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A number sign (#) is used with this entry because X-linked lissencephaly with ambiguous genitalia (LISX2, XLAG), as well as hydranencephaly and abnormal genitalia, can be caused by mutation in the ARX gene (300382). See also Proud syndrome (300004), an allelic disorder with an overlapping phenotype. Early infant...
LISSENCEPHALY, X-LINKED, 2
c1846171
7,400
omim
https://www.omim.org/entry/300215
2019-09-22T16:20:40
{"doid": ["0050453"], "mesh": ["C564563"], "omim": ["300215"], "orphanet": ["452"], "synonyms": ["Alternative titles", "LISSENCEPHALY, X-LINKED, WITH AMBIGUOUS GENITALIA", "XLISG"]}
A form of hereditary cerebral hemorrhage with amyloidosis characterized by an age of onset between 50-70 years of age, recurrent lobar intracerebral hemorrhages and cognitive decline. This subtype is due to a mutation in the APP gene (21q21.2), encoding the beta-amyloid precursor protein. This mutation causes an incr...
ABetaL34V amyloidosis
c2931672
7,401
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=324703
2021-01-23T19:00:18
{"mesh": ["C537944"], "omim": ["605714"], "icd-10": ["E85.4+", "I68.0*"], "synonyms": ["ABeta amyloidosis, Piedmont type", "ABetaL34V-related amyloidosis", "HCHWA, Piedmont type", "Hereditary cerebral hemorrhage with amyloidosis, Piedmont type"]}
A form of hereditary cerebral hemorrhage with amyloidosis characterized by an age of onset of 20-30 years, major systemic amyloidosis and recurrent lobar intracerebral hemorrhages. Unlike other forms of hereditary cerebral hemorrhage with amyloidosis, this subtype is due to a mutation in the CST3 gene (20p11.2), enco...
ACys amyloidosis
c1527338
7,402
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=100008
2021-01-23T18:30:24
{"mesh": ["D028243"], "omim": ["105150"], "umls": ["C1527338"], "icd-10": ["E85.4+", "I68.0*"], "synonyms": ["CST3-related amyloidosis", "Cystatin amyloidosis", "HCHWA, Icelandic type", "Hereditary cerebral hemorrhage with amyloidosis, Icelandic type", "Hereditary cystatin C amyloid angiopathy"]}
Acrocallosal syndrome is a rare condition characterized by a brain abnormality called agenesis of the corpus callosum, the presence of extra fingers and toes (polydactyly), and distinctive facial features. The signs and symptoms of this disorder are present at birth, and their severity varies widely among affected in...
Acrocallosal syndrome
c0796147
7,403
medlineplus
https://medlineplus.gov/genetics/condition/acrocallosal-syndrome/
2021-01-27T08:25:26
{"gard": ["5721"], "mesh": ["D055673"], "omim": ["200990"], "synonyms": []}
## Clinical Features Headington and Astle (1987) described a 14-year-old girl and her mother who had patchy hair loss present from early childhood. When studied in transverse section, biopsy specimens from both women showed marked anagen-telogen transformation that appeared to be irreversible. Preservation of telog...
ALOPECIA, FAMILIAL FOCAL
c1863092
7,404
omim
https://www.omim.org/entry/104110
2019-09-22T15:41:17
{"mesh": ["C566301"], "omim": ["104110"]}
Von Hippel-Lindau syndrome is an inherited disorder characterized by the formation of tumors and fluid-filled sacs (cysts) in many different parts of the body. Tumors may be either noncancerous or cancerous and most frequently appear during young adulthood; however, the signs and symptoms of von Hippel-Lindau syndrom...
Von Hippel-Lindau syndrome
c0019562
7,405
medlineplus
https://medlineplus.gov/genetics/condition/von-hippel-lindau-syndrome/
2021-01-27T08:24:53
{"gard": ["7855"], "mesh": ["D006623"], "omim": ["193300"], "synonyms": []}
A number sign (#) is used with this entry because autosomal dominant mental retardation-13 (MRD13) is caused by heterozygous mutation in the DYNC1H1 gene (600112) on chromosome 14q32. Description MRD13 is an autosomal dominant form of mental retardation associated with variable neuronal migration defects resulting ...
MENTAL RETARDATION, AUTOSOMAL DOMINANT 13
c3281202
7,406
omim
https://www.omim.org/entry/614563
2019-09-22T15:54:52
{"doid": ["0070043"], "omim": ["614563"], "orphanet": ["178469"], "synonyms": ["Alternative titles", "MENTAL RETARDATION, AUTOSOMAL DOMINANT 13, WITH NEURONAL MIGRATION DEFECTS"]}
A number sign (#) is used with this entry because of evidence that nonsyndromic autosomal recessive deafness-18A (DFNB18A) is caused by homozygous mutation in the gene encoding harmonin (605242) on chromosome 11p15. Mutations in the harmonin gene also cause Usher syndrome type IC (USH1C; 276904). A form of autosomal...
DEAFNESS, AUTOSOMAL RECESSIVE 18A
c1865870
7,407
omim
https://www.omim.org/entry/602092
2019-09-22T16:13:56
{"doid": ["0110473"], "mesh": ["C566580"], "omim": ["602092"], "orphanet": ["90636"], "synonyms": ["Autosomal recessive non-syndromic neurosensory deafness type DFNB", "Alternative titles", "Autosomal recessive isolated sensorineural deafness type DFNB", "DEAFNESS, AUTOSOMAL RECESSIVE 18", "Autosomal recessive isolated...
## Clinical Features In 2 daughters of Iraqi first-cousin parents, Harbord et al. (1990) observed a progressive neurologic disorder characterized by megalencephaly, spasticity, ataxia, and seizures. Onset of manifestations occurred between ages 2 and 3. Computerized tomography scans showed diffuse hypodensity of th...
MEGALENCEPHALY WITH DYSMYELINATION
c1855309
7,408
omim
https://www.omim.org/entry/249240
2019-09-22T16:25:30
{"mesh": ["C565408"], "omim": ["249240"], "synonyms": ["Alternative titles", "MEGALENCEPHALY WITH DIFFUSE WHITE MATTER HYPODENSITY"]}
## Clinical Features Coats disease, also called retinal telangiectasis, is a sporadic disorder characterized by a defect of retinal vascular development that results in vessel leakage, subretinal exudation, and retinal detachment. The disorder was first reported by Coats (1908) in 6 children. Initially, the conditi...
COATS DISEASE
c0154832
7,409
omim
https://www.omim.org/entry/300216
2019-09-22T16:20:39
{"doid": ["7765"], "mesh": ["D058456"], "omim": ["300216"], "icd-9": ["362.12"], "icd-10": ["H35.02", "H35.07"], "orphanet": ["190"], "synonyms": ["Alternative titles", "RETINAL TELANGIECTASIS"], "genereviews": ["NBK1331"]}
## Clinical Features Cockshott and Omololu (1958) described a father and his infant daughter with congenital posterior dislocation of the radial head. Neither could extend their elbows below the right angle, whereas pronation and supination were unrestricted. The tendons of insertion of both biceps stood out promin...
RADIAL HEADS, POSTERIOR DISLOCATION OF
c1867398
7,410
omim
https://www.omim.org/entry/179200
2019-09-22T16:35:21
{"mesh": ["C566728"], "omim": ["179200"]}
The superior and inferior lumbar triangles with a cross section at the level of the superior lumbar triangle Grynfeltt-Lesshaft hernia is a herniation of abdominal contents through the back, specifically through the superior lumbar triangle, which is defined by the quadratus lumborum muscle, twelfth rib, and interna...
