text
stringlengths
297
230k
title
stringlengths
4
145
cui
stringlengths
4
10
idx
int64
0
30.7k
source
stringclasses
6 values
source_url
stringlengths
33
155
retrieved_date
timestamp[s]
classification_map
stringlengths
2
1.45k
Hereditary elliptocytosis (HE) refers to a group of inherited blood conditions where the red blood cells are abnormally shaped. Symptoms vary from very mild to severe and can include fatigue, shortness of breath, gallstones, and yellowing of the skin and eyes (jaundice). Some people with this condition have an enlarg...
Hereditary elliptocytosis
c0013902
1,100
gard
https://rarediseases.info.nih.gov/diseases/6621/hereditary-elliptocytosis
2021-01-18T18:00:03
{"mesh": ["D004612"], "umls": ["C0013902"], "orphanet": ["288"], "synonyms": []}
Bannayan-Riley-Ruvalcaba syndrome (BRRS) is a genetic condition that leads to the growth of both non-cancerous and cancerous tumors. Symptoms of BRRS may include large head size, increased birth weight, developmental delay, and intellectual disability. Other symptoms include the appearance of non-cancerous tumors in ...
Bannayan-Riley-Ruvalcaba syndrome
c0265326
1,101
gard
https://rarediseases.info.nih.gov/diseases/5887/bannayan-riley-ruvalcaba-syndrome
2021-01-18T18:01:54
{"mesh": ["D006223"], "omim": ["158350"], "umls": ["C0265326"], "orphanet": ["109"], "synonyms": ["BRRS", "Riley-Smith syndrome", "Macrocephaly multiple lipomas and hemangiomata", "Ruvalcaba -Myhre-Smith syndrome", "RMSS", "Bannayan-Zonana syndrome", "BZS", "Macrocephaly pseudopapilledema and multiple hemangiomas"]}
Albuminuria SpecialtyNephrology Albuminuria is a pathological condition wherein the protein albumin is abnormally present in the urine. It is a type of proteinuria. Albumin is a major plasma protein (normally circulating in the blood); in healthy people, only trace amounts of it are present in urine, whereas l...
Albuminuria
c0001925
1,102
wikipedia
https://en.wikipedia.org/wiki/Albuminuria
2021-01-18T18:50:58
{"mesh": ["D000419"], "umls": ["C0001925"], "wikidata": ["Q974792"]}
A number sign (#) is used with this entry because of evidence that ventriculomegaly with cystic kidney disease (VMCKD) is caused by homozygous or compound heterozygous mutation in the CRB2 gene (609720) on chromosome 9q33. Biallelic mutation in the CRB2 gene can also cause isolated focal segmental glomeruloscler...
VENTRICULOMEGALY WITH CYSTIC KIDNEY DISEASE
c1857423
1,103
omim
https://www.omim.org/entry/219730
2019-09-22T16:29:01
{"mesh": ["C565657"], "omim": ["219730"], "orphanet": ["443988"]}
Condition in which severely overweight people fail to breathe rapidly or deeply enough Obesity hypoventilation syndrome Other namesPickwickian syndrome Obesity hypoventilation syndrome often improves with positive airway pressure treatment administered overnight by a machine such as this device SpecialtyRespir...
Obesity hypoventilation syndrome
c0031880
1,104
wikipedia
https://en.wikipedia.org/wiki/Obesity_hypoventilation_syndrome
2021-01-18T18:37:40
{"mesh": ["D010845"], "umls": ["C0031880"], "icd-9": ["278.03"], "icd-10": ["E66.2"], "wikidata": ["Q202394"]}
A number sign (#) is used with this entry because of evidence that autosomal dominant dilated cardiomyopathy-1G (CMD1G) is caused by heterozygous mutation in the titin gene (TTN; 188840) on chromosome 2q31. For a general phenotypic description and a discussion of genetic heterogeneity of dilated cardiomyopathy (...
CARDIOMYOPATHY, DILATED, 1G
c0340427
1,105
omim
https://www.omim.org/entry/604145
2019-09-22T16:12:27
{"doid": ["0110430"], "mesh": ["C536231"], "omim": ["604145"], "orphanet": ["154"], "genereviews": ["NBK1309"]}
Lachiewicz–Sibley syndrome is a rare autosomal dominant disorder characterized by preauricular pits and renal disease. Persons with this disease may have hypoplasic kidneys or proteinuria. This disease was first described in a Caucasian family of British and Irish descent that emigrated to Ohio in the 19th century be...
