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A number sign (#) is used with this entry because of evidence that a retinitis pigmentosa-deafness syndrome is due to mutation in the MTTS2 gene (590085). Clinical Features Kumar-Singh et al. (1993) reported an extensive Irish kindred segregating retinitis pigmentosa and deafness. Affected members usually presented...
RETINITIS PIGMENTOSA-DEAFNESS SYNDROME
c0271097
6,400
omim
https://www.omim.org/entry/500004
2019-09-22T16:16:59
{"doid": ["0110829"], "mesh": ["D052245"], "omim": ["500004"], "orphanet": ["886", "231183"], "synonyms": ["Alternative titles", "RETINITIS PIGMENTOSA 8, FORMERLY", "RETINITIS PIGMENTOSA 21, FORMERLY"]}
A number sign (#) is used with this entry because progressive familial intrahepatic cholestasis-4 (PFIC4) is caused by homozygous or compound heterozygous mutation in the TJP2 gene (607709) on chromosome 9q21. For a phenotypic description and a discussion of genetic heterogeneity of progressive familial intrahepatic...
CHOLESTASIS, PROGRESSIVE FAMILIAL INTRAHEPATIC, 4
c0268312
6,401
omim
https://www.omim.org/entry/615878
2019-09-22T15:50:46
{"doid": ["0070224"], "omim": ["615878"], "orphanet": ["172", "79304", "480483"]}
Prion diseases are a group of rare transmissible disorders characterized by progressive debilitating neurological manifestations due to spongiform changes with an invariably fatal course. The disorders all involve accumulation of an abnormal prion protein in the central nervous system with no specific immunological r...
Human prion disease
c0162534
6,402
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=56970
2021-01-23T17:27:03
{"mesh": ["D017096"], "umls": ["C0162534"], "icd-10": ["A81.0", "A81.1", "A81.8", "A81.9"], "synonyms": ["TSE", "Transmissible spongiform encephalopathy"]}
A rare frontonasal dysplasia characterized by median cleft of the upper lip (MCL), midline polyps of the facial skin, nasal mucosa, and pericallosal lipomas. Hypertelorism with ocular anomalies are also observed, generally with normal neuropsychological development. ## Epidemiology Pai syndrome (PS) has been report...
Pai syndrome
c1835087
6,403
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1993
2021-01-23T18:10:11
{"gard": ["3439"], "mesh": ["C536135"], "omim": ["155145"], "umls": ["C1835087"], "icd-10": ["Q87.8"], "synonyms": ["Median cleft of the upper lip-corpus callosum lipoma-midline facial cutaneous polyps syndrome"]}
Glycogen storage disease type I (also known as GSDI or von Gierke disease) is an inherited disorder caused by the buildup of a complex sugar called glycogen in the body's cells. The accumulation of glycogen in certain organs and tissues, especially the liver, kidneys, and small intestines, impairs their ability to fu...
Glycogen storage disease type I
c0017920
6,404
medlineplus
https://medlineplus.gov/genetics/condition/glycogen-storage-disease-type-i/
2021-01-27T08:25:35
{"gard": ["7864", "2515"], "mesh": ["D005953"], "omim": ["232200", "232220"], "synonyms": []}
Hemangioma Hemangioma SpecialtyOncology A hemangioma or haemangioma is a usually benign vascular tumor derived from blood vessel cell types. The most common form is infantile hemangioma, known colloquially as a "strawberry mark", most commonly seen on the skin at birth or in the first weeks of life. A hemang...
Hemangioma
c0018916
6,405
wikipedia
https://en.wikipedia.org/wiki/Hemangioma
2021-01-18T18:30:47
{"mesh": ["D006391"], "umls": ["C0018916"], "wikidata": ["Q861028"]}
Distal muscular dystrophy Other namesDistal myopathy DYSF SpecialtyNeurology Distal muscular dystrophy is a group of disorders characterized by onset in the hands or feet. Many types involve dysferlin, but it has been suggested that not all cases do.[1] ## Contents * 1 Types * 2 Cause * 3 Diagn...
Distal muscular dystrophy
c1864706
6,406
wikipedia
https://en.wikipedia.org/wiki/Distal_muscular_dystrophy
2021-01-18T18:49:33
{"mesh": ["C566445", "D049310"], "umls": ["C1864706"], "icd-9": ["359.1"], "orphanet": ["5448", "59135", "63273", "599", "399096"], "wikidata": ["Q5282843"]}
A number sign (#) is used with this entry because of evidence that autosomal recessive limb-girdle muscular dystrophy-23 (LGMDR23) is caused by homozygous or compound heterozygous mutation in the LAMA2 gene (156225) on chromosome 6q22. Biallelic mutation in the LAMA2 gene can also cause congenital muscular dystr...
MUSCULAR DYSTROPHY, LIMB-GIRDLE, AUTOSOMAL RECESSIVE 23
c1263858
6,407
omim
https://www.omim.org/entry/618138
2019-09-22T15:43:31
{"mesh": ["C537384"], "omim": ["618138"], "orphanet": ["258"], "genereviews": ["NBK97333"]}
For the scientific journals, see Carcinogenesis (journal) and Oncogenesis (journal). The formation of cancer Cancers and tumors are caused by a series of mutations. Each mutation alters the behavior of the cell somewhat. Carcinogenesis, also called oncogenesis or tumorigenesis, is the formation of a cancer, whereb...
Carcinogenesis
c0596263
6,408
wikipedia
https://en.wikipedia.org/wiki/Carcinogenesis
2021-01-18T18:52:00
{"mesh": ["D063646"], "wikidata": ["Q1637543"]}
A rare disorder of fatty acid oxidation characterized by a wide clinical spectrum ranging from severe neonatal manifestations including cardiomyopathy, hypoglycemia, metabolic acidosis, skeletal myopathy and neuropathy, liver disease and death to a mild phenotype with peripheral polyneuropathy, episodic rhabdomyolysi...
Mitochondrial trifunctional protein deficiency
c1969443
6,409
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=746
2021-01-23T17:42:21
{"gard": ["3684"], "mesh": ["C566945", "D024741"], "omim": ["609015"], "umls": ["C0342786", "C1969443"], "icd-10": ["G71.3"], "synonyms": ["TFP deficiency", "TFPD"]}
Alpha-1 antitrypsin deficiency (AATD) is an inherited disease that causes an increased risk of having chronic obstructive pulmonary disease (COPD), liver disease, skin problems (panniculitis), and inflammation of the blood vessels (vasculitis). Lung (pulmonary) problems almost always occur in adults, whereas liver an...
Alpha-1 antitrypsin deficiency
c0221757
6,410
gard
https://rarediseases.info.nih.gov/diseases/5784/alpha-1-antitrypsin-deficiency
2021-01-18T18:02:11
{"mesh": ["D019896"], "omim": ["613490"], "umls": ["C0221757"], "orphanet": ["60"], "synonyms": ["AAT deficiency", "A1AT deficiency", "AATD", "Alpha 1 antitrypsin deficiency"]}
CLOVE syndrome is characterized by Congenital Lipomatous Overgrowth, progressive, complex and mixed truncal Vascular malformations, and Epidermal nevi. ## Clinical description Patients also present with disproportionate fat distribution. CLOVE syndrome may be associated with varying degrees of scoliosis and enlarge...
CLOVES syndrome
c2752042
6,411
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=140944
2021-01-23T17:30:32
{"gard": ["10939"], "mesh": ["C567863"], "omim": ["612918"], "icd-10": ["Q87.3"], "synonyms": ["Congenital lipomatous overgrowth-vascular malformation-epidermal nevi-skeletal anomaly syndrome", "Congenital lipomatous overgrowth-vascular malformation-epidermal nevi-spinal anomaly syndrome"]}
Not to be confused with Central hypoventilation syndrome. A sleep-related disorder in which the effort to breathe is diminished Central sleep apnea Other namesprimary alveolar hypoventilation, alveolar hypoventilation secondary to neurologic disease, idiopathic acquired central hypoventilation syndrome Specialt...