Grynfeltt-Lesshaft hernia
None
7,411
wikipedia
https://en.wikipedia.org/wiki/Grynfeltt-Lesshaft_hernia
2021-01-18T18:33:07
{"wikidata": ["Q5612430"]}
Congenital hemorrhagic diathesis due to an excess of a clotting inhibitor has not been fully established. Quick (1957) diagnosed congenital hyperheparinemia in a woman with abnormal bleeding from age 3. Heni and Krauss (1956) described a similar condition in a father and daughter. In both instances the in vitro c...
HYPERHEPARINEMIA
c3203346
7,412
omim
https://www.omim.org/entry/144050
2019-09-22T16:39:58
{"mesh": ["C562723"], "omim": ["144050"], "icd-10": ["D68.32"]}
A number sign (#) is used with this entry because of evidence that acid-labile subunit deficiency (ACLSD) is caused by homozygous or compound heterozygous mutation in the IGFALS gene (601489) on chromosome 16p13. Description Acid-labile subunit deficiency is characterized by severely reduced serum insulin-like grow...
ACID-LABILE SUBUNIT DEFICIENCY
c4321359
7,413
omim
https://www.omim.org/entry/615961
2019-09-22T15:50:27
{"omim": ["615961"], "orphanet": ["140941"], "synonyms": []}
Paroxysmal exercise-induced dystonia Other namesParoxysmal exertion-induced dyskinesia This condition is inherited in an autosomal dominant manner SpecialtyNeurology Paroxysmal exercise-induced dystonia or PED is a rare neurological disorder characterized by sudden, transient, involuntary movements, often ...
Paroxysmal exercise-induced dystonia
c1842534
7,414
wikipedia
https://en.wikipedia.org/wiki/Paroxysmal_exercise-induced_dystonia
2021-01-18T18:37:47
{"gard": ["10541"], "mesh": ["C564288"], "umls": ["C1842534"], "orphanet": ["98811"], "wikidata": ["Q7139585"]}
Congenital malformation of the cerebellar vermis Dandy–Walker malformation Other namesDandy–Walker syndrome (DWS),[1] Dandy–Walker complex (DWC),[2] Dandy–Walker continuum[3] T2-weighted sagittal MRI of Dandy–Walker variant (DWV) with dysplasia of the pons and cerebellar vermis in an 8-year old SpecialtyMe...
Dandy–Walker malformation
c0010964
7,415
wikipedia
https://en.wikipedia.org/wiki/Dandy%E2%80%93Walker_malformation
2021-01-18T19:02:03
{"gard": ["6242"], "mesh": ["D003616"], "umls": ["C0010964"], "icd-9": ["742.3"], "orphanet": ["217"], "wikidata": ["Q733493"]}
A number sign (#) is used with this entry because of evidence that hereditary sensory neuropathy type IF (HSN1F) is caused by heterozygous mutation in the ATL3 gene (609369) on chromosome 11q13. Description Hereditary sensory neuropathy type IF is an autosomal dominant sensory neuropathy affecting the lower lim...
NEUROPATHY, HEREDITARY SENSORY, TYPE IF
c0020071
7,416
omim
https://www.omim.org/entry/615632
2019-09-22T15:51:22
{"doid": ["0070154"], "mesh": ["D009477"], "omim": ["615632"], "orphanet": ["36386"], "synonyms": ["Alternative titles", "HSN IF"]}
A form of lissencephaly with cerebellar hypoplasia characterized by pronounced microcephaly (at least ± 3 SD), intellectual disability, spastic diplegia and moderate to severe cerebellar hypoplasia involving both vermis and hemispheres. *[v]: View this template *[t]: Discuss this template *[e]: Edit this templ...
Lissencephaly with cerebellar hypoplasia type D
c4274991
7,417
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=100014
2021-01-23T17:36:48
{"icd-10": ["Q04.3"]}
This article is about the kind of muscle injury. For other uses, see Strain (disambiguation). Not to be confused with Sprain. Strain Other namesMuscle strain, pulled muscle, torn muscle Two images of the same strain to the hamstring and associated bruising. One of the pictures was shot through a mirror. Speci...
Strain (injury)
c0080194
7,418
wikipedia
https://en.wikipedia.org/wiki/Strain_(injury)
2021-01-18T18:31:06
{"mesh": ["D013180"], "umls": ["C0080194"], "icd-9": ["848.9"], "icd-10": ["M62.6", "T14.3"], "wikidata": ["Q576145"]}
Erythromelanosis follicularis faciei et colli SpecialtyDermatology Erythromelanosis follicularis faciei et colli is an erythematous pigmentary disease involving the follicles, characterized by a reddish-brown, sharply demarcated, symmetrical discoloration involving the preauricular and maxillary regions.[1...
Erythromelanosis follicularis faciei et colli
c0263577
7,419
wikipedia
https://en.wikipedia.org/wiki/Erythromelanosis_follicularis_faciei_et_colli
2021-01-18T18:39:33
{"umls": ["C0263577"], "wikidata": ["Q5396486"]}
A number sign (#) is used with this entry because of evidence that susceptibility to thyrotoxic periodic paralysis-1 (TTPP1) is conferred by variation in the CACNA1S gene on chromosome 1q32. Description Thyrotoxic periodic paralysis is a sporadic muscle disorder characterized by episodic attacks of weakness ass...
THYROTOXIC PERIODIC PARALYSIS, SUSCEPTIBILITY TO, 1
c0268446
7,420
omim
https://www.omim.org/entry/188580
2019-09-22T16:32:32
{"omim": ["188580"], "orphanet": ["79102"]}
Chronic sclerosing sialadenitis SpecialtyDentistry Chronic sclerosing sialadenitis is a chronic (long-lasting) inflammatory condition affecting the salivary gland. Relatively rare in occurrence, this condition is benign, but presents as hard, indurated and enlarged masses that are clinically indistinguishable ...
Chronic sclerosing sialadenitis
c2826557
7,421
wikipedia
https://en.wikipedia.org/wiki/Chronic_sclerosing_sialadenitis
2021-01-18T18:39:21
{"wikidata": ["Q17083598"]}
The arm of a patient with familial multiple lipomatosis. Familial multiple lipomatosis is a hereditary adipose tissue disorder that is characterized by the formation of multiple lipomas that occur in a particular distribution.[1] The lipomas are well-encapsulated, slow-growing, benign fatty tumors. The distribut...
Familial multiple lipomatosis
c1275273
7,422
wikipedia
https://en.wikipedia.org/wiki/Familial_multiple_lipomatosis
2021-01-18T18:53:19
{"mesh": ["D000071070"], "wikidata": ["Q85760447"]}
Gianotti–Crosti syndrome SpecialtyDermatology Gianotti–Crosti syndrome (/dʒəˈnɒti ˈkrɒsti/), also known as infantile papular acrodermatitis,[1] papular acrodermatitis of childhood,[1] and papulovesicular acrolocated syndrome,[2]:389 is a reaction of the skin to a viral infection.[3] Hepatitis B virus[4] and Ep...
Gianotti–Crosti syndrome
None
7,423
wikipedia
https://en.wikipedia.org/wiki/Gianotti%E2%80%93Crosti_syndrome
2021-01-18T19:00:53
{"gard": ["6499"], "icd-9": ["057.8"], "icd-10": ["L44.4"], "wikidata": ["Q475972"]}
## Clinical Features The Wildervanck syndrome consists of congenital perceptive deafness, Klippel-Feil anomaly (see 118100), and abducens palsy with retractio bulbi (Duane syndrome). The disorder is limited, or almost completely limited, to females, raising the question of sex-linked dominance with lethality in...