Lachiewicz–Sibley syndrome
c2931742
1,106
wikipedia
https://en.wikipedia.org/wiki/Lachiewicz%E2%80%93Sibley_syndrome
2021-01-18T18:54:07
{"gard": ["3157"], "mesh": ["C538131"], "umls": ["C2931742"], "wikidata": ["Q6468402"]}
For a general phenotypic description and a discussion of genetic heterogeneity of basal cell carcinoma, see BCC1 (605462). Mapping In a genomewide SNP association study of 930 Icelanders with BCC and 33,117 controls, Stacey et al. (2008) observed signals from loci at chromosomes 1p36 (BCC1; 605462) and 1q42. Th...
BASAL CELL CARCINOMA, SUSCEPTIBILITY TO, 2
c2751606
1,107
omim
https://www.omim.org/entry/613058
2019-09-22T15:59:54
{"omim": ["613058"]}
Aggressive periodontitis describes a type of periodontal disease and includes two of the seven classifications of periodontitis as defined by the 1999 classification system:[1] 1. Localized aggressive periodontitis (LAP) 2. Generalized aggressive periodontitis (GAP) LAP is localised to first molar or incisor in...
Aggressive periodontitis
c0031106
1,108
wikipedia
https://en.wikipedia.org/wiki/Aggressive_periodontitis
2021-01-18T18:45:27
{"mesh": ["D010520"], "umls": ["C0031106"], "wikidata": ["Q4692285"]}
See GGTQTL2 (612366) on chromosome 12q24 for another locus associated with the plasma level of gamma glutamyltransferase. Mapping Bathum et al. (2001) found evidence for a substantial genetic influence on the plasma level of gamma glutamyltransferase (GGT, or GGT1; 612346). Heritability ranged from 35 to 61% am...
GAMMA GLUTAMYLTRANSFERASE, PLASMA LEVEL OF, QUANTITATIVE TRAIT LOCUS 1
c2676495
1,109
omim
https://www.omim.org/entry/612365
2019-09-22T16:01:47
{"omim": ["612365"], "synonyms": ["Alternative titles", "GGTQTL1"]}
Deafness-vitiligo-achalasia syndrome is characterized by the association of deafness, short stature, vitiligo, muscle wasting, and achalasia. ## Epidemiology It has been described in a brother and his sister born to first-cousin parents. ## Genetic counseling It is likely to be transmitted as an autosomal recessi...
Deafness-vitiligo-achalasia syndrome
c1857339
1,110
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=3239
2021-01-23T18:58:06
{"gard": ["1705"], "mesh": ["C565642"], "omim": ["221350"], "umls": ["C1857339"], "icd-10": ["Q87.8"], "synonyms": ["Hearing loss-vitiligo-achalasia syndrome"]}
A number sign (#) is used with this entry because of evidence that autosomal recessive deafness-53 (DFNB53) is caused by homozygous mutation in the COL11A2 gene (120290) on chromosome 6p21. Clinical Features Chen et al. (2005) reported a consanguineous Iranian family with a prelingual, profound, nonprogressive, and...
DEAFNESS, AUTOSOMAL RECESSIVE 53
c1864746
1,111
omim
https://www.omim.org/entry/609706
2019-09-22T16:05:45
{"doid": ["0110509"], "mesh": ["C566453"], "omim": ["609706"], "orphanet": ["90636"], "synonyms": ["Autosomal recessive isolated neurosensory deafness type DFNB", "Autosomal recessive isolated sensorineural deafness type DFNB", "Autosomal recessive non-syndromic neurosensory deafness type DFNB"]}
A number sign (#) is used with this entry because of evidence that Alagille syndrome-2 (ALGS2) is caused by heterozygous mutation in the NOTCH2 gene (600275) on chromosome 1p12. For a general phenotypic description and a discussion of genetic heterogeneity of Alagille syndrome, see ALGS1 (118450). Clinical Features...
