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A number sign (#) is used with this entry because of evidence that combined oxidative phosphorylation deficiency-31 (COXPD31) is caused by homozygous or compound heterozygous mutation in the MIPEP gene (602241) on chromosome 13q12. Description Combined oxidative phosphorylation deficiency-31 is an autosomal recessi...
COMBINED OXIDATIVE PHOSPHORYLATION DEFICIENCY 31
c4310661
30,200
omim
https://www.omim.org/entry/617228
2019-09-22T15:46:25
{"omim": ["617228"], "orphanet": ["478049"], "synonyms": []}
Pseudohypoaldosteronism In pseudohypoaldosteronism, aldosterone is elevated (hyperaldosteronism), but because the body fails to respond to it, it appears similar to hypoaldosteronism. SpecialtyNephrology Pseudohypoaldosteronism (PHA) is a condition that mimics hypoaldosteronism.[1] However, the condition is ...
Pseudohypoaldosteronism
c0033805
30,201
wikipedia
https://en.wikipedia.org/wiki/Pseudohypoaldosteronism
2021-01-18T18:45:46
{"gard": ["4671"], "mesh": ["D011546"], "umls": ["CL495850", "C0033805"], "icd-10": ["N25.8"], "orphanet": ["444916"], "wikidata": ["Q200745"]}
Woods et al. (1995) reported the case of an infant with pre- and postnatal microcephaly and growth retardation, a distinctive face, and developmental delay. Seckel syndrome was the initial diagnosis. The infant became pancytopenic at 16 months of age and died soon thereafter. His bone marrow was of normal cellula...
INTRAUTERINE GROWTH RETARDATION WITH INCREASED MITOMYCIN C SENSITIVITY
c0265202
30,202
omim
https://www.omim.org/entry/600546
2019-09-22T16:16:03
{"omim": ["600546"], "orphanet": ["808"]}
A number sign (#) is used with this entry because juvenile-onset Parkinson disease-19A (PARK19A) and early-onset Parkinson disease-19B (PARK19B) are caused by homozygous mutation in the DNAJC6 gene (608375) on chromosome 1p31. Description Parkinson disease-19A is an autosomal recessive neurodegenerative disorder ch...
PARKINSON DISEASE 19A, JUVENILE-ONSET
c4310802
30,203
omim
https://www.omim.org/entry/615528
2019-09-22T15:51:49
{"doid": ["0060891"], "omim": ["615528"], "orphanet": ["2828", "391411"], "synonyms": ["Early-onset Parkinson disease", "Alternative titles", "YOPD", "PARK19, FORMERLY"]}
A very rare acrofacial dysostosis characterized by normal intelligence, shortness of stature, and mild acrofacial dysostosis (malar hypoplasia, micrognathia and webbing of digits with shortening of the fourth metacarpals) associated with oligodontia, normal or high arched palate, aplasia cutis verticis with pili tort...
Acrofacial dysostosis, Palagonia type
c1866168
30,204
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1787
2021-01-23T18:45:50
{"gard": ["499"], "mesh": ["C538185"], "omim": ["601829"], "umls": ["C1866168"], "icd-10": ["Q75.4"]}
Collins et al. (1995) described a woman with congenital dislocation of the hips, epicanthus, flat face, and slight joint laxity. Her growth was normal. Her 3 daughters were relatively short and had congenital dislocation of the hips, hyperextensibility of joints, and characteristic facial appearance (flat face with b...
DISLOCATION OF HIP, CONGENITAL, WITH HYPEREXTENSIBILITY OF FINGERS AND FACIAL DYSMORPHISM
c1832353
30,205
omim
https://www.omim.org/entry/601450
2019-09-22T16:14:43
{"mesh": ["C563315"], "omim": ["601450"], "orphanet": ["2412"], "synonyms": ["Collins-Pope syndrome", "Alternative titles", "HIP, CONGENITAL DISLOCATION OF, WITH HYPEREXTENSIBILITY OF FINGERS AND FACIAL DYSMORPHISM"]}
Sudden Wealth Syndrome (SWS) SpecialtyAbnormal Psychology SymptomsSocial isolation, paranoia, uncertainty, shock[1] DurationDependent on situation[2] CausesSudden lottery winnings, large inheritances, gambling winnings, trading cryptocurrencies (Bitcoin)[3] Risk factorsDepression (mood), Anxiety Disorders, ...
Sudden wealth syndrome
None
30,206
wikipedia
https://en.wikipedia.org/wiki/Sudden_wealth_syndrome
2021-01-18T18:31:48
{"wikidata": ["Q7633608"]}
Teebi (1991) described brother and sister, offspring of healthy first-cousin Palestinian Arab parents, who had trigonocephaly, brachycephaly, bulbous nose which was slightly bifid at the tip, micrognathia, and relatively broad metatarsals and phalanges. Both showed severe psychomotor retardation. The metopic sutu...
TRIGONOBRACHYCEPHALY, BULBOUS BIFID NOSE, MICROGNATHIA, AND ABNORMALITIES OF THE HANDS AND FEET
c1848743
30,207
omim
https://www.omim.org/entry/275595
2019-09-22T16:21:29
{"mesh": ["C564759"], "omim": ["275595"], "orphanet": ["3368"]}
Familial Amyloidosis, Finnish Type Other namesGelsolin amyloidosis This condition is inherited in an autosomal dominant manner Familial Amyloidosis, Finnish Type (FAF), also called hereditary gelsolin amyloidosis and AGel amyloidosis (AGel), is an amyloid condition with a number of associated cutaneous and n...
Familial Amyloidosis, Finnish Type
c0936273
30,208
wikipedia
https://en.wikipedia.org/wiki/Familial_Amyloidosis,_Finnish_Type
2021-01-18T19:04:43
{"mesh": ["D028227"], "umls": ["C0936273"], "orphanet": ["85448"], "wikidata": ["Q4064296"]}
A number sign (#) is used with this entry because of evidence that neurodevelopmental disorder with visual defects and brain anomalies (NEDVIBA) is caused by heterozygous mutation in the HK1 gene (142600) on chromosome 10q22. Description Neurodevelopmental disorder with visual defects and brain anomalies (NEDVI...
NEURODEVELOPMENTAL DISORDER WITH VISUAL DEFECTS AND BRAIN ANOMALIES
None
30,209
omim
https://www.omim.org/entry/618547
2019-09-22T15:41:31
{"omim": ["618547"]}
Orthostatic hypotension is a drop in blood pressure that occurs when moving from a laying down (supine) position to a standing (upright) position. The word "orthostasis" means to stand up, so the condition is defined as low blood pressure (hypotension) that occurs upon standing. When standing up, gravity moves blood...
Orthostatic hypotension
c0020651
30,210
medlineplus
https://medlineplus.gov/genetics/condition/orthostatic-hypotension/
2021-01-27T08:24:52
{"gard": ["12959"], "mesh": ["D007024"], "synonyms": []}
A number sign (#) is used with this entry because of evidence that lung disease, immunodeficiency, and chromosome breakage syndrome (LICS) is caused by homozygous or compound heterozygous mutation in the NSMCE3 gene (608243) on chromosome 15q13. Description LICS is an autosomal recessive chromosome breakage syndrom...