Central sleep apnea
c0520680
6,412
wikipedia
https://en.wikipedia.org/wiki/Central_sleep_apnea
2021-01-18T19:05:09
{"mesh": ["D020182"], "umls": ["C0520680"], "wikidata": ["Q3620651"]}
AREDYLD syndrome AREDYLD syndrome is inherited in an autosomal recessive manner AREDYLD stands for acral renal ectodermal dysplasia lipoatrophic diabetes. AREDLYD is categorized as a rare disease, meaning it affects fewer than 200,000 people in the American population at any given time. It was characteriz...
AREDYLD syndrome
c0342280
6,413
wikipedia
https://en.wikipedia.org/wiki/AREDYLD_syndrome
2021-01-18T18:33:52
{"gard": ["8509"], "mesh": ["C537427"], "umls": ["C0342280"], "orphanet": ["1133"], "wikidata": ["Q4653653"]}
## Summary ### Clinical characteristics. Spinocerebellar ataxia type 6 (SCA6) is characterized by adult-onset, slowly progressive cerebellar ataxia, dysarthria, and nystagmus. The age of onset ranges from 19 to 73 years; mean age of onset is between 43 and 52 years. Initial symptoms are gait unsteadiness, stumb...
Spinocerebellar Ataxia Type 6
c0752124
6,414
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1140/
2021-01-18T20:54:58
{"mesh": ["D020754"], "synonyms": ["SCA6"]}
Ictal asystole is a rare occurrence for patients that have temporal lobe epilepsy.[1] It can often be identified by loss of muscle tone or the presence of bilateral asymmetric jerky limb movements during a seizure, although ECG monitoring is necessary to provide a firm result.[2] Ictal asystole and Ictal bradycardia ...
Ictal asystole
None
6,415
wikipedia
https://en.wikipedia.org/wiki/Ictal_asystole
2021-01-18T19:05:56
{"wikidata": ["Q5986769"]}
A rare mitochondrial disease characterized by bilateral auditory neuropathy and optic atrophy. Patients present hearing and visual impairment in the first or second decade of life, while psychomotor development is normal. Bilateral retinitis pigmentosa has been reported in association. *[v]: View this template...
Auditory neuropathy-optic atrophy syndrome
c4521678
6,416
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=542585
2021-01-23T17:09:36
{"omim": ["617717"]}
Chemical eye injury Other namesChemical burns to the eye An alkali burn to the human cornea can cause ocular surface failure with neovascularisation, opacification and blindness resulting from LESC deficiency. SpecialtyOphthalmology Chemical eye injury are due to either an acidic or alkali substance gettin...
Chemical eye injury
c1096387
6,417
wikipedia
https://en.wikipedia.org/wiki/Chemical_eye_injury
2021-01-18T18:46:09
{"icd-10": ["T26.9"], "wikidata": ["Q5090456"]}
A number sign (#) is used with this entry because of evidence that glycogen storage disease XIII (GSD13) is caused by compound heterozygous mutation in the ENO3 gene (131370), which encodes beta-enolase, on chromosome 17p13. One such patient has been reported. Clinical Features Comi et al. (2001) described a 47...
GLYCOGEN STORAGE DISEASE XIII
c2752027
6,418
omim
https://www.omim.org/entry/612932
2019-09-22T16:00:20
{"mesh": ["C567861"], "omim": ["612932"], "orphanet": ["99849"], "synonyms": ["Alternative titles", "GSD XIII", "ENOLASE 3 DEFICIENCY", "ENOLASE-BETA DEFICIENCY"]}
## Summary ### Clinical characteristics. Epimerase deficiency galactosemia (GALE deficiency galactosemia) is a continuum comprising three forms: * Generalized. Enzyme activity is profoundly decreased in all tissues tested. * Peripheral. Enzyme activity is deficient in red blood cells (RBC) and circulating whi...
Epimerase Deficiency Galactosemia
c0268151
6,419
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK51671/
2021-01-18T21:28:31
{"mesh": ["D005693"], "synonyms": ["GALE Deficiency", "Galactosemia Type III", "UDP-Galactose-4'-Epimerase Deficiency"]}
A rare, potentially lethal intoxication characterized by life-threatening arrhythmias (sinus tachycardias, premature ventricular contractions, ventricular arrhythmias), anticholinergic toxidrome (mydriasis, dry mucous membrane, tachycardia, hypertension), central nervous system toxicity (lethargy, coma, myoclonic jer...
Acute tricyclic antidepressant poisoning
None
6,420
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=43117
2021-01-23T18:32:41
{"icd-10": ["T43.0"]}
A number sign (#) is used with this entry because of evidence that spinocerebellar ataxia-43 (SCA43) is caused by heterozygous mutation in the MME gene (120520) on chromosome 3q25. One such family has been reported. Description Spinocerebellar ataxia-43 is an autosomal dominant, slowly progressive neurologic disord...
SPINOCEREBELLAR ATAXIA 43
c4310763
6,421
omim
https://www.omim.org/entry/617018
2019-09-22T15:47:14
{"omim": ["617018"]}
A number sign (#) is used with this entry because osteogenesis imperfecta type VII (OI7) is caused by homozygous or compound heterozygous mutation in the CRTAP gene (605497) on chromosome 3p22. Description Osteogenesis imperfecta is a connective tissue disorder characterized by bone fragility and low bone mass. OI ...
OSTEOGENESIS IMPERFECTA, TYPE VII
c0268362
6,422
omim
https://www.omim.org/entry/610682
2019-09-22T16:04:13
{"doid": ["0110337"], "mesh": ["C536044"], "omim": ["610682"], "orphanet": ["216812", "216804", "216820", "666"], "synonyms": ["Alternative titles", "OI, TYPE VII", "OSTEOGENESIS IMPERFECTA, TYPE IIB, FORMERLY"]}
A number sign (#) is used with this entry because of evidence that a reduced level of plasma LDL cholesterol is caused by heterozygous mutation in the LIMA1 gene (608364) on chromosome 12q13. Description LDLCQ8 is a quantitative trait affecting LDL cholesterol levels that is effected through the LIMA1 gene, which h...
LOW DENSITY LIPOPROTEIN CHOLESTEROL LEVEL QUANTITATIVE TRAIT LOCUS 8
None
6,423
omim
https://www.omim.org/entry/618079
2019-09-22T15:43:49
{"omim": ["618079"]}
This article has an unclear citation style. The references used may be made clearer with a different or consistent style of citation and footnoting. (October 2017) (Learn how and when to remove this template message) Neuromuscular junction disease SpecialtyNeurology Neuromuscular junction disease is a med...
Neuromuscular junction disease
c0751950
6,424
wikipedia
https://en.wikipedia.org/wiki/Neuromuscular_junction_disease
2021-01-18T18:45:19
{"mesh": ["D020511"], "umls": ["C0751950"], "orphanet": ["98491"], "wikidata": ["Q7002430"]}
Late-onset junctional epidermolysis bullosa is a subtype of junctional epidermolysis bullosa (JEB, see this term) occurring in childhood or young adulthood. ## Epidemiology Prevalence is unknown. 22 patients in 12 families have been reported to date. ## Clinical description Blistering occurs at first around n...
