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A number sign (#) is used with this entry because of evidence that normophosphatemic familial tumoral calcinosis can be caused by mutation in the gene encoding the sterile alpha motif domain-containing-9 protein (SAMD9; 610456). Clinical Features Familial tumoral calcinosis (FTC) is an uncommon life-threatening...
TUMORAL CALCINOSIS, NORMOPHOSPHATEMIC, FAMILIAL
c1864861
5,800
omim
https://www.omim.org/entry/610455
2019-09-22T16:04:29
{"doid": ["0080170"], "mesh": ["C566473"], "omim": ["610455"], "orphanet": ["306658", "53715"], "synonyms": ["Alternative titles", "CALCINOSIS, TUMORAL, WITH NORMOPHOSPHATEMIA"]}
Chromosome 16p13.3 deletion syndrome is a chromosome abnormality that can affect many parts of the body. People with this condition are missing a small piece (deletion) of chromosome 16 at a location designated p13.3. Although once thought to be a severe form of Rubinstein-Taybi syndrome, it is now emerging as a uniq...
Chromosome 16p13.3 deletion syndrome
c1864648
5,801
gard
https://rarediseases.info.nih.gov/diseases/10754/chromosome-16p133-deletion-syndrome
2021-01-18T18:01:25
{"omim": ["610543"], "synonyms": ["16p13.3 deletion syndrome"]}
A rare, genetic, syndromic intellectual disability characterized by psychomotor delay, hypotonia, feeding difficulties, failure to thrive, anomalies of the hands and feet (clinodactyly, camptodactyly, brachydactyly, feet malposition), and craniofacial dysmorphism. Associated prenatal growth retardation, and gastroint...
20q11.2 microdeletion syndrome
None
5,802
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=444051
2021-01-23T19:09:59
{"icd-10": ["Q93.5"], "synonyms": ["Del(20)(q11.2)", "Monosomy 20q11"]}
A number sign (#) is used with this entry because Hermansky-Pudlak syndrome-1 (HPS1) is caused by homozygous or compound heterozygous mutation in the HPS1 gene (604982) on chromosome 10q24. Description Hermansky-Pudlak syndrome (HPS) is a rare autosomal recessive disorder in which oculocutaneous albinism, bleeding,...
HERMANSKY-PUDLAK SYNDROME 1
c0079504
5,803
omim
https://www.omim.org/entry/203300
2019-09-22T16:31:25
{"doid": ["0060539"], "mesh": ["D022861"], "omim": ["203300"], "orphanet": ["79430", "231500"], "synonyms": ["Alternative titles", "ALBINISM WITH HEMORRHAGIC DIATHESIS AND PIGMENTED RETICULOENDOTHELIAL CELLS", "DELTA STORAGE POOL DISEASE"], "genereviews": ["NBK1287"]}
Alopecia totalis (AT) is a condition characterized by the complete loss of hair on the scalp. It is an advanced form of alopecia areata a condition that causes round patches of hair loss. Although the exact cause of AT is unknown, it is thought to be an autoimmune condition in which the immune system mistakenly attac...
Alopecia totalis
c0263504
5,804
gard
https://rarediseases.info.nih.gov/diseases/613/alopecia-totalis
2021-01-18T18:02:11
{"orphanet": ["700"], "synonyms": ["Loss of all scalp hair"]}
The rare combination of muscle weakness with electrical myotonia but without clinical myotonia has been reported in acid maltase deficiency and in centronuclear myopathy. Juguilon et al. (1982) described 3 adult patients with profound selective muscle wasting and weakness, electrical myotonia, and unusual findings on...
MYOPATHY, GRANULOVACUOLAR LOBULAR, WITH ELECTRICAL MYOTONIA
c1850745
5,805
omim
https://www.omim.org/entry/254950
2019-09-22T16:24:38
{"mesh": ["C564974"], "omim": ["254950"]}
Neuroendocrine tumor of the anal canal is an epithelial tumor of anal canal arising from enterochromaffin cells in the colorectal-type epithelium above the dentate line and in the anal transition zone. The tumors are slow growing and the majority of cases are diagnosed in later advanced stages. It may present with sy...
Neuroendocrine tumor of anal canal
None
5,806
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=100082
2021-01-23T18:14:17
{"synonyms": ["NET of anal canal"]}
Granulosa cell tumour Other namesGranulosa-theca cell tumours or Folliculoma Micrograph of a juvenile granulosa cell tumour with hyaline globules. H&E stain. SpecialtyGynecologic oncology, obstetrics and gynaecology, oncology, endocrinology Granulosa cell tumours are tumours that arise from granulosa cells...
Granulosa cell tumour
c0018206
5,807
wikipedia
https://en.wikipedia.org/wiki/Granulosa_cell_tumour
2021-01-18T18:57:00
{"mesh": ["D006106"], "umls": ["C0018206", "C0334401"], "icd-9": ["183", "236.2"], "icd-10": ["C56"], "wikidata": ["Q612093"]}
Neuroma cutis is a relatively rare type of neuroma, or tumor involving nervous tissue, in the skin.[1] There are three types of true neuromas of the skin and mucous membranes known to exist: traumatic neuromas, multiple mucosal neuromas, and solitary palisaded encapsulated neuromas.[2] ## See also[edit] * Ski...
Neuroma cutis
c0346057
5,808
wikipedia
https://en.wikipedia.org/wiki/Neuroma_cutis
2021-01-18T18:49:16
{"umls": ["C0346057"], "wikidata": ["Q16937037"]}
Part of a series on Psychology * Outline * History * Subfields Basic types * Abnormal * Behavioral genetics * Biological * Cognitive/Cognitivism * Comparative * Cross-cultural * Cultural * Differential * Developmental * Evolutionary * Experimental * Mathematical * Ne...
Cognitive disorder
c0029227
5,809
wikipedia
https://en.wikipedia.org/wiki/Cognitive_disorder
2021-01-18T18:47:05
{"mesh": ["D019965", "D003072"], "umls": ["C0029227"], "wikidata": ["Q3065932"]}
Psychomotor retardation Other namesPsychomotor impairment, motormental retardation, psychomotor slowing SpecialtyPsychiatry Psychomotor retardation involves a slowing-down of thought and a reduction of physical movements in an individual. Psychomotor retardation can cause a visible slowing of physical and em...
Psychomotor retardation
c0424230
5,810
wikipedia
https://en.wikipedia.org/wiki/Psychomotor_retardation
2021-01-18T18:44:52
{"icd-9": ["308.2"], "wikidata": ["Q3064951"]}
Very rare, incurable and fatal neurodegenerative disorder that was formerly common among the Fore people of Papua New Guinea. Kuru is a form of transmissible spongiform encephalopathy (TSE) Not to be confused with Koro (medicine). Kuru A Fore child with advanced kuru. He is unable to walk or sit upright witho...
Kuru (disease)
c0022802
5,811
wikipedia
https://en.wikipedia.org/wiki/Kuru_(disease)
2021-01-18T18:32:10
{"gard": ["7617"], "mesh": ["D007729"], "umls": ["C0022802"], "orphanet": ["454745"], "wikidata": ["Q274615"]}
## Clinical Features Neuhauser et al. (1977) described a brother and sister, with nonconsanguineous parents, who had severe mental retardation, spastic cerebral palsy, seizures, progressive or intermittent jaundice, and recurrent infections. They died at ages 3 and 4 years. One showed a small brain with almost ...