LUNG DISEASE, IMMUNODEFICIENCY, AND CHROMOSOME BREAKAGE SYNDROME
c4310653
30,211
omim
https://www.omim.org/entry/617241
2019-09-22T15:46:23
{"omim": ["617241"]}
Dipygus Myrtle Corbin, a famous dipygus. SymptomsBody axis forks left and right partway along the torso with the posterior end (pelvis and legs) duplicated CausesCongenital deformity This article needs additional citations for verification. Please help improve this article by adding citations to reliable s...
Dipygus
c0266688
30,212
wikipedia
https://en.wikipedia.org/wiki/Dipygus
2021-01-18T18:46:52
{"gard": ["1164"], "mesh": ["C564315"], "umls": ["C0266688"], "orphanet": ["1756"], "wikidata": ["Q5280135"]}
A number sign (#) is used with this entry because of evidence that osteoglophonic dysplasia (OGD) is caused by heterozygous mutation in the gene encoding fibroblast growth factor receptor-1 (FGFR1; 136350) on chromosome 8p11. Clinical Features Beighton et al. (1980) described a seemingly 'new' form of dwarfism ...
OSTEOGLOPHONIC DYSPLASIA
c0432283
30,213
omim
https://www.omim.org/entry/166250
2019-09-22T16:37:01
{"mesh": ["C536050"], "omim": ["166250"], "orphanet": ["2645"], "synonyms": ["Alternative titles", "OSTEOGLOPHONIC DWARFISM"]}
Giant-cell fibroma is a type of fibroma not associated with trauma or irritation. It can occur at any age and on a mucous membrane surface. The most common oral locations are on the gingiva of the mandible, tongue, and palate. It is a localized reactive proliferation of fibrous connective tissue. Giant-cell fibroma ...
Giant-cell fibroma
None
30,214
wikipedia
https://en.wikipedia.org/wiki/Giant-cell_fibroma
2021-01-18T18:45:24
{"wikidata": ["Q5558339"]}
A rare bone development disorder characterized by abnormal bowing of the fibula with subsequent non-healing fractures and formation of a false joint (pseudoarthrosis), and instability and angulation at the pseudoarthrosis site. The defect is typically unilateral and often associated with pseudoarthrosis of the ti...
Congenital pseudoarthrosis of the fibula
None
30,215
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=295022
2021-01-23T17:01:21
{"icd-10": ["Q74.2"], "synonyms": ["Congenital pseudarthrosis of the fibula"]}
## Summary ### Clinical characteristics. Duane syndrome is a strabismus condition clinically characterized by congenital non-progressive limited horizontal eye movement accompanied by globe retraction which results in narrowing of the palpebral fissure. The lateral movement anomaly results from failure of the abduc...
Duane Syndrome
c0013261
30,216
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1190/
2021-01-18T21:30:00
{"mesh": ["D004370"], "synonyms": ["Duane Anomaly", "Isolated; Duane Retraction Syndrome; Stilling-Turk-Duane Syndrome"]}
Ketotic hypoglycemia is a medical term used in two ways: (1) broadly, to refer to any circumstance in which low blood glucose is accompanied by ketosis, and (2) in a much more restrictive way to refer to recurrent episodes of hypoglycemic symptoms with ketosis and, often, vomiting, in young children. The first usage ...
Ketotic hypoglycemia
c0271713
30,217
wikipedia
https://en.wikipedia.org/wiki/Ketotic_hypoglycemia
2021-01-18T19:01:05
{"wikidata": ["Q1403928"]}
Propionic acidemia (PA) is an organic aciduria caused by the deficient activity of the propionyl Coenzyme A carboxylase and is characterized by life threatening episodes of metabolic decompensation, neurological dysfunction and that may be complicated by cardiomyopathy. ## Epidemiology The prevalence rate is pr...
Propionic acidemia
c0268579
30,218
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=35
2021-01-23T18:29:48
{"gard": ["467"], "mesh": ["D056693"], "omim": ["606054"], "umls": ["C0268579", "C0311298", "C2717876"], "icd-10": ["E71.1"], "synonyms": ["Ketotic hyperglycinemia", "Propionic aciduria", "Propionyl-CoA carboxylase deficiency"]}
CHD2 myoclonic encephalopathy is a condition characterized by recurrent seizures (epilepsy), abnormal brain function (encephalopathy), and intellectual disability. Epilepsy begins in childhood, typically between ages 6 months and 4 years. Each individual may experience a variety of seizure types. The most common are ...
CHD2 myoclonic encephalopathy
c3809278
30,219
medlineplus
https://medlineplus.gov/genetics/condition/chd2-myoclonic-encephalopathy/
2021-01-27T08:24:49
{"omim": ["615369"], "synonyms": []}
Lopez-Hernandez syndrome, which may be classified among the neurocutaneous syndromes, associates abnormalities of the cerebellum (rhombencephalosynapsis), cranial nerves (trigeminal anesthesia), and scalp (alopecia). It has been reported in 11 individuals so far. Other features observed in patients were craniosynosto...
Gómez-López-Hernández syndrome
c0795959
30,220
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1532
2021-01-23T18:21:36
{"gard": ["1586", "229"], "mesh": ["C537285"], "omim": ["601853"], "umls": ["C0795959"], "icd-10": ["Q07.8"], "synonyms": ["Cerebellotrigeminal-dermal dysplasia syndrome", "Craniosynostosis-alopecia-brain defect syndrome"]}
By the study of mouse-human lymphocyte hybrids, Nikinmaa et al. (1983) assigned to chromosome 11 the gene for a cell surface glycoprotein recognized by a mouse monoclonal antibody, Mab4. The antigen is present on all human peripheral blood leukocytes on human fibroblasts and on human lymphoid and erythroid cell lines...
SURFACE ANTIGEN, GLYCOPROTEIN 75
c1861423
30,221
omim
https://www.omim.org/entry/185540
2019-09-22T16:34:03
{"omim": ["185540"], "synonyms": ["Alternative titles", "SURFACE GLYCOPROTEIN 75"]}
A number sign (#) is used with this entry because combined oxidative phosphorylation deficiency-7 (COXPD7) is caused by homozygous mutation in the C12ORF65 gene (613541) on chromosome 12q24. For a discussion of genetic heterogeneity of combined oxidative phosphorylation deficiency, see COXPD1 (609060). Clinical Fea...
COMBINED OXIDATIVE PHOSPHORYLATION DEFICIENCY 7
c3150801
30,222
omim
https://www.omim.org/entry/613559
2019-09-22T15:58:17
{"doid": ["0060286"], "omim": ["613559"], "orphanet": ["254930"], "synonyms": ["COXPD7", "Severe C12ORF65-related COXPD", "Severe C12ORF65-related combined oxidative phosphorylation defect"]}
Craniosynostosis-dental anomalies is a rare, genetic, cranial malformation syndrome characterized by premature fusion of multiple or all calvarial sutures (resulting in variable abnormal shape of the head), midface hypoplasia, delayed and ectopic tooth eruption and supernumerary teeth. Associated facial dysmorphism i...
Craniosynostosis-dental anomalies
c3280073
30,223
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=284149
2021-01-23T18:23:10
{"omim": ["614188"], "icd-10": ["Q87.0"], "synonyms": ["Kreiborg-Pakistani syndrome"]}
A number sign (#) is used with this entry because hereditary nonpolyposis colorectal cancer-4 (HNPCC4) is caused by heterozygous mutation in the PMS2 gene (600259) on chromosome 7p22. Clinical Features Nicolaides et al. (1994) identified a germline deletion in the PMS2 gene in a patient with a family history of HNP...