Late-onset junctional epidermolysis bullosa
c4304724
6,425
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=79406
2021-01-23T18:44:23
{"gard": ["12921"], "icd-10": ["Q81.8"], "synonyms": ["Epidermolysis bullosa progressiva", "JEB-lo", "Late-onset JEB"]}
In 4 generations of a family in Germany, Hamann et al. (1992) observed the combination of multiple exostoses of typical nature (133700) in association with spastic tetraparesis. There were no exostoses in the spine or cranium to account for the tetraspastic disorder. The pedigree pattern was consistent with autosomal...
MULTIPLE EXOSTOSES WITH SPASTIC TETRAPARESIS
c1834724
6,426
omim
https://www.omim.org/entry/158345
2019-09-22T16:37:58
{"mesh": ["C563566"], "omim": ["158345"]}
A number sign (#) is used with this entry because of evidence that Fontaine progeroid syndrome (FPS) is caused by heterozygous mutation in the SLC25A24 gene (608744) on chromosome 1p36. Description Fontaine progeroid syndrome is characterized by prenatal and postnatal growth retardation, decreased subcutaneous fat ...
FONTAINE PROGEROID SYNDROME
c2931653
6,427
omim
https://www.omim.org/entry/612289
2019-09-22T16:01:53
{"mesh": ["C537886"], "omim": ["612289"], "orphanet": ["2963", "2095"], "synonyms": ["Alternative titles", "GORLIN-CHAUDHRY-MOSS SYNDROME", "PROGEROID SYNDROME, CONGENITAL, PETTY TYPE", "CRANIOFACIAL DYSOSTOSIS, HYPERTRICHOSIS, HYPOPLASIA OF LABIA MAJORA, DENTAL AND EYE ANOMALIES, PATENT DUCTUS ARTERIOSUS, AND NORMAL I...
Keratitis-ichthyosis-deafness (KID) syndrome is characterized by eye problems, skin abnormalities, and hearing loss. People with KID syndrome usually have keratitis, which is inflammation of the front surface of the eye (the cornea). The keratitis may cause pain, increased sensitivity to light (photophobia), abnorma...
Keratitis-ichthyosis-deafness syndrome
c0265336
6,428
medlineplus
https://medlineplus.gov/genetics/condition/keratitis-ichthyosis-deafness-syndrome/
2021-01-27T08:25:31
{"gard": ["2946", "3113"], "mesh": ["C536168"], "omim": ["148210", "242150"], "synonyms": []}
Fetal valproate syndrome (FVS) may occur if a developing baby is exposed to valproic acid during pregnancy. Valproic acid, also known as valproate, is a medication that is often used to treat epilepsy, bipolar disorder, and migraines. Many babies who are exposed to this medication during pregnancy are born healthy wi...
Fetal valproate syndrome
c0236026
6,429
gard
https://rarediseases.info.nih.gov/diseases/5447/fetal-valproate-syndrome
2021-01-18T18:00:29
{"mesh": ["C536525"], "omim": ["609442"], "orphanet": ["1906"], "synonyms": ["Valproic acid embryopathy", "Susceptibility to valproate embryopathy", "FVS", "Fetal valproic acid syndrome"]}
A number sign (#) is used with this entry because of evidence that peripheral neuropathy, myopathy, hoarseness, and hearing loss (PNMHH) is caused by heterozygous mutation in the MYH14 gene (608568) on chromosome 19q13. One such family has been reported. Clinical Features Choi et al. (2011) reported a large 5-gener...
PERIPHERAL NEUROPATHY, MYOPATHY, HOARSENESS, AND HEARING LOSS
c3280556
6,430
omim
https://www.omim.org/entry/614369
2019-09-22T15:55:39
{"omim": ["614369"], "orphanet": ["397744"], "synonyms": ["Peripheral neuropathy-myopathy-hoarseness-deafness syndrome"]}
A number sign (#) is used with this entry because spastic paraplegia-2 can be caused by mutation in the myelin proteolipid protein gene (PLP1; 300401) and is therefore allelic to Pelizaeus-Merzbacher disease (PMD; 312080). Description The hereditary spastic paraplegias (SPG) are a group of clinically and geneticall...
SPASTIC PARAPLEGIA 2, X-LINKED
c1839264
6,431
omim
https://www.omim.org/entry/312920
2019-09-22T16:17:15
{"doid": ["0110773"], "mesh": ["C536857"], "omim": ["312920"], "orphanet": ["99015"], "synonyms": ["Alternative titles", "SPPX2"], "genereviews": ["NBK1182"]}
For a general discussion of susceptibility to infection by Mycobacterium tuberculosis, see 607948. Bellamy et al. (2000) conducted a 2-stage genomewide linkage study of 136 African families to search for regions of the human genome containing tuberculosis susceptibility genes. They used sib-pair families that contai...
MYCOBACTERIUM TUBERCULOSIS, SUSCEPTIBILITY TO, X-LINKED
c1866629
6,432
omim
https://www.omim.org/entry/300259
2019-09-22T16:20:36
{"omim": ["300259"], "synonyms": ["Alternative titles", "MTBSX"]}
The endemic nephropathy commonly called 'Balkan' is more properly called Danubian. It occurs in a relatively restricted rural area of Roumania, Bulgaria and Yugoslavia near the Danubian Iron Gates. Clinical, epidemiologic and laboratory investigations are thought to have excluded selected forms (although not necessar...
DANUBIAN ENDEMIC FAMILIAL NEPHROPATHY
c0004698
6,433
omim
https://www.omim.org/entry/124100
2019-09-22T16:42:35
{"doid": ["3052"], "mesh": ["D001449"], "omim": ["124100"], "icd-10": ["N15.0"], "synonyms": ["Alternative titles", "DEFN", "BALKAN ENDEMIC NEPHROPATHY", "NEPHROPATHIA EPIDEMICA"]}
A number sign (#) is used with this entry because of evidence that Joubert syndrome-25 (JBTS25) is caused by homozygous or compound heterozygous mutation in the CEP104 gene (616690) on chromosome 1p36. Description Joubert syndrome-25 is an autosomal recessive ciliopathy characterized by delayed psychomotor developm...
JOUBERT SYNDROME 25
c4084842
6,434
omim
https://www.omim.org/entry/616781
2019-09-22T15:47:56
{"doid": ["0110994"], "omim": ["616781", "213300"], "orphanet": ["475"], "synonyms": ["CPD IV", "Cerebelloparenchymal disorder IV", "Classic Joubert syndrome", "Joubert syndrome type A", "Joubert-Boltshauser syndrome", "Pure Joubert syndrome"], "genereviews": ["NBK1325"]}
A rare glial tumor originating from pituicytes, the specialized glial cells of the neurohypophysis, characterized by a sellar or suprasellar mass manifesting with clinical signs secondary to mass effect. Typical manifestations are visual disturbances, headaches, and hypopituitarism. Pituicytomas are low-grade tumors,...
Pituicytoma
c2986550
6,435
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=251623
2021-01-23T17:07:41
{"umls": ["C2986550"], "icd-10": ["C71.9"]}
A number sign (#) is used with this entry because autosomal recessive nonsyndromic mental retardation-3 can be caused by homozygous mutation in the CC2D1A gene (610055). Clinical Features Basel-Vanagaite et al. (2003) studied nonsyndromic mental retardation in 4 consanguineous families of Israeli-Arab origin with 1...
MENTAL RETARDATION, AUTOSOMAL RECESSIVE 3
c1838023
6,436
omim
https://www.omim.org/entry/608443
2019-09-22T16:07:51
{"doid": ["0060308"], "mesh": ["C563929"], "omim": ["608443"], "orphanet": ["88616"], "synonyms": ["AR-NSID", "NS-ARID"]}
## Summary ### Clinical characteristics. KCNQ2-related disorders represent a continuum of overlapping neonatal epileptic phenotypes caused by a heterozygous pathogenic variant in KCNQ2. The clinical features of KCNQ2-related disorders range from KCNQ2-related benign familial neonatal epilepsy (KCNQ2-BFNE) at the mi...