ALAGILLE SYNDROME 2
c0085280
1,112
omim
https://www.omim.org/entry/610205
2019-09-22T16:04:57
{"doid": ["9245"], "mesh": ["D016738"], "omim": ["610205"], "orphanet": ["52", "261629"], "genereviews": ["NBK1273"]}
A number sign (#) is used with this entry because Bowen-Conradi syndrome (BWCNS) is caused by homozygous mutation in the EMG1 gene (611531) on chromosome 12p13. Clinical Features Among the offspring of second-cousin Hutterite parents, Bowen and Conradi (1976) described 2 males with a distinctive syndrome: prominent...
BOWEN-CONRADI SYNDROME
c1859405
1,113
omim
https://www.omim.org/entry/211180
2019-09-22T16:30:21
{"doid": ["0050684"], "mesh": ["C537081"], "omim": ["211180"], "orphanet": ["1270"], "synonyms": ["Alternative titles", "BOWEN HUTTERITE SYNDROME, FORMERLY"]}
A rare respiratory malformation characterized by a hamartomatous mass of non-functioning lung tissue of variable extent and with variable degrees of cystic or adenomatoid change. Clinical presentation, prognosis, and presence of associated abnormalities depend on the subtype of the lesion. Based on histopathological ...
Congenital pulmonary airway malformation
c0010668
1,114
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2444
2021-01-23T18:43:13
{"mesh": ["D015615"], "umls": ["C0010668", "C0158641"], "icd-10": ["Q33.0"], "synonyms": ["CCAM", "CPAM", "Congenital cystic adenomatoid malformation of the lung", "Congenital cystic adenomatous malformation of the lung", "Congenital cystic disease of the lung"]}
For the condition characterized by comorbidity of a specific set of impairments to executive functioning, see Dysexecutive syndrome. In psychology and neuroscience, executive dysfunction, or executive function deficit, is a disruption to the efficacy of the executive functions, which is a group of cognitive processe...
Executive dysfunction
c2748208
1,115
wikipedia
https://en.wikipedia.org/wiki/Executive_dysfunction
2021-01-18T18:44:10
{"umls": ["C2748208"], "wikidata": ["Q5419936"]}
Fascial hernias in the form of nodules appear in the skin where the deep and superficial veins meet going through the fascia, most frequently occurring on the lower extremities, becoming prominent when the underlying muscles contract.[1]:610 ## See also[edit] * Skin lesion ## References[edit] 1. ^ James, Will...
Fascial hernia
c1695781
1,116
wikipedia
https://en.wikipedia.org/wiki/Fascial_hernia
2021-01-18T19:03:31
{"umls": ["C1695781"], "wikidata": ["Q5436636"]}
Grisel's syndrome SpecialtyRheumatology Grisel’s syndrome is a non-traumatic subluxation of the atlanto-axial joint caused by inflammation of the adjacent tissues. This is a rare disease that usually affects children. Progressive throat and neck pain and neck stiffness can be followed by neurologic symptom...
Grisel's syndrome
c0263885
1,117
wikipedia
https://en.wikipedia.org/wiki/Grisel%27s_syndrome
2021-01-18T18:28:01
{"umls": ["C0263885"], "icd-9": ["723.5"], "wikidata": ["Q3508650"]}
Traumatic alopecia SpecialtyDermatology Traumatic alopecia is a cutaneous condition that results from the forceful pulling out of the scalp hair.[1] ## See also[edit] * Traction alopecia * List of cutaneous conditions ## References[edit] 1. ^ Rapini, Ronald P.; Bolognia, Jean L.; Jorizzo, Joseph ...
Traumatic alopecia
c0002182
1,118
wikipedia
https://en.wikipedia.org/wiki/Traumatic_alopecia
2021-01-18T18:49:56
{"umls": ["C0002182"], "wikidata": ["Q7835819"]}
A number sign (#) is used with this entry because X-linked dystonia-parkinsonism (XDP) is caused by an SVA (short interspersed nuclear element, variable number of tandem repeats, and Alu composite) retrotransposon insertion in an intron of the TATA-binding protein-associated factor-1 gene (TAF1; 313650) on chromo...