DYSMYELINATION WITH JAUNDICE
c1857143
5,812
omim
https://www.omim.org/entry/224250
2019-09-22T16:28:28
{"mesh": ["C565610"], "omim": ["224250"]}
Orofaciodigital syndromes refers to numerous conditions in which the oral cavity (mouth, tongue, teeth, and jaw), facial structures (head, eyes, and nose), and digits (fingers and toes) may be formed differently. When changes happen to many different parts of the body, this is called a syndrome. The literature report...
Orofaciodigital syndromes
c0029294
5,813
gard
https://rarediseases.info.nih.gov/diseases/10692/orofaciodigital-syndromes
2021-01-18T17:58:33
{"mesh": ["D009958"], "orphanet": ["140997"], "synonyms": ["Orofaciodigital syndrome", "Oral-facial-digital syndromes", "Oral facial digital syndromes", "OFD", "Oral-facial-digital syndrome"]}
A number sign (#) is used with this entry because of evidence that Charcot-Marie-Tooth type 2B1 (CMT2B1) is caused by homozygous mutation in the lamin A/C gene (LMNA; 150330) on chromosome 1q22. Description Charcot-Marie-Tooth disease constitutes a clinically and genetically heterogeneous group of hereditary motor ...
CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2B1
c1854154
5,814
omim
https://www.omim.org/entry/605588
2019-09-22T16:11:10
{"doid": ["0110156"], "mesh": ["C537990"], "omim": ["605588"], "orphanet": ["98856"], "synonyms": ["Alternative titles", "CHARCOT-MARIE-TOOTH DISEASE, NEURONAL, TYPE 2B1", "CHARCOT-MARIE-TOOTH DISEASE, AXONAL, AUTOSOMAL RECESSIVE, TYPE 2B1", "CHARCOT-MARIE-TOOTH NEUROPATHY, TYPE 2B1"]}
Frontometaphyseal dysplasia is a disorder involving abnormalities in skeletal development and other health problems. It is a member of a group of related conditions called otopalatodigital spectrum disorders, which also includes otopalatodigital syndrome type 1, otopalatodigital syndrome type 2, Melnick-Needles syndr...
Frontometaphyseal dysplasia
c4281559
5,815
medlineplus
https://medlineplus.gov/genetics/condition/frontometaphyseal-dysplasia/
2021-01-27T08:24:47
{"gard": ["826"], "omim": ["305620"], "synonyms": []}
Hepatic veno-occlusive disease Other namesVeno-occlusive disease with immunodeficiency Sinusoidal obstruction syndrome SpecialtyGastroenterology SymptomsWeight gain, tender enlargement of the liver, ascites, jaundice Diagnostic methodLiver biopsy Differential diagnosisBudd–Chiari syndrome PreventionUrso...
Hepatic veno-occlusive disease
c0019156
5,816
wikipedia
https://en.wikipedia.org/wiki/Hepatic_veno-occlusive_disease
2021-01-18T18:37:01
{"gard": ["13004"], "mesh": ["D006504"], "umls": ["C0019156"], "icd-10": ["K76.5"], "orphanet": ["890"], "wikidata": ["Q5731687"]}
A vaccine-associated sarcoma (VAS) or feline injection-site sarcoma (FISS) is a type of malignant tumor found in cats (and often, dogs and ferrets) which has been linked to certain vaccines. VAS has become a concern for veterinarians and cat owners alike and has resulted in changes in recommended vaccine protocol...
Vaccine-associated sarcoma
None
5,817
wikipedia
https://en.wikipedia.org/wiki/Vaccine-associated_sarcoma
2021-01-18T18:54:37
{"wikidata": ["Q7907937"]}
Fluid accumulation in the air spaces and parenchyma of the lungs tissue Pulmonary edema Other namesPulmonary oedema Pulmonary edema with small pleural effusions on both sides. SpecialtyCardiology, critical care medicine Pulmonary edema is fluid accumulation in the tissue and air spaces of the lungs.[1] It...
Pulmonary edema
c0034063
5,818
wikipedia
https://en.wikipedia.org/wiki/Pulmonary_edema
2021-01-18T18:55:44
{"mesh": ["D011654"], "umls": ["C0034063"], "icd-9": ["518.4", "514"], "wikidata": ["Q857667"]}
Hereditary fibrosing poikiloderma with tendon contractures, myopathy, and pulmonary fibrosis (abbreviated POIKTMP), is a disorder that affects many parts of the body, particularly the skin, muscles, lungs, and pancreas. Signs and symptoms vary among affected individuals. People with POIKTMP have patchy changes i...
Hereditary fibrosing poikiloderma with tendon contractures, myopathy, and pulmonary fibrosis
c3810325
5,819
medlineplus
https://medlineplus.gov/genetics/condition/hereditary-fibrosing-poikiloderma-with-tendon-contractures-myopathy-and-pulmonary-fibrosis/
2021-01-27T08:25:01
{"gard": ["13218"], "omim": ["615704"], "synonyms": []}
Enterocutaneous fistula SpecialtyGastroenterology An enterocutaneous fistula (ECF) is an abnormal communication between the small or large bowel and the skin that allows the contents of the stomach or intestines to leak through an opening in the skin.[1] ## Contents * 1 Causes * 2 Diagnosis * 2.1 Cla...
Enterocutaneous fistula
c0341318
5,820
wikipedia
https://en.wikipedia.org/wiki/Enterocutaneous_fistula
2021-01-18T18:54:26
{"mesh": ["D007412"], "umls": ["C0341318"], "wikidata": ["Q1344610"]}
## Description Pediatric trigger thumb is caused by a mismatch between the flexor pollicis longus tendon and its sheath. Patients present with a hard, palpable nodule (Notta's node) at the base of the metacarpal and an inability to extend the thumb beyond 30 degrees, which can rarely be accompanied by triggering, s...
TRIGGER THUMB
c0410060
5,821
omim
https://www.omim.org/entry/190410
2019-09-22T16:32:23
{"mesh": ["D052582"], "omim": ["190410"], "icd-10": ["M65.31"]}
A rare, hereditary amyloidosis with primary renal involvement characterized by renal interstitial and medullary deposition of amyloid, low plasma levels of ApoA-1 and slow disease progression. Main clinical signs and symptoms are hypertension, proteinuria, hematuria and edema due to chronic renal insufficiency leadin...
AApoAI amyloidosis
None
5,822
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=93560
2021-01-23T19:04:44
{"icd-10": ["E85.0"], "synonyms": ["Apolipoprotein A-I amyloidosis", "Familial amyloid nephropathy due to apolipoprotein A-I variant", "Familial renal amyloidosis due to apolipoprotein A-I variant", "Hereditary amyloid nephropathy due to apolipoprotein A-I variant", "Hereditary renal amyloidosis due to apolipoprotein A...
Olivopontocerebellar atrophy-deafness syndrome is characterised by infancy-onset olivopontocerebellar atrophy, sensorineural deafness and speech impairment. It has been described in less than 15 children. Most cases were sporadic, but autosomal recessive inheritance was suggested in three cases. *[v]: View this te...
Olivopontocerebellar atrophy-deafness syndrome
None
5,823
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2732
2021-01-23T18:12:53
{"gard": ["4070"], "icd-10": ["Q04.8"], "synonyms": ["Olivopontocerebellar atrophy-hearing loss syndrome"]}
A number sign (#) is used with this entry because this phenotype is associated with early embryonic postzygotic somatic activating mutations in the GNAS1 gene (139320). Description Activating or gain-of-function GNAS1 mutations in patients with the McCune-Albright syndrome are present in the mosaic state, resulting...