KCNQ2-Related Disorders
None
6,437
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK32534/
2021-01-18T21:16:41
{"synonyms": []}
A number sign (#) is used with this entry because immunodeficiency-31A (IMD31A) is caused by heterozygous mutation in the STAT1 gene (600555) on chromosome 2q32. Immunodeficiency-31B (IMD31B; 613796), an autosomal recessive disorder, and immunodeficiency-31C (IMD31C; 614162), an autosomal dominant disorder, are alle...
IMMUNODEFICIENCY 31A
c4013950
6,438
omim
https://www.omim.org/entry/614892
2019-09-22T15:53:48
{"omim": ["614892"], "orphanet": ["319595"], "synonyms": ["MSMD due to partial STAT1 deficiency", "Mendelian susceptibility to mycobacterial diseases due to partial signal transducer and activator of transcription 1 deficiency", "IMMUNODEFICIENCY 31A, MYCOBACTERIOSIS, AUTOSOMAL DOMINANT", "Alternative titles", "MSMD du...
A number sign (#) is used with this entry because, as reviewed in 168600, parkinsonism is a conspicuous and even predominant feature of some of the various neurologic disorders and, as reviewed here, mitochondrial mutations may be involved. The electron transport chain (ETC) of mitochondria is the last step in cellu...
PARKINSON DISEASE, MITOCHONDRIAL
c1838867
6,439
omim
https://www.omim.org/entry/556500
2019-09-22T16:16:46
{"mesh": ["C564015"], "omim": ["556500"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Myoclonic astatic epilepsy" – news · newspapers · books · scholar · JSTOR (March 2018) (Learn how and when to remove th...
Myoclonic astatic epilepsy
c4085238
6,440
wikipedia
https://en.wikipedia.org/wiki/Myoclonic_astatic_epilepsy
2021-01-18T19:05:34
{"gard": ["2169"], "umls": ["C4085238"], "orphanet": ["1942"], "wikidata": ["Q6947909"]}
A rare congenital anomaly of the inferior vena cava characterized by complete interruption of the vessel in which no direct continuity exists between the inferior vena cava and the azygos/hemiazygos system. Clinical manifestations depend on the variant drainage patterns or collaterals and include lower extremity ...
Inferior vena cava interruption without azygos continuation
None
6,441
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=99123
2021-01-23T17:45:48
{"icd-10": ["Q26.8"], "synonyms": ["IVC interruption", "Inferior caval vein interruption"]}
Serine-deficiency syndrome is a very rare infantile-onset potentially treatable neurometabolic disorder characterized clinically by microcephaly, neurodevelopmental disorders and seizures. Three serine-deficiency syndromes have been described: 3-phosphoglycerate dehydrogenase (3-PGDH) deficiency, 3-phosphoserine phos...
Neurometabolic disorder due to serine deficiency
None
6,442
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=35705
2021-01-23T18:02:25
{"icd-10": ["E72.8"], "synonyms": ["Serine deficiency"]}
## Description The CYP1A2 gene encodes a P450 enzyme involved in O-deethylation of phenacetin. It is 1 of several forms of cytochrome P-450 that have been purified to electrophoretic homogeneity from human liver microsomes (Guengerich et al., 1986). P1-450 (CYP1A1; 108330) and P3-450 are 2 members of the dioxin-ind...
CYTOCHROME P450, SUBFAMILY I, POLYPEPTIDE 2
c1852336
6,443
omim
https://www.omim.org/entry/124060
2019-09-22T16:42:36
{"omim": ["124060"], "synonyms": ["Alternative titles", "CYTOCHROME P-450, AROMATIC COMPOUND-INDUCIBLE", "DIOXIN-INDUCIBLE P3-450"]}
Not to be confused with Carney's triad. Carney complex Other namesLAMB syndrome SpecialtyOncology, cardiology Carney complex and its subsets LAMB syndrome[1] and NAME syndrome[1] are autosomal dominant conditions comprising myxomas of the heart and skin, hyperpigmentation of the skin (lentiginosis), and end...
Carney complex
c2607929
6,444
wikipedia
https://en.wikipedia.org/wiki/Carney_complex
2021-01-18T18:52:57
{"gard": ["1119"], "mesh": ["D056733"], "umls": ["C2607929"], "orphanet": ["1359"], "wikidata": ["Q1044007"]}
A number sign (#) is used with this entry because Ehlers-Danlos syndrome kyphoscoliotic type 1 (EDSKSCL1), previously designated EDS6, is caused by homozygous or compound heterozygous mutation in the gene encoding lysyl hydroxylase (PLOD1; 153454) on chromosome 1p36. Description The Ehlers-Danlos syndromes (EDS...
EHLERS-DANLOS SYNDROME, KYPHOSCOLIOTIC TYPE, 1
c0268342
6,445
omim
https://www.omim.org/entry/225400
2019-09-22T16:28:23
{"mesh": ["C536198"], "omim": ["225400"], "orphanet": ["1900"], "synonyms": ["Alternative titles", "EHLERS-DANLOS SYNDROME, TYPE VI", "EDS VI", "EHLERS-DANLOS SYNDROME, OCULAR-SCOLIOTIC TYPE", "NEVO SYNDROME", "EHLERS-DANLOS SYNDROME, TYPE VIA, FORMERLY"], "genereviews": ["NBK1462"]}
This article includes a list of references, related reading or external links, but its sources remain unclear because it lacks inline citations. Please help to improve this article by introducing more precise citations. (May 2018) (Learn how and when to remove this template message) Rose spots on the chest of a ...
Rose spots
c1274375
6,446
wikipedia
https://en.wikipedia.org/wiki/Rose_spots
2021-01-18T19:01:29
{"umls": ["C1274375"], "wikidata": ["Q3941500"]}
Sohval and Soffer (1953) described 2 brothers who were identically affected with mental retardation, multiple skeletal anomalies, and hypogonadism. The testicular histopathology was distinctive. All the seminiferous tubules were involved by one of two distinct processes: true germinal aplasia or complete fibrosis, wi...
HYPOGONADISM, MALE, WITH MENTAL RETARDATION AND SKELETAL ANOMALIES
c2931285
6,447
omim
https://www.omim.org/entry/307500
2019-09-22T16:18:10
{"mesh": ["C536679"], "omim": ["307500"], "orphanet": ["2234"]}
A number sign (#) is used with this entry because the lethal neonatal form of carnitine palmitoyltransferase II (CPT2) deficiency is caused by homozygous or compound heterozygous mutation in the CPT2 gene (600650) on chromosome 1p32. Description Carnitine palmitoyltransferase II deficiency is an inherited disorder ...
CARNITINE PALMITOYLTRANSFERASE II DEFICIENCY, LETHAL NEONATAL
c0342790
6,448
omim
https://www.omim.org/entry/608836
2019-09-22T16:07:06
{"doid": ["0060235"], "mesh": ["C535589"], "omim": ["608836"], "orphanet": ["157", "228308"], "synonyms": ["Alternative titles", "CARNITINE PALMITOYLTRANSFERASE II DEFICIENCY, NEONATAL", "CARNITINE PALMITOYLTRANSFERASE II DEFICIENCY, ANTENATAL", "CPT II DEFICIENCY, LETHAL NEONATAL", "CPT2 DEFICIENCY, LETHAL NEONATAL"],...
