serial-number
stringlengths
6
9
pmcid
stringclasses
138 values
text
stringclasses
138 values
context
stringclasses
138 values
role
stringclasses
18 values
role-name
stringclasses
18 values
raw-initial-ground-truth
listlengths
0
18
test-1901
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Eyes-Ears-Nose-Throat
EENT
[]
test-1902
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Dermatology
DERM
[ "apparent reduction of the subcutaneous adipose tissue", "inverted triangular face, sparse subcutaneous tissue", "generalized reduction in the subcutaneous adipose tissue" ]
test-1903
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Pregnancy
Pregnancy
[ "born at 36 wk of gestational age", "born to non - consanguineous Japanese parents at 38 wk of gestational age" ]
test-1904
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Lymphatic-System
LYMPH
[]
test-1905
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Age-at-Presentation
Age (at case presentation)
[ "16 yr and 4 mo of age" ]
test-1906
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Age-of-Onset
Age (of onset)
[ "1 mo of age .", "3 mo of age" ]
test-1907
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
Confirmed-Diagnosis-IEM
Confirmed_Diagnosis(IEM)
[ "CGL", "She was therefore diagnosed with CGL ( Berardinelli - Seip syndrome ) ." ]
test-1908
6801357
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
{'Case 2': 'The male patient who was born at 36 wk of gestational age was the younger (3 yr younger) brother of case 1. He also showed apparent reduction of the subcutaneous adipose tissue at 1 mo of age. At that time, he already had characteristic symptoms of CGL, including an inverted triangular face, sparse subcutan...
IEM-Treatment
IEM_Treatment
[ "At 11 yr and 6 mo of age , metreleptin was introduced at a dose of 0.04 mg / kg / d , and there was an immediate improvement of hyperinsulinemia and hyperlipidemia", "At 11 yr and 5 mo of age , she was enrolled in a clinical trial of metreleptin . Metreleptin treatment was initiated at a dose of 0.06 mg / kg / d...
test-1909
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Vitals-and-Hematology
Vitals_Hema
[ "( height=107 cm, z -score=-0.4, 32nd percentile; weight=20.8 kg, z -score=+0.8, 80th percentile; body mass index=18.2 kg / m 2 )", "height=170 cm, z -score=-0.8, 21st percentile; weight=110 kg, z -score=+2.4, 99th percentile; BMI=38.1 kg / m 2", "height=94 cm, z -score=-0.05, 48th percentile; weight=14 kg, z -...
test-1910
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Gastrointestinal-System
GI
[]
test-1911
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Patient-History
History
[ "The proband was a male born to consanguineous parents ( Fig. 1 ). He had an acute viral fever at 4 years of age, and was found to have mild hyponatremia and hyperkalemia ( sodium 131 mEq / L and potassium 6.1 mEq / L, respectively )", "no history of prostration with illness, and normally - timed pubertal changes...
test-1912
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Neurology
Neuro
[]
test-1913
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Laboratory-and-Imaging
Lab_Image
[ "mild hyponatremia and hyperkalemia ( sodium 131 mEq / L and potassium 6.1 mEq / L, respectively ). Further investigation revealed increased 17 - hydroxyprogesterone ( 17 - OHP ) and adrenocorticotropic hormone ( ACTH ) levels ( Table 1 ), and a suboptimal rise in cortisol levels following ACTH1 - 24 stimulation ( ...
test-1914
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Cardiovascular-System
CVS
[]
test-1915
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Endocrinology
ENDO
[ "mild hyponatremia and hyperkalemia ( sodium 131 mEq / L and potassium 6.1 mEq / L, respectively ). Further investigation revealed increased 17 - hydroxyprogesterone ( 17 - OHP ) and adrenocorticotropic hormone ( ACTH ) levels ( Table 1 ), and a suboptimal rise in cortisol levels following ACTH1 - 24 stimulation ( ...
