheritance of low-risk variants contributes to the 2-fold increased risk of glioma in relatives of individuals with primary brain tumors, Shete et al. (2009) condu...
GLIOMA SUSCEPTIBILITY 6
c0017638
1,551
omim
https://www.omim.org/entry/613031
2019-09-22T15:59:55
{"mesh": ["D005910"], "omim": ["613031"], "orphanet": ["182067"]}
Aspartylglucosaminuria is a condition that causes a progressive decline in mental functioning. Infants with aspartylglucosaminuria appear healthy at birth, and development is typically normal throughout early childhood. The first sign of this condition, evident around the age of 2 or 3, is usually delayed speech. Mi...
Aspartylglucosaminuria
c0268225
1,552
medlineplus
https://medlineplus.gov/genetics/condition/aspartylglucosaminuria/
2021-01-27T08:25:19
{"gard": ["5854"], "mesh": ["D054880"], "omim": ["208400"], "synonyms": []}
## Clinical Features In a family of Yemenite Jewish extraction, Frydman et al. (1992) described an autosomal recessive syndrome of blepharophimosis and ptosis with weakness of extraocular and frontal muscles. Prognathism, synophrys, and thick eyebrows added to a typical facial appearance. Additional findings includ...
BLEPHAROPHIMOSIS WITH PTOSIS, SYNDACTYLY, AND SHORT STATURE
c1859432
1,553
omim
https://www.omim.org/entry/210745
2019-09-22T16:30:22
{"mesh": ["C536235"], "omim": ["210745"], "orphanet": ["2057"]}
A number sign (#) is used with this entry because autosomal dominant progressive external ophthalmoplegia-6 (PEOA6) is caused by heterozygous mutation in the DNA2 gene (601810) on chromosome 10q. Description PEOA6 is characterized by muscle weakness, mainly affecting the lower limbs, external ophthalmoplegia, exerc...
PROGRESSIVE EXTERNAL OPHTHALMOPLEGIA WITH MITOCHONDRIAL DNA DELETIONS, AUTOSOMAL DOMINANT 6
c3554599
1,554
omim
https://www.omim.org/entry/615156
2019-09-22T15:53:01
{"omim": ["615156"], "orphanet": ["352470"], "synonyms": ["Mitochondrial DNA deletion syndrome with limb-girdle weakness", "PROGRESSIVE EXTERNAL OPHTHALMOPLEGIA, AUTOSOMAL DOMINANT 6", "mtDNA deletion syndrome with progressive myopathy", "Mitochondrial DNA deletion syndrome with progressive myopathy", "Alternative titl...
A number sign (#) is used with this entry because hereditary persistence of alpha-fetoprotein (HPAFP) is caused by heterozygous mutation in the AFP gene (104150) on chromosome 4q13. Description Hereditary persistence of alpha-fetoprotein (HPAFP) is a clinically benign autosomal dominant condition characterized by c...
ALPHA-FETOPROTEIN, HEREDITARY PERSISTENCE OF
c1863080
1,555
omim
https://www.omim.org/entry/615970
2019-09-22T15:50:23
{"omim": ["615970"], "orphanet": ["168615"], "synonyms": []}
Chromosome 2p duplication is a chromosome abnormality that occurs when there is an extra copy of genetic material on the short arm (p) of chromosome 2. The severity of the condition and the signs and symptoms depend on the size and location of the duplication and which genes are involved. Features that often occur in...
Chromosome 2p duplication
c0795803
1,556
gard
https://rarediseases.info.nih.gov/diseases/5337/chromosome-2p-duplication
2021-01-18T18:01:22
{"mesh": ["C538318"], "umls": ["C0795803"], "synonyms": ["Duplication 2p", "Trisomy 2p", "2p duplication", "2p trisomy", "Partial trisomy 2p"]}
Actinic conjunctivitis Actinic conjunctivitis causes a redness of the eyes, as well as swelling and often grayness around the eyes. Actinic conjunctivitis is an inflammation of the eye contracted from prolonged exposure to actinic (ultraviolet) rays. Symptoms are redness and swelling of the eyes. Most often th...