COLORECTAL CANCER, HEREDITARY NONPOLYPOSIS, TYPE 4
c1333990
30,224
omim
https://www.omim.org/entry/614337
2019-09-22T15:55:39
{"doid": ["0070275"], "mesh": ["D003123"], "omim": ["614337"], "orphanet": ["144"]}
A number sign (#) is used with this entry because nephrotic syndrome type 9 (NPHS9) is caused by homozygous or compound heterozygous mutation in the ADCK4 gene (COQ8B; 615567) on chromosome 19q13. Description Nephrotic syndrome type 9 (NPHS9) is an autosomal recessive chronic kidney disorder characterized by signif...
NEPHROTIC SYNDROME, TYPE 9
c1868672
30,225
omim
https://www.omim.org/entry/615573
2019-09-22T15:51:37
{"doid": ["0080391"], "mesh": ["C536404"], "omim": ["615573"], "orphanet": ["656"]}
A number sign (#) is used with this entry because of evidence that autosomal recessive deafness-101 (DFNB101) is caused by homozygous mutation in the GRXCR2 gene (615762) on chromosome 5q32. One such family has been reported. Clinical Features Imtiaz et al. (2014) reported 3 sibs, born of consanguineous Pakistani p...
DEAFNESS, AUTOSOMAL RECESSIVE 101
c3892049
30,226
omim
https://www.omim.org/entry/615837
2019-09-22T15:50:51
{"doid": ["0110462"], "omim": ["615837"], "orphanet": ["90636"], "synonyms": ["Autosomal recessive isolated neurosensory deafness type DFNB", "Autosomal recessive isolated sensorineural deafness type DFNB", "Autosomal recessive non-syndromic neurosensory deafness type DFNB"]}
Isolated lissencephaly type 1 without known genetic defects belongs to the genetically heterogeneous group, classic lissencephaly (see this term). It is a diagnosis of exclusion, when neither associated malformations nor family history are present, and in the absence of mutations of genes known to be involved in clas...
Isolated lissencephaly type 1 without known genetic defects
None
30,227
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1084
2021-01-23T17:21:31
{"icd-10": ["Q04.3"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Drug-induced pigmentation" – news · newspapers · books · scholar · JSTOR (September 2018) (Learn how and when to remove...
Drug-induced pigmentation
c0406698
30,228
wikipedia
https://en.wikipedia.org/wiki/Drug-induced_pigmentation
2021-01-18T18:43:17
{"umls": ["C0406698"], "wikidata": ["Q5308816"]}
Ectasia of the right atrial appendage is a rare cardiac malformation characterized by the enlargement of the right auricle without any other associated cardiac lesions. It can be asymptomatic and diagnosed fortuitously, prenatally or during routine clinical examinations or it can present with heart murmur, palpit...
Ectasia of the right atrial appendage
None
30,229
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=99101
2021-01-23T18:57:44
{"icd-10": ["Q20.8"], "synonyms": ["Dilatation of the right atrial appendage", "Dilatation of the right atrial auricle", "Ectasia of the right atrial auricle"]}
A rare hepatic disease characterized by intrahepatic cholestasis and deterioration of liver function in patients receiving parenteral nutrition for extended periods of time (signs may appear as early as within the first two weeks of initiation of parenteral nutrition). The condition commonly occurs in neonates and us...
Parenteral nutrition-associated cholestasis
None
30,230
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=567983
2021-01-23T17:55:02
{"synonyms": ["PNAC"]}
## Summary ### Clinical characteristics. KCNQ3-related disorders include benign familial neonatal epilepsy (BFNE) and benign familial infantile epilepsy (BFIE), seizure disorders that occur in children who typically have normal psychomotor development. An additional KCNQ3-related disorder involves developmental dis...
KCNQ3-Related Disorders
None
30,231
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK201978/
2021-01-18T21:16:39
{"synonyms": []}
A number sign (#) is used with this entry because of evidence that nongoitrous congenital hypothyroidism-6 (CHNG6) is caused by heterozygous mutation in the THRA gene (190120) on chromosome 17q21. For a general phenotypic description and a discussion of genetic heterogeneity of congenital nongoitrous hypothyroidism,...
HYPOTHYROIDISM, CONGENITAL, NONGOITROUS, 6
c3280817
30,232
omim
https://www.omim.org/entry/614450
2019-09-22T15:55:12
{"doid": ["0070128"], "omim": ["614450"], "orphanet": ["97927"], "synonyms": []}
Metabolic acidosis The level of bicarbonate in the blood (HCO3-) determines the severity of acidosis. Bicarbonate measurements are part of routine metabolic panels. SpecialtyNephrology ComplicationsAcute: poor morbidity and mortality outcomes; Chronic: adverse outcomes on kidney function, musculoskeletal syst...
Metabolic acidosis
c0220981
30,233
wikipedia
https://en.wikipedia.org/wiki/Metabolic_acidosis
2021-01-18T18:47:21
{"mesh": ["D000138"], "icd-9": ["276.2"], "icd-10": ["E87.2"], "wikidata": ["Q1598200"]}
A number sign (#) is used with this entry because primary ciliary dyskinesia-9 (CILD9) can be caused by homozygous mutation in the DNAI2 gene (605483) on chromosome 17q25. For a general description and a discussion of genetic heterogeneity of primary ciliary dyskinesia and Kartagener syndrome, see CILD1 (244400)...
CILIARY DYSKINESIA, PRIMARY, 9
c2676235
30,234
omim
https://www.omim.org/entry/612444
2019-09-22T16:01:30
{"doid": ["0110622"], "mesh": ["C567310"], "omim": ["612444", "244400"], "orphanet": ["244"], "synonyms": ["Alternative titles", "CILIARY DYSKINESIA, PRIMARY, 9, WITH OR WITHOUT SITUS INVERSUS", "PCD"], "genereviews": ["NBK1122"]}
This article needs more medical references for verification or relies too heavily on primary sources. Please review the contents of the article and add the appropriate references if you can. Unsourced or poorly sourced material may be challenged and removed. Find sources: "Overriding aorta" – news · newspapers · bo...
Overriding aorta
c0265886
30,235
wikipedia
https://en.wikipedia.org/wiki/Overriding_aorta
2021-01-18T18:49:12
{"icd-9": ["747.21"], "icd-10": ["Q25.4"], "wikidata": ["Q2142075"]}
Glucagonoma is a rare, functioning type of pancreatic neuroendocrine tumor (PNET; see this term) that hypersecretes glucagon, leading to a syndrome comprised of necrolytic migratory erythema, diabetes mellitus, anemia, weight loss, mucosal abnormalities, thromboembolism, gastrointestinal and neuropsychiatric symp...
Glucagonoma
c0017689
30,236
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=97280
2021-01-23T18:36:01
{"gard": ["2496", "9399"], "mesh": ["D005935"], "umls": ["C0017689"], "icd-10": ["E16.8"], "synonyms": ["Glucagonoma syndrome"]}
Erythrocyanosis crurum SpecialtyDermatology Erythrocyanosis crurum is a skin condition, a variant of acrocyanosis caused by chronic exposure to cold. ## See also[edit] * Chilblains * List of cutaneous conditions ## References[edit] * Otto Braun-Falco; G. Plewig; H. H. Wolff; Walter H. C. Burgdorf (20...