MCCUNE-ALBRIGHT SYNDROME
c0242292
5,824
omim
https://www.omim.org/entry/174800
2019-09-22T16:36:01
{"doid": ["1858"], "mesh": ["D005359"], "omim": ["174800"], "icd-9": ["756.54"], "icd-10": ["Q78.1"], "orphanet": ["562"], "synonyms": ["Alternative titles", "ALBRIGHT SYNDROME"], "genereviews": ["NBK274564"]}
## Clinical Features Stanescu et al. (1963) described 9 members of a kindred with an apparently 'new' syndrome. The features included a peculiar form of craniofacial dysostosis with small skull, thin cranial bone, depressions over the frontoparietal and occipitoparietal sutures, poorly developed mandible, and exoph...
CRANIOFACIAL DYSOSTOSIS WITH DIAPHYSEAL HYPERPLASIA
c0432263
5,825
omim
https://www.omim.org/entry/122900
2019-09-22T16:42:46
{"mesh": ["C562974"], "omim": ["122900"], "orphanet": ["1798"], "synonyms": ["Alternative titles", "OSTEOSCLEROSIS, STANESCU TYPE"]}
Lichenoid eruption SpecialtyDermatology A lichenoid eruption is a skin disease characterized by damage and infiltration between the epidermis and dermis.[1] Examples include lichen planus, lichen sclerosus and lichen nitidus. It can also be associated with abrasion or drug use.[2] It has been observed in conj...
Lichenoid eruption
c0162848
5,826
wikipedia
https://en.wikipedia.org/wiki/Lichenoid_eruption
2021-01-18T19:04:17
{"mesh": ["D017512"], "icd-9": ["697"], "icd-10": ["L43"], "wikidata": ["Q6543234"]}
A rare large granular lymphocyte leukemia characterized by persistent (> 6 months) natural killer cell lymphocytosis in the absence of clinical diagnosis of leukemia/lymphoma, autoimmune disease, or chronic viral infections. The clinical course is variable, but generally indolent. Patients often remain asymptomat...
Chronic lymphoproliferative disorder of natural killer cells
c1512709
5,827
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=512017
2021-01-23T17:52:46
{"synonyms": ["CLPD-NK", "CNKL", "Chronic NK lymphocytosis", "Chronic NK-cell lymphocytosis", "Chronic lymphoproliferative disorder of NK-cells", "NK-cell lineage granular lymphocyte proliferative disorder"]}
A number sign (#) is used with this entry because susceptibility to the development of atypical hemolytic uremic syndrome-1 (AHUS1) can be conferred by variation in the gene encoding complement factor H (CFH; 134370) on chromosome 1q31. Deficiency of the CFH-related proteins CFHR1 (134371) and CFHR3 (605336) may be ...
HEMOLYTIC UREMIC SYNDROME, ATYPICAL, SUSCEPTIBILITY TO, 1
c2931788
5,828
omim
https://www.omim.org/entry/235400
2019-09-22T16:27:10
{"mesh": ["D065766"], "omim": ["235400"], "icd-10": ["D59.3"], "orphanet": ["90038", "93581", "2134", "544472"], "synonyms": ["Atypical HUS with anti-factor H antibodies", "Stx-HUS", "Shiga-like toxin-associated HUS", "Alternative titles", "Hemolytic-uremic syndrome without diarrhea with anti-factor H antibodies", "AHU...
High bone mass osteogenesis imperfecta is a rare, genetic, primary bone dysplasia disorder characterized by increased bone fragility, manifesting with mutiple, childhood-onset, vertebral and peripheral fractures, associated with increased bone mass density on radiometric examination. Patients typically present normal...
High bone mass osteogenesis imperfecta
None
5,829
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=314029
2021-01-23T17:40:40
{"icd-10": ["Q78.0"], "synonyms": ["High bone mass OI"]}
Plasminogen activator inhibitor type 1 (PAI1) deficiency is a rare bleeding disorder that causes excessive or prolonged bleeding due to blood clots being broken down too early. PAI1 is a protein in the body needed for normal blood clotting. When the body does not have enough functional PAI1, the body's ability keep b...
Plasminogen activator inhibitor type 1 deficiency
c2750067
5,830
gard
https://rarediseases.info.nih.gov/diseases/4381/plasminogen-activator-inhibitor-type-1-deficiency
2021-01-18T17:58:17
{"mesh": ["C567640"], "omim": ["613329"], "orphanet": ["465"], "synonyms": ["Plasminogen activator inhibitor 1 deficiency", "PAI-1 deficiency", "Hyperfibrinolysis due to PAI1 deficiency", "PAI1 deficiency"]}
Subungual exostosis Other namesDupuytren subungual exostosis[1] Subungual exostosis (1/3), in a boy of 15 years old SpecialtyOrthopedic Subungual exostoses are bony projections which arise from the dorsal surface of the distal phalanx, most commonly of the hallux (the big toe).[2] ## Contents * 1 Prese...
Subungual exostosis
c0038604
5,831
wikipedia
https://en.wikipedia.org/wiki/Subungual_exostosis
2021-01-18T18:46:22
{"gard": ["8280"], "mesh": ["C535723"], "umls": ["C0038604"], "wikidata": ["Q7632311"]}
Miller-Dieker Syndrome (MDS) is a contiguous gene deletion syndrome of chromosome 17p13.3, characterised by classical lissencephaly (lissencephaly type 1) and distinct facial features. Additional congenital malformations can be part of the condition. ## Epidemiology MDS is undoubtedly a rare condition with a re...
Miller-Dieker syndrome
c0265219
5,832
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=531
2021-01-23T17:46:40
{"gard": ["3669"], "mesh": ["D054221"], "omim": ["247200"], "umls": ["C0265219"], "icd-10": ["Q04.3"], "synonyms": ["Lissencephaly due to 17p13.3 deletion", "Monosomy 17p13.3", "Telomeric deletion 17p"]}
Jalili syndrome is characterized by the association of amelogenesis imperfecta (AI; see this term) and cone-rod retinal dystrophy (CORD; see this term). ## Epidemiology It has been described in only one family with 29 affected individuals. ## Clinical description AI is a generic term for an inherited group of den...
Jalili syndrome
c2931074
5,833
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1873
2021-01-23T18:34:13
{"gard": ["1463"], "mesh": ["C535976"], "omim": ["217080"], "umls": ["C2931074", "C3495589"], "icd-10": ["H35.5"], "synonyms": ["Cone rod dystrophy-amelogenesis imperfecta syndrome"]}
Ganglioglioma is a rare, usually benign, well-circumscribed, often cystic, mixed neuronal-glial tumor (composed of both neoplastic glial and ganglionic elements) which is typically located in the temporal lobe and rarely invades the surrounding tissue. Patients usually present with seizures refractory to medical trea...
Ganglioglioma
c0206716
5,834
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=251949
2021-01-23T19:04:02
{"gard": ["2430"], "mesh": ["D018303"], "umls": ["C0206716"]}
## Description Cloverleaf skull, or Kleeblattschaedel, consists of a trilobular skull with craniosynostosis. The condition shows pathogenetic variability and etiologic heterogeneity. The cause of isolated cloverleaf skull is unknown (Cohen, 2009). Cohen (1975) pointed out that Kleeblattschaedel is a component of m...
KLEEBLATTSCHAEDEL
c1860050
5,835
omim
https://www.omim.org/entry/148800
2019-09-22T16:39:18
{"omim": ["148800"], "orphanet": ["2343"], "synonyms": ["Alternative titles", "KLEEBLATTSCHADEL", "CLOVERLEAF SKULL"]}
## Clinical Features Kozlowski et al. (1973) and Danks et al. (1974) reported 3 patients with precocious osteodysplasty, of whom 2 were sibs of Albanian extraction. All 3 died at less than 1 year of age. They suffered from a generalized disturbance of modeling of the long and tubular bones and pelvis with severe hy...