WILDERVANCK SYNDROME
c0265239
7,424
omim
https://www.omim.org/entry/314600
2019-09-22T16:17:04
{"mesh": ["C535326"], "omim": ["314600"], "orphanet": ["3456"], "synonyms": ["Alternative titles", "CERVICOOCULOACOUSTIC SYNDROME"]}
"Trich" redirects here. For the hair-pulling disorder, see Trichotillomania. Not to be confused with Trichinosis or Trichuriasis. Trichomoniasis Other namesTrich[1] Micrograph showing a positive result for trichomoniasis. A trichomonas organism is seen on the top-right of the image. SpecialtyGynecology Symp...
Trichomoniasis
c0040921
7,425
wikipedia
https://en.wikipedia.org/wiki/Trichomoniasis
2021-01-18T18:56:50
{"mesh": ["D014245"], "umls": ["C0040921"], "wikidata": ["Q745865"]}
toxic effects of thallium Thallium poisoning Other namesThallium Toxicity Thallium SpecialtyToxicology Thallium poisoning is poisoning due to thallium and its compounds which are often highly toxic.[1] Contact with skin is dangerous, and adequate ventilation should be provided when melting this metal....
Thallium poisoning
c0238452
7,426
wikipedia
https://en.wikipedia.org/wiki/Thallium_poisoning
2021-01-18T19:05:58
{"icd-9": ["985.8"], "icd-10": ["T60.4"], "wikidata": ["Q374832"]}
Oculocerebrorenal syndrome Other namesLowe syndrome Oculocerebrorenal syndrome is X-linked recessive. SpecialtyObstetrics and gynaecology, urology, neurology, medical genetics, endocrinology SymptomsCataracts[1] CausesMutations in OCRL gene[1] Diagnostic methodMRI, urinalysis[2] TreatmentPhysical th...
Oculocerebrorenal syndrome
c2713392
7,427
wikipedia
https://en.wikipedia.org/wiki/Oculocerebrorenal_syndrome
2021-01-18T18:42:53
{"gard": ["3295"], "mesh": ["D009800"], "umls": ["C2713392"], "icd-9": ["270.8"], "orphanet": ["534"], "wikidata": ["Q1200839"]}
Axillary nerve dysfunction Axillary nerve(green arrow) SpecialtyNeurology Axillary nerve dysfunction is any disorder caused by damage to the axillary nerve.[1] The axillary nerve is a branch of the brachial plexus that innervates the deltoid and teres minor muscles. This nerve can be injured or damaged i...
Axillary nerve dysfunction
None
7,428
wikipedia
https://en.wikipedia.org/wiki/Axillary_nerve_dysfunction
2021-01-18T18:58:54
{"wikidata": ["Q4830469"]}
A rare genetic syndrome with limb malformations as a major feature characterized by preaxial polydactyly of the hands and feet with variable phenotypic expressivity in combination with hypertrichosis extending from the posterior hairline to the middle of the back. Reported limb malformations include triphalangeal...
Autosomal dominant preaxial polydactyly-upperback hypertrichosis syndrome
None
7,429
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=476119
2021-01-23T17:04:24
{}
Colon polyps Polyp of sigmoid colon as revealed by colonoscopy. Approximately 1 cm in diameter. The polyp was removed by snare cautery. SpecialtyGastroenterology A colorectal polyp is a polyp (fleshy growth) occurring on the lining of the colon or rectum.[1] Untreated colorectal polyps can develop into color...
Colorectal polyp
c0009376
7,430
wikipedia
https://en.wikipedia.org/wiki/Colorectal_polyp
2021-01-18T18:47:10
{"mesh": ["D003111"], "umls": ["C0009376"], "icd-10": ["K63.5"], "wikidata": ["Q1209892"]}
TANGO2-related metabolic encephalopathy and arrhythmias is a disease that can cause episodes of metabolic crises and abnormal heart rhythms (arrhythmia). A metabolic crisis is caused by having low blood sugar (hypoglycemia) and the buildup of toxic products in the blood. A metabolic crisis can occur in any person...
TANGO2-Related Metabolic Encephalopathy and Arrhythmias
c4225171
7,431
gard
https://rarediseases.info.nih.gov/diseases/13423/tango2-related-metabolic-encephalopathy-and-arrhythmias
2021-01-18T17:57:25
{"omim": ["616878"], "orphanet": ["480864"], "synonyms": ["TANGO2 related disease", "Metabolic encephalomyopathic crises, recurrent, with rhabdomyolysis, cardiac arrhythmias, and neurodegeneration", "Recurrent metabolic encephalomyopathic crises-rhabdomyolysis-cardiac arrhythmia-intellectual disability syndrome", "TANG...
A number sign (#) is used with this entry because Charcot-Marie-Tooth disease type 4B2 is caused by mutation in the SBF2 gene (607697). Description Autosomal recessive Charcot-Marie-Tooth disease type 4B is a demyelinating hereditary motor and sensory neuropathy characterized by abnormal folding of myelin sheaths. ...
CHARCOT-MARIE-TOOTH DISEASE, TYPE 4B2
c1858278
7,432
omim
https://www.omim.org/entry/604563
2019-09-22T16:11:52
{"doid": ["0110190"], "mesh": ["C535421"], "omim": ["604563"], "orphanet": ["99956"], "synonyms": ["Alternative titles", "CHARCOT-MARIE-TOOTH DISEASE, WITH FOCALLY FOLDED MYELIN SHEATHS, AUTOSOMAL RECESSIVE, TYPE 4B2", "CHARCOT-MARIE-TOOTH NEUROPATHY, TYPE 4B2"]}
Inflammatory skin disease with redness and scaling Erythroderma Other namesExfoliative dermatitis, Dermatitis exfoliativa Red skin syndrome SpecialtyDermatology Erythroderma is an inflammatory skin disease with redness and scaling that affects nearly the entire cutaneous surface.[1][2] This term applies w...
Erythroderma
c0011606
7,433
wikipedia
https://en.wikipedia.org/wiki/Erythroderma
2021-01-18T18:40:10
{"gard": ["6393"], "mesh": ["D003873"], "umls": ["C0011606"], "icd-9": ["695.9"], "icd-10": ["L26"], "wikidata": ["Q1363741"]}
A rare syndrome characterized by hypokalemic metabolic alkalosis in combination with significant hypomagnesemia and low urinary calcium excretion. ## Epidemiology Gitelman syndrome (GS) prevalence is estimated at 1 to 10 per 40,000 and potentially higher in Asia. GS is arguably the most frequent inherited tubul...
Gitelman syndrome
c0268450
7,434
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=358
2021-01-23T18:39:01
{"gard": ["8547"], "mesh": ["D053579"], "omim": ["263800"], "umls": ["C0268450"], "icd-10": ["N15.8"], "synonyms": ["Primary renal tubular hypokalemic hypomagnesemia with hypocalciuria"]}
A number sign (#) is used with this entry because of evidence that autosomal recessive familial adenomatous polyposis-2 (FAP2) is caused by homozygous or compound heterozygous mutation in the MUTYH (MYH) gene (604933) on chromosome 1p34. Description Autosomal recessive colorectal adenomatous polyposis is a disorder...
FAMILIAL ADENOMATOUS POLYPOSIS 2
c2674616
7,435
omim
https://www.omim.org/entry/608456
2019-09-22T16:07:52
{"doid": ["0080410"], "mesh": ["C538265"], "omim": ["608456"], "orphanet": ["220460", "247798"], "synonyms": ["Alternative titles", "COLORECTAL ADENOMATOUS POLYPOSIS, AUTOSOMAL RECESSIVE", "ADENOMAS, MULTIPLE COLORECTAL, AUTOSOMAL RECESSIVE"], "genereviews": ["NBK107219"]}
A number sign (#) is used with this entry because malonyl-CoA decarboxylase deficiency is caused by homozygous or compound heterozygous mutation in the MLYCD gene (606761) on chromosome 16q23. Description Malonyl-CoA decarboxylase deficiency is an uncommon inherited metabolic disease. The characteristic phenotype i...