test-1916
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Genitourinary-System
GU
[ "mild hyponatremia and hyperkalemia ( sodium 131 mEq / L and potassium 6.1 mEq / L, respectively )", "normal male genitalia, descended testes, and no evidence of precocious adrenarche or puberty", "normal testes with Tanner stage V pubic hair", "normal serum electrolytes" ]
test-1917
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Respiratory-System
RESP
[]
test-1918
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Musculoskeletal-System
MSK
[ ". At the time of diagnosis proband was of normal growth and stature ( height=107 cm, z -score=-0.4, 32nd percentile; weight=20.8 kg, z -score=+0.8, 80th percentile; body mass index=18.2 kg / m 2 ).", "He was obese with normal stature ( height=170 cm, z -score=-0.8, 21st percentile; weight=110 kg, z -score=+2.4, ...
test-1919
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Eyes-Ears-Nose-Throat
EENT
[]
test-1920
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Dermatology
DERM
[ "no hirsutism" ]
test-1921
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Pregnancy
Pregnancy
[]
test-1922
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Lymphatic-System
LYMPH
[]
test-1923
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Age-at-Presentation
Age (at case presentation)
[ "17 years of age", "age of 15 and 11 months" ]
test-1924
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Age-of-Onset
Age (of onset)
[ "4 years of age ,", "3 - year - old" ]
test-1925
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
Confirmed-Diagnosis-IEM
Confirmed_Diagnosis(IEM)
[ "If p. R124C is pathogenic , the most likely phenotype due to compound heterozygosity for p. R124C and a large deletion would be NC CAH", "a diagnosis of NC CAH was confirmed" ]
test-1926
6177667
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
{'Case report': 'This research related to human use has been complied with all the relevant national regulations, institutional policies and in accordance with the tenants of the Helsinki declaration, and has been approved by the author\'s or equivalent committee. Informed consent was obtained from the parents of the p...
IEM-Treatment
IEM_Treatment
[ "replacement doses of hydrocortisone and fludrocortisone" ]
test-1927
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Vitals-and-Hematology
Vitals_Hema
[ "height 149.0 cm, weight 39.2 kg, BMI 17.7 kg / m 2" ]
test-1928
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Gastrointestinal-System
GI
[ "no history of neonatal jaundice or chronic infantile diarrhea" ]
test-1929
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Patient-History
History
[ "The patient was a 50 - year - old Japanese woman from non - consanguineous parents. She has no siblings but had a child. There was no apparent family history ( parents, child and parent ’s siblings ) of neurological disorders, cardiovascular diseases or any lipid storage diseases inducing xanthomas, including CTX....
test-1930
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Neurology
Neuro
[ "did not have dementia based on the Revised Hasegawa Dementia Scale ( HSD - R; 26/30 ), Mini - Mental State Examination ( MMSE; 27/30 ), and Frontal Assessment Battery ( FAB; 16/18 ) scores. On a neurological examination, her gait appeared somewhat spastic, and all of her deep tendon reflexes were mildly enhanced b...
test-1931
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Laboratory-and-Imaging
Lab_Image
[ "no elevation in the levels of serum cholesterol or triglycerides or deficiencies in apolipoproteins or thyroid hormones", "The primary bile acids were extremely low in the serum and urine when measured by both high - performance liquid chromatography ( HPLC ) and gas chromatography / mass spectrometer ( GC / MS ...
test-1932
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Cardiovascular-System
CVS
[ "Ultrasound of the carotid arteries showed a slightly thickened intima - media complex at the left common carotid artery ( maximum intima - media thickness, 1.2 mm ). However, there was no evidence of cardiovascular disease on electrocardiogram, echocardiography and MR angiography of the brain and lower extremities...
test-1933
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Endocrinology
ENDO
[]
test-1934
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Genitourinary-System
GU
[]
test-1935
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Respiratory-System
RESP
[]
test-1936
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Musculoskeletal-System
MSK
[ "xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle", "osteoporosis as determined by dual - energy X - ray absorptiometry, which showed a bone density of 61 % and 75 % the young - adult - mean in the lumbar vertebra and femoral neck, respectively", "painless tendon thickness of the...