Actinic conjunctivitis
c1504543
1,557
wikipedia
https://en.wikipedia.org/wiki/Actinic_conjunctivitis
2021-01-18T18:35:04
{"icd-9": ["370.24"], "wikidata": ["Q3507879"]}
Pseudohypoparathyroidism type 1B (PHP-1b) is a type of pseudohypoparathyroidism (PHP; see this term) characterized by localized resistance to parathyroid hormone (PTH) mainly in the renal tissues which manifests with hypocalcemia, hyperphosphatemia and elevated PTH levels. About 60-70% of patients also present wi...
Pseudohypoparathyroidism type 1B
c1864100
1,558
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=94089
2021-01-23T16:54:22
{"gard": ["10680"], "mesh": ["C548075", "D011547"], "omim": ["603233"], "umls": ["C1864100", "C2932715"], "icd-10": ["E20.1"]}
This article needs more medical references for verification or relies too heavily on primary sources. Please review the contents of the article and add the appropriate references if you can. Unsourced or poorly sourced material may be challenged and removed. Find sources: "Neuromyotonia" – news · newspapers · books...
Neuromyotonia
c0242287
1,559
wikipedia
https://en.wikipedia.org/wiki/Neuromyotonia
2021-01-18T18:59:20
{"gard": ["6793"], "mesh": ["D020386"], "umls": ["C0751919", "C0242287"], "icd-9": ["333.90"], "icd-10": ["G71.1"], "orphanet": ["84142"], "wikidata": ["Q520797"]}
Limbic encephalitis with caspr2 antibodies is a rare neuroimmunological disorder characterized by the onset of cognitive deficits, psychiatric disturbances (e.g. personality changes), seizures, peripheral nerve hyperexcitability, dysautonomia, neuropathic pain, insomnia and weight loss, in association with detect...
Limbic encephalitis with caspr2 antibodies
c4706582
1,560
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=276402
2021-01-23T17:45:19
{"icd-10": ["G13.1"]}
A number sign (#) is used with this entry because of evidence that polycystic kidney disease-5 (PKD5) is caused by homozygous mutation in the DZIP1L gene (617570) on chromosome 3q22. Description PKD5, a form of autosomal recessive polycystic kidney disease (ARPKD), is characterized by early childhood onset of progr...
POLYCYSTIC KIDNEY DISEASE 5
c0085548
1,561
omim
https://www.omim.org/entry/617610
2019-09-22T15:45:20
{"doid": ["0080273"], "mesh": ["D017044"], "omim": ["617610"], "orphanet": ["731"]}
Trematodiases Eggs of trematodes found in liver cell SpecialtyInfectious disease SymptomsChest pain, Abdominal pain, Fever, digestion issues, Cough, Diarrhea, change in appetite [1][2] CausesTrematoda Diagnostic methodImmunodiagnosis, Parasitological diagnosis [3] PreventionEducation, food safety practice...
Trematodiases
c0040820
1,562
wikipedia
https://en.wikipedia.org/wiki/Trematodiases
2021-01-18T19:10:32
{"gard": ["1891"], "mesh": ["D014201"], "umls": ["C0040820"], "icd-9": ["121.9"], "orphanet": ["1685"], "wikidata": ["Q3030745"]}
Split hand split foot nystagmus is a rare congenital syndrome characterized by split hand and split foot deformity and eye abnormalities, especially nystagmus. It is thought to have an autosomal dominant mode of inheritance. Currently, the underlying genetic defect has not been identified. The outlook for childre...
Split hand split foot nystagmus
c1866740
1,563
gard
https://rarediseases.info.nih.gov/diseases/4967/split-hand-split-foot-nystagmus
2021-01-18T17:57:34
{"mesh": ["C537319"], "omim": ["183800"], "umls": ["C1866740"], "orphanet": ["2329"], "synonyms": ["Split hand nystagmus syndrome", "Karsch-Neugebauer syndrome", "KNS"]}
A narrow strip of hardened skin, a constricting ring, forms on the little toe at the level of the digitoplantar fold and progresses to spontaneous amputation of the digit. Familial occurrence has been noted by Maass (1926) and by DaSilva Lima (1880). Simon (1921) reported ainhum in father and 2 sons. Ainhum-like cons...