MALONYL-CoA DECARBOXYLASE DEFICIENCY
c0342793
7,436
omim
https://www.omim.org/entry/248360
2019-09-22T16:25:41
{"mesh": ["C535702"], "omim": ["248360"], "orphanet": ["943"]}
Glucose-6-phosphate dehydrogenase deficiency is a genetic disorder that occurs almost exclusively in males. This condition mainly affects red blood cells, which carry oxygen from the lungs to tissues throughout the body. In affected individuals, a defect in an enzyme called glucose-6-phosphate dehydrogenase causes re...
Glucose-6-phosphate dehydrogenase deficiency
c4016516
7,437
medlineplus
https://medlineplus.gov/genetics/condition/glucose-6-phosphate-dehydrogenase-deficiency/
2021-01-27T08:25:50
{"gard": ["6520"], "omim": ["305900"], "synonyms": []}
Chancroid is a bacterial infection that is spread through sexual contact. It is caused by a type of bacteria called Haemophilus ducreyi. Chancroid is characterized by a small bump on the genital which becomes a painful ulcer. Men may have just one ulcer, but women often develop four or more. About half of the people ...
Chancroid
c0007947
7,438
gard
https://rarediseases.info.nih.gov/diseases/9522/chancroid
2021-01-18T18:01:32
{"mesh": ["D002602"], "umls": ["C0007947"], "synonyms": []}
A number sign (#) is used with this entry because of evidence that Adie pupil is a characteristic of Charcot-Marie-Tooth disease type 2J (607736), which is caused by mutation in the MPZ gene (159440). Adie (1932) described a stationary, benign disorder characterized by tonic, sluggishly reacting pupil and hypoactive...
ADIE PUPIL
c0001519
7,439
omim
https://www.omim.org/entry/103100
2019-09-22T16:45:17
{"doid": ["11549"], "mesh": ["D000270"], "omim": ["103100"], "icd-9": ["379.46"], "icd-10": ["H57.05"], "orphanet": ["454718"], "synonyms": ["Alternative titles", "ADIE SYNDROME", "POORLY REACTING PUPILS"]}
This article is about theileriosis caused by Theileria parva in cattle. For diseases caused by other Theileria species, see Theileriosis (disambiguation). Kinete stage of Theileria parva in the transmitting tick Rhipicephalus appendiculatus Brisket -edema-in theileriosis by Mitun Sarkar East Coast fever, also know...
East Coast fever
c0039753
7,440
wikipedia
https://en.wikipedia.org/wiki/East_Coast_fever
2021-01-18T18:56:03
{"mesh": ["D013801"], "umls": ["C0039753"], "wikidata": ["Q481392"]}
Binge drinking 1912 U.S. Happy New Year postcard SpecialtyPsychiatry Binge drinking, or heavy episodic drinking, is a modern epithet for drinking alcoholic beverages with an intention of becoming intoxicated by heavy consumption of alcohol over a short period of time, but definitions (see below) vary conside...
Binge drinking
None
7,441
wikipedia
https://en.wikipedia.org/wiki/Binge_drinking
2021-01-18T19:07:46
{"mesh": ["D063425"], "icd-9": ["305"], "icd-10": ["F10"], "wikidata": ["Q1521260"]}
A number sign (#) is used with this entry because autosomal dominant deafness-11 (DFNA11) is caused by heterozygous mutation in the gene encoding myosin VIIA (MYO7A; 276903) on chromosome 11q13. Autosomal recessive nonsyndromic deafness (DFNB2; 600060) and Usher syndrome type IB (276900) are allelic disorders. ...
DEAFNESS, AUTOSOMAL DOMINANT 11
c1832475
7,442
omim
https://www.omim.org/entry/601317
2019-09-22T16:15:09
{"doid": ["0110543"], "mesh": ["C563353"], "omim": ["601317"], "orphanet": ["90635"], "synonyms": ["Autosomal dominant isolated neurosensory deafness type DFNA", "Autosomal dominant isolated neurosensory hearing loss type DFNA", "Autosomal dominant isolated sensorineural deafness type DFNA", "Autosomal dominant isolate...
Isolated cleft lip is a fissure type embryopathy extending from the upper lip to the nasal base. ## Epidemiology The annual incidence is 1/4,000 to 1/10,000 births with major variation occurring between geographic locations and ethnic groups. Cleft lip is twice as common in boys as girls and is seen more frequently...
Isolated cleft lip
c0008924
7,443
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=199302
2021-01-23T17:27:32
{"mesh": ["D002971"], "omim": ["119530", "129400", "225060", "600757", "602966", "608371", "608874", "610361", "612858"], "umls": ["C0008924"], "icd-10": ["Q36.0", "Q36.1", "Q36.9"]}
ROHHAD Other namesROHHADNET A photograph of a child who has been diagnosed with ROHHAD Symptomsrapid onset obesity, hypothalamic dysfunction, hypoventilation, autonomic dysfunction, neuroendocrine tumors, behavior problems Usual onset1.5-11 years of age Causesunknown PrognosisLife Limiting Frequency158 ...
ROHHAD
c4053506
7,444
wikipedia
https://en.wikipedia.org/wiki/ROHHAD
2021-01-18T18:33:59
{"gard": ["10407"], "umls": ["C4053506"], "orphanet": ["293987"], "wikidata": ["Q4420133"]}
A number sign (#) is used with this entry because of evidence that Bartsocas-Papas syndrome (BPS), also known as the lethal type of popliteal pterygium syndrome, is caused by homozygous mutation in the RIPK4 gene (605706) on chromosome 21q22. Biallelic mutation in the RIPK4 gene can also cause CHAND syndrome (CHANDS...
BARTSOCAS-PAPAS SYNDROME
c1849718
7,445
omim
https://www.omim.org/entry/263650
2019-09-22T16:23:15
{"doid": ["0060055"], "mesh": ["C564874"], "omim": ["263650"], "orphanet": ["1234"], "synonyms": ["Alternative titles", "POPLITEAL PTERYGIUM SYNDROME, LETHAL TYPE", "PTERYGIUM, POPLITEAL, LETHAL TYPE", "MULTIPLE PTERYGIUM SYNDROME, ASLAN TYPE"]}
Pelger–Huët anomaly Other namesPHA[1] blood smear of a patient with myelodysplastic syndrome: red blood cells showing marked poikilocytosis, in part related to post-splenectomy status, and central a hypogranular neutrophil with a pseudo-Pelger-Huet nucleus. Pronunciation * US: /ˈpɛlɡər ˈhuːɛt/ Dutch pronun...
Pelger–Huët anomaly
c0030779
7,446
wikipedia
https://en.wikipedia.org/wiki/Pelger%E2%80%93Hu%C3%ABt_anomaly
2021-01-18T18:51:59
{"gard": ["9148"], "mesh": ["D010381"], "umls": ["C0030779", "C4023351"], "icd-9": ["288.2"], "icd-10": ["D72.0"], "wikidata": ["Q975182"]}
Cystic fibrosis-gastritis-megaloblastic anemia, or Lubani-Al Saleh-Teebi syndrome, is a rare genetic disease reported in two siblings of consanguineous Arab parents and is characterized by cystic fibrosis, gastritis associated with Helicobacter pylori, folate deficiency megaloblastic anemia, and intellectual disa...