test-1937
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Eyes-Ears-Nose-Throat
EENT
[ "age - appropriate slight cataracts in the bilateral eyes" ]
test-1938
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Dermatology
DERM
[]
test-1939
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Pregnancy
Pregnancy
[ "no history of neonatal jaundice" ]
test-1940
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Lymphatic-System
LYMPH
[]
test-1941
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Age-at-Presentation
Age (at case presentation)
[ "50 - year - old" ]
test-1942
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Age-of-Onset
Age (of onset)
[ "7 to 10 years of age" ]
test-1943
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
Confirmed-Diagnosis-IEM
Confirmed_Diagnosis(IEM)
[ "the patient was diagnosed with CTX" ]
test-1944
6028668
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
{'Clinical, laboratory and imaging examinations': 'The patient was lean (height 149.0 cm, weight 39.2 kg, BMI 17.7 kg/m 2 ), and the findings of a physical examination were unremarkable except for confirmation of xanthomas on the bilateral Achilles tendons ( Fig. 1B ) and right triceps muscle. She had age-appropriate s...
IEM-Treatment
IEM_Treatment
[]
test-1945
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Vitals-and-Hematology
Vitals_Hema
[]
test-1946
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Gastrointestinal-System
GI
[ "poor feeding by breast and bottle" ]
test-1947
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Patient-History
History
[]
test-1948
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Neurology
Neuro
[ "hypotonic, irritable, and demonstrated poor feeding by breast and bottle", "in utero hiccups", "seizure - like activity", "seizures since birth", "MRI showed myelination confined to the brainstem, central cerebellum, and posterior limbs of the internal capsule ( Fig. 1 ). There was T2 hyperintensity of the...
test-1949
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Laboratory-and-Imaging
Lab_Image
[ "MRI showed myelination confined to the brainstem, central cerebellum, and posterior limbs of the internal capsule ( Fig. 1 ). There was T2 hyperintensity of the white matter ( Fig. 2 ) and superior vermian volume loss ( Fig. 3 ). The corpus callosum was unmyelinated. MRI spectroscopy revealed a low N - acetylaspar...
test-1950
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Cardiovascular-System
CVS
[]
test-1951
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Endocrinology
ENDO
[]
test-1952
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Genitourinary-System
GU
[]
test-1953
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Respiratory-System
RESP
[]
test-1954
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Musculoskeletal-System
MSK
[]
test-1955
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Eyes-Ears-Nose-Throat
EENT
[]
test-1956
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Dermatology
DERM
[]
test-1957
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Pregnancy
Pregnancy
[ "born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate" ]
test-1958
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Lymphatic-System
LYMPH
[]
test-1959
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Age-at-Presentation
Age (at case presentation)
[ "age of 3 months" ]
test-1960
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Age-of-Onset
Age (of onset)
[ "in utero" ]
test-1961
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
Confirmed-Diagnosis-IEM
Confirmed_Diagnosis(IEM)
[ "The elevation of these 2 compounds confirmed the diagnosis of adenylosuccinate lyase deficiency ." ]
test-1962
6260459
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
{'Case report': "A male child was born at term by an uncomplicated pregnancy. The patient was hypotonic, irritable, and demonstrated poor feeding by breast and bottle in the first week of life. He had a history of in utero hiccups, which persisted as a neonate. At the age of 3 months, he was admitted to the hospital wi...
IEM-Treatment
IEM_Treatment
[]
test-1963
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Vitals-and-Hematology
Vitals_Hema
[]
test-1964
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Gastrointestinal-System
GI
[]
test-1965
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Patient-History
History
[ "This patient was a 4 - year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added", "Reports of head drop attacks were found in the history", "This patient was a 4 year -...
test-1966
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Neurology
Neuro
[ "head drop attacks", "deep tendon reflexes were diminished or absent. Although cognitive function of this patient was normal, motor and speech development was delayed. Two years later, development of seizure and tremor was reported. Tremor was evident in all limbs on physical examination", "development of neuro...
test-1967
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Laboratory-and-Imaging
Lab_Image
[ "Laboratory serologic tests were normal. Radiography of both hands showed reduction in density of bones, swelling of both wrists, deformity of wrist bones, marginal erosion of wrist bones and distal phalanges in PIP and DIP joints which all were suggestive of advanced juvenile idiopathic arthritis ( JIA ). Chest X ...