Erythrocyanosis crurum
c0264946
30,237
wikipedia
https://en.wikipedia.org/wiki/Erythrocyanosis_crurum
2021-01-18T18:43:38
{"umls": ["C0264946"], "icd-10": ["I73.8"], "wikidata": ["Q5396458"]}
A number sign (#) is used with this entry because Waardenburg syndrome type 1 (WS1) is caused by heterozygous mutation in the PAX3 gene (606597) on chromosome 2q36. Waardenburg syndrome type 3 (WS3; 148820) is also caused by mutation in the PAX3 gene. Description Waardenburg syndrome type 1 is an autosomal dom...
WAARDENBURG SYNDROME, TYPE 1
c3266898
30,238
omim
https://www.omim.org/entry/193500
2019-09-22T16:31:57
{"doid": ["0110948"], "mesh": ["D014849"], "omim": ["193500"], "orphanet": ["3440", "894"], "synonyms": ["Alternative titles", "WAARDENBURG SYNDROME WITH DYSTOPIA CANTHORUM"], "genereviews": ["NBK1531"]}
A number sign (#) is used with this entry because of evidence that susceptibility to acute infection-induced (herpes-specific) encephalopathy-7 (IIAE7) is caused by heterozygous mutation in the IRF3 gene (603734) on chromosome 19q13. For a phenotypic description of herpes simplex encephalitis (HSE) and a discussion ...
ENCEPHALOPATHY, ACUTE, INFECTION-INDUCED (HERPES-SPECIFIC), SUSCEPTIBILITY TO, 7
c0276226
30,239
omim
https://www.omim.org/entry/616532
2019-09-22T15:48:37
{"mesh": ["D020803"], "omim": ["616532"], "orphanet": ["1930"], "synonyms": ["Alternative titles", "HERPES SIMPLEX ENCEPHALITIS, SUSCEPTIBILITY TO, 5"]}
Spinocerebellar ataxia type 41 is a rare autosomal dominant cerebellar ataxia type III disorder characterized by adult-onset progressive imbalance and loss of coordination associated with an ataxic gait. Mild atrophy of the cerebellar vermis has been reported on brain magnetic resonance imaging. *[v]: View this te...
Spinocerebellar ataxia type 41
c4225158
30,240
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=458798
2021-01-23T17:28:46
{"omim": ["616410"], "icd-10": ["G11.2"], "synonyms": ["SCA41"]}
Fragile X-associated tremor/ataxia syndrome (FXTAS) is characterized by problems with movement and thinking ability (cognition). FXTAS is a late-onset disorder, usually occurring after age 50, and its signs and symptoms worsen with age. This condition affects males more frequently and severely than females. Affected ...
Fragile X-associated tremor/ataxia syndrome
c1839780
30,241
medlineplus
https://medlineplus.gov/genetics/condition/fragile-x-associated-tremor-ataxia-syndrome/
2021-01-27T08:24:46
{"mesh": ["C564105"], "omim": ["300623"], "synonyms": []}
Kapur-Toriello syndrome is an extremely rare syndrome characterized by facial dysmorphism, severe intellectual deficiency, cardiac and intestinal anomalies, and growth retardation. ## Epidemiology Only four cases have been reported in the literature, in three unrelated families. ## Clinical description Dysmorphic...
Kapur-Toriello syndrome
c0796005
30,242
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2328
2021-01-23T18:38:08
{"gard": ["3078"], "mesh": ["C537008"], "omim": ["244300"], "umls": ["C0796005"], "icd-10": ["Q87.8"], "synonyms": ["Cleft lip/palate-facial, eye, heart and intestinal anomalies syndrome"]}
This article includes a list of general references, but it remains largely unverified because it lacks sufficient corresponding inline citations. Please help to improve this article by introducing more precise citations. (June 2019) (Learn how and when to remove this template message) This article is an orphan, ...
HIDEA syndrome
None
30,243
wikipedia
https://en.wikipedia.org/wiki/HIDEA_syndrome
2021-01-18T18:51:39
{"umls": ["CL1371252"], "wikidata": ["Q65063382"]}
Mouth and genital ulcers with inflamed cartilage syndrome Other namesMAGIC syndrome SpecialtyDermatology Mouth and genital ulcers with inflamed cartilage syndrome (also known as "MAGIC syndrome") is a cutaneous condition with features of both Behçet's disease and relapsing polychondritis.[1][2] Recently ...
Mouth and genital ulcers with inflamed cartilage syndrome
c0406568
30,244
wikipedia
https://en.wikipedia.org/wiki/Mouth_and_genital_ulcers_with_inflamed_cartilage_syndrome
2021-01-18T18:34:10
{"gard": ["13371"], "orphanet": ["324972"], "synonyms": ["Mouth and genital ulcers-inflamed cartilage syndrome"], "wikidata": ["Q16937724"]}
A number sign (#) is used with this entry because cystic leukoencephalopathy without megalencephaly is caused by homozygous or compound heterozygous mutation in the RNASET2 gene (612944) on chromosome 6q27. Cystic leukoencephalopathy with megalencephaly (604004) is a clinically and genetically distinct disorder....
LEUKOENCEPHALOPATHY, CYSTIC, WITHOUT MEGALENCEPHALY
c2751843
30,245
omim
https://www.omim.org/entry/612951
2019-09-22T16:00:12
{"mesh": ["C567845"], "omim": ["612951"], "orphanet": ["85136"]}
Connective tissue nevus Other namesCollagenoma, Elastoma, and Shagreen patch[1] Storiform collagenoma, H&E stain SpecialtyDermatology A connective tissue nevus may be present at birth or appear within the first few years, is elevated, soft to firm, varying from 0.5 to several centimeters in diameter, and m...
Connective tissue nevus
c0334083
30,246
wikipedia
https://en.wikipedia.org/wiki/Connective_tissue_nevus
2021-01-18T18:31:53
{"mesh": ["C562737"], "umls": ["C0334083", "C0265978"], "wikidata": ["Q5161704"]}
A number sign (#) is used with this entry because of evidence that type I xanthinuria (XAN1) is caused by homozygous or compound heterozygous mutation in the gene encoding xanthine dehydrogenase (XDH; 607633) on chromosome 2p23. Description Xanthinuria, which was first described by Dent and Philpot (1954), is c...
XANTHINURIA, TYPE I
c0268118
30,247
omim
https://www.omim.org/entry/278300
2019-09-22T16:21:09
{"doid": ["0060236"], "mesh": ["C562584"], "omim": ["278300"], "orphanet": ["3467", "93601"], "synonyms": ["Xanthic urolithiasis", "XANTHINE DEHYDROGENASE DEFICIENCY", "Alternative titles", "Xanthine stone disease", "Classic xanthinuria", "XDH DEFICIENCY", "XANTHINE OXIDASE DEFICIENCY"]}
Kamm et al. (1991) described a family in which at least 1 member in each of 5 successive generations had severe proctalgia fugax beginning in the third to fifth decades of life. They studied in detail 3 members of the family demonstrating a 'new' myopathy of the internal anal sphincter. Each affected member had sever...
ANAL SPHINCTER MYOPATHY, INTERNAL
c1862935
30,248
omim
https://www.omim.org/entry/105565
2019-09-22T16:45:12
{"mesh": ["C566287"], "omim": ["105565"], "synonyms": ["Alternative titles", "PROCTALGIA FUGAX DUE TO ANAL SPHINCTER MYOPATHY"]}
A number sign (#) is used with this entry because of evidence that Pelger-Huet anomaly with mild skeletal anomalies (PHASK) is caused by homozygous or compound heterozygous mutation in the LBR gene (600024) on chromosome 1q42. Homozygous mutation in the LBR gene can also cause Greenberg dysplasia (215140), a lethal ...