Not to be confused with Dysphasia. Dysphagia SpecialtyGastroenterology CausesEsophageal cancer Esophagitis Stomach cancer Dysphagia is difficulty in swallowing.[1][2] Although classified under "symptoms and signs" in ICD-10,[3] in some contexts it is classified as a condition in its own right.[4][5][6] It ...
Dysphagia
c0011168
6,449
wikipedia
https://en.wikipedia.org/wiki/Dysphagia
2021-01-18T18:52:13
{"mesh": ["D003680"], "icd-9": ["787.2", "438.82"], "icd-10": ["R13"], "wikidata": ["Q623289"]}
Congenital nephrotic syndrome is a kidney condition that begins in infancy and typically leads to irreversible kidney failure (end-stage renal disease) by early childhood. Children with congenital nephrotic syndrome begin to have symptoms of the condition between birth and 3 months. The features of congenital ne...
Congenital nephrotic syndrome
c0403399
6,450
medlineplus
https://medlineplus.gov/genetics/condition/congenital-nephrotic-syndrome/
2021-01-27T08:25:04
{"gard": ["1500"], "mesh": ["C535761"], "omim": ["256300", "600995"], "synonyms": []}
Hidrotic ectodermal dysplasia, Halal type is a form of ectodermal dysplasia syndrome (see this term) characterized by trichodysplasia, with absent eyebrows and eyelashes, onychodysplasia, mild retrognathia, abnormal dermatoglyphics (excess of whorls on fingertips, radial loop on finger, hypothenar pattern), intellect...
Hidrotic ectodermal dysplasia, Halal type
c2930953
6,451
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1809
2021-01-23T18:35:02
{"gard": ["280"], "mesh": ["C535621"], "umls": ["C2930953"], "icd-10": ["Q82.8"], "synonyms": ["Halal-Setton-Wang syndrome", "Trichodysplasia-abnormal dermatoglyphics-intellectual disability syndrome"]}
Maternal uniparental disomy of chromosome 6 is an uniparental disomy of maternal origin characterized by intrauterine growth retardation. Homozygosity for a recessive disease mutation for which only a mother is a carrier may lead to other phenotypes. *[v]: View this template *[t]: Discuss this template *[e]: E...
Maternal uniparental disomy of chromosome 6
c4707720
6,452
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=96181
2021-01-23T18:01:39
{"icd-10": ["Q99.8"], "synonyms": ["UPD(6)mat"]}
Infestation of parasitic maggots Myiasis Other namesFlystrike, blowfly strike, fly-blown Cutaneous myiasis in the shoulder of a human Pronunciation * /ˈmaɪ.əsɪs/ or /maɪˈaɪ.əsɪs/ SpecialtyInfectious disease Myiasis is the parasitic infestation of the body of a live animal by fly larvae (maggots)...
Myiasis
c0027030
6,453
wikipedia
https://en.wikipedia.org/wiki/Myiasis
2021-01-18T18:58:30
{"mesh": ["D009198"], "umls": ["C0027030"], "orphanet": ["75110"], "wikidata": ["Q304601"]}
A number sign (#) is used with this entry because generalized glucocorticoid resistance (GCCR) is caused by heterozygous mutation in the glucocorticoid receptor gene (NR3C1, GCCR; 138040) on chromosome 5q31. Description Generalized glucocorticoid resistance is an autosomal dominant disease characterized by incr...
GLUCOCORTICOID RESISTANCE, GENERALIZED
c1841972
6,454
omim
https://www.omim.org/entry/615962
2019-09-22T15:50:32
{"mesh": ["C564221"], "omim": ["615962"], "orphanet": ["786"], "synonyms": ["Alternative titles", "GLUCOCORTICOID RECEPTOR DEFICIENCY", "GCCR DEFICIENCY", "GCR DEFICIENCY", "GRL DEFICIENCY", "CORTISOL RESISTANCE FROM GLUCOCORTICOID RECEPTOR DEFECT"]}
Neurodegenerative disease This article is about the neurodegenerative disease. For other uses, see ALS (disambiguation). Amyotrophic lateral sclerosis (ALS) Other namesLou Gehrig's disease; Charcot's disease; motor neurone disease (MND)[1] An MRI of the brain with increased T2 signal in the posterior part...
Amyotrophic lateral sclerosis
c0002736
6,455
wikipedia
https://en.wikipedia.org/wiki/Amyotrophic_lateral_sclerosis
2021-01-18T18:58:10
{"gard": ["5786"], "mesh": ["D000690"], "umls": ["C0002736"], "orphanet": ["803"], "wikidata": ["Q206901"]}
Amblyaudia (amblyos- blunt; audia-hearing) is a term coined by Dr. Deborah Moncrieff to characterize a specific pattern of performance from dichotic listening tests. Dichotic listening tests are widely used to assess individuals for binaural integration, a type of auditory processing skill. During the tests, indi...
Amblyaudia
None
6,456
wikipedia
https://en.wikipedia.org/wiki/Amblyaudia
2021-01-18T18:32:00
{"wikidata": ["Q4741549"]}
"IMID" redirects here. For IMiD, see immunomodulatory imide drug. An immune-mediated inflammatory disease (IMID) is any of a group of conditions or diseases that lack a definitive etiology, but which are characterized by common inflammatory pathways leading to inflammation, and which may result from, or be triggered...
Immune-mediated inflammatory diseases
None
6,457
wikipedia
https://en.wikipedia.org/wiki/Immune-mediated_inflammatory_diseases
2021-01-18T19:05:00
{"wikidata": ["Q6005412"]}
Cockayne syndrome is a rare disease which causes short stature, premature aging (progeria), severe photosensitivity, and moderate to severe learning delay. This syndrome also includes failure to thrive in the newborn, very small head (microcephaly), and impaired nervous system development. Other symptoms may include ...
Cockayne syndrome type III
c0751037
6,458
gard
https://rarediseases.info.nih.gov/diseases/1417/cockayne-syndrome-type-iii
2021-01-18T18:01:15
{"mesh": ["D003057"], "omim": ["216411"], "umls": ["C0751037"], "orphanet": ["90324"], "synonyms": ["Cockayne syndrome type C", "Cockayne syndrome type 3"]}
Autoimmune polyendocrinopathy-candidiasis-ectodermal dystrophy (APECED) is an inherited condition that affects many of the body's organs. It is one of many autoimmune diseases, which are disorders that occur when the immune system malfunctions and attacks the body's own tissues and organs by mistake. In most cases, ...
Autoimmune polyendocrinopathy-candidiasis-ectodermal dystrophy
c1855869
6,459
medlineplus
https://medlineplus.gov/genetics/condition/autoimmune-polyendocrinopathy-candidiasis-ectodermal-dystrophy/
2021-01-27T08:24:33
{"gard": ["8466"], "mesh": ["C538275"], "omim": ["240300"], "synonyms": []}
Fitzsimmons et al. (1988) presented a family in which at least 4 persons had evidence of an inherited disorder manifested by variable spastic paraplegia, bilateral sensorineural deafness, intellectual retardation, and progressive nephropathy. Focal segmental proliferative lesions with sclerosis suggestive of mesangia...
SPASTIC PARAPLEGIA, SENSORINEURAL DEAFNESS, MENTAL RETARDATION, AND PROGRESSIVE NEPHROPATHY
c2931667
6,460
omim
https://www.omim.org/entry/182690
2019-09-22T16:34:46
{"mesh": ["C537937"], "omim": ["182690"], "orphanet": ["2820"]}
Flystrike in sheep is a myiasis condition, in which domestic sheep are infected by one of several species of flies which are external parasites of sheep. Sheep are particularly susceptible to flystrike because their thick wool, if sufficiently contaminated with urine and faecal material, can provide effective breedin...