DYSTONIA 3, TORSION, X-LINKED
c1839130
1,119
omim
https://www.omim.org/entry/314250
2019-09-22T16:17:17
{"doid": ["0090057"], "mesh": ["C564048"], "omim": ["314250"], "orphanet": ["53351"], "synonyms": ["Alternative titles", "DYSTONIA-PARKINSONISM, X-LINKED", "TORSION DYSTONIA-PARKINSONISM, FILIPINO TYPE"], "genereviews": ["NBK1489"]}
A rare histiocytic tumor characterized by a malignant proliferation of cells showing morphological and immunophenotypic features of mature tissue histiocytes. Most cases occur in extranodal sites, most commonly the intestinal tract, skin, and soft tissue. Patients may present with a solitary mass, lymphadenopathy, a ...
Histiocytic sarcoma
c0334663
1,120
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=86896
2021-01-23T17:36:47
{"mesh": ["D054747"], "umls": ["C0334663"], "icd-10": ["C96.8"]}
A heart muscle disease that consists in progressive dystrophy of primarily the right ventricular myocardium with fibro-fatty replacement and ventricular dilation, and that is clinically characterized by ventricular arrhythmias and a risk of sudden cardiac death. ## Epidemiology Arrhythmogenic right ventricular card...
Arrhythmogenic right ventricular cardiomyopathy
c0349788
1,121
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=247
2021-01-23T17:18:23
{"gard": ["5847"], "mesh": ["D019571"], "umls": ["C0349788"], "icd-10": ["I42.8"], "synonyms": ["ARVC", "ARVD", "Arrhythmogenic right ventricular dysplasia"]}
Autosomal dominant tubulointerstitial kidney disease due to UMOD mutations (ADTKD–UMOD) is an inherited disorder that causes a gradual loss of kidney function that eventually leads to the need for kidney transplantation or dialysis between the ages of 30 and 70. Patients with ADTKD-UMOD have high blood levels of uric...
Autosomal dominant tubulointerstitial kidney disease due to UMOD mutations
c1859040
1,122
gard
https://rarediseases.info.nih.gov/diseases/10679/autosomal-dominant-tubulointerstitial-kidney-disease-due-to-umod-mutations
2021-01-18T18:01:56
{"mesh": ["C548033"], "omim": ["162000"], "umls": ["C1859040"], "orphanet": ["88950"], "synonyms": ["ADTKD-UMOD", "Autosomal dominant medullary cystic kidney disease type 2 (former)", "UMOD-related ADTKD", "Autosomal dominant medullary cystic kidney disease type 2", "MCKD2", "UMOD-related autosomal dominant tubulointer...
The first HIV/AIDS case in Malaysia made its debut in 1986. Since then, HIV/AIDS has become one of the country's most serious health and development challenges.[1] As of 2019, the Ministry of Health estimated that there were 87,581 people living with HIV (PLHIV) in Malaysia. However, only 77,903 are aware of their st...
HIV/AIDS in Malaysia
None
1,123
wikipedia
https://en.wikipedia.org/wiki/HIV/AIDS_in_Malaysia
2021-01-18T18:42:18
{"wikidata": ["Q5629859"]}
Hennekam syndrome is an inherited disorder resulting from malformation of the lymphatic system, which is part of both the circulatory system and immune system. The lymphatic system consists of a network of vessels that transport lymph fluid and immune cells throughout the body. The characteristic signs and sympt...
Hennekam syndrome
c4012050
1,124
medlineplus
https://medlineplus.gov/genetics/condition/hennekam-syndrome/
2021-01-27T08:25:43
{"gard": ["3318"], "mesh": ["C537255"], "omim": ["235510", "616006"], "synonyms": []}
A rare skeletal dysplasia characterized by short stature, prominent abnormalities in hands and feet, and a characteristic facial appearance (described as happy''). ## Epidemiology Fewer than 30 cases have been reported to date. ## Clinical description The characteristic facial appearance (''happy'' face) consists...
Geleophysic dysplasia
c3489726
1,125
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2623
2021-01-23T18:54:36
{"gard": ["2449"], "mesh": ["C537677", "C535662"], "omim": ["231050", "614185", "617809"], "umls": ["C3489726"], "icd-10": ["Q87.1"], "synonyms": ["Geleophysic dwarfism"]}
See also: Pseudomembranous colitis Antibiotic-associated diarrhea Antibiotic-associated diarrhea (AAD) results from an imbalance in the colonic microbiota caused by antibiotics. Microbiotal alteration changes carbohydrate metabolism with decreased short-chain fatty acid absorption and an osmotic diarrhea as a r...