OSTEODYSPLASTY, PRECOCIOUS, OF DANKS, MAYNE, AND KOZLOWSKI
c1850185
5,836
omim
https://www.omim.org/entry/259270
2019-09-22T16:23:53
{"mesh": ["C564922"], "omim": ["259270"]}
This article has multiple issues. Please help improve it or discuss these issues on the talk page. (Learn how and when to remove these template messages) This article needs more medical references for verification or relies too heavily on primary sources. Please review the contents of the article and add the appropr...
Biotin deficiency
c0268680
5,837
wikipedia
https://en.wikipedia.org/wiki/Biotin_deficiency
2021-01-18T18:31:29
{"mesh": ["C531633"], "icd-9": ["266.2"], "icd-10": ["E53.8"], "wikidata": ["Q10264745"]}
A rare epidermal disease characterized by rough, dry skin with prominent, plate-like scaling. It is non-hereditary and usually arises during adulthood in the context of a variety of diseases or conditions, like various types of cancer, autoimmune diseases, endocrine disorders, nutritional deficiencies, but also a...
Acquired ichthyosis
c0263386
5,838
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=454
2021-01-23T18:49:16
{"mesh": ["C538175"], "icd-10": ["L85.0"]}
A rare genetic disorder of lipid metabolism characterized by neonatal to childhood onset of impaired absorption of dietary fat with greasy/oily and voluminous stools, but normal growth and development. Decreased levels of fecal elastase, as well as low serum levels of the fat-soluble vitamins A, D, and E, have been r...
Pancreatic triacylglycerol lipase deficiency
c0268240
5,839
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=309031
2021-01-23T17:59:56
{"omim": ["614338"], "umls": ["C0268240"], "icd-10": ["K90.3"], "synonyms": ["Pancreatic triglyceride lipase deficiency"]}
Hereditary motor and sensory neuropathy Onion bulb formations in a nerve biopsy in a case of HMSN type I SpecialtyNeurology Hereditary motor and sensory neuropathies (HMSN) is a name sometimes given to a group of different neuropathies which are all characterized by their impact upon both afferent and effere...
Hereditary motor and sensory neuropathy
c0027888
5,840
wikipedia
https://en.wikipedia.org/wiki/Hereditary_motor_and_sensory_neuropathy
2021-01-18T18:50:32
{"gard": ["6634"], "mesh": ["D015417"], "umls": ["C0027888"], "wikidata": ["Q15270307"]}
Condition characterized by a loss of height of the nose, because of the collapse of the bridge Saddle nose Sketch of a saddle nose deformity SpecialtyPlastic surgery Saddle nose is a condition associated with nasal trauma, congenital syphilis, relapsing polychondritis, granulomatosis with polyangiitis, ...
Saddle nose
c0264169
5,841
wikipedia
https://en.wikipedia.org/wiki/Saddle_nose
2021-01-18T18:44:04
{"icd-10": ["M95.0"], "wikidata": ["Q478112"]}
Glucocorticoid remediable aldosteronism Other namesGRA SpecialtyEndocrinology Glucocorticoid remediable aldosteronism also describable as aldosterone synthase hyperactivity, is an autosomal dominant disorder in which the increase in aldosterone secretion produced by ACTH is no longer transient. It is a ...
Glucocorticoid remediable aldosteronism
c1260386
5,842
wikipedia
https://en.wikipedia.org/wiki/Glucocorticoid_remediable_aldosteronism
2021-01-18T19:07:58
{"gard": ["2790"], "mesh": ["C563177"], "umls": ["C1260386"], "orphanet": ["403"], "wikidata": ["Q17149181"]}
A number sign (#) is used with this entry because persistent mullerian duct syndrome (PMDS) is caused by heterozygous mutation in the gene encoding anti-mullerian hormone (AMH; 600957) or in the AMH receptor gene (AMHR; 600956). These 2 forms of persistent mullerian duct syndrome are referred to as type I and typ...
PERSISTENT MULLERIAN DUCT SYNDROME, TYPES I AND II
c1849930
5,843
omim
https://www.omim.org/entry/261550
2019-09-22T16:23:33
{"doid": ["0050791"], "mesh": ["C536665"], "omim": ["261550"], "orphanet": ["2856"], "synonyms": ["Alternative titles", "PSEUDOHERMAPHRODITISM, MALE INTERNAL", "HERNIA UTERI INGUINALE", "PERSISTENT OVIDUCT SYNDROME", "FEMALE GENITAL DUCTS IN OTHERWISE NORMAL MALE"]}
Carcinoma of the gallbladder (GBC) is the most common and aggressive form of biliary tract cancer (BTC; see this term) usually arising in the fundus of the gallbladder, rapidly metastasizing to lymph nodes and distant sites. ## Epidemiology Annual incidence rates vary from 1/100,000 to 1/ 4,350 between different et...
Carcinoma of gallbladder and extrahepatic biliary tract
c0153452
5,844
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=56044
2021-01-23T18:50:25
{"mesh": ["D005706"], "umls": ["C0153452", "C0235782"], "synonyms": ["Carcinoma of gallbladder and EBT"]}
Kraus (1951) was of the opinion that homozygosity of a gene is responsible for a pronounced tubercle, whereas the heterozygote shows slight grooves, pits, tubercles or bulge. He provided good pictures of the anomaly. Lee and Goose (1972) studied the inheritance of this and four other common dental traits, namely, sho...
CARABELLI ANOMALY OF MAXILLARY MOLAR TEETH
c1861897
5,845
omim
https://www.omim.org/entry/114700
2019-09-22T16:43:43
{"mesh": ["C566175"], "omim": ["114700"]}
A number sign (#) is used with this entry because of evidence that combined oxidative phosphorylation deficiency-39 (COXPD39) is caused by homozygous or compound heterozygous mutation in the GFM2 gene (606544) on chromosome 5q13. Description Combined oxidative phosphorylation deficiency-39 (COXPD39) is an autosomal...
COMBINED OXIDATIVE PHOSPHORYLATION DEFICIENCY 39
None
5,846
omim
https://www.omim.org/entry/618397
2019-09-22T15:42:10
{"omim": ["618397"]}
Cleft lip - retinopathy is an exceedingly rare association characterized by cleft lip and progressive retinopathy. *[v]: View this template *[t]: Discuss this template *[e]: Edit this template *[c.]: circa *[AA]: Adrenergic agonist *[AD]: Acetaldehyde dehydrogenase *[HAART]: highly active antiretrovira...
Cleft lip-retinopathy syndrome
c2931789
5,847
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1995
2021-01-23T17:35:39
{"gard": ["435"], "mesh": ["C538272"], "umls": ["C2931789"], "icd-10": ["Q87.8"], "synonyms": ["Ausems-Wittebol Post-Hennekam syndrome", "Cleft lip-cone rod dystrophy syndrome", "Cleft lip-progressive retinopathy syndrome"]}
A rare, hereditary nephrotic syndrome characterized by proteinuria, hypoalbuminemia, edema, and hyperlipidemia, with an absence of response to an initial trial of corticosteroids (i.e. steroid-resistant nephrotic syndrome; SRNS) and a generally complicated course. ## Epidemiology The annual incidence is 1/ 200,000-...
Genetic steroid-resistant nephrotic syndrome
c1868672
5,848
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=656
2021-01-23T18:52:24
{"gard": ["3946"], "mesh": ["C536404"], "omim": ["256370", "301028", "600995", "603278", "603965", "607832", "610725", "612551", "613237", "614131", "614196", "615244", "615573", "615861", "616002", "616032", "616220", "616730", "616892", "616893", "618176", "618177", "618178", "618179"], "umls": ["C1868672"], "icd-10"...