Fly strike in sheep
None
6,461
wikipedia
https://en.wikipedia.org/wiki/Fly_strike_in_sheep
2021-01-18T19:08:27
{"wikidata": ["Q16251787"]}
This article lacks ISBNs for the books listed in it. Please make it easier to conduct research by listing ISBNs. If the {{Cite book}} or {{citation}} templates are in use, you may add ISBNs automatically, or discuss this issue on the talk page. (July 2017) Boanthropy is a psychological disorder in which a human ...
Boanthropy
None
6,462
wikipedia
https://en.wikipedia.org/wiki/Boanthropy
2021-01-18T18:53:37
{"wikidata": ["Q4931259"]}
A rare congenital disorder of copper metabolism that is principally characterized by bony exostoses (including the pathognomonic occipital horns), and connective tissue manifestations with cutis laxa and bladder diverticula. Central nervous system involvement is variable. ## Epidemiology Occipital horn syndrome (OH...
Occipital horn syndrome
c0268353
6,463
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=198
2021-01-23T18:27:50
{"gard": ["4017"], "mesh": ["C537860"], "omim": ["304150"], "umls": ["C0268353", "C1096660"], "icd-10": ["E83.0"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Autoimmune optic neuropathy" – news · newspapers · books · scholar · JSTOR (September 2013) (Learn how and when to remo...
Autoimmune optic neuropathy
None
6,464
wikipedia
https://en.wikipedia.org/wiki/Autoimmune_optic_neuropathy
2021-01-18T18:46:58
{"wikidata": ["Q17080979"]}
Dentinogenesis imperfecta is a disorder of tooth development. This condition causes the teeth to be discolored (most often a blue-gray or yellow-brown color) and translucent. Teeth are also weaker than normal, making them prone to rapid wear, breakage, and loss. These problems can affect both primary (baby) teeth and...
Dentinogenesis imperfecta
c0399380
6,465
medlineplus
https://medlineplus.gov/genetics/condition/dentinogenesis-imperfecta/
2021-01-27T08:25:12
{"gard": ["6258", "12796", "10144"], "mesh": ["D003784"], "omim": ["125420", "125490", "125500"], "synonyms": []}
Radiation colitis SpecialtyGastroenterology CausesRadiation therapy Radiation colitis is injury to the colon caused by radiation therapy.[1] It is usually associated with treatment for prostate cancer or cervical cancer.[1] Common symptoms are diarrhea, a feeling of being unable to empty the bowel,[2] gastro...
Radiation colitis
c0341339
6,466
wikipedia
https://en.wikipedia.org/wiki/Radiation_colitis
2021-01-18T18:57:39
{"umls": ["C0341339"], "icd-10": ["K52.0"], "wikidata": ["Q2353003"]}
Type 1 plasminogen deficiency is a genetic condition associated with inflammed growths on the mucous membranes, the moist tissues that line body openings such as the eye, mouth, nasopharynx, trachea, and female genital tract. The growths may be triggered by local injury and/or infection and often recur after removal....
Type 1 plasminogen deficiency
c0398621
6,467
gard
https://rarediseases.info.nih.gov/diseases/4380/type-1-plasminogen-deficiency
2021-01-18T17:57:16
{"mesh": ["C580017"], "omim": ["217090"], "umls": ["C0398621"], "orphanet": ["722"], "synonyms": ["Hypoplasminogenemia"]}
Retinitis pigmentosa (RP) is an inherited retinal dystrophy leading to progressive loss of the photoreceptors and retinal pigment epithelium and resulting in blindness usually after several decades. ## Epidemiology Prevalence of RP is reported to be 1/3,000 to 1/5,000. No ethnic specificities have been reported alt...
Retinitis pigmentosa
c0035334
6,468
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=791
2021-01-23T17:13:41
{"gard": ["5694"], "mesh": ["D012174"], "omim": ["180100", "180104", "180105", "180210", "268000", "268025", "268060", "300029", "300155", "300424", "300605", "312600", "312612", "400004", "600059", "600105", "600132", "600138", "600852", "601414", "601718", "602594", "602772", "604232", "604393", "606068", "607921", "...
Cystic leukoencephalopathy without megalencephaly is characterised by non-progressive leukoencephalopathy, bilateral cysts in the anterior part of the temporal lobe, cerebral white matter anomalies and severe psychomotor impairment. Less than 50 patients have been described in the literature so far. Inheritance is mo...
Cystic leukoencephalopathy without megalencephaly
c2751843
6,469
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=85136
2021-01-23T17:30:28
{"mesh": ["C567845"], "omim": ["612951"], "umls": ["C2751843"], "icd-10": ["E75.2"], "synonyms": ["CLWM"]}
A rare genetic neurovascular malformation characterized by sac-like bulging of cerebral arteries due to weakening of the endothelial layer. Familial occurrence is suspected when two or more affected first- to third-degree relatives are present in a family. Aneurysms may remain asymptomatic throughout life, or rupture...
Familial cerebral saccular aneurysm
c1862932
6,470
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=231160
2021-01-23T18:59:52
{"mesh": ["C566284"], "omim": ["105800", "300870", "608542", "609122", "610213", "611892", "612161", "612162", "612586", "612587", "614252", "618734"], "icd-10": ["I67.1"], "synonyms": ["Familial berry aneurysm", "Familial intracranial saccular aneurysm"]}
Legal since 1937 Abortion in Puerto Rico is legal. Attitudes and laws in Puerto Rico relating to abortion have been significantly impacted by decisions of the federal government of the United States. Abortion effectively became legal in 1937 after a series of changes in the law by the Puerto Rico legislature based o...
Abortion in Puerto Rico
None
6,471
wikipedia
https://en.wikipedia.org/wiki/Abortion_in_Puerto_Rico
2021-01-18T18:54:51
{"wikidata": ["Q64876951"]}
Cerebral creatine deficiency Other namesCCD SpecialtyPediatrics, medical genetics, neurology Symptomsintellectual disability, developmental delay, seziures Usual onsetearly childhood CausesGenetic Diagnostic methodBlood, and urine tests, genetic testing, brain MRS Treatmentdietary modification, crea...
Cerebral creatine deficiency
c0268238
6,472
wikipedia
https://en.wikipedia.org/wiki/Cerebral_creatine_deficiency
2021-01-18T18:55:27
{"mesh": ["C536560"], "icd-10": ["E72.8"], "orphanet": ["79172"], "synonyms": ["CCDS", "CDS", "Cerebral creatine deficiency syndrome"], "wikidata": ["Q16908143"]}
Group of conditions resulting from maternal alcohol consumption during pregnancy "FASD" redirects here. For other uses, see FASD (disambiguation). Fetal alcohol spectrum disorders Other namesFoetal alcohol spectrum disorders Baby with fetal alcohol syndrome, showing some of the characteristic facial features ...
Fetal alcohol spectrum disorder
c0814154
6,473
wikipedia
https://en.wikipedia.org/wiki/Fetal_alcohol_spectrum_disorder
2021-01-18T18:28:18
{"mesh": ["D063647"], "icd-9": ["12"], "icd-10": ["Q86.0"], "orphanet": ["1915"], "wikidata": ["Q400277"]}
A number sign (#) is used with this entry because of evidence that Seckel syndrome-6 (SCKL6) can be caused by homozygous mutation in the CEP63 gene (614724) on chromosome 3q22. One such family has been reported. For a general phenotypic description and a discussion of genetic heterogeneity of Seckel syndrome, se...
SECKEL SYNDROME 6
c3553582
6,474
omim
https://www.omim.org/entry/614728
2019-09-22T15:54:22
{"omim": ["614728"]}
Injury to the main nerve bundle in the back of humans Spinal cord injury MRI of fractured and dislocated neck vertebra that is compressing the spinal cord SpecialtyNeurosurgery TypesComplete, incomplete[1] Diagnostic methodBased on symptoms, medical imaging[1] TreatmentSpinal motion restriction, intravenou...