PELGER-HUET ANOMALY WITH MILD SKELETAL ANOMALIES
None
30,249
omim
https://www.omim.org/entry/618019
2019-09-22T15:43:54
{"omim": ["618019"], "orphanet": ["448267"], "synonyms": ["Alternative titles", "REGRESSIVE SPONDYLOMETAPHYSEAL DYSPLASIA"]}
## Clinical Features Swanson and Brown (1962) described a family in which 30 persons in 5 generations had 5 triphalangeal digits of each hand and apparently lacked a true thumb. The 'thumb' could not be opposed. No associated internal malformations were detected. Triphalangeal thumb of this type occurs in some case...
TRIPHALANGEAL THUMB, NONOPPOSABLE
c2931238
30,250
omim
https://www.omim.org/entry/190600
2019-09-22T16:32:16
{"mesh": ["C536562"], "omim": ["190600"]}
A number sign (#) is used with this entry because of evidence that a skeletal malformation with features overlapping those of brachydactyly types E and D (BDD; 113200) is caused by heterozygous mutation in the HOXD13 gene (142989) on chromosome 2q31. Another form of brachydactyly type E, BDE2 (613382), is caused by ...
BRACHYDACTYLY, TYPE E1
c0265312
30,251
omim
https://www.omim.org/entry/113300
2019-09-22T16:44:08
{"doid": ["0110972"], "omim": ["113300"], "orphanet": ["93387"], "synonyms": ["Alternative titles", "BRACHYDACTYLY, TYPE E"]}
Papular mucinosis of infancy Other namesCutaneous mucinosis of infancy SpecialtyDermatology Papular mucinosis of infancy is a skin condition caused by fibroblasts producing abnormally large amounts of mucopolysaccharides, characterized by skin-colored or translucent papules.[1]:186[2] ## See also[edit] *...
Papular mucinosis of infancy
c4273966
30,252
wikipedia
https://en.wikipedia.org/wiki/Papular_mucinosis_of_infancy
2021-01-18T18:29:03
{"orphanet": ["90395"], "synonyms": ["Cutaneous mucinosis of infancy"], "wikidata": ["Q7133225"]}
Hydroxyprolinemia is an inherited metabolic condition characterized by elevated levels of the amino acid hydroxyproline in the blood and urine. This condition usually does not cause physical or cognitive abnormalities. Hydroxyprolinemia was initially described in association with intellectual disabilities; howeve...
Hydroxyprolinemia
c0268531
30,253
gard
https://rarediseases.info.nih.gov/diseases/10717/hydroxyprolinemia
2021-01-18T17:59:56
{"mesh": ["C562669"], "omim": ["237000"], "umls": ["C0268531"], "synonyms": ["4-hydroxy-L-proline oxidase deficiency", "4 alpha hydroxy-L-proline oxidase deficiency"]}
A number sign (#) is used with this entry because of evidence that ventricular septal defect-3 (VSD3) is caused by heterozygous mutation in the NKX2-5 gene (600584) on chromosome 5q35. Description Ventricular septal defect (VSD) is the most common form of congenital cardiovascular anomaly, occurring in nearly 50% o...
VENTRICULAR SEPTAL DEFECT 3
c3280785
30,254
omim
https://www.omim.org/entry/614432
2019-09-22T15:55:19
{"omim": ["614432"]}
A rare neurologic biological anomaly characterized by persistent elevation of the serum creatine phosphokinase (CK) without any clinical, neurophysical or histopathological evidence of neuromuscular disease using the available laboratory procedures. It is usually an incidental finding, diagnosed after exclusion of ot...
Isolated asymptomatic elevation of creatine phosphokinase
None
30,255
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=206599
2021-01-23T18:25:20
{"synonyms": ["Idiopathic asymptomatic hyperCKemia", "Isolated asymptomatic hyperCKemia"]}
This article is an orphan, as no other articles link to it. Please introduce links to this page from related articles; try the Find link tool for suggestions. (April 2014) Ametropic amblyopia Human eye anatomy(retina) SpecialtyNeurology Ametropic amblyopia, is a medical condition in which the retina can...
Ametropic amblyopia
c0152190
30,256
wikipedia
https://en.wikipedia.org/wiki/Ametropic_amblyopia
2021-01-18T18:46:28
{"umls": ["C0152190"], "wikidata": ["Q16002876"]}
A number sign (#) is used with this entry because of evidence that Charcot-Marie-Tooth disease type 2W (CMT2W) is caused by heterozygous mutation in the HARS gene (HARS1; 142810) on chromosome 5q31. Description Charcot-Marie-Tooth disease type 2W is an autosomal dominant neurologic disorder characterized by a p...
CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2W
c4225265
30,257
omim
https://www.omim.org/entry/616625
2019-09-22T15:48:23
{"doid": ["0110162"], "omim": ["616625"], "orphanet": ["488333"], "synonyms": ["CHARCOT-MARIE-TOOTH NEUROPATHY, TYPE 2W", "Autosomal dominant Charcot-Marie-Tooth disease type 2 due to HARS mutation", "CMT2W", "Alternative titles", "CHARCOT-MARIE-TOOTH DISEASE, AXONAL, AUTOSOMAL DOMINANT, TYPE 2W"]}
## Description PHACE is an acronym for a neurocutaneous syndrome encompassing the following features: posterior fossa brain malformations, hemangiomas of the face (large or complex), arterial anomalies, cardiac anomalies, and eye abnormalities. The association is referred to as PHACES when ventral developmental def...
PHACE ASSOCIATION
c1847874
30,258
omim
https://www.omim.org/entry/606519
2019-09-22T16:10:22
{"mesh": ["C537892"], "omim": ["606519"], "orphanet": ["42775"], "synonyms": ["Alternative titles", "PHACES ASSOCIATION", "AORTIC ANEURYSM, GIANT CONGENITAL"]}
A number sign (#) is used with this entry because of evidence that spastic paraplegia, intellectual disability, nystagmus, and obesity (SINO) is caused by heterozygous mutation in the KIDINS220 gene (615759) on chromosome 2p25. Description Spastic paraplegia, intellectual disability, nystagmus, and obesity (SINO) i...
SPASTIC PARAPLEGIA, INTELLECTUAL DISABILITY, NYSTAGMUS, AND OBESITY
c4284592
30,259
omim
https://www.omim.org/entry/617296
2019-09-22T15:46:10
{"omim": ["617296"], "orphanet": ["521390"], "synonyms": ["SINO syndrome"]}
A number sign (#) is used with this entry because of evidence that central core disease (CCD) and its variants can be caused by heterozygous, homozygous, or compound heterozygous mutation in the ryanodine receptor-1 gene (RYR1; 180901) on chromosome 19q13. Biallelic mutation in the RYR1 gene can also cause minicore ...
CENTRAL CORE DISEASE OF MUSCLE
c0751951
30,260
omim
https://www.omim.org/entry/117000
2019-09-22T16:43:33
{"doid": ["3529"], "mesh": ["D020512"], "omim": ["117000"], "icd-10": ["G71.2"], "orphanet": ["597", "598", "178145"], "synonyms": ["Alternative titles", "CCO"], "genereviews": ["NBK1391"]}
## Description Astigmatism (from the Greek 'a' meaning absence and 'stigma' meaning point) is a condition in which the parallel rays of light entering the eye through the refractive media are not focused on a single point. Both corneal and noncorneal factors contribute to refractive astigmatism. Corneal astigmatism...