Cystic fibrosis-gastritis-megaloblastic anemia syndrome
c2931402
7,447
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2575
2021-01-23T17:30:56
{"gard": ["3303"], "mesh": ["C537039"], "omim": ["219721"], "umls": ["C2931402"], "synonyms": ["Lubani-Al Saleh-Teebi syndrome"]}
Pseudohypoparathyroidism (PHP) is a heterogeneous group of endocrine disorders characterized by normal renal function and resistance to the action of parathyroid hormone (PTH), manifesting with hypocalcemia, hyperphosphatemia and elevated PTH levels and that includes the subtypes PHP type 1a (PHP-1a) , PHP type 1b (P...
Pseudohypoparathyroidism
c0033806
7,448
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=97593
2021-01-23T16:54:25
{"gard": ["10758"], "mesh": ["D011547"], "umls": ["C0033806"], "icd-10": ["E20.1"]}
Eruptive pseudoangiomatosis SpecialtyDermatology Eruptive pseudoangiomatosis is a cutaneous condition characterized by the sudden appearance of 2- to 4-mm blanchable red papules.[1]:399 It can appear in children or adults.[2] The papules appear similar to hemangiomas[3] (hence the name). Viruses found in pa...
Eruptive pseudoangiomatosis
c2242648
7,449
wikipedia
https://en.wikipedia.org/wiki/Eruptive_pseudoangiomatosis
2021-01-18T19:01:59
{"umls": ["C2242648"], "wikidata": ["Q17120185"]}
A number sign (#) is used with this entry because of evidence that an autosomal dominant form of Bernard-Soulier syndrome can be caused by heterozygous mutations in the gene encoding platelet glycoprotein Ib-alpha (GP1BA; 606672) on chromosome 17p. Homozygous or compound heterozygous mutations in the GP1BA gene ...
BERNARD-SOULIER SYNDROME, TYPE A2, AUTOSOMAL DOMINANT
c0005129
7,450
omim
https://www.omim.org/entry/153670
2019-09-22T16:38:41
{"doid": ["0111059"], "mesh": ["D001606"], "omim": ["153670"], "orphanet": ["274"]}
Hyperandrogenism Other namesAndrogen excess Testosterone is a type of androgen that is important in the development of hyperandrogenism since high levels of it can cause this condition. Pronunciation * 'hīpər'andrəjənizəm SpecialtyEndocrinology SymptomsAcne, hair loss on scalp, increased body or fa...
Hyperandrogenism
c0206081
7,451
wikipedia
https://en.wikipedia.org/wiki/Hyperandrogenism
2021-01-18T18:56:17
{"mesh": ["D017588"], "umls": ["C0206081"], "icd-10": ["E28.1"], "wikidata": ["Q10529545"]}
## Clinical Features Efe Pygmies from the Ituri forest of northeast Zaire have the shortest mean adult stature of any population on earth, with a mean adult male height of 4 feet, 8 inches, and a mean adult female height of 4 feet, 5 inches (Diamond, 1991). Biochemical Features Rimoin et al. (1969) found that...
PYGMY
c1849524
7,452
omim
https://www.omim.org/entry/265850
2019-09-22T16:22:58
{"omim": ["265850"], "synonyms": ["Alternative titles", "PYGMY, AFRICAN"]}
Klumpke's paralysis Other namesKlumpke's palsy, Dejerine–Klumpke palsy Brachial plexus. Klumpke paralysis primarily affects C8 and T1. SpecialtyNeurology Klumpke's paralysis is a variety of partial palsy of the lower roots of the brachial plexus.[1][2] The brachial plexus is a network of spinal nerves that...
Klumpke paralysis
c0270898
7,453
wikipedia
https://en.wikipedia.org/wiki/Klumpke_paralysis
2021-01-18T19:06:45
{"gard": ["3123"], "mesh": ["D020516"], "umls": ["C0270898"], "icd-9": ["767.6"], "icd-10": ["P14.1"], "wikidata": ["Q2336817"]}
Cataract-hypertrichosis-intellectual disability syndrome is characterized by congenital cataract, generalized hypertrichosis and intellectual deficit. It has been described in two Egyptian sibs born to consanguineous parents. It is transmitted as an autosomal recessive trait. *[v]: View this template *[t]: D...
Cataract-hypertrichosis-intellectual disability syndrome
c0796282
7,454
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1375
2021-01-23T19:01:03
{"mesh": ["C537959"], "omim": ["211770"], "umls": ["C0796282"], "icd-10": ["Q87.8"], "synonyms": ["CAHMR syndrome"]}
## Clinical Features Mondino and Brown (1976) described a family of Irish descent in which 5 persons in 4 generations showed markedly deficient lacrimation from infancy and punctate corneal epithelial erosions. Male-to-male transmission was observed. Hypoplasia of the lacrimal glands was suggested by pharmacologic ...
ALACRIMA, CONGENITAL, AUTOSOMAL DOMINANT
c1863199
7,455
omim
https://www.omim.org/entry/103420
2019-09-22T15:41:19
{"mesh": ["C566307"], "omim": ["103420"], "orphanet": ["91416"], "synonyms": ["Alternative titles", "ALACRIMIA CONGENITA, AUTOSOMAL DOMINANT"]}
For other uses, see Red eye (disambiguation). This article may be too technical for most readers to understand. Please help improve it to make it understandable to non-experts, without removing the technical details. (April 2012) (Learn how and when to remove this template message) Red eye Subconjunctival hem...
Red eye (medicine)
c0235267
7,456
wikipedia
https://en.wikipedia.org/wiki/Red_eye_(medicine)
2021-01-18T18:37:31
{"umls": ["C0235267"], "icd-9": ["379.93"], "icd-10": ["H57.9"], "wikidata": ["Q2610154"]}
A rare multiple congenital anomalies/dysmorphic syndrome with intellectual disability characterized by mild global developmental delay, intellectual disability or learning difficulties, behavioral problems (like autistic, hyperactive, or aggressive behavior), variable dysmorphic craniofacial features, and abnorma...
Micrognathia-recurrent infections-behavioral abnormalities-mild intellectual disability syndrome
c4310740
7,457
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=476126
2021-01-23T17:26:32
{"omim": ["617061"]}
Spinocerebellar ataxia 13 (SCA13) is a rare sub-type of spinocerebellar ataxias (SCA), a group of neurological diseases that causes degeneration of the brain and spinal cord. The age when symptoms begin and the type and severity of symptoms of SCA13 can be different from person to person even in the same family. In a...
Spinocerebellar ataxia 13
c1854488
7,458
gard
https://rarediseases.info.nih.gov/diseases/9611/spinocerebellar-ataxia-13
2021-01-18T17:57:37
{"mesh": ["C537195"], "omim": ["605259"], "umls": ["C1854488"], "orphanet": ["98768"], "synonyms": ["SCA13", "Spinocerebellar ataxia type 13", "Cerebellar ataxia, autosomal dominant with mental retardation", "Autosomal dominant cerebellar ataxia with mental retardation"]}
A rare mycosis characterized by granulomatous inflammation primarily of the lung after inhalation of spores of Histoplasma capsulatum. The severity of clinical disease depends on the immune status of the individual and the size of the inoculum. In immunocompetent persons, the infection usually takes a self-limiting a...
Histoplasmosis
c0019655
7,459
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=390
2021-01-23T19:03:27
{"mesh": ["D006660"], "umls": ["C0019655", "C0153261"], "icd-10": ["B39.0", "B39.1", "B39.2", "B39.3", "B39.4", "B39.5", "B39.9"], "synonyms": ["Darling disease"]}
Chronic graft versus host disease (GVHD) is a complication that can occur after a stem cell or bone marrow transplant in which the newly transplanted donor cells attack the transplant recipient's body. Symptoms may include skin rash, mouth sores, dry eyes, liver inflammation, development of scar tissue in the skin an...