test-1968
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Cardiovascular-System
CVS
[]
test-1969
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Endocrinology
ENDO
[]
test-1970
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Genitourinary-System
GU
[]
test-1971
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Respiratory-System
RESP
[ "Chest X - ray also showed alveolar opacities with air bronchogram in the upper lobe of right lung which were in favor of pneumonia", "Bronchoscopy showed a circular contraction in subglottic region of larynx", "wheezing", "admitted 4 times due to respiratory distress. Finally she died from respiratory failur...
test-1972
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Musculoskeletal-System
MSK
[ "wrist swelling", "Swelling of other joints were gradually added", "swelling and limitation in range of motion was detected in PIP, MCP, wrist, elbow and shoulder joints of upper limbs and PIP, MTP, tarsal joints and ankle in lower limbs. Multiple firm subcutaneous nodules were found on joints – mainly on exten...
test-1973
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Eyes-Ears-Nose-Throat
EENT
[ "Progressive hoarseness was present", "Progressive hoarseness was also present. Extensive mucosal lesions were detected in the oral cavity", "nasal swelling", "progression of hoarseness", "admitted 4 times due to respiratory distress. Finally she died from respiratory failure in one episode at 4 years old",...
test-1974
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Dermatology
DERM
[ "Cutaneous lesions were also seen on abdomen", "appearance of cutaneous lesions on the body" ]
test-1975
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Pregnancy
Pregnancy
[ "delivered by cesarean section without any insult", "delivered by NVD who was term on birth", "delivered by NVD without any insult" ]
test-1976
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Lymphatic-System
LYMPH
[]
test-1977
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Age-at-Presentation
Age (at case presentation)
[ "4 - year old", "4 year - old", "9 - month old" ]
test-1978
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Age-of-Onset
Age (of onset)
[ "6 months of age", "7 months of age" ]
test-1979
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
Confirmed-Diagnosis-IEM
Confirmed_Diagnosis(IEM)
[ "confirmed the presence of Farber disease in this patient" ]
test-1980
6944811
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
{'1 st case': 'This patient was a 4-year old girl, second child of related parents, delivered by cesarean section without any insult. This child developed wrist swelling at 6 months of age. Swelling of other joints were gradually added. On examination, swelling and limitation in range of motion was detected in PIP, MCP...
IEM-Treatment
IEM_Treatment
[ "Bone marrow transplantation was suggested as a treatment strategy for the patient" ]
test-1981
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Vitals-and-Hematology
Vitals_Hema
[ "His heart rate was 120 beats per minute and his blood pressure was 100/65 mmHg. His weight and height were 12.8 kg ( 1.5 SDS ) and 86 cm ( 2 SDS ), respectively", "his body weight and length were 16.7 kg ( 0.5 SDS ) and 99.7 cm ( 1.5 SDS ), respectively" ]
test-1982
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Gastrointestinal-System
GI
[ "imperforate anus", "tracheoesophageal fistula was not suspected clinically", "anal atresia", "abdomen was distended and discolored", "bowel necrosis", "peritonitis", "peritonitis", "occasional nausea and vomiting" ]
test-1983
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Patient-History
History
[ "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score ) and 52.5 cm ( z -score, +1.4 SDS ), respectively. There ...
test-1984
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Neurology
Neuro
[ "He was able to ascend stairs with the support of a hand grasp. He could stack 3 cubes, eat without assistance, and pronounce 10 words, meaning that the patient ’s developmental status was normal for his age", "normal growth and development" ]
test-1985
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Laboratory-and-Imaging
Lab_Image
[ "echocardiography revealed a patent ductus arteriosus", "Bilateral grade 3 vesicoureteral reflux ( VUR ) was revealed via voiding cystourethrography. Spine ultrasound revealed no vertebral anomalies, and tracheoesophageal fistula was not suspected clinically", "Laboratory test results, including electrolyte lev...