ASTIGMATISM
c0004106
30,261
omim
https://www.omim.org/entry/603047
2019-09-22T16:13:20
{"doid": ["11782"], "mesh": ["D001251"], "omim": ["603047"], "icd-9": ["367.2", "367.20"], "icd-10": ["H52.2", "H52.20"]}
Disease affecting a small percentage of the population A rare disease is any disease that affects a small percentage of the population. In some parts of the world, an orphan disease is a rare disease whose rarity means there is a lack of a market large enough to gain support and resources for discovering treatments ...
Rare disease
c0678236
30,262
wikipedia
https://en.wikipedia.org/wiki/Rare_disease
2021-01-18T18:54:47
{"mesh": ["D035583"], "umls": ["C0678236"], "orphanet": ["377794"], "wikidata": ["Q929833"]}
Cloacal exstrophy Other namesOmphalocele-cloacal exstrophy-imperforate anus-spinal defect syndrome SpecialtyMedical genetics Complicationslimb deformities, open neural tube defects [1] TreatmentSurgical intervention Cloacal exstrophy (EC) is a severe birth defect wherein much of the abdominal organs ...
Cloacal exstrophy
c0345217
30,263
wikipedia
https://en.wikipedia.org/wiki/Cloacal_exstrophy
2021-01-18T18:43:03
{"orphanet": ["93929"], "wikidata": ["Q5134736"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Neu–Laxova syndrome" – news · newspapers · books · scholar · JSTOR (December 2018) (Learn how and when to remove th...
Neu–Laxova syndrome
c0265218
30,264
wikipedia
https://en.wikipedia.org/wiki/Neu%E2%80%93Laxova_syndrome
2021-01-18T18:40:10
{"gard": ["102"], "mesh": ["C536405"], "umls": ["C0265218"], "orphanet": ["2671"], "wikidata": ["Q667681"]}
## Summary ### Clinical characteristics. Most infants with short-chain acyl-CoA dehydrogenase deficiency (SCADD) identified through newborn screening programs have remained well, and asymptomatic relatives who meet diagnostic criteria are reported. Thus, SCADD is now viewed as a biochemical phenotype rather tha...
Short-Chain Acyl-CoA Dehydrogenase Deficiency
c0342783
30,265
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK63582/
2021-01-18T20:57:08
{"mesh": ["C537596"], "synonyms": ["SCADD", "SCAD Deficiency"]}
Trochleitis is the swelling of structures in the eye that help control eye movement, specifically the oblique tendon and surrounding tissues. Trochleitis may be isolated (occur alone or with migraine) or develop in association with an inflammatory condition, such as lupus or arthritis. Signs and symptoms include achi...
Trochleitis
None
30,266
gard
https://rarediseases.info.nih.gov/diseases/12113/trochleitis
2021-01-18T17:57:16
{"synonyms": ["trochleodynia"]}
Immunodeficiency due to CD25 deficiency is a rare, genetic, primary immunodeficiency due to a defect in adaptive immunity disorder characterized by severe immunodeficiency, presenting with profound susceptibility to viral, fungal and bacterial infections due to impaired CD25-mediated T-regulatory cell function, in as...
Immunodeficiency due to CD25 deficiency
c1853392
30,267
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=169100
2021-01-23T17:59:13
{"mesh": ["C565232"], "omim": ["606367"], "icd-10": ["D81.2"], "synonyms": ["Interleukin-2 receptor alpha chain deficiency"]}
## Summary ### Clinical characteristics. Optic atrophy type 1 (OPA1, or Kjer type optic atrophy) is characterized by bilateral and symmetric optic nerve pallor associated with insidious decrease in visual acuity (usually between ages 4 and 6 years), visual field defects, and color vision defects. Visual impairment ...
Optic Atrophy Type 1
c0338508
30,268
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1248/
2021-01-18T21:06:33
{"mesh": ["D029241"], "synonyms": []}
A number sign (#) is used with this entry because this form of limb-girdle muscular dystrophy-dystroglycanopathy (type C7; MDDGC7), also known as LGMDR20 and LGMD2U, is caused by homozygous mutation in the ISPD gene (614631) on chromosome 7p21. ISPD encodes an isoprenoid synthase domain-containing protein. Mutation ...
MUSCULAR DYSTROPHY-DYSTROGLYCANOPATHY (LIMB-GIRDLE), TYPE C, 7
c4015095
30,269
omim
https://www.omim.org/entry/616052
2019-09-22T15:50:02
{"doid": ["0110295"], "omim": ["616052"], "orphanet": ["352479"], "synonyms": ["LGMD2U", "Alternative titles", "MUSCULAR DYSTROPHY, LIMB-GIRDLE, AUTOSOMAL RECESSIVE 20", "MUSCULAR DYSTROPHY, LIMB-GIRDLE, TYPE 2U", "Autosomal recessive limb-girdle muscular dystrophy due to ISPD deficiency"]}
Necrotising hepatopancreatitis (NHP), is also known as Texas necrotizing hepatopancreatitis (TNHP), Texas Pond Mortality Syndrome (TPMS) and Peru necrotizing hepatopancreatitis (PNHP),[1] is a lethal epizootic disease of farmed shrimp. It is not very well researched yet, but generally assumed to be caused by a bacter...
Necrotising hepatopancreatitis
None
30,270
wikipedia
https://en.wikipedia.org/wiki/Necrotising_hepatopancreatitis
2021-01-18T18:57:15
{"wikidata": ["Q3144984"]}
A number sign (#) is used with this entry because of evidence that Abruzzo-Erickson syndrome (ABERS) is caused by mutation in the TBX22 gene (300307) on chromosome Xq21. One such family has been reported. Clinical Features Abruzzo and Erickson (1977) reported an apparently 'new' syndrome of cleft palate, colobo...
ABRUZZO-ERICKSON SYNDROME
c1844862
30,271
omim
https://www.omim.org/entry/302905
2019-09-22T16:18:41
{"mesh": ["C535559"], "omim": ["302905"], "orphanet": ["921"], "synonyms": ["Alternative titles", "CHARGE-LIKE SYNDROME, X-LINKED"]}
A number sign (#) is used with this entry because it represents a contiguous gene syndrome caused by deletion of chromosome 17p13.1 Clinical Features Krepischi-Santos et al. (2009) reported a girl from the United Kingdom and 3 Brazilian boys, who were each found to have a microdeletion within or spanning chromosome...
CHROMOSOME 17p13.1 DELETION SYNDROME
c3151069
30,272
omim
https://www.omim.org/entry/613776
2019-09-22T15:57:33
{"omim": ["613776"]}
Tuberculous cellulitis SpecialtyDermatology Tuberculous cellulitis is a skin condition resulting from infection with mycobacterium, and presenting as cellulitis.[1]:336 ## See also[edit] * Lupus vulgaris * Metastatic tuberculous abscess or ulceration * Miliary tuberculosis * Skin lesion ## Reference...
Tuberculous cellulitis
None
30,273
wikipedia
https://en.wikipedia.org/wiki/Tuberculous_cellulitis
2021-01-18T19:03:26
{"wikidata": ["Q7850851"]}
A rare, inherited disorder characterized by widespread calcifications of basal ganglia and cortex, developmental delay, small stature, retinopathy and microcephaly. The absence of progressive deterioration of the neurological functions is characteristic of the disease. ## Epidemiology The syndrome has been desc...