AINHUM
c0001860
1,564
omim
https://www.omim.org/entry/103400
2019-09-22T15:41:19
{"doid": ["11329"], "mesh": ["D000387"], "omim": ["103400"], "icd-9": ["136.0"], "icd-10": ["L94.6"]}
Feline zoonosis SpecialtyInfectious disease, veterinary medicine A feline zoonosis is a viral, bacterial, fungal, protozoan, nematode or arthropod infection that can be transmitted to humans from the domesticated cat, Felis catus. Some of these are diseases are reemerging and newly emerging infections or infes...
Feline zoonosis
None
1,565
wikipedia
https://en.wikipedia.org/wiki/Feline_zoonosis
2021-01-18T18:54:55
{"wikidata": ["Q28136278"]}
Palpation thyroiditis refers to the development of thyroid inflammation due to mechanical damage to thyroid follicles.[1] This can occur by vigorous repeated palpation (as with thyroid examination) or surgical manipulation (as can occur with radical neck dissection). It is a type of subacute thyroiditis. Patholog...
Palpation thyroiditis
c2960048
1,566
wikipedia
https://en.wikipedia.org/wiki/Palpation_thyroiditis
2021-01-18T18:52:45
{"umls": ["C2960048"], "wikidata": ["Q7128690"]}
Waardenburg syndrome is a group of genetic conditions that can cause hearing loss and changes in coloring (pigmentation) of the hair, skin, and eyes. Although most people with Waardenburg syndrome have normal hearing, moderate to profound hearing loss can occur in one or both ears. The hearing loss is present fro...
Waardenburg syndrome
c1847800
1,567
medlineplus
https://medlineplus.gov/genetics/condition/waardenburg-syndrome/
2021-01-27T08:24:40
{"gard": ["5525", "5519", "5520", "5523", "5524"], "mesh": ["D014849"], "omim": ["193500", "193510", "600193", "606662", "608890", "611584", "148820", "277580", "613265", "613266"], "synonyms": []}
A rare developmental defect with connective tissue involvement characterized by joint hyperextensibility and multiple dislocations of large joints, severe myopia, and short stature. Other common features include retinal detachment, iris and chorioretinal coloboma, kyphoscoliosis and other spine deformities, pectus ca...
Severe myopia-generalized joint laxity-short stature syndrome
c4540020
1,568
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=527450
2021-01-23T17:09:57
{"omim": ["617662"]}
Epidermolysis bullosa simplex with mottled pigmentation is a rare form of epidermolysis bullosa (EB). EB is a group of genetic conditions that cause the skin to be very fragile and to blister easily. Erosions and blisters form in response to minor injury or friction, such as rubbing or scratching.[2310] In EB simplex...
Epidermolysis bullosa simplex with mottled pigmentation
c0432316
1,569
gard
https://rarediseases.info.nih.gov/diseases/9737/epidermolysis-bullosa-simplex-with-mottled-pigmentation
2021-01-18T18:00:41
{"mesh": ["C535959"], "omim": ["131960"], "umls": ["C0432316"], "orphanet": ["79397"], "synonyms": ["EBS with mottled pigmentation", "EBS-MP", "Speckled hyperpigmentation, palmo-plantar punctate keratoses and childhood blistering"]}
Pseudohyperaldosteronism (also pseudoaldosteronism) is a medical condition which mimics the effects of elevated aldosterone (hyperaldosteronism) by presenting with high blood pressure (hypertension), low blood potassium levels (hypokalemia), metabolic alkalosis, and low levels of plasma renin activity (PRA).[1][2] Ho...
Pseudohyperaldosteronism
c0221043
1,570
wikipedia
https://en.wikipedia.org/wiki/Pseudohyperaldosteronism
2021-01-18T18:41:00
{"mesh": ["D056929"], "wikidata": ["Q524766"]}
For a phenotypic description and a discussion of genetic heterogeneity of schizophrenia, see 181500. Mapping Cao et al. (1997) studied 2 independent datasets and reported evidence of a susceptibility locus for schizophrenia on 6q but could not confirm linkage to 6p They used a 2-stage approach and nonparametric...