Antibiotic-associated diarrhea
c0578159
1,126
wikipedia
https://en.wikipedia.org/wiki/Antibiotic-associated_diarrhea
2021-01-18T18:33:00
{"umls": ["C0578159"], "wikidata": ["Q574891"]}
## Summary The purpose of this overview is to increase clinician awareness of the genetic basis of dilated cardiomyopathy (DCM) and the benefits of early diagnosis and management to individuals with genetic DCM. The following are the goals of this overview. ### Goal 1. Define DCM. ### Goal 2. Identify the c...
Dilated Cardiomyopathy Overview
None
1,127
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1309/
2021-01-18T21:30:11
{"synonyms": []}
Frontal fibrosing alopecia (FFA) is a rare variant of lichen planopilaris (see this term) characterized by symmetrical, progressive, band-like anterior hair loss of the scalp. ## Epidemiology Prevalence is unknown. It most commonly affects postmenopausal women, although it has also been reported in men and premenop...
Frontal fibrosing alopecia
c1274700
1,128
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=254492
2021-01-23T18:26:05
{"gard": ["10886"], "umls": ["C1274700"], "icd-10": ["L66.1"], "synonyms": ["FFA"]}
Median arcuate ligament syndrome Other namesCeliac artery compression syndrome Celiac axis syndrome Celiac trunk compression syndrome Dunbar syndrome Median arcuate ligament syndrome results from compression of the celiac artery by the median arcuate ligament. The median arcuate ligament is a fibrous arch f...
Median arcuate ligament syndrome
c1861783
1,129
wikipedia
https://en.wikipedia.org/wiki/Median_arcuate_ligament_syndrome
2021-01-18T18:41:30
{"gard": ["12308"], "mesh": ["D000074742"], "umls": ["C1861783"], "orphanet": ["293208"], "wikidata": ["Q2456424"]}
A number sign (#) is used with this entry because familial infantile convulsions with paroxysmal choreoathetosis (ICCA) is caused by heterozygous mutation in the PRRT2 gene (614386) on chromosome 16p11. Description Benign familial infantile convulsions (BFIC; see 601764) is an autosomal dominant disorder charac...
CONVULSIONS, FAMILIAL INFANTILE, WITH PAROXYSMAL CHOREOATHETOSIS
c1865926
1,130
omim
https://www.omim.org/entry/602066
2019-09-22T16:14:03
{"mesh": ["C535522"], "omim": ["602066"], "orphanet": ["31709"], "synonyms": ["Alternative titles", "INFANTILE CONVULSIONS AND PAROXYSMAL CHOREOATHETOSIS, FAMILIAL", "ICCA SYNDROME", "PAROXYSMAL KINESIGENIC DYSKINESIA WITH INFANTILE CONVULSIONS"], "genereviews": ["NBK475803"]}
Abortion in Nevada is legal. 62% of adults said in a poll by the Pew Research Center that abortion should be legal in all or most cases. Legislation by 2007 required informed consent. Attempts were successfully made to pass abortion legislation in May 2019, being pushed through a largely Democratic controlled state l...
Abortion in Nevada
None
1,131
wikipedia
https://en.wikipedia.org/wiki/Abortion_in_Nevada
2021-01-18T18:54:48
{"wikidata": ["Q64876938"]}
An extremely rare, major congenital malformation consisting of an absence of the nose ranging from hyporrhinia (absence of external nasal structures) to total arrhinia (absence of external nose, nasal airways, olfactory bulbs, or olfactory nerve) often causing respiratory distress and requiring surgical correctio...
Isolated arrhinia
c0265740
1,132
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1134
2021-01-23T17:27:42
{"gard": ["364"], "mesh": ["C537438"], "umls": ["C0265740"], "icd-10": ["Q30.1"], "synonyms": ["Isolated nose agenesis"]}
For a phenotypic description and a discussion of genetic heterogeneity of chronic lymphocytic leukemia (CLL), see 151400. Clinical Features Lynch et al. (2002) described a family in which the father and all 4 of his children had CLL. All of the children were male, and 2 were identical twins. CLL was diagnosed at th...