Brain calcification, Rajab type
c3150910
30,274
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=178506
2021-01-23T18:37:25
{"omim": ["613658"]}
Osteoma Osteoma of external auditory meatus SpecialtyOncology An osteoma (plural: "osteomata") is a new piece of bone usually growing on another piece of bone, typically the skull. It is a benign tumor. When the bone tumor grows on other bone it is known as "homoplastic osteoma"; when it grows on other tiss...
Osteoma
c0029440
30,275
wikipedia
https://en.wikipedia.org/wiki/Osteoma
2021-01-18T19:10:01
{"mesh": ["D010016"], "umls": ["C0029440"], "icd-9": ["213.0"], "icd-10": ["C40"], "wikidata": ["Q1675957"]}
Batten (1910) and later Turner (1949) and Turner and Lees (1962) provided 50 years' observations on a family in which 6 sibs presented in infancy the picture of 'amyotonia congenita' and later in life a nonprogressive myopathy. The parents were not related. Muscle \- Congenital myopathy Neuro \- Amyotonia con...
MYOPATHY, CONGENITAL
c0027127
30,276
omim
https://www.omim.org/entry/255300
2019-09-22T16:24:33
{"doid": ["0080100"], "mesh": ["D009224"], "omim": ["255300"], "icd-9": ["359.22"], "synonyms": ["Alternative titles", "BATTEN-TURNER CONGENITAL MYOPATHY"]}
Vesicopustular dermatosis SpecialtyDermatology Vesicopustular dermatosis is a cutaneous condition characterized by neutrophils, and associated with bowel disorders.[1] ## See also[edit] * Pyostomatitis vegetans * List of cutaneous conditions ## References[edit] 1. ^ Rapini, Ronald P.; Bolognia, Jean ...
Vesicopustular dermatosis
None
30,277
wikipedia
https://en.wikipedia.org/wiki/Vesicopustular_dermatosis
2021-01-18T18:34:52
{"wikidata": ["Q7923219"]}
Steatocystoma simplex Other namesSimple sebaceous duct cyst, solitary steatocystoma Micrograph of a steatocystoma showing the characteristic corrugated eosinophilic lining. H&E stain SpecialtyDermatology Relative incidence of cutaneous cysts. Steatocystoma is labeled at right. Steatocystoma simplex is...
Steatocystoma simplex
c1997005
30,278
wikipedia
https://en.wikipedia.org/wiki/Steatocystoma_simplex
2021-01-18T18:31:26
{"wikidata": ["Q7605540"]}
A number sign (#) is used with this entry because autosomal dominant erythrocytosis-6 (ECYT6) can be caused by heterozygous mutation in the beta globin gene (HBB; 141900) that results in a high oxygen affinity hemoglobin. Description Familial erythrocytosis-6 is characterized by an increased oxygen affinity of ...
ERYTHROCYTOSIS, FAMILIAL, 6
c4693822
30,279
omim
https://www.omim.org/entry/617980
2019-09-22T15:44:09
{"omim": ["617980"], "synonyms": ["Alternative titles", "ERYTHROCYTOSIS, BETA-GLOBIN TYPE", "POLYCYTHEMIA, BETA-GLOBIN TYPE"]}
Mental suffering among settlers of the North American plains. Great Plains of Nebraska Prairie madness or prairie fever was an affliction that affected settlers in the Great Plains during the migration to, and settlement of, the Canadian Prairies and the Western United States in the nineteenth century. Settlers mov...
Prairie madness
None
30,280
wikipedia
https://en.wikipedia.org/wiki/Prairie_madness
2021-01-18T18:44:57
{"wikidata": ["Q7238040"]}
CASK-related disorders are a group of genetic disorders that affect brain development. The two main related disorders include microcephaly with pontine and cerebellar hypoplasia (MICPCH) and X-linked intellectual disability (XL-ID) with or without nystagmus. Males with these disorders usually have more severe symptom...
CASK-Related Disorders
c2677903
30,281
gard
https://rarediseases.info.nih.gov/diseases/12670/cask-related-disorders
2021-01-18T18:01:36
{"mesh": ["C567466"], "omim": ["300749", "300422"], "synonyms": []}
A number sign (#) is used with this entry because of evidence that Coffin-Siris syndrome-3 (CSS3) is caused by heterozygous mutation in the SMARCB1 gene (601607) on chromosome 22q11. The SMARCB1 gene is one of several genes encoding subunits of the SWI/SNF complex, also known as the BAF complex, which functions as a ...
COFFIN-SIRIS SYNDROME 3
c0265338
30,282
omim
https://www.omim.org/entry/614608
2019-09-22T15:54:48
{"doid": ["0070045"], "mesh": ["C536436"], "omim": ["614608"], "orphanet": ["1465"], "synonyms": ["Alternative titles", "MENTAL RETARDATION, AUTOSOMAL DOMINANT 15"]}
Triphalangeal thumbs-brachyectrodactyly syndrome is characterised by triphalangeal thumbs and brachydactyly of the hands. It has been described in four families and in one isolated case. Ectrodactyly of the feet and, more rarely, ectrodactyly of the hands were also reported in some family members. Transmission is aut...
Triphalangeal thumbs-brachyectrodactyly syndrome
c1860804
30,283
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2947
2021-01-23T18:49:29
{"gard": ["5290"], "mesh": ["C536564"], "omim": ["190680"], "umls": ["C1860804"], "icd-10": ["Q74.8"], "synonyms": ["Carnevale-Hernández-del Castillo syndrome"]}
Syndrome characterised by eye, central nervous system and skin malformations Oculocerebrocutaneous syndrome Other namesDelleman–Oorthuys syndrome[1] Oculocerebrocutaneous syndrome is a condition characterized by orbital cysts, microphthalmia, porencephaly, agenesis of the corpus callosum, and facial skin tags...
Oculocerebrocutaneous syndrome
c0796092
30,284
wikipedia
https://en.wikipedia.org/wiki/Oculocerebrocutaneous_syndrome
2021-01-18T18:38:42
{"gard": ["106"], "mesh": ["C538088"], "umls": ["C0796092"], "orphanet": ["1647"], "wikidata": ["Q7077152"]}
A number sign (#) is used with this entry because of evidence that autosomal recessive spinocerebellar ataxia-7 (SCAR7) is caused by compound heterozygous mutation in the TPP1 gene (607998) on chromosome 11p15. Biallelic mutation in the TPP1 gene can also cause neuronal ceroid lipofuscinosis-2 (CLN2; 204500). D...
SPINOCEREBELLAR ATAXIA, AUTOSOMAL RECESSIVE 7
c1836474
30,285
omim
https://www.omim.org/entry/609270
2019-09-22T16:06:20
{"doid": ["0080059"], "mesh": ["C563753"], "omim": ["609270"], "orphanet": ["284324"]}
This article does not deal with the more general topic of childhood arthritis. Juvenile idiopathic arthritis Other namesJuvenile rheumatoid arthritis SpecialtyRheumatology Frequency1 in 1,000[1] Juvenile idiopathic arthritis (JIA), is the most common, chronic rheumatic disease of childhood, affecting appr...