SCHIZOPHRENIA 5
c1864153
1,571
omim
https://www.omim.org/entry/603175
2019-09-22T16:13:15
{"omim": ["603175"], "synonyms": ["Alternative titles", "SCHIZOPHRENIA 5 WITH OR WITHOUT AN AFFECTIVE DISORDER", "SCHIZOPHRENIA SUSCEPTIBILITY LOCUS, CHROMOSOME 6q-RELATED"]}
A number sign (#) is used with this entry because of evidence that hydrops, lactic acidosis, and sideroblastic anemia (HLASA) is caused by compound heterozygous mutation in the LARS2 gene (604544) on chromosome 3p21. One such patient has been reported. Clinical Features Riley et al. (2016) reported a female infant,...
HYDROPS, LACTIC ACIDOSIS, AND SIDEROBLASTIC ANEMIA
c4310761
1,572
omim
https://www.omim.org/entry/617021
2019-09-22T15:47:13
{"omim": ["617021"], "orphanet": ["528091"], "synonyms": []}
A rare, genetic, slowly progressive neurodegenerative disease resulting from GRID2 deficiency characterized by motor, speech and cognitive delay, hypotonia, truncal and appendicular ataxia, and eye movement abnormalities (tonic upgaze, nystagmus, oculomotor apraxia). Intention tremor may also be associated. Brain ima...
Autosomal recessive congenital cerebellar ataxia due to GRID2 deficiency
c4015505
1,573
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=363432
2021-01-23T17:28:16
{"omim": ["616204"], "icd-10": ["G11.1"], "synonyms": ["Autosomal recessive congenital cerebellar ataxia due to ionotropic glutamate receptor delta-2 subunit deficiency", "SCAR18"]}
This article has multiple issues. Please help improve it or discuss these issues on the talk page. (Learn how and when to remove these template messages) This article is an orphan, as no other articles link to it. Please introduce links to this page from related articles; try the Find link tool for suggestions. (Sep...
Face distortion
c4072832
1,574
wikipedia
https://en.wikipedia.org/wiki/Face_distortion
2021-01-18T19:03:17
{"umls": ["C4072832"], "wikidata": ["Q5428354"]}
A number sign (#) is used with this entry because congenital disorder of glycosylation type If (CDG1F) is caused by homozygous or compound heterozygous mutation in the MPDU1 gene (604041) on chromosome 17p13. Description Congenital disorders of glycosylation (CDGs) are metabolic deficiencies in glycoprotein biosynt...
CONGENITAL DISORDER OF GLYCOSYLATION, TYPE If
c1836669
1,575
omim
https://www.omim.org/entry/609180
2019-09-22T16:06:33
{"doid": ["0080558"], "mesh": ["C535744"], "omim": ["609180"], "orphanet": ["79323"], "synonyms": ["Alternative titles", "CDG If"]}
## Summary ### Clinical characteristics. Alkaptonuria is caused by deficiency of homogentisate 1,2-dioxygenase, an enzyme that converts homogentisic acid (HGA) to maleylacetoacetic acid in the tyrosine degradation pathway. The three major features of alkaptonuria are the presence of HGA in the urine, ochronosis (bl...
Alkaptonuria
c0002066
1,576
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1454/
2021-01-18T20:46:50
{"mesh": ["D000474"], "synonyms": ["Alcaptonuria"]}
Post-traumatic epilepsy SpecialtyNeurology Post-traumatic epilepsy (PTE) is a form of acquired epilepsy that results from brain damage caused by physical trauma to the brain (traumatic brain injury, abbreviated TBI).[1] A person with PTE suffers repeated post-traumatic seizures (PTS, seizures that result from ...
Post-traumatic epilepsy
c0014557
1,577
wikipedia
https://en.wikipedia.org/wiki/Post-traumatic_epilepsy
2021-01-18T18:46:06
{"gard": ["7437"], "mesh": ["D004834"], "wikidata": ["Q7233592"]}
Glycogen storage disease Fanconi–Bickel syndrome is a form of glycogen storage disease. It is also known for Guido Fanconi and Horst Bickel,[1][2] who first described it in 1949. It is associated with GLUT2,[3][4] a glucose transport protein which, when functioning normally, allows glucose to exit several tissu...
Fanconi–Bickel syndrome
c3495427
1,578
wikipedia
https://en.wikipedia.org/wiki/Fanconi%E2%80%93Bickel_syndrome
2021-01-18T18:48:28
{"gard": ["2268"], "mesh": ["D005198"], "umls": ["C3495427"], "orphanet": ["2088"], "wikidata": ["Q5572613"]}
Redness of the skin or mucous membranes Not to be confused with Arrythmia. This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Erythema" – news · newspapers · books ...