A number sign (#) is used with this entry because of evidence that ectopia lentis et pupillae can be caused by homozygous or compound heterozygous mutation in the ADAMTSL4 gene (610113) on chromosome 1q21. Autosomal recessive isolated ectopia lentis-2 (ECTO2; 225100) is also caused by mutation in the ADAMTSL4 gene. ...
ECTOPIA LENTIS ET PUPILLAE
c0013581
5,849
omim
https://www.omim.org/entry/225200
2019-09-22T16:28:25
{"mesh": ["D004479"], "omim": ["225200"], "orphanet": ["1885"], "synonyms": ["Alternative titles", "ECTOPIA LENTIS WITH ECTOPIA OF PUPIL"], "genereviews": ["NBK84111"]}
Hypertrichosis lanuginosa congenita is a rare congenital skin disease characterized by the presence of 3 to 5cm long lanugo-type hair on the entire body, with the exception of palms, soles, and mucous membranes. *[v]: View this template *[t]: Discuss this template *[e]: Edit this template *[c.]: circa *[AA...
Hypertrichosis lanuginosa congenita
c0235864
5,850
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2222
2021-01-23T17:17:12
{"gard": ["12754", "2865"], "mesh": ["C538389"], "omim": ["145700", "145701", "307150"], "umls": ["C0235864", "C2936812"], "icd-10": ["Q84.2"], "synonyms": ["Hypertrichosis universalis"]}
## Clinical Features An historically notable example is the Scipion family in which the malformation was transmitted for over two thousand years (Manoiloff, 1931). The thumb is replaced by one or two triphalangeal digits, which may or may not be opposable (Swanson and Brown, 1962). The feet, in some cases, show pre...
POLYDACTYLY, PREAXIAL III
c1868113
5,851
omim
https://www.omim.org/entry/174600
2019-09-22T16:36:01
{"mesh": ["C566784"], "omim": ["174600"], "orphanet": ["93337"], "synonyms": ["Alternative titles", "INDEX FINGER POLYDACTYLY"]}
A number sign (#) is used with this entry because autosomal recessive nonsyndromic mental retardation-7 (MRT7) can be caused by homozygous mutation in the TUSC3 gene (601385) on chromosome 8p22. Clinical Features Garshasbi et al. (2008) reported a highly consanguineous Iranian kindred in which 7 individuals had non...
MENTAL RETARDATION, AUTOSOMAL RECESSIVE 7
c1970197
5,852
omim
https://www.omim.org/entry/611093
2019-09-22T16:03:39
{"doid": ["0060308"], "mesh": ["C567016"], "omim": ["611093"], "orphanet": ["88616"], "synonyms": ["MENTAL RETARDATION, AUTOSOMAL RECESSIVE 22", "Alternative titles", "NS-ARID", "AR-NSID"], "genereviews": ["NBK1332"]}
Joubert syndrome with orofaciodigital defect (or oral-facial-digital syndrome type 6, OFD6) is a very rare subtype of Joubert syndrome and related disorders (JSRD, see this term) characterized by the neurological features of JS associated with orofacial anomalies and often polydactyly. ## Epidemiology Prevalence is...
Orofaciodigital syndrome type 6
c2745997
5,853
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2754
2021-01-23T18:29:01
{"gard": ["4412"], "mesh": ["C536531"], "omim": ["277170", "300804", "614815", "615665", "617127", "618763"], "umls": ["C2745997"], "icd-10": ["Q04.3"], "synonyms": ["Joubert syndrome with oral-facial-digital syndrome", "Joubert syndrome with orofaciodigital defect", "OFD6", "Oral-facial-digital syndrome type 6", "Poly...
Horse with parrot mouth Brachygnathism or colloquially parrot mouth, is the uneven alignment of the upper and lower teeth in animals. In serious cases, the upper teeth protrude beyond the lower teeth. Problem with parrot mouth occur if the molars at the back of the mouth are also uneven, resulting in large hooks for...
Brachygnathism
c1305740
5,854
wikipedia
https://en.wikipedia.org/wiki/Brachygnathism
2021-01-18T19:05:39
{"mesh": ["D057887"], "wikidata": ["Q4953452"]}
Dilated cardiomyopathy with ataxia (DCMA) syndrome is an inherited condition characterized by heart problems, movement difficulties, and other features affecting multiple body systems. Beginning in infancy to early childhood, most people with DCMA syndrome develop dilated cardiomyopathy, which is a condition tha...
Dilated cardiomyopathy with ataxia syndrome
c1857776
5,855
medlineplus
https://medlineplus.gov/genetics/condition/dilated-cardiomyopathy-with-ataxia-syndrome/
2021-01-27T08:25:38
{"gard": ["12964"], "mesh": ["C565706"], "omim": ["610198"], "synonyms": []}
## Clinical Features Esser (1939) reported 4 affected sibs (2 males, 2 females) and an affected male first cousin. Boo-Chai (1965) described 3 cases in sibs of Asiatic Indian descent. A dominant form of bifid nose without hypertelorism (109740) has been proposed. Ocular hypertelorism (sometimes a dominant) is occas...
BIFID NOSE, AUTOSOMAL RECESSIVE
c0221363
5,856
omim
https://www.omim.org/entry/210400
2019-09-22T16:30:27
{"mesh": ["C535441"], "omim": ["210400"], "orphanet": ["2695"], "synonyms": ["Alternative titles", "MEDIAN FISSURE OF NOSE", "NOSE, MEDIAN CLEFT OF"]}
Congenital fiber-type disproportion is a condition that primarily affects skeletal muscles, which are muscles used for movement. People with this condition typically experience muscle weakness (myopathy), particularly in the muscles of the shoulders, upper arms, hips, and thighs. Weakness can also affect the muscles ...
Congenital fiber-type disproportion
c0546264
5,857
medlineplus
https://medlineplus.gov/genetics/condition/congenital-fiber-type-disproportion/
2021-01-27T08:24:49
{"gard": ["6161"], "mesh": ["D020914"], "omim": ["255310"], "synonyms": []}
Renal hypouricemia is a kidney (renal) disorder that results in a reduced amount of urate in the blood. Urate is a byproduct of certain normal chemical reactions in the body. In the bloodstream it acts as an antioxidant, protecting cells from the damaging effects of unstable molecules called free radicals. However, h...
Renal hypouricemia
c0473219
5,858
medlineplus
https://medlineplus.gov/genetics/condition/renal-hypouricemia/
2021-01-27T08:25:03
{"gard": ["9496"], "mesh": ["C537757"], "omim": ["220150", "612076"], "synonyms": []}
A number sign (#) is used with this entry because of evidence that mitochondrial complex III deficiency nuclear type 3 (MC3DN3) is caused by homozygous mutation in the UQCRB gene (191330) on chromosome 8q22. For a general phenotypic description and a discussion of genetic heterogeneity of mitochondrial complex III d...
MITOCHONDRIAL COMPLEX III DEFICIENCY, NUCLEAR TYPE 3
c3554606
5,859
omim
https://www.omim.org/entry/615158
2019-09-22T15:53:00
{"doid": ["0080112"], "omim": ["615158"], "orphanet": ["1460"], "synonyms": ["Isolated CoQ-cytochrome C reductase deficiency", "Isolated coenzyme Q-cytochrome C reductase deficiency", "Isolated mitochondrial respiratory chain complex III deficiency", "Isolated ubiquinone-cytochrome C reductase deficiency"]}
Chitayat et al. (1991) described a combination of mental retardation with distal arthrogryposis in 2 sisters, one of whom died of respiratory failure due to hypoplastic lungs shortly after birth. The chin showed a grooving like that seen in the Freeman-Sheldon syndrome (193700) but the patients did not have other fea...