Juvenile idiopathic arthritis
c0157917
30,286
wikipedia
https://en.wikipedia.org/wiki/Juvenile_idiopathic_arthritis
2021-01-18T18:46:13
{"gard": ["3067"], "umls": ["C0157916", "C0157918", "C0409667", "C0157917"], "orphanet": ["92"], "wikidata": ["Q861224"]}
Foodborne botulism is the most common form of botulism (see this term), a rare acquired neuromuscular junction disease with descending flaccid paralysis due to botulinum neurotoxins (BoNTs). It is caused by consumption of contaminated food containing BoNTs. ## Epidemiology Prevalence is unknown. The annual inci...
Foodborne botulism
c1739094
30,287
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=228371
2021-01-23T18:11:15
{"mesh": ["D001906"], "umls": ["C1739094"], "icd-10": ["A05.1"], "synonyms": ["Intoxication botulism"]}
A number sign (#) is used with this entry because of evidence that Pelger-Huet anomaly (PHA) can be caused by heterozygous mutation in the gene encoding the lamin B receptor (LBR; 600024) on chromosome 1q42. Homozygous mutation in the LBR gene can cause PHA with mild skeletal anomalies (PHASK; 618019) or Greenberg d...
PELGER-HUET ANOMALY
c0030779
30,288
omim
https://www.omim.org/entry/169400
2019-09-22T16:36:30
{"doid": ["9631"], "mesh": ["D010381"], "omim": ["169400"]}
This article has multiple issues. Please help improve it or discuss these issues on the talk page. (Learn how and when to remove these template messages) This article needs more medical references for verification or relies too heavily on primary sources. Please review the contents of the article and add the appropr...
Digital phobic
None
30,289
wikipedia
https://en.wikipedia.org/wiki/Digital_phobic
2021-01-18T19:10:34
{"wikidata": ["Q18206542"]}
A number sign (#) is used with this entry because of evidence that retinitis pigmentosa and erythrocytic microcytosis (RPEM) is caused by compound heterozygous mutation in the TRNT1 gene (612907) on chromosome 3p26. Mutation in the TRNT1 gene also causes a more severe syndrome, consisting of sideroblastic anemia wit...
RETINITIS PIGMENTOSA AND ERYTHROCYTIC MICROCYTOSIS
c4310776
30,290
omim
https://www.omim.org/entry/616959
2019-09-22T15:47:26
{"omim": ["616959"]}
Langer mesomelic dysplasia is a disorder of bone growth. Affected individuals typically have extreme shortening of the long bones in the arms and legs (mesomelia). As a result of the shortened leg bones, people with Langer mesomelic dysplasia have very short stature. A bone in the forearm called the ulna and a bone i...
Langer mesomelic dysplasia
c0432230
30,291
medlineplus
https://medlineplus.gov/genetics/condition/langer-mesomelic-dysplasia/
2021-01-27T08:25:09
{"gard": ["3553"], "mesh": ["C537267"], "omim": ["249700"], "synonyms": []}
A number sign (#) is used with this entry because of evidence that multiple self-healing palmoplantar carcinoma (MSPC) is caused by heterozygous mutation in the NLRP1 gene (606636) on chromosome 17p13. Description Multiple self-healing palmoplantar carcinoma (MSPC) is characterized by recurrent keratoacanthomas in ...
PALMOPLANTAR CARCINOMA, MULTIPLE SELF-HEALING
c3808876
30,292
omim
https://www.omim.org/entry/615225
2019-09-22T15:52:58
{"omim": ["615225"], "orphanet": ["352662"], "synonyms": ["Alternative titles", "CORNEAL INTRAEPITHELIAL DYSKERATOSIS AND ECTODERMAL DYSPLASIA, FORMERLY"]}
Abortion in Chad was prohibited by law prior to December 2016, when the National Assembly of Chad passed an updated penal code decriminalising abortion under limited circumstances. Article 358 of that codestates that abortion is allowed in case of sexual assault, rape, incest or when the pregnancy endangers the menta...
Abortion in Chad
None
30,293
wikipedia
https://en.wikipedia.org/wiki/Abortion_in_Chad
2021-01-18T18:45:59
{"wikidata": ["Q42417647"]}
Acute coronary syndrome Blockage of a coronary artery SpecialtyCardiology Acute coronary syndrome (ACS) is a syndrome (set of signs and symptoms) due to decreased blood flow in the coronary arteries such that part of the heart muscle is unable to function properly or dies.[1] The most common symptom is c...
Acute coronary syndrome
c0948089
30,294
wikipedia
https://en.wikipedia.org/wiki/Acute_coronary_syndrome
2021-01-18T18:28:02
{"mesh": ["D054058"], "umls": ["C0948089"], "icd-10": ["I20.0"], "wikidata": ["Q266018"]}
Long-term symptoms and/or sequelae of COVID-19 Part of a series on the COVID-19 pandemic * SARS-CoV-2 (virus) * COVID-19 (disease) Timeline 2019 2020 * January * February * responses * March * responses * April * responses * May * responses * June * response...
Long COVID
None
30,295
wikipedia
https://en.wikipedia.org/wiki/Long_COVID
2021-01-18T18:51:55
{"wikidata": ["Q100732653"]}
A form of oculocutaneous albinism (OCA) characterized by skin and hair hypopigmentation (light blond to dark brown), nystagmus, iris transillumination, visual acuity ranging from 6/9 to 3/60 and hypopigmentation of the peripheral ocular fundus. Photophobia is not a major feature. *[v]: View this template *[t]: D...
Oculocutaneous albinism type 7
c3808786
30,296
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=352745
2021-01-23T18:27:50
{"omim": ["615179"], "icd-10": ["E70.3"], "synonyms": ["OCA7"]}
## Clinical Features Van Steensel et al. (2001) described a 4-generation Dutch kindred with 27 individuals, 14 of whom were affected in a pattern that was consistent with autosomal dominant inheritance. The proposita was evaluated at 35 years of age and presented with unruly, brittle hair with premature hair loss, ...
CURLY HAIR-ACRAL KERATODERMA-CARIES SYNDROME
c1843291
30,297
omim
https://www.omim.org/entry/607656
2019-09-22T16:08:57
{"mesh": ["C536220"], "omim": ["607656"], "orphanet": ["307766"], "synonyms": ["Alternative titles", "CHACS"]}
A rare genetic multiple congenital anomalies/dysmorphic syndrome characterized by global developmental delay, intellectual disability, and dysmorphic facial features (such as facial asymmetry, prominent forehead, short palpebral fissures, low nasal bridge, smooth and long philtrum, thin upper lip, and low-set, poster...
X-linked female restricted facial dysmorphism-short stature-choanal atresia-intellectual disability
c4225416
30,298
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=480880
2021-01-23T19:11:45
{"omim": ["300968"], "synonyms": ["X-linked facial dysmorphism-short stature-choanal atresia-intellectual disability syndrome limited to females"]}
A number sign (#) is used with this entry because of evidence that hyperekplexia-2 (HKPX2) is caused by compound heterozygous or homozygous mutation in the GLRB gene (138492) on chromosome 4q32. For a general phenotypic description and a discussion of genetic heterogeneity of hyperekplexia, see HKPX1 (149400). Clin...
HYPEREKPLEXIA 2
c1835614
30,299
omim
https://www.omim.org/entry/614619
2019-09-22T15:54:48
{"doid": ["0060697"], "mesh": ["C538136"], "omim": ["614619"], "orphanet": ["3197"], "genereviews": ["NBK1260"]}