LEUKEMIA, CHRONIC LYMPHOCYTIC, SUSCEPTIBILITY TO, 3
c0855095
1,133
omim
https://www.omim.org/entry/612557
2019-09-22T16:01:14
{"doid": ["1040"], "omim": ["612557"], "orphanet": ["67038"], "synonyms": ["Alternative titles", "CLLS3"]}
Zlotogora-Ogur syndrome is an ectodermal dysplasia syndrome characterized by hair, skin and teeth anomalies, facial dysmophism with cleft lip and palate, cutaneous syndactyly and, in some cases, intellectual disability. ## Epidemiology The prevalence is unknown but to date, less than 50 cases have been described in...
Cleft lip/palate-ectodermal dysplasia syndrome
c2931488
1,134
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=3253
2021-01-23T17:33:12
{"gard": ["375"], "mesh": ["C536726"], "omim": ["225060"], "umls": ["C2931488"], "synonyms": ["CLPED1", "Cleft lip/palate-syndactyly-pili torti syndrome", "Syndactyly-ectodermal dysplasia-cleft/lip palate", "Zlotogora-Zilberman-Tenenbaum syndrome"]}
A number sign (#) is used with this entry because of evidence that anauxetic dysplasia-2 (ANXD2) is caused by homozygous or compound heterozygous mutation in the POP1 gene (602486) on chromosome 8q22. Description Anauxetic dysplasia is a spondyloepimetaphyseal dysplasia characterized by severe short stature of pren...
ANAUXETIC DYSPLASIA 2
c1846796
1,135
omim
https://www.omim.org/entry/617396
2019-09-22T15:45:54
{"mesh": ["C538256"], "omim": ["617396"], "orphanet": ["93347"]}
Intravascular papillary endothelial hyperplasia Other namesMasson's hemangio-endotheliome vegetant intravasculaire,[1] Masson's lesion,[1] Masson's pseudoangiosarcoma,[1] Masson's tumor,[1] and Papillary endothelial hyperplasia[1] SpecialtyOncology, rheumatology Intravascular papillary endothelial hyperplasi...
Intravascular papillary endothelial hyperplasia
c0343083
1,136
wikipedia
https://en.wikipedia.org/wiki/Intravascular_papillary_endothelial_hyperplasia
2021-01-18T18:41:34
{"gard": ["10733"], "umls": ["C0343083"], "icd-10": ["D21"], "wikidata": ["Q6058576"]}
Neurocutaneous melanosis (NCM) is a rare, non-inherited condition of the central nervous system. It is characterized by melanocytic nevi in both the skin and the brain. Two-thirds of people with NCM have giant congenital melanocytic nevi, and the remaining one-third have numerous lesions but no giant lesions. The...
Neurocutaneous melanosis
c0544862
1,137
gard
https://rarediseases.info.nih.gov/diseases/7186/neurocutaneous-melanosis
2021-01-18T17:58:45
{"mesh": ["C537387"], "omim": ["249400"], "umls": ["C0544862"], "orphanet": ["2481"], "synonyms": ["Melanosis, neurocutaneous", "Neurocutaneous melanosis syndrome"]}
RAB18 deficiency causes two conditions with similar signs and symptoms that primarily affect the eyes, brain, and reproductive system. These two conditions, called Warburg micro syndrome and Martsolf syndrome, were once thought to be distinct disorders but are now considered to be part of the same disease spectrum be...
RAB18 deficiency
c0796037
1,138
medlineplus
https://medlineplus.gov/genetics/condition/rab18-deficiency/
2021-01-27T08:24:45
{"gard": ["3406", "5534"], "mesh": ["C536028"], "omim": ["212720", "600118", "614225", "614222", "615663"], "synonyms": []}
A number sign (#) is used with this entry because of evidence that isolated congenital digital clubbing can be caused by homozygous mutation in the 15-hydroxyprostaglandin dehydrogenase gene (HPGD; 601688) on chromosome 4q34. Description Digital clubbing is characterized by enlargement of the nail plate and termina...