Chronic graft versus host disease
c0867389
7,460
gard
https://rarediseases.info.nih.gov/diseases/10964/chronic-graft-versus-host-disease
2021-01-18T18:01:18
{"synonyms": ["Chronic GVHD"]}
A number sign (#) is used with this entry because of evidence that intellectual developmental disorder with dysmorphic facies and behavioral abnormalities (IDDFBA) is caused by heterozygous mutation in the FBXO11 gene (607871) on chromosome 2p16. Clinical Features Gregor et al. (2018) reported 18 unrelated patients...
INTELLECTUAL DEVELOPMENTAL DISORDER WITH DYSMORPHIC FACIES AND BEHAVIORAL ABNORMALITIES
None
7,461
omim
https://www.omim.org/entry/618089
2019-09-22T15:43:45
{"omim": ["618089"]}
Glycogen storage disease type VII (GSDVII) is an inherited disorder caused by an inability to break down a complex sugar called glycogen in muscle cells. A lack of glycogen breakdown interferes with the function of muscle cells. There are four types of GSDVII. They are differentiated by their signs and symptoms and ...
Glycogen storage disease type VII
c0017926
7,462
medlineplus
https://medlineplus.gov/genetics/condition/glycogen-storage-disease-type-vii/
2021-01-27T08:25:19
{"gard": ["5686"], "mesh": ["D006014"], "omim": ["232800"], "synonyms": []}
Khosravi et al. (1998) described 3 sibs (2 males, 1 female) with multiple congenital anomalies, poor growth, seizures, and progressive central nervous system degeneration leading to death in infancy. Radiographic changes were similar and included moderate shortness of long bones, platyspondyly, and hypoplastic pelvis...
SKELETAL DYSPLASIA AND PROGRESSIVE CENTRAL NERVOUS SYSTEM DEGENERATION, LETHAL
c1865117
7,463
omim
https://www.omim.org/entry/602613
2019-09-22T16:13:34
{"mesh": ["C566514"], "omim": ["602613"]}
Septo-optic dysplasia Other namesde Morsier syndrome[1][2] The optic nerve is underdeveloped in this condition SpecialtyOphthalmology Septo-optic dysplasia (SOD), known also as de Morsier syndrome, is a rare congenital malformation syndrome that features a combination of the underdevelopment of the optic n...
Septo-optic dysplasia
c0338503
7,464
wikipedia
https://en.wikipedia.org/wiki/Septo-optic_dysplasia
2021-01-18T18:28:38
{"gard": ["7627"], "mesh": ["D025962"], "umls": ["C0338503"], "icd-9": ["742.2"], "orphanet": ["3157"], "wikidata": ["Q2756703"]}
Donohue syndrome insulin receptor SpecialtyEndocrinology, rheumatology, medical genetics Donohue syndrome (also known as leprechaunism) is an extremely rare and severe genetic disorder. Leprechaunism derives its name from the hallmark elvish features (small stature, bulging eyes, thick lips, and upturned...
Donohue syndrome
c0271695
7,465
wikipedia
https://en.wikipedia.org/wiki/Donohue_syndrome
2021-01-18T18:28:00
{"gard": ["6885"], "mesh": ["D056731"], "umls": ["C0271695", "C0265344"], "orphanet": ["508"], "wikidata": ["Q2467739"]}
Pseudoxanthoma elasticum Other namesGrönblad–Strandberg syndrome;[1] Groenblad-Strandberg syndrome Pseudoxanthoma elasticum of the posterior lateral neck. Note the yellowish slightly raised bumps characteristic of this condition. SpecialtyMedical genetics Pseudoxanthoma elasticum (PXE) is a genetic dis...
Pseudoxanthoma elasticum
c3279393
7,466
wikipedia
https://en.wikipedia.org/wiki/Pseudoxanthoma_elasticum
2021-01-18T18:29:41
{"gard": ["9643"], "mesh": ["D011561"], "umls": ["C3279393", "C0376359", "C3279392"], "orphanet": ["758"], "wikidata": ["Q1052391"]}
A number sign (#) is used with this entry because of evidence that Perrault syndrome-2 (PRLTS2) is caused by compound heterozygous mutation in the HARS2 gene (600783) on chromosome 5q31. One such family has been reported. Description Perrault syndrome-2 is an autosomal recessive disorder characterized by sensor...
PERRAULT SYNDROME 2
c0685838
7,467
omim
https://www.omim.org/entry/614926
2019-09-22T15:53:46
{"doid": ["0050857"], "mesh": ["C537286"], "omim": ["614926"], "orphanet": ["2855"], "genereviews": ["NBK242617"]}
Familial thoracic aortic aneurysm and dissection (familial TAAD) involves problems with the aorta, which is the large blood vessel that distributes blood from the heart to the rest of the body. Familial TAAD affects the upper part of the aorta, near the heart. This part of the aorta is called the thoracic aorta becau...
Familial thoracic aortic aneurysm and dissection
c0392775
7,468
medlineplus
https://medlineplus.gov/genetics/condition/familial-thoracic-aortic-aneurysm-and-dissection/
2021-01-27T08:25:41
{"gard": ["2249"], "mesh": ["C536230"], "omim": ["607086", "607087", "132900", "611788", "613780", "615436"], "synonyms": []}
Lhermitte-Duclos disease (LDD) is a very rare, benign (non-cancerous) brain tumor, called a dysplastic gangliocytoma of the cerebellum, that is characterized by abnormal development and enlargement of the cerebellum, and an increased intracranial pressure. LDD manifests most commonly in the third and fourth decades o...
Lhermitte-Duclos disease
c0391826
7,469
gard
https://rarediseases.info.nih.gov/diseases/6901/lhermitte-duclos-disease
2021-01-18T17:59:25
{"mesh": ["D006223"], "omim": ["158350"], "umls": ["C0391826"], "orphanet": ["65285"], "synonyms": ["Dysplastic gangliocytoma of the cerebellum"]}
For a phenotypic description and a discussion of genetic heterogeneity of bipolar disorder, see 125480. Mapping Ferreira et al. (2008) tested 1.8 million variants in 4,387 cases of bipolar disorder and 6,209 controls from 3 independent samples and identified a region of strong association with SNP rs1006737 in the ...
MAJOR AFFECTIVE DISORDER 9
c2700440
7,470
omim
https://www.omim.org/entry/612372
2019-09-22T16:01:40
{"mesh": ["C567531"], "omim": ["612372"], "synonyms": ["Alternative titles", "BIPOLAR AFFECTIVE DISORDER"]}
A rare neurologic disease characterized by an unremitting bilateral symmetrical burning sensation of the oral mucosa without clinical evidence of causative lesions. It most frequently occurs in postmenopausal women and typically affects the tongue, less often the palate, lips, or buccal mucosa. It is often associated...
Burning mouth syndrome
c0006430
7,471
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=353253
2021-01-23T18:44:03
{"gard": ["5974"], "mesh": ["D002054"], "umls": ["C0006430", "C2930806"], "icd-10": ["K14.6"], "synonyms": ["BMS", "Oral dysesthesia", "Orodynia", "Stomatodynia", "Stomatopyrosis"]}
A rare joint formation defect characterized by a bony connection between the humerus and the ulna, resulting in fixed flexion of the forearm, usually near 90°. The condition may be associated with upper limb hypoplasia. It may be sporadic or familial and occur uni- or bilaterally. *[v]: View this template *[t]: ...
Humero-ulnar synostosis
c0431799
7,472
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=94056
2021-01-23T17:26:50
{"umls": ["C0431799"], "icd-10": ["Q74.0"], "synonyms": ["Humero-ulnar fusion"]}
A number sign (#) is used with this entry because mitochondrial phosphate carrier deficiency can be caused by mutation in the SLC25A3 gene (600370). Clinical Features Mayr et al. (2007) described 2 sisters, offspring of nonconsanguineous Turkish parents, with mitochondrial phosphate carrier deficiency. The younger ...