ARTHROGRYPOSIS, DISTAL, WITH MENTAL RETARDATION AND CHARACTERISTIC FACIES
c1859723
5,860
omim
https://www.omim.org/entry/208081
2019-09-22T16:30:51
{"mesh": ["C565940"], "omim": ["208081"]}
Pfeiffer syndrome is a genetic disorder characterized by the premature fusion of certain skull bones (craniosynostosis). This early fusion prevents the skull from growing normally and affects the shape of the head and face. Pfeiffer syndrome also affects bones in the hands and feet. Many of the characteristic facial...
Pfeiffer syndrome
c0220658
5,861
medlineplus
https://medlineplus.gov/genetics/condition/pfeiffer-syndrome/
2021-01-27T08:24:52
{"gard": ["7380"], "mesh": ["D000168"], "omim": ["101600"], "synonyms": []}
Multinucleate cell angiohistiocytoma SpecialtyDermatology Multinucleate cell angiohistiocytoma is a cutaneous condition that presents as slowly growing, multiple, discrete but grouped, red to violaceous papules[1] ## See also[edit] * Mast cell sarcoma * List of cutaneous conditions ## References[edit] ...
Multinucleate cell angiohistiocytoma
c4049285
5,862
wikipedia
https://en.wikipedia.org/wiki/Multinucleate_cell_angiohistiocytoma
2021-01-18T18:30:39
{"umls": ["C4049285"], "wikidata": ["Q6934824"]}
This article needs more medical references for verification or relies too heavily on primary sources. Please review the contents of the article and add the appropriate references if you can. Unsourced or poorly sourced material may be challenged and removed. Find sources: "Nonsyndromic deafness" – news · newspa...
Nonsyndromic deafness
c3711374
5,863
wikipedia
https://en.wikipedia.org/wiki/Nonsyndromic_deafness
2021-01-18T19:10:19
{"gard": ["6410"], "mesh": ["C580334"], "icd-10": ["H90.5"], "orphanet": ["87884"], "synonyms": ["Isolated genetic deafness"], "wikidata": ["Q9079046"]}
Porencephaly is a rare condition that affects the central nervous system. People with porencephaly develop fluid-filled cysts or cavities in the brain either before or shortly after birth. The severity of the condition and the associated signs and symptoms vary significantly based on the size, location, and numbe...
Porencephaly
c0302892
5,864
gard
https://rarediseases.info.nih.gov/diseases/7430/porencephaly
2021-01-18T17:58:14
{"mesh": ["D065708"], "orphanet": ["2940"], "synonyms": []}
Billard et al. (1989) described apparently monozygotic twins (their patients 13 and 14) who suffered from mild and nonprogressive mental retardation without motor deficit or visual disorders, but with moderate dysmorphia, craniosynostosis, and small stature due to growth hormone deficiency. CT scan showed dense calci...
ENCEPHALOPATHY WITH INTRACRANIAL CALCIFICATION, GROWTH HORMONE DEFICIENCY, MICROCEPHALY, AND RETINAL DEGENERATION
c1856973
5,865
omim
https://www.omim.org/entry/225755
2019-09-22T16:28:15
{"mesh": ["C565594"], "omim": ["225755"], "orphanet": ["1261"]}
Osteogenesis imperfecta (OI) is a group of genetic disorders that mainly affect the bones. Osteogenesis imperfecta type 1 is the mildest form of OI and is characterized by bone fractures during childhood and adolescence that often result from minor trauma. Fractures occur less frequently in adulthood. People with mil...
Osteogenesis imperfecta type I
c0023931
5,866
gard
https://rarediseases.info.nih.gov/diseases/8694/osteogenesis-imperfecta-type-i
2021-01-18T17:58:33
{"mesh": ["D010013"], "omim": ["166200"], "umls": ["C0023931"], "orphanet": ["216796"], "synonyms": ["OI type 1", "Osteogenesis imperfecta tarda", "Osteogenesis imperfecta with blue sclerae", "Adair-Dighton syndrome", "Mild osteogenesis imperfecta", "Non-deforming osteogenesis imperfecta", "Van der Hoeve syndrome", "Cl...
Malouf syndrome Other namesDilated cardiomyopathy-hypergonadotropic hypogonadism syndrome Malouf syndrome (also known as "congestive cardiomyopathy-hypergonadotropic hypogonadism syndrome") is a congenital disorder that causes one or more of the following symptoms: mental retardation, ovarian dysgenesis, conge...
Malouf syndrome
c0796083
5,867
wikipedia
https://en.wikipedia.org/wiki/Malouf_syndrome
2021-01-18T19:01:18
{"mesh": ["C535580"], "umls": ["C0796083", "C0796031"], "orphanet": ["2229"], "wikidata": ["Q6744557"]}
Autosomal recessive spastic paraplegia type 64 is an extremely rare and complex form of hereditary spastic paraplegia (see this term), reported in only 4 patients from 2 families to date, characterized by spastic paraplegia (presenting between the ages of 1 to 4 years with abnormal gait) associated with microceph...
Autosomal recessive spastic paraplegia type 64
c3810289
5,868
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=401810
2021-01-23T17:00:54
{"omim": ["615683"], "icd-10": ["G11.4"], "synonyms": ["SPG64"]}
A number sign (#) is used with this entry because of evidence that multiple types of cataract (CTRCT39) are caused by heterozygous mutation in the CRYGB gene (123670) on chromosome 2q34. Description Mutations in the CRYGB gene have been found to cause multiple types of cataract, which have been described as lamella...
CATARACT 39, MULTIPLE TYPES
c3808800
5,869
omim
https://www.omim.org/entry/615188
2019-09-22T15:52:58
{"doid": ["0110236"], "omim": ["615188"], "icd-10": ["Q12.0"], "orphanet": ["91492"], "synonyms": []}
A number sign (#) is used with this entry because rare germline mutations have been found in the MSR1 (153622), ASCC1 (614215), and CTHRC1 (610635) genes in patients with Barrett esophagus and/or esophageal adenocarcinoma. Description Barrett esophagus, or Barrett metaplasia, describes the phenotypic change of norm...
BARRETT ESOPHAGUS
c0279628
5,870
omim
https://www.omim.org/entry/614266
2019-09-22T15:55:53
{"doid": ["9206"], "mesh": ["C562730"], "omim": ["614266"], "icd-9": ["530.85"], "icd-10": ["K22.7", "K22.70"], "orphanet": ["99976"], "synonyms": ["Alternative titles", "BARRETT METAPLASIA"]}
Eccrine carcinoma Other namesSyringoid carcinoma Eccrine carcinoma, alveolar type SpecialtyDermatology Eccrine carcinoma is a rare skin condition characterized by a plaque or nodule on the scalp, trunk, or extremities.[1]:669 It originates from the eccrine sweat glands of the skin, accounting for less than...
Eccrine carcinoma
c1302864
5,871
wikipedia
https://en.wikipedia.org/wiki/Eccrine_carcinoma
2021-01-18T18:36:18
{"umls": ["C1302864"], "wikidata": ["Q5332314"]}
Fragile XE syndrome (FRAXE) is a genetic condition associated with mild to borderline intellectual disabilities with physical features differing from person to person. The characteristic features are learning difficulties, often a consequence of communication problems (speech delay, poor writing skills), hyperact...