DIGITAL CLUBBING, ISOLATED CONGENITAL
c0345408
1,139
omim
https://www.omim.org/entry/119900
2019-09-22T16:43:08
{"mesh": ["D010004"], "omim": ["119900"], "orphanet": ["217059"], "synonyms": ["Alternative titles", "CLUBBING OF DIGITS", "ACROPACHY, HEREDITARY"]}
Factor VII deficiency is a rare bleeding disorder. The age of onset and severity varies from person to person. While severe cases may become apparent in infancy, very mild cases may never cause any bleeding problems. Signs and symptoms may include nosebleeds; easy bruising; bleeding gums; excessive or prolonged bleed...
Factor VII deficiency
c0015503
1,140
gard
https://rarediseases.info.nih.gov/diseases/2238/factor-vii-deficiency
2021-01-18T18:00:36
{"mesh": ["D005168"], "omim": ["227500"], "umls": ["C0015503"], "orphanet": ["327"], "synonyms": ["Factor 7 deficiency", "F7 deficiency", "Hypoproconvertinemia", "Congenital proconvertin deficiency"]}
Cerebrospinal fluid (CSF) otorrhea is the leakage of cerebrospinal fluid (CSF) though the ear. It is a rare but very serious condition that requires rapid intervention. Symptoms include leak of clear fluid through the ear, inflammation of the membranes that cover the brain (meningitis), hearing loss, and seizures. Th...
Cerebrospinal fluid leak
c0023182
1,141
gard
https://rarediseases.info.nih.gov/diseases/10166/cerebrospinal-fluid-leak
2021-01-18T18:01:32
{"mesh": ["D065634"], "synonyms": ["CSF leak", "CSF rhinorrhea", "CSF otorrhea", "Spinal CSF leak"]}
A number sign (#) is used with this entry because of evidence that distal arthrogryposis type 1A (DA1A) and type 2B4 (DA2B4) are caused by heterozygous mutation in the TPM2 gene (190990) on chromosome 9p13. Heterozygous mutation in the TPM2 gene can also cause nemaline myopathy-4 (NEM4; 609285), which shows similar ...
ARTHROGRYPOSIS, DISTAL, TYPE 1A
c1852085
1,142
omim
https://www.omim.org/entry/108120
2019-09-22T16:44:46
{"doid": ["0050646"], "mesh": ["C565097"], "omim": ["108120"], "orphanet": ["1146"], "synonyms": ["Alternative titles", "ARTHROGRYPOSIS, DISTAL, TYPE 1", "ARTHROGRYPOSIS MULTIPLEX CONGENITA, DISTAL, TYPE I"]}
Aldolase A deficiency Other namesALDOA deficiency, Red cell aldolase deficiency,[1] or Glycogen storage disease type 12 (GSD XII)[2] Aldolase A deficiency has an autosomal recessive pattern of inheritance SpecialtyEndocrinology Aldolase A deficiency, is an autosomal recessive[3] metabolic disorder resultin...
Aldolase A deficiency
c0272066
1,143
wikipedia
https://en.wikipedia.org/wiki/Aldolase_A_deficiency
2021-01-18T18:36:35
{"gard": ["600"], "mesh": ["C562718"], "umls": ["C0272066"], "icd-10": ["E74.1"], "orphanet": ["57"], "wikidata": ["Q4713937"]}
Nasopharyngeal carcinoma Other namesNasopharyngeal cancer, nasopharynx cancer, NPC Micrograph showing a nasopharyngeal carcinoma positive for Epstein-Barr virus-encoded small RNAs (EBER). SpecialtyOncology Nasopharyngeal carcinoma (NPC), or nasopharynx cancer, is the most common cancer originating in t...
Nasopharyngeal carcinoma
c2750548
1,144
wikipedia
https://en.wikipedia.org/wiki/Nasopharyngeal_carcinoma
2021-01-18T18:46:22
{"gard": ["7163"], "mesh": ["D000077274"], "umls": ["C2750548"], "orphanet": ["150"], "wikidata": ["Q1693598"]}
Medical condition in which gallstones cause acute pain Biliary colic Other namesGallstone attack, gallbladder attack Biliary colic is often related to a stone in the gallbladder SpecialtyGastroenterology Biliary colic, also known as symptomatic cholelithiasis, a gallbladder attack or gallstone attack,...