MITOCHONDRIAL PHOSPHATE CARRIER DEFICIENCY
c1835845
7,473
omim
https://www.omim.org/entry/610773
2019-09-22T16:04:05
{"mesh": ["C563665"], "omim": ["610773"], "orphanet": ["91130"], "synonyms": ["Alternative titles", "MPCD"]}
Halogenoderma SpecialtyDermatology Halogenodermas are skin eruptions that result after exposure to halogen-containing drugs or substances. This may last several weeks after drug use is discontinued. This is because of the slow elimination rate of iodides and bromides.[1] Fluoroderma is a particular type of hal...
Halogenoderma
c1274946
7,474
wikipedia
https://en.wikipedia.org/wiki/Halogenoderma
2021-01-18T18:41:53
{"umls": ["C1274946"], "wikidata": ["Q5643382"]}
Prader-Willi syndrome (PWS) is a genetic condition that affects many parts of the body. Infants with PWS have severe hypotonia (low muscle tone), feeding difficulties, and slow growth. In later infancy or early childhood, affected children typically begin to eat excessively and become obese. Other signs and sympt...
Prader-Willi syndrome
c0032897
7,475
gard
https://rarediseases.info.nih.gov/diseases/5575/prader-willi-syndrome
2021-01-18T17:58:13
{"mesh": ["D011218"], "omim": ["176270"], "umls": ["C0032897"], "orphanet": ["739"], "synonyms": ["PWS", "Willi-Prader syndrome", "Prader-Labhart-Willi syndrome", "Obesity, muscular hypotonia, mental retardation, short stature, hypogonadotropic hypogonadism, and small hands and feet"]}
Behavioral disorder in which an adult fakes an illness in another, most commonly their child Factitious disorder imposed on another Other namesFactitious disorder by proxy, Munchausen syndrome by proxy (MSbP, MbP), fabricated or induced illness by carers (FII), medical child abuse Overview of factitious disorder...
Factitious disorder imposed on another
c0085277
7,476
wikipedia
https://en.wikipedia.org/wiki/Factitious_disorder_imposed_on_another
2021-01-18T18:35:48
{"gard": ["7117"], "mesh": ["D016735"], "umls": ["C0085277"], "wikidata": ["Q1414765"]}
Homocystinuria Other namesCystathionine beta synthase deficiency or CBS deficiency[1] Homocysteine SpecialtyEndocrinology, medical genetics Homocystinuria or HCU[2] is an inherited disorder of the metabolism of the amino acid methionine due to a deficiency of cystathionine beta synthase or methionine synth...
Homocystinuria
c0019880
7,477
wikipedia
https://en.wikipedia.org/wiki/Homocystinuria
2021-01-18T19:01:19
{"gard": ["10770"], "mesh": ["D006712"], "umls": ["C0019880"], "icd-9": ["270.4"], "orphanet": ["394"], "wikidata": ["Q994859"]}
A rare staphylococcal toxemia caused by epidermolytic toxins of Staphylococcus aureus and characterized by the appearance of widespread erythematous patches, on which large blisters develop. Upon rupture of these blisters, the skin appears reddish and scalded. The lesions typically begin in the face and rapidly e...
Staphylococcal scalded skin syndrome
c0038165
7,478
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=36236
2021-01-23T18:54:22
{"mesh": ["D013206"], "umls": ["C0038165"], "icd-10": ["L00"], "synonyms": ["Generalized exfoliative disease", "SSSS"]}
This article has multiple issues. Please help improve it or discuss these issues on the talk page. (Learn how and when to remove these template messages) This article needs attention from an expert in Medicine. Please add a reason or a talk parameter to this template to explain the issue with the article. WikiProjec...
Physical disorder
c0683323
7,479
wikipedia
https://en.wikipedia.org/wiki/Physical_disorder
2021-01-18T18:30:12
{"wikidata": ["Q30314000"]}
Intra-operative gross photograph of the spleen attached to the left testis in a 1-year old boy with splenogonadal fusion Splenogonadal fusion is a rare congenital malformation that results from an abnormal connection between the primitive spleen and gonad during gestation. A portion of the splenic tissue then descen...
Splenogonadal fusion
c0266636
7,480
wikipedia
https://en.wikipedia.org/wiki/Splenogonadal_fusion
2021-01-18T18:55:47
{"orphanet": ["457083"], "synonyms": ["SGF"], "wikidata": ["Q7578553"]}
Porcine orthorubulavirus Virus classification (unranked): Virus Realm: Riboviria Kingdom: Orthornavirae Phylum: Negarnaviricota Class: Monjiviricetes Order: Mononegavirales Family: Paramyxoviridae Genus: Orthorubulavirus Species: Porcine orthorubulavirus Member virus[1] * La-P...
Blue eye disease
None
7,481
wikipedia
https://en.wikipedia.org/wiki/Blue_eye_disease
2021-01-18T18:32:19
{"wikidata": ["Q4929100"]}
A rare genetic syndromic intellectual disability characterized by aplasia or hypoplasia of the distal phalanx or nail of the fifth digit, developmental delay, coarse facial features, and other variable clinical manifestations. ## Epidemiology More than 150 cases of genetically confirmed Coffin-Siris syndrome (C...
Coffin-Siris syndrome
c0265338
7,482
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1465
2021-01-23T17:23:20
{"gard": ["6124"], "mesh": ["C536436"], "omim": ["135900", "614607", "614608", "614609", "615866", "616938", "617808", "618027", "618362", "618779"], "umls": ["C0265338"], "icd-10": ["Q87.1"], "synonyms": ["CSS"]}
Shoulder injury This article relies largely or entirely on a single source. Relevant discussion may be found on the talk page. Please help improve this article by introducing citations to additional sources. Find sources: "Glenolabral articular disruption" – news · newspapers · books · scholar · JSTOR (April 2014)...
Glenolabral articular disruption
None
7,483
wikipedia
https://en.wikipedia.org/wiki/Glenolabral_articular_disruption
2021-01-18T18:30:28
{"wikidata": ["Q16004474"]}
Purine nucleoside phosphorylase deficiency Other namesPNP-deficiency Purine nucleoside phosphorylase deficiency has an autosomal recessive pattern of inheritance TreatmentAllegeneic hemotopoietic stem cell transplantation (HSCT) Purine nucleoside phosphorylase deficiency, is a rare autosomal recessive[...
Purine nucleoside phosphorylase deficiency
c0268125
7,484
wikipedia
https://en.wikipedia.org/wiki/Purine_nucleoside_phosphorylase_deficiency
2021-01-18T19:06:50
{"gard": ["4606"], "mesh": ["C562587"], "umls": ["C0268125"], "icd-9": ["277.2"], "orphanet": ["760"], "wikidata": ["Q3043155"]}
North Carolina macular dystrophy (NCMD) is an inherited eye disorder that affects the development of the macula, the small, but important part of the eye located in the center of the retina. The macula allows a person to see fine details and do tasks that require central vision, such as reading and driving. It is...
North Carolina macular dystrophy
c0730294
7,485
gard
https://rarediseases.info.nih.gov/diseases/9179/north-carolina-macular-dystrophy
2021-01-18T17:58:39
{"mesh": ["C537835"], "omim": ["136550"], "umls": ["C0730294"], "orphanet": ["75327"], "synonyms": ["NCMD", "Macular dystrophy retinal 1 North Carolina type", "MCDR1", "Central areolar pigment epithelial dystrophy", "CAPED", "Retinal pigment epithelial dystrophy central", "Foveal dystrophy progressive"]}
Underterminate colitis designates a rare inflammatory bowel disease that clinically resembles Crohn’s disease and ulcerative colitis (see these terms) but that cannot be diagnosed as one of them after examination of an intestinal resection specimen. *[v]: View this template *[t]: Discuss this template *[e]: Ed...