Erythema
c0332575
1,579
wikipedia
https://en.wikipedia.org/wiki/Erythema
2021-01-18T18:50:00
{"mesh": ["D004890"], "umls": ["C0332575"], "icd-9": ["695"], "icd-10": ["L51", "L54"], "wikidata": ["Q1166142"]}
A number sign (#) is used with this entry because of evidence that microtia, hearing impairment, and cleft palate is caused by homozygous mutation in the HOXA2 gene (604685) on chromosome 7p15. One such family has been reported. There is also evidence that microtia with or without hearing impairment is caused by...
MICROTIA, HEARING IMPAIRMENT, AND CLEFT PALATE
c2676772
1,580
omim
https://www.omim.org/entry/612290
2019-09-22T16:02:01
{"mesh": ["C567359"], "omim": ["612290"], "orphanet": ["140963"]}
A number sign (#) is used with this entry because posterior column ataxia with retinitis pigmentosa (AXPC1) is caused by homozygous mutation in the FLVCR1 gene (609144) on chromosome 1q32. Description Posterior column ataxia with retinitis pigmentosa is an autosomal recessive neurologic disorder characterized by ch...
POSTERIOR COLUMN ATAXIA WITH RETINITIS PIGMENTOSA
c1836916
1,581
omim
https://www.omim.org/entry/609033
2019-09-22T16:06:48
{"mesh": ["C536343"], "omim": ["609033"], "orphanet": ["88628"], "synonyms": ["Alternative titles", "PCARP"]}
Xq27.3q28 duplication syndrome is a recently described syndrome characterized by short stature, hypogonadism, developmental delay and facial dysmorphism. ## Epidemiology It has been clinically and molecularly characterized in 3 male members from the same family. ## Clinical description Facial features include dee...
Xq27.3q28 duplication syndrome
c3275521
1,582
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=261483
2021-01-23T17:45:25
{"omim": ["300869"], "icd-10": ["Q99.8"], "synonyms": ["Dup(X)(q27.3q28)", "Trisomy Xq27.3-q28", "Trisomy Xq27.3q28", "Xq27.3-q28 microduplication syndrome"]}
Pontine tegmental cap dysplasia is a rare, central nervous system malformation characterized by specific pattern of congenital anomalies affecting the pons, medulla, and cerebellum. Clinical manifestations of multiple cranial nerves deficits, pyramidal and cerebellar signs include neonatal hypotonia, ataxia, sensorin...
Pontine tegmental cap dysplasia
c3541340
1,583
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=269229
2021-01-23T17:03:10
{"gard": ["10919"], "omim": ["614688"], "icd-10": ["Q04.8"], "synonyms": ["PTCD"]}
A rare genetic interstitial lung disease characterized by diffuse lung disease of variable phenotype ranging from severe respiratory insufficiency in infancy to asymptomatic adults, due to surfactant protein C deficiency. Typical presentation in infancy includes dyspnea, cough, wheezing, and gradual cyanosis, with or...
Interstitial lung disease due to SP-C deficiency
c1970470
1,584
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=440392
2021-01-23T17:34:06
{"mesh": ["C567048"], "omim": ["610913"], "icd-10": ["J84.8"], "synonyms": ["Interstitial lung disease due to surfactant protein C deficiency"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Chauffeur's fracture" – news · newspapers · books · scholar · JSTOR (February 2009) (Learn how and when to remove this ...
Chauffeur's fracture
c1961067
1,585
wikipedia
https://en.wikipedia.org/wiki/Chauffeur%27s_fracture
2021-01-18T19:05:27
{"umls": ["C1961067"], "wikidata": ["Q3572829"]}
A rare, benign tumor of the pancreas characterized by variable number and size of the cysts lined with glycogen rich epithelial cells. Clinical manifestation may include epigastric or abdominal pain, weight loss, diabetes, jaundice and palpable abdominal mass. Some patients have no symptoms and the tumor is disco...