Spinal cord injury
c0037929
6,475
wikipedia
https://en.wikipedia.org/wiki/Spinal_cord_injury
2021-01-18T18:37:11
{"mesh": ["D013119"], "umls": ["90058"], "icd-10": ["T09.3", "G95.9"], "orphanet": ["90058"], "wikidata": ["Q1415275"]}
Sotos syndrome is a condition characterized mainly by distinctive facial features; overgrowth in childhood; and learning disabilities or delayed development. Facial features may include a long, narrow face; a high forehead; flushed (reddened) cheeks; a small, pointed chin; and down-slanting palpebral fissures. Af...
Sotos syndrome
c0175695
6,476
gard
https://rarediseases.info.nih.gov/diseases/10091/sotos-syndrome
2021-01-18T17:57:40
{"mesh": ["D058495"], "omim": ["117550"], "umls": ["C0175695"], "orphanet": ["821"], "synonyms": ["Cerebral gigantism", "Distinctive facial appearance, overgrowth in childhood, and learning disabilities or delayed development"]}
Bartter syndrome is a group of very similar kidney disorders that cause an imbalance of potassium, sodium, chloride, and related molecules in the body. In some cases, Bartter syndrome becomes apparent before birth. The disorder can cause polyhydramnios, which is an increased volume of fluid surrounding the fetus...
Bartter syndrome
c0004775
6,477
gard
https://rarediseases.info.nih.gov/diseases/5893/bartter-syndrome
2021-01-18T18:01:53
{"mesh": ["D001477"], "omim": ["601678", "241200", "607364", "602522", "613090"], "umls": ["C0004775"], "orphanet": ["112"], "synonyms": ["Potassium wasting", "Bartter's syndrome", "Hypokalemic alkalosis with hypercalciuria"]}
Toluene toxicity Chemical structure of toluene SpecialtyEmergency medicine Toluene toxicity refers to the harmful effects caused by toluene on the body. ## Contents * 1 Metabolism in humans * 2 Environmental influences * 3 Measure of exposure * 4 Effects of long-term exposure * 5 References * 6...
Toluene toxicity
None
6,478
wikipedia
https://en.wikipedia.org/wiki/Toluene_toxicity
2021-01-18T18:52:57
{"icd-10": ["T52.2"], "wikidata": ["Q3153686"]}
Temtamy preaxial brachydactyly syndrome is a rare, genetic dysostosis syndrome characterized by bilateral, symmetrical, preaxial brachydactyly associated with hyperphalangy, motor developmental delay and intellectual disability, growth retardation, sensorineural hearing loss, dental abnormalities (incuding misali...
Temtamy preaxial brachydactyly syndrome
c1854466
6,479
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=363417
2021-01-23T17:46:35
{"gard": ["9679"], "mesh": ["C536958"], "omim": ["605282"], "umls": ["C1854466"], "icd-10": ["Q87.2"]}
Often called "albino", this amelanistic python owes its yellow color to unaffected carotenoid pigments. Amelanism (also known as amelanosis) is a pigmentation abnormality characterized by the lack of pigments called melanins, commonly associated with a genetic loss of tyrosinase function. Amelanism can affect fish, ...
Amelanism
None
6,480
wikipedia
https://en.wikipedia.org/wiki/Amelanism
2021-01-18T18:35:51
{"wikidata": ["Q4742182"]}
Fusarium wilt A tobacco plant suffering from Fusarium wilt Causal agentsFusarium oxysporum HostsTomato, tobacco, legumes, cucurbits, sweet potatoes and banana EPPO CodeFUSAOX Fusarium wilt is a common vascular wilt fungal disease, exhibiting symptoms similar to Verticillium wilt. This disease h...
Fusarium wilt
None
6,481
wikipedia
https://en.wikipedia.org/wiki/Fusarium_wilt
2021-01-18T18:57:58
{"wikidata": ["Q1475267"]}
Rickettsiosis SpecialtyInfectious disease A rickettsiosis is a disease caused by intracellular bacteria. ## Contents * 1 Cause * 2 Diagnosis * 3 Treatment * 4 References * 5 External links ## Cause[edit] Rickettsioses can be divided into a spotted fever group (SPG) and typhus group (TG).[1] In t...
Rickettsiosis
c0035585
6,482
wikipedia
https://en.wikipedia.org/wiki/Rickettsiosis
2021-01-18T19:08:18
{"mesh": ["D012282", "D012288"], "icd-9": ["083", "083.9", "080"], "icd-10": ["A75", "A79"], "orphanet": ["102021"], "wikidata": ["Q646664"]}
Chondrodermatitis nodularis chronica helicis Other namesChondrodermatitis nodularis helicis[1]:782 Chondrodermatitis helicis nodularis in a 67-year-old man SpecialtyDermatology Chondrodermatitis nodularis chronica helicis is a small, nodular, tender, chronic inflammatory lesion occurring on the helix o...
Chondrodermatitis nodularis chronica helicis
c0271415
6,483
wikipedia
https://en.wikipedia.org/wiki/Chondrodermatitis_nodularis_chronica_helicis
2021-01-18T18:47:28
{"wikidata": ["Q1076057"]}
This article may be confusing or unclear to readers. Please help us clarify the article. There might be a discussion about this on the talk page. (January 2010) (Learn how and when to remove this template message) Focal dermal hypoplasia Other namesGoltz syndrome This condition is inherited in an X-linke...
Focal dermal hypoplasia
c0016395
6,484
wikipedia
https://en.wikipedia.org/wiki/Focal_dermal_hypoplasia
2021-01-18T18:53:29
{"gard": ["6457"], "mesh": ["D005489"], "umls": ["C0016395"], "icd-9": ["759.89"], "icd-10": ["Q82.8"], "orphanet": ["2092"], "wikidata": ["Q5463847"]}
A number sign (#) is used with this entry because of evidence that some patients with Cohen syndrome have homozygous or compound heterozygous mutations in the COH1 gene (VPS13B; 607817) on chromosome 8q22. Description Cohen syndrome is an autosomal recessive multisystem disorder characterized by many clinical f...
COHEN SYNDROME
c0265223
6,485
omim
https://www.omim.org/entry/216550
2019-09-22T16:29:31
{"mesh": ["C536438"], "omim": ["216550"], "orphanet": ["193"], "synonyms": ["Alternative titles", "COH", "HYPOTONIA, OBESITY, AND PROMINENT INCISORS", "PEPPER SYNDROME", "CHS1, FORMERLY"], "genereviews": ["NBK1482"]}
Mastocytoma Other namesMast cell tumor Mast cell tumor cytology SpecialtyOncology A mastocytoma or mast cell tumor is a type of round-cell tumor consisting of mast cells. It is found in humans and many animal species; it also can refer to an accumulation or nodule of mast cells that resembles a tumor. Mas...
Mastocytoma
c0024897
6,486
wikipedia
https://en.wikipedia.org/wiki/Mastocytoma
2021-01-18T19:10:19
{"umls": ["C0024897"], "icd-9": ["238.5"], "wikidata": ["Q6785569"]}
Abortion in Lithuania is legal and available on request until the twelfth week of pregnancy, and up to 22 weeks for medical reasons.[1] [2] While Lithuania was a Republic of the Soviet Union (as the Lithuanian Soviet Socialist Republic), abortions were regulated by the Government of the Soviet Union.[1] ## Histo...