Fragile XE syndrome
c0751157
5,872
gard
https://rarediseases.info.nih.gov/diseases/2378/fragile-xe-syndrome
2021-01-18T18:00:26
{"mesh": ["D005600"], "omim": ["309548"], "orphanet": ["100973"], "synonyms": ["X-linked mental retardation associated with fragile site FRAXE", "Fragile site, folic acid type", "Intellectual disability associated with fragile site FRAXE", "FRAXE syndrome"]}
Gates (1946) cited a family in which the grandfather showed bilaterally a radial artery that passed over the supinator longus muscle 3 to 4 cm above the wrist and ran over the radial extensors above the styloid process. All his children were said to have the same anomaly on the left side. Among his grandchildren the ...
ARTERIES, ANOMALIES OF
c1876179
5,873
omim
https://www.omim.org/entry/108000
2019-09-22T16:44:45
{"omim": ["108000"]}
Cronkhite-Canada syndrome is a rare gastrointestinal disorder characterized by widespread colon polyps, unhealthy looking (dystrophic) nails, hair loss (alopecia), darkening skin (such as on the hands, arms, neck and face), diarrhea, weight loss, stomach pain, and/or excess fluid accumulation in arms and legs (periph...
Cronkhite-Canada disease
c0282207
5,874
gard
https://rarediseases.info.nih.gov/diseases/4427/cronkhite-canada-disease
2021-01-18T18:01:02
{"mesh": ["D044483"], "omim": ["175500"], "orphanet": ["2930"], "synonyms": ["Polyposis skin pigmentation alopecia fingernail changes"]}
A rare acquired immunodeficiency disorder characterized by the appearance of susceptibility to disseminated opportunistic infections (in particular, disseminated nontuberculous mycobacterial infection, salmonellosis, penicillosis, and varicella zoster virus infection) in previously healthy (HIV-negative) adults, asso...
Adult-onset immunodeficiency with anti-interferon-gamma autoantibodies
None
5,875
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=306431
2021-01-23T18:52:48
{"gard": ["11992"], "icd-10": ["D84.8"], "synonyms": ["Acquired adult-onset immunodeficiency", "Adult-onset immunodeficiency with acquired anti-interferon-gamma autoantibodies"]}
For a phenotypic description and a discussion of genetic heterogeneity of familial thoracic aortic aneurysm, see 607086. Mapping Guo et al. (2001) reported a number of families with clear autosomal dominant inheritance of thoracic aneurysms and dissections. In 2 large families, linkage to FBN1 (134797) was excluded...
AORTIC ANEURYSM, FAMILIAL THORACIC 2
c1846837
5,876
omim
https://www.omim.org/entry/607087
2019-09-22T16:09:43
{"doid": ["14004"], "mesh": ["C564627"], "omim": ["607087"], "orphanet": ["91387"], "synonyms": ["FAA2", "Alternative titles", "Familial TAAD"], "genereviews": ["NBK1120"]}
## Clinical Features Rotenstein et al. (1982) described a family in which 4 females in 3 successive generations shared the clinical triad of fever, hypertension, and juvenile polyarthritis, along with the pathologic feature of noncaseating granulomas in vascular and extravascular distribution. The proband was a 5-y...
ARTERITIS, FAMILIAL GRANULOMATOUS, WITH JUVENILE POLYARTHRITIS
c1862510
5,877
omim
https://www.omim.org/entry/108050
2019-09-22T16:44:45
{"mesh": ["C566253"], "omim": ["108050"]}
For a phenotypic description and a discussion of genetic heterogeneity of absorptive hypercalciuria, see 143870. Imamura et al. (1998) reported the cases of 2 unrelated girls with multiple malformations, each of whom had an unbalanced translocation chromosome with deletion of the 4q33-qter segment and addition of a ...
HYPERCALCIURIA, ABSORPTIVE, 1
c0543800
5,878
omim
https://www.omim.org/entry/607258
2019-09-22T16:09:28
{"omim": ["607258"], "orphanet": ["2197"], "synonyms": ["Alternative titles", "HCA1"]}
Not to be confused with polydipsia. Dipsomania, an 18th-century woodcarving by Josef Stammel in the library of Admont Abbey. Dipsomania is a historical term describing a medical condition involving an uncontrollable craving for alcohol. In the 19th century, the term dipsomania was used to refer to a variety of alco...
Dipsomania
c0001973
5,879
wikipedia
https://en.wikipedia.org/wiki/Dipsomania
2021-01-18T18:57:54
{"mesh": ["D000437"], "wikidata": ["Q2717096"]}
Coral dermatitis SpecialtyDermatology Coral dermatitis is a cutaneous condition caused by injury from the exoskeleton of certain corals.[1]:430 ## See also[edit] * Skin lesion ## References[edit] 1. ^ James, William D.; Berger, Timothy G.; et al. (2006). Andrews' Diseases of the Skin: clinical Dermatol...
Coral dermatitis
c0413141
5,880
wikipedia
https://en.wikipedia.org/wiki/Coral_dermatitis
2021-01-18T18:28:24
{"umls": ["C0413141"], "wikidata": ["Q5169523"]}
A number sign (#) is used with this entry because of evidence that retinitis pigmentosa-67 (RP67) is caused by homozygous mutation in the NEK2 gene (604043) on chromosome 1q32. One such family has been reported. Description Retinitis pigmentosa (RP) is the name given to a group of hereditary retinal conditions ...
RETINITIS PIGMENTOSA 67
c0035334
5,881
omim
https://www.omim.org/entry/615565
2019-09-22T15:51:37
{"doid": ["0110359"], "mesh": ["D012174"], "omim": ["615565"], "orphanet": ["791"]}
Allochiria Allochiria is most frequently associated with a lesion of the right parietal lobe (in yellow, at top) SpecialtyNeurology Allochiria is a neurological disorder in which the patient responds to stimuli presented to one side of their body as if the stimuli had been presented at the opposite side.[1] ...
Allochiria
c0422885
5,882
wikipedia
https://en.wikipedia.org/wiki/Allochiria
2021-01-18T18:44:41
{"mesh": ["D066190"], "umls": ["C0422885"], "wikidata": ["Q570126"]}
A number sign (#) is used with this entry because of evidence that brachydactyly-syndactyly syndrome is caused by heterozygous mutation in the HOXD13 gene (142989) on chromosome 2q31. One such family has been reported. Heterozygous mutation in HOXD13 can also cause brachydactyly and syndactyly in association with ol...
BRACHYDACTYLY-SYNDACTYLY SYNDROME
c1853137
5,883
omim
https://www.omim.org/entry/610713
2019-09-22T16:04:11
{"doid": ["0050689"], "mesh": ["C565193"], "omim": ["610713"], "orphanet": ["93409"], "synonyms": []}
Serratia infection SpecialtyInfectious disease Serratia infection refers to a disease caused by a species in the genus Serratia. The species involved is usually Serratia marcescens. It can cause nosocomial infections.[1] ## References[edit] 1. ^ Hejazi A, Falkiner FR (November 1997). "Serratia marcescens...
Serratia infection
c0085394
5,884
wikipedia
https://en.wikipedia.org/wiki/Serratia_infection
2021-01-18T18:42:49
{"mesh": ["D016868"], "wikidata": ["Q16935263"]}
Coloboma of superior eyelid is a rare developmental defect during embryogenesis characterized by a typically unilateral, partial or full-thickness, variably sized defect of the superior eyelid, ranging from a small notch to complete absence of the entire lid, which is commonly triangular in shape (with base at ey...
Coloboma of superior eyelid
c1863872
5,885
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=155884
2021-01-23T17:20:39
{"icd-10": ["Q10.3"], "synonyms": ["Superior palpebral coloboma"]}
## Summary ### Clinical characteristics. DYT-GNAL caused by a heterozygous GNAL pathogenic variant has been reported in more than 60 individuals to date. It is characterized by adult-onset isolated dystonia (i.e., no neurologic abnormalities other than tremor are evident on neurologic examination). The dystonia is ...