Adenoma of pancreas
c1142432
1,586
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=93292
2021-01-23T18:21:49
{"gard": ["4204"], "mesh": ["C538110"], "umls": ["C1142432"], "icd-10": ["D13.6"], "synonyms": ["Pancreatic adenoma"]}
A number sign (#) is used with this entry because antigens of the Ss blood group result from variation in the gene encoding glycophorin B (GYPB; 617923) on chromosome 4q31. Description Ss blood group antigens reside on the red-cell glycoprotein GYPB. The S and s antigens result from a polymorphism at amino acid 29 ...
BLOOD GROUP, Ss
None
1,587
omim
https://www.omim.org/entry/111740
2019-09-22T16:44:12
{"omim": ["111740"], "synonyms": ["Alternative titles", "Ss BLOOD GROUP"]}
Niemann-Pick disease is an inherited condition involving lipid metabolism, which is the breakdown, transport, and use of fats and cholesterol in the body. In people with this condition, abnormal lipid metabolism causes harmful amounts of lipids to accumulate in the spleen, liver, lungs, bone marrow, and brain. Nieman...
Niemann-Pick disease type A
c0268242
1,588
gard
https://rarediseases.info.nih.gov/diseases/7206/niemann-pick-disease-type-a
2021-01-18T17:58:41
{"mesh": ["D052536"], "omim": ["257200"], "orphanet": ["77292"], "synonyms": ["Sphingomyelin lipidosis", "Sphingomyelinase deficiency"]}
## Description Congenital dysplasia of the hip (CDH) is an abnormality of the seating of the femoral head in the acetabulum. Its severity ranges from mild instability of the femoral head with slight capsular laxity, through moderate lateral displacement of the femoral head, without loss of contact of the head with ...
DEVELOPMENTAL DYSPLASIA OF THE HIP 1
c4551649
1,589
omim
https://www.omim.org/entry/142700
2019-09-22T16:40:11
{"mesh": ["D006618"], "omim": ["142700"], "synonyms": ["Alternative titles", "HIP DYSPLASIA, DEVELOPMENTAL", "HIP DYSPLASIA, CONGENITAL", "ACETABULAR DYSPLASIA"]}
A number sign (#) is used with this entry because of the demonstration that the disorder is caused by mutations in the human homolog of the mouse 'hairless' gene (HR; 602302); see 203655. Clinical Features Papillary lesions over most of the body and almost complete absence of hair are features. The patients are bor...
ATRICHIA WITH PAPULAR LESIONS
c1859592
1,590
omim
https://www.omim.org/entry/209500
2019-09-22T16:30:37
{"doid": ["0060689"], "mesh": ["C565924"], "omim": ["209500"], "orphanet": ["86819"], "synonyms": ["Alternative titles", "PAPULAR ATRICHIA"]}
Giant-cell reticulohistiocytoma SpecialtyDermatology Giant-cell reticulohistiocytoma (also known as Solitary reticulohistiocytoma and Solitary reticulohistiocytosis)[1] is a cutaneous condition characterized by a solitary skin lesion.[1] ## See also[edit] * Indeterminate cell histiocytosis * List of cuta...
Giant-cell reticulohistiocytoma
None
1,591
wikipedia
https://en.wikipedia.org/wiki/Giant-cell_reticulohistiocytoma
2021-01-18T18:32:54
{"wikidata": ["Q5558340"]}
Multisystemic smooth muscle dysfunction syndrome is a disease in which the activity of smooth muscle throughout the body is impaired. This leads to widespread problems including blood vessel abnormalities, a decreased response of the pupils to light, a weak bladder, and weakened contractions of the muscles used f...
Multisystemic smooth muscle dysfunction syndrome
c3151201
1,592
gard
https://rarediseases.info.nih.gov/diseases/12811/multisystemic-smooth-muscle-dysfunction-syndrome
2021-01-18T17:58:53
{"omim": ["613834"], "orphanet": ["404463"], "synonyms": ["Congenital mydriasis, patent ductus arteriosus, thoracic aortic aneurysm, and vasculopathy"]}
A number sign (#) is used with this entry because of evidence that spinocerebellar ataxia-29 (SCA29), also known as congenital nonprogressive cerebellar ataxia (CNPCA), is caused by heterozygous mutation in the ITPR1 gene (147265) on chromosome 3p26. Description Spinocerebellar ataxia-29 is an autosomal dominant ne...