Abortion in Lithuania
None
6,487
wikipedia
https://en.wikipedia.org/wiki/Abortion_in_Lithuania
2021-01-18T18:32:09
{"wikidata": ["Q16057982"]}
For a discussion of genetic heterogeneity of multiple sclerosis (MS), see MS1 (126200). Mapping In a genomewide association study of 45 patients with multiple sclerosis and 195 controls in a genetically isolated Dutch population, Aulchenko et al. (2008) found an association between MS and the C allele of rs1049...
MULTIPLE SCLEROSIS, SUSCEPTIBILITY TO, 4
c2675476
6,488
omim
https://www.omim.org/entry/612596
2019-09-22T16:01:01
{"omim": ["612596"]}
A number sign (#) is used with this entry because of evidence that meconium ileus can be caused by homozygous mutation in the GUCY2C gene (601330) on chromosome 12p. Description Meconium ileus refers to intestinal obstruction due to inspissated meconium in the distal ileum and cecum, which develops in utero and pre...
MECONIUM ILEUS
c2939175
6,489
omim
https://www.omim.org/entry/614665
2019-09-22T15:54:35
{"mesh": ["D000074270"], "omim": ["614665"], "icd-10": ["P76.0"], "orphanet": ["314376"], "synonyms": ["Meconium ileus due to guanylate cyclase 2C deficiency"]}
A rare form of axonal peripheral sensorimotor neuropathy characterized by classical CMT2 signs and symptoms (progressive weakness and atrophy of distal limb muscles, mild sensory deficits of position, vibration and pain/temperature, pes cavus, and symmetrically absent or reduced muscle and sensory action potentials w...
Autosomal dominant Charcot-Marie-Tooth disease type 2 due to KIF5A mutation
c4707173
6,490
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=324611
2021-01-23T17:30:18
{"icd-10": ["G60.0"], "synonyms": ["CMT2 due to KIF5A mutation"]}
## Clinical Features Asch and Myers (1976) described 5 males in 2 generations of a family with occipitofrontal head circumferences greater than 2 SD above the mean. All were neurologically and mentally normal. A maternal uncle of the first generation was said to have a large head. All were dolichocephalic. By sonog...
MACROCEPHALY, BENIGN FAMILIAL
c0220690
6,491
omim
https://www.omim.org/entry/153470
2019-09-22T16:38:46
{"mesh": ["C537717"], "omim": ["153470"], "synonyms": ["Alternative titles", "COLE-HUGHES SYNDROME"]}
## Clinical Features Smith (1972) documented 8 cases of midgut volvulus in 1 kindred. The propositus, his 2 sons and 3 daughters, and his 2 grandchildren demonstrated this midgut malrotation syndrome. The midgut volvulus caused great discomfort. Six of the affected had undergone a total of 24 operative procedures t...
VOLVULUS OF MIDGUT
c0221210
6,492
omim
https://www.omim.org/entry/193250
2019-09-22T16:31:54
{"mesh": ["C562456"], "omim": ["193250"], "synonyms": ["Alternative titles", "INTESTINAL MALROTATION, FAMILIAL"]}
## Clinical Features Lewkonia and Buxton (1973) described myositis in father and daughter. The daughter's illness resembled childhood dermatomyositis and progressed to systemic involvement with death less than 4 years after onset. The father's illness followed the course of adult polymyositis, with little evidence ...
MYOSITIS
c3888318
6,493
omim
https://www.omim.org/entry/160750
2019-09-22T16:37:40
{"doid": ["633"], "mesh": ["C000598744"], "omim": ["160750"], "icd-10": ["M60.9", "M60", "G72.49"], "synonyms": ["Alternative titles", "MYOPATHY, FAMILIAL IDIOPATHIC INFLAMMATORY"]}
Congenital condition characterised by fusion of two or more vertebrae in the neck Klippel-Feil syndrome Other namesCongenital dystrophia brevicollis, cervical vertebral fusion syndrome Woman with Klippel–Feil syndrome Pronunciation * /ˌklɪ.pəl ˈfaɪl/ SpecialtyPaediatrics, orthopaedics SymptomsCervi...
Klippel–Feil syndrome
c0022738
6,494
wikipedia
https://en.wikipedia.org/wiki/Klippel%E2%80%93Feil_syndrome
2021-01-18T18:55:16
{"gard": ["10280"], "mesh": ["D007714"], "umls": ["C0022738"], "orphanet": ["2345"], "wikidata": ["Q1774751"]}
Smouldering myeloma Other namesSmoldering myeloma, Smoldering multiple myeloma, Indolent myeloma or Asymptomatic myeloma SpecialtyHematology/oncology Smouldering myeloma, is a disease classified as intermediate in a spectrum of step-wise progressive diseases termed plasma cell dyscrasias. In this spectru...
Smouldering myeloma
c1531608
6,495
wikipedia
https://en.wikipedia.org/wiki/Smouldering_myeloma
2021-01-18T18:33:57
{"mesh": ["D000075122"], "umls": ["C1531608"], "wikidata": ["Q17146000"]}
A hereditary disorder of hepatic bilirubin conjugation, characterized by severe neonatal unconjugated hyperbilirubinemia due to a complete absence of hepatic bilirubin glucuronosyltransferase (BGT). ## Epidemiology The prevalence of Crigler-Najjar syndrome type 1 (CNS1) is unknown. Crigler-Najjar syndrome (CNS) has...
Crigler-Najjar syndrome type 1
c0010324
6,496
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=79234
2021-01-23T18:50:48
{"gard": ["47"], "mesh": ["D003414", "C536212"], "omim": ["218800"], "umls": ["C0010324", "C2931131"], "icd-10": ["E80.5"], "synonyms": ["Bilirubin uridinediphosphate glucuronosyltransferase deficiency type 1", "Bilirubin-UGT deficiency type 1", "Hereditary unconjugated hyperbilirubinemia type 1", "UGT deficiency type ...
A number sign (#) is used with this entry because of evidence that cone-rod dystrophy-11 (CORD11) is caused by heterozygous mutation in the RAXL1 gene (RAX2, 610362) on chromosome 19p13. For a phenotypic description and a discussion of genetic heterogeneity of cone-rod dystrophy, see 120970. Clinical Features Yang...
CONE-ROD DYSTROPHY 11
c3489532
6,497
omim
https://www.omim.org/entry/610381
2019-09-22T16:04:37
{"doid": ["0111018"], "mesh": ["D000071700"], "omim": ["120970", "610381"], "orphanet": ["1872"], "synonyms": []}
Severe combined immunodeficiency (SCID) due to CTPS1 deficiency is a rare primary immunodeficiency disorder due to impaired capacity of activated T- and B-cells to proliferate in response to antigen receptor-mediated activation characterized by early-onset, severe, persistent and/or recurrent viral infections due to ...
Severe combined immunodeficiency due to CTPS1 deficiency
c4014617
6,498
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=420573
2021-01-23T17:22:06
{"omim": ["615897"], "icd-10": ["D81.2"], "synonyms": ["SCID due to CTPS1 deficiency"]}
Pallister-Killian syndrome Other namesTetrasomy 12p mosaicism, Pallister mosaic aneuploidy syndrome Pallister–Killian syndrome (also tetrasomy 12p mosaicism or Pallister mosaic aneuploidy syndrome) is an extremely rare genetic disorder occurring in humans. Pallister–Killian occurs due to the presence of the an...
Pallister–Killian syndrome
c0265449
6,499
wikipedia
https://en.wikipedia.org/wiki/Pallister%E2%80%93Killian_syndrome
2021-01-18T19:04:08
{"mesh": ["C538105"], "umls": ["C0265449"], "icd-9": ["758.5"], "icd-10": ["Q99.8"], "orphanet": ["884"], "wikidata": ["Q1425018"]}