DYT-GNAL
c3554447
5,886
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK535640/
2021-01-18T21:31:14
{"synonyms": ["DYT25", "GNAL-Related Dystonia"]}
Clear-cell adenocarcinoma SpecialtyOncology/gynecology Clear-cell adenocarcinoma (CCA) of the vagina or cervix is a rare adenocarcinoma often linked to prenatal exposure to diethylstilbestrol (DES), a drug which was prescribed in high-risk pregnancy. ## Contents * 1 Presentation * 2 Diagnosis * 3 Treat...
Clear-cell adenocarcinoma of the vagina
None
5,887
wikipedia
https://en.wikipedia.org/wiki/Clear-cell_adenocarcinoma_of_the_vagina
2021-01-18T18:43:25
{"wikidata": ["Q5130801"]}
Classic congenital adrenal hyperplasia due to 21-hydroxylase deficiency (classic 21-OHD CAH) affects the adrenal glands which are responsible for producing specific hormones. There are two types of classic 21-OHD CAH, the salt-wasting form and the simple-virilizing form. Symptoms include abnormal development of t...
Classic congenital adrenal hyperplasia due to 21-hydroxylase deficiency
c2936858
5,888
gard
https://rarediseases.info.nih.gov/diseases/12665/classic-congenital-adrenal-hyperplasia-due-to-21-hydroxylase-deficiency
2021-01-18T18:01:17
{"mesh": ["C535979"], "orphanet": ["90794"], "synonyms": ["Classic 21-OHD CAH"]}
GRFoma is a type of pancreatic endocrine tumor (see this term) that hypersecretes growth hormone-releasing factor (GRF or GHRH) and that clinically resembles a pituitary adenoma (see this term) as patients present with acromegaly. In addition to the pancreas, this tumor can also occur in the lungs or small intestine,...
GRFoma
None
5,889
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=97261
2021-01-23T18:00:47
{"icd-10": ["E16.8"], "synonyms": ["GRF tumor", "Growth hormone releasing factor tumor"]}
A rare benign follicular hamartoma that develops primarily on the face of adults, with a particular predilection for the back of the nose, but also on the neck or scalp. It presents as a solitary hemispheric flesh-colored nodule with a central pore or black dot that may contain a tuft of hair. *[v]: View this temp...
Trichofolliculoma
c0334262
5,890
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=864
2021-01-23T17:22:25
{"gard": ["5263"], "mesh": ["C536553"], "umls": ["C0334262"]}
A rare, congenital disorder of glycosylation-related bone disorder characterized by hypotonia, severe developmental delay, intellectual disability, seizures, increased serum alkaline phosphatase, short distal phalanges with hypoplastic nails, and dysmorphic facial features. In some cases, cleft palate, megacolon, ano...
Hyperphosphatasia-intellectual disability syndrome
c1855923
5,891
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=247262
2021-01-23T18:33:53
{"mesh": ["C565495"], "omim": ["239300", "614207", "614749", "615716", "616025", "616809"], "umls": ["C1855923"], "synonyms": ["Mabry syndrome"]}
For a discussion of the genetic heterogeneity of quantitative trait loci (QTL) for mean platelet volume (MPV)/platelet count (PLT), see MPVCQTL1 (612573). Mapping Gieger et al. (2011) performed metaanalyses of genomewide association studies (GWAS) for MPV and PLT. Their analyses included 18,600 (13 studies, MPV) an...
MEAN PLATELET VOLUME/COUNT QUANTITATIVE TRAIT LOCUS 4
c3553339
5,892
omim
https://www.omim.org/entry/614644
2019-09-22T15:54:39
{"omim": ["614644"]}
Rare dental anomaly resulting in teeth having more than one cusp Talon cusp Other namesEagle's talon, dens evaginatus, interstitial cusp, tuberculated premolar, evaginated odontoma, supernumerary cusp[1] Periapical radiograph of talon cusp on a partially erupted upper left permanent maxillary incisor in an 8 yea...
Talon cusp
c0399357
5,893
wikipedia
https://en.wikipedia.org/wiki/Talon_cusp
2021-01-18T18:40:42
{"icd-9": ["520.2"], "icd-10": ["K00.2"], "wikidata": ["Q7680290"]}
Monographella nivalis var. nivalis Pink snow mold in a lawn in Brno Komín, Czech Republic Scientific classification Kingdom: Fungi Phylum: Ascomycota Class: Sordariomycetes Subclass: Xylariomycetidae Order: Xylariales Family: Incertae sedis Genus: Monographella Spec...
Fusarium patch
None
5,894
wikipedia
https://en.wikipedia.org/wiki/Fusarium_patch
2021-01-18T18:39:49
{"wikidata": ["Q7548416"]}
Abortion in Finland is legal and free of charge under a broad range of circumstances. By international standards, political controversy is mild, and incidence is low. ## Contents * 1 Legal framework * 2 History * 3 See also * 4 References ## Legal framework[edit] According to law, approval for an abor...
Abortion in Finland
None
5,895
wikipedia
https://en.wikipedia.org/wiki/Abortion_in_Finland
2021-01-18T18:30:26
{"wikidata": ["Q4668458"]}
Hemoglobin E (HbE) disease is a mild, inherited blood disorder characterized by an abnormal form of hemoglobin, called hemoglobin E. People with this condition may have very mild anemia, but the condition typically does not cause any symptoms. It is inherited in an autosomal recessive manner and is caused by a mu...
Hemoglobin E disease
c0238159
5,896
gard
https://rarediseases.info.nih.gov/diseases/2641/hemoglobin-e-disease
2021-01-18T18:00:07
{"umls": ["C0238159"], "orphanet": ["2133"], "synonyms": []}
Dissociative or psychogenic nonepileptic seizures (PNES) are involuntary episodes of movement, sensation, or behaviors (vocalizations, crying, and other expressions of emotion) that do not result from abnormal brain discharges. The seizures can look like any kind of epileptic seizure. They are somatic manifestations ...
Dissociative seizures
c0349245
5,897
gard
https://rarediseases.info.nih.gov/diseases/13028/dissociative-seizures
2021-01-18T18:00:51
{"synonyms": ["Psychogenic nonepileptic seizures", "Psychogenic seizures", "Pseudoseizures", "Functional seizures", "Non-epileptic attack disorder (NEAD)", "PNES"]}
Dyskeratosis congenita Other namesZinsser-Cole-Engman syndrome,[1][2]:570 Dyskeratosis congenital is inherited in an X-linked recessive manner SpecialtyMedical genetics Dyskeratosis congenita (DKC),also known as Zinsser-Engman-Cole syndrome, is a rare progressive congenital disorder with a highly variable ...
Dyskeratosis congenita
c0265965
5,898
wikipedia
https://en.wikipedia.org/wiki/Dyskeratosis_congenita
2021-01-18T18:59:31
{"gard": ["10905"], "mesh": ["D019871"], "umls": ["C0265965"], "orphanet": ["1775"], "wikidata": ["Q3709312"]}
Necrolytic migratory erythema Other namesNME Necrolytic migratory erythema in the gluteal area SpecialtyDermatology Necrolytic migratory erythema is a red, blistering rash that spreads across the skin. It particularly affects the skin around the mouth and distal extremities; but may also be found on th...
Necrolytic migratory erythema
c0221243
5,899
wikipedia
https://en.wikipedia.org/wiki/Necrolytic_migratory_erythema
2021-01-18T18:55:08
{"mesh": ["D058568"], "umls": ["C0221243"], "wikidata": ["Q776790"]}