test-1986
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Cardiovascular-System
CVS
[ "A grade 2 systolic murmur was heard in the left upper sternal border and echocardiography revealed a patent ductus arteriosus", "hypotensive" ]
test-1987
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Endocrinology
ENDO
[]
test-1988
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Genitourinary-System
GU
[ "normal male genitalia, with both testes palpable", "Bilateral grade 3 vesicoureteral reflux ( VUR ) was revealed via voiding cystourethrography", "renal anomalies", "normal male genitalia", "slightly decreased sodium level ( 132 mmol / L ) but normal potassium ( 4.8 mEq / L )", "no abnormalities, such as...
test-1989
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Respiratory-System
RESP
[]
test-1990
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Musculoskeletal-System
MSK
[ "postaxial polydactyly of the left foot", "Spine ultrasound revealed no vertebral anomalies", "limb abnormalities", "postaxial polydactyly of the left foot" ]
test-1991
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Eyes-Ears-Nose-Throat
EENT
[]
test-1992
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Dermatology
DERM
[ "slight bronzing of the patient ’s skin after repeated surgeries", "generalized hyperpigmentation", "child 's hyperpigmentation was markedly exacerbated after exploratory laparotomy for the episode of peritonitis with sepsis", "hyperpigmentation", "generalized hyperpigmentation", "generalized hyperpigment...
test-1993
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Pregnancy
Pregnancy
[ "born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score ) and 52.5 cm ( z -score, +1.4 SDS ), respectively" ]
test-1994
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Lymphatic-System
LYMPH
[]
test-1995
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Age-at-Presentation
Age (at case presentation)
[]
test-1996
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Age-of-Onset
Age (of onset)
[]
test-1997
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
Confirmed-Diagnosis-IEM
Confirmed_Diagnosis(IEM)
[ "This variant has been previously reported in association with CLAH ." ]
test-1998
7136505
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
{'Case report': "A male child was born at a gestational age of 39 weeks with no history of antenatal or perinatal problems. Apgar scores were 9 points at one minute and 10 points at 5 minutes. His birth weight and height were 3,800 g ( z -score, +1 standard deviation score) and 52.5 cm ( z -score, +1.4 SDS), respective...
IEM-Treatment
IEM_Treatment
[ "Hydrocortisone ( 7.8 mg / m 2 /day ) and fludrocortisone ( 50 μg / day ) were started as therapy for primary adrenal insufficiency . The dose of hydrocortisone was gradually increased until the age of 24 months for sufficient ACTH suppression and levels of ACTH and cortisol were subsequently decreased to the optim...
test-1999
7890005
{'Case presentation': 'We report a 38-year old woman who presented with chronic diarrhea and progressive spastic paraparesis in her twenties. Brain magnetic resonance imaging (MRI) showed cerebral atrophy with diffuse periventricular white matter hyperintensities. Spinal MRI was normal. CYP27A1 gene sequencing confirme...
{'Case presentation': 'We report a 38-year old woman who presented with chronic diarrhea and progressive spastic paraparesis in her twenties. Brain magnetic resonance imaging (MRI) showed cerebral atrophy with diffuse periventricular white matter hyperintensities. Spinal MRI was normal. CYP27A1 gene sequencing confirme...
Vitals-and-Hematology
Vitals_Hema
[]
test-2000
7890005
{'Case presentation': 'We report a 38-year old woman who presented with chronic diarrhea and progressive spastic paraparesis in her twenties. Brain magnetic resonance imaging (MRI) showed cerebral atrophy with diffuse periventricular white matter hyperintensities. Spinal MRI was normal. CYP27A1 gene sequencing confirme...
{'Case presentation': 'We report a 38-year old woman who presented with chronic diarrhea and progressive spastic paraparesis in her twenties. Brain magnetic resonance imaging (MRI) showed cerebral atrophy with diffuse periventricular white matter hyperintensities. Spinal MRI was normal. CYP27A1 gene sequencing confirme...
Gastrointestinal-System
GI
[ "chronic diarrhea", "remission of diarrhea", "chronic diarrhea", "Three months later, diarrhea was disappeared", "diarrhea recurred" ]