SPINOCEREBELLAR ATAXIA 29
c1861732
1,593
omim
https://www.omim.org/entry/117360
2019-09-22T16:43:31
{"doid": ["0050978"], "mesh": ["C537206"], "omim": ["117360"], "orphanet": ["208513"], "synonyms": ["Alternative titles", "CEREBELLAR ATAXIA, CONGENITAL NONPROGRESSIVE, AUTOSOMAL DOMINANT", "CEREBELLAR VERMIS APLASIA", "APLASIA OF CEREBELLAR VERMIS"]}
A rare, non-syndromic, posterior fossa malformation characterized by a cisterna magna that measures above 15 mm in length, 5 mm in height and 20 mm in width (or greater than 10 mm in fetuses) associated with a normal cerebellar vermis and absence of hydrocephalus. The majority of patients are asymptomatic; however, v...
Mega-cisterna magna
c3164501
1,594
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=97252
2021-01-23T17:48:27
{"umls": ["C3164501"], "icd-10": ["Q07.8"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Dieterich's disease" – news · newspapers · books · scholar · JSTOR (December 2018) (Learn how and when to remove this t...
Dieterich's disease
c2931124
1,595
wikipedia
https://en.wikipedia.org/wiki/Dieterich%27s_disease
2021-01-18T19:00:24
{"gard": ["204"], "mesh": ["C536172"], "umls": ["C2931124"], "wikidata": ["Q55790152"]}
A number sign (#) is used with this entry because of evidence that GPI biosynthesis defect-1 (GPIBD1) is caused by homozygous mutation in the PIGM gene (610273) on chromosome 1q23. Description Glycosylphosphatidylinositol is a glycolipid that anchors more than 150 proteins to the cell surface, and these proteins, t...
GLYCOSYLPHOSPHATIDYLINOSITOL BIOSYNTHESIS DEFECT 1
c1853205
1,596
omim
https://www.omim.org/entry/610293
2019-09-22T16:04:44
{"mesh": ["C537277"], "omim": ["610293"], "orphanet": ["83639"], "synonyms": ["Alternative titles", "PORTAL HYPERTENSION WITH SEIZURES AND/OR MACROCEPHALY", "GLYCOSYLPHOSPHATIDYLINOSITOL DEFICIENCY"]}
Acholia SpecialtyGastroenteritis Acholia is the lack or absence of bile secretion.[1] It can also be referred to as hypocholia.[2] Acholia is a sign, meaning lack of the normal brown color in feces, pale feces, suggesting interference with liver function.[3] ## Contents * 1 Etymology * 2 Cause * 3 See ...
Acholia
c0948198
1,597
wikipedia
https://en.wikipedia.org/wiki/Acholia
2021-01-18T18:42:26
{"umls": ["C0948198"], "icd-9": ["575.8"], "icd-10": ["K82.8"], "wikidata": ["Q8187550"]}
In 95% of cases worldwide, Leber hereditary optic atrophy (LHON) is due to 1 of 3 point mutations of mitochondrial DNA in genes that code for complex I of the respiratory chain: 3460G-A in MTND1 (516000.0001), 11778G-A in MTND4 (516003.0001), and 14484T-C in MTND6 (516006.0001). That only approximately 50% of mal...
LEBER OPTIC ATROPHY, SUSCEPTIBILITY TO
c0917796
1,598
omim
https://www.omim.org/entry/308905
2019-09-22T16:17:56
{"mesh": ["D029242"], "omim": ["308905"], "orphanet": ["104"], "synonyms": ["Alternative titles", "LOAS", "LEBER HEREDITARY OPTIC NEUROPATHY, MODIFIER OF", "LHON, MODIFIER OF"]}
A rare variant of Guillain-Barré syndrome characterized by acute onset monophasic sensory neuropathy with diminished or absent tendon reflexes, loss of proprioception, positive Romberg sign and nerve conduction features of demyelination. It presents several weeks after acute infection with paresthesias, ataxia and ne...
Acute sensory ataxic neuropathy
c4707661
1,599
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=231466
2021-01-23T18:32:33
{"icd-10": ["G61.0"], "synonyms": ["ASAN", "Acute sensory ataxic GBS", "Acute sensory ataxic Guillain-Barré syndrome"]}