Undetermined colitis
None
7,486
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=103920
2021-01-23T17:46:15
{"icd-10": ["K52.3"]}
## Description Restless legs syndrome (RLS) is a neurologic sleep/wake disorder characterized by uncomfortable and unpleasant sensations in the legs that appear at rest, usually at night, inducing an irresistible desire to move the legs. The disorder results in nocturnal insomnia and chronic sleep deprivation (Bona...
RESTLESS LEGS SYNDROME, SUSCEPTIBILITY TO, 4
c1864874
7,487
omim
https://www.omim.org/entry/610439
2019-09-22T16:04:39
{"omim": ["610439"]}
Pseudotyphus of California is a rare, flea-borne Rickettsial disease caused by a Rickettsia felis infection. Patients can be asymptomatic or can present with unspecific symptoms (such as fever, headache, generalized maculopapular rash, myalgia, arthralgia and, ocasionally, eschar, lymphadenopathy, nausea, vomiting, ...
Pseudotyphus of California
c4706680
7,488
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=83316
2021-01-23T16:54:22
{"icd-10": ["A79.8"]}
A number sign (#) is used with this entry because of evidence that autosomal recessive deafness-1A (DFNB1A) is caused by homozygous or compound heterozygous mutation in the GJB2 gene (121011), which encodes the gap junction protein connexin-26 (CX26), on chromosome 13q12. Autosomal dominant deafness-3A (DFNA3A; 6015...
DEAFNESS, AUTOSOMAL RECESSIVE 1A
c2673761
7,489
omim
https://www.omim.org/entry/220290
2019-09-22T16:28:59
{"doid": ["0110475"], "mesh": ["C567134"], "omim": ["220290"], "orphanet": ["90636"], "synonyms": ["Autosomal recessive isolated neurosensory deafness type DFNB", "Autosomal recessive isolated sensorineural deafness type DFNB", "Autosomal recessive non-syndromic neurosensory deafness type DFNB"], "genereviews": ["NBK14...
Schizophrenia is a brain disorder classified as a psychosis, which means that it affects a person's thinking, sense of self, and perceptions. The disorder typically becomes evident during late adolescence or early adulthood. Signs and symptoms of schizophrenia include false perceptions called hallucinations. Auditor...
Schizophrenia
c0036341
7,490
medlineplus
https://medlineplus.gov/genetics/condition/schizophrenia/
2021-01-27T08:25:12
{"mesh": ["D012559"], "omim": ["181500"], "synonyms": []}
A number sign (#) is used with this entry because alpha/beta T-cell lymphopenia with gamma/delta T-cell expansion, severe cytomegalovirus (CMV) infection, and autoimmunity is caused by mutations in the RAG1 gene (179615). Mutations in the RAG1 gene also cause T cell-negative, B cell-negative, natural killer (NK) cell...
ALPHA/BETA T-CELL LYMPHOPENIA WITH GAMMA/DELTA T-CELL EXPANSION, SEVERE CYTOMEGALOVIRUS INFECTION, AND AUTOIMMUNITY
c1835931
7,491
omim
https://www.omim.org/entry/609889
2019-09-22T16:05:30
{"mesh": ["C563691"], "omim": ["609889"], "orphanet": ["231154"]}
Chester porphyria is a unique type of porphyria with the signs and symptoms of acute intermittent porphyria (AIP) and the biochemical defects of both AIP and variegate porphyria (VP). Chester porphyria does not conform to any of the recognized types of acute porphyria. The symptoms associated with Chester porphyria a...
Chester porphyria
c0268322
7,492
gard
https://rarediseases.info.nih.gov/diseases/10185/chester-porphyria
2021-01-18T18:01:30
{"mesh": ["C536341"], "omim": ["176010"], "umls": ["C0268322"], "synonyms": ["Porphyria, Chester type", "PORC"]}
Straddling or overriding tricuspid valve is a rare, congenital, tricuspid valve malformation characterized by the tricuspid valve that overrides the ventricular septum and communicates with both ventricles, as part of the tension apparatus of the valve crosses the ventricular septal defect and is attached in the left...
Straddling or overriding tricuspid valve
None
7,493
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=95461
2021-01-23T16:56:08
{"icd-10": ["Q22.8"]}
## Summary ### Clinical characteristics. All FOXP2-related speech and language disorders, regardless of the underlying genetic alteration, have a core phenotype: childhood apraxia of speech (CAS), a disorder of speech motor programming or planning that affects the production, sequencing, timing, and stress of sound...
FOXP2-Related Speech and Language Disorders
None
7,494
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK368474/
2021-01-18T21:27:20
{"synonyms": []}
Lowe syndrome is a condition that primarily affects the eyes, brain, and kidneys. This disorder occurs almost exclusively in males. Infants with Lowe syndrome are born with thick clouding of the lenses in both eyes (congenital cataracts), often with other eye abnormalities that can impair vision. About half of affec...
Lowe syndrome
c0028860
7,495
medlineplus
https://medlineplus.gov/genetics/condition/lowe-syndrome/
2021-01-27T08:25:07
{"gard": ["3295"], "mesh": ["D009800"], "omim": ["309000"], "synonyms": []}
A rare, clinically heterogeneous, multisystemic inflammatory disease characterized by inflammation of the cartilage and proteoglycan rich structures leading to cartilage damage along with joint, ocular and cardiovascular involvement. ## Epidemiology The prevalence and annual incidence of Relapsing polychondritis (R...
Relapsing polychondritis
c0032453
7,496
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=728
2021-01-23T17:18:13
{"gard": ["7417"], "mesh": ["D011081"], "umls": ["C0032453"], "icd-10": ["M94.1"], "synonyms": ["Polychondropathia"]}
A lysosomal storage disease belonging to the group of sphingolipidoses. ## Epidemiology It is very rare with less than 10 cases reported in the literature so far. ## Clinical description Clinically, it is a severe neurovisceral disease manifesting immediately after birth and following a rapidly progressive fatal ...
Encephalopathy due to prosaposin deficiency
c2673635
7,497
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=139406
2021-01-23T18:51:02
{"gard": ["12505"], "mesh": ["C567125"], "omim": ["611721"], "icd-10": ["E75.2"], "synonyms": ["Combined prosaposin deficiency"]}
Maffucci syndrome is a disorder that primarily affects the bones and skin. It is characterized by multiple enchondromas, which are noncancerous (benign) growths of cartilage that develop within the bones. These growths most commonly occur in the limb bones, especially in the bones of the hands and feet; however, they...
Maffucci syndrome
c0024454
7,498
medlineplus
https://medlineplus.gov/genetics/condition/maffucci-syndrome/
2021-01-27T08:25:51
{"gard": ["6958"], "mesh": ["D004687"], "omim": ["614569"], "synonyms": []}
Glycogenic acanthosis Endoscopic image of glycogenic acanthosis found incidentally SpecialtyGastroenterology Glycogenic acanthosis are small raised white plaques commonly seen in the esophageal mucosa.[1] It is seen incidentally in 3.5% of gastroscopies.[2] ## Contents * 1 Signs and symptoms * 2 Diagno...
Glycogenic acanthosis
c1963768
7,499
wikipedia
https://en.wikipedia.org/wiki/Glycogenic_acanthosis
2021-01-18T18:29:02
{"umls": ["C1963768"], "wikidata": ["Q5572612"]}