Biliary colic
c0151824
1,145
wikipedia
https://en.wikipedia.org/wiki/Biliary_colic
2021-01-18T19:03:28
{"icd-9": ["574.20"], "icd-10": ["K80.5"], "wikidata": ["Q2727106"]}
Plexopathy is a disorder affecting a network of nerves, blood vessels, or lymph vessels.[1] The region of nerves it affects are at the brachial or lumbosacral plexus. Symptoms include pain, loss of motor control, and sensory deficits.[2] ## Contents * 1 Types * 2 Cause * 3 Diagnosis * 4 Treatment * 5 ...
Plexopathy
c1335437
1,146
wikipedia
https://en.wikipedia.org/wiki/Plexopathy
2021-01-18T18:53:05
{"umls": ["C1335437"], "wikidata": ["Q7204901"]}
A number sign (#) is used with this entry because of evidence that some cases of preaxial polydactyly type IV are caused by heterozygous mutation in the GLI3 gene (165240) on chromosome 7p14. Description Although both preaxial polydactyly and syndactyly are cardinal features of this malformation, it is classifi...
POLYDACTYLY, PREAXIAL IV
c0265553
1,147
omim
https://www.omim.org/entry/174700
2019-09-22T16:36:02
{"doid": ["1148"], "mesh": ["D013576"], "omim": ["174700"], "orphanet": ["93338"], "synonyms": ["Alternative titles", "POLYSYNDACTYLY, UNCOMPLICATED"]}
Mucinous cystadenocarcinoma of the lung Other namesMucinous multilocular cyst carcinoma, Pseudomyxomatous pulmonary adenocarcinoma, Mucinous cystic tumor of low malignant potential[1] SpecialtyOncology Mucinous cystadenocarcinoma of the lung (MCACL) is a very rare malignant mucus-producing neoplasm arising f...
Mucinous cystadenocarcinoma of the lung
None
1,148
wikipedia
https://en.wikipedia.org/wiki/Mucinous_cystadenocarcinoma_of_the_lung
2021-01-18T18:57:20
{"umls": ["C1711166"], "wikidata": ["Q17155516"]}
A rare inherited cancer-predisposing syndrome characterized by early-onset hepatocellular carcinoma, genomic instability, and progeroid features, such as short stature, low body weight, muscular atrophy, lipodystrophy, bilateral cataracts, and premature hair graying. Dysmorphic craniofacial features include trian...
Progeroid features-hepatocellular carcinoma predisposition syndrome
c4015461
1,149
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=435953
2021-01-23T17:06:56
{"omim": ["616200"], "synonyms": ["Ruijs-Aalfs syndrome"]}
MBD25–related intellectual disability, or MBD25 haploinsufficiency, is a neurological and developmental disorder characterized by developmental delay, intellectual disability, speech problems, seizures, sleep troubles, and abnormal behaviors. Most children lack speech entirely or may only be able to use single words,...
MBD25–related intellectual disability
c1969562
1,150
gard
https://rarediseases.info.nih.gov/diseases/12852/mbd25-related-intellectual-disability
2021-01-18T17:59:12
{"mesh": ["C566947"], "omim": ["156200"], "synonyms": ["Autosomal dominant intellectual disability 1", "MBD5 Haploinsufficiency"]}
Sturge–Weber syndrome Other namesSturge–Weber–Krabbe disease CT scan of Sturge-Weber syndrome SpecialtyMedical genetics Sturge–Weber syndrome, sometimes referred to as encephalotrigeminal angiomatosis, is a rare congenital neurological and skin disorder. It is one of the phakomatoses and is often associate...
Sturge–Weber syndrome
c0038505
1,151
wikipedia
https://en.wikipedia.org/wiki/Sturge%E2%80%93Weber_syndrome
2021-01-18T18:52:04
{"gard": ["7706"], "mesh": ["D013341"], "umls": ["C0038505"], "icd-9": ["759.6"], "icd-10": ["Q85.8"], "orphanet": ["3205"], "wikidata": ["Q1886238"]}
A number sign (#) is used with this entry because idiopathic basal ganglia calcification-4 (IBGC4) is caused by heterozygous mutation in the PDGFRB gene (173410) on chromosome 5q32. Description Idiopathic basal ganglia calcification-4 is an autosomal dominant condition characterized by the accumulation of calci...
BASAL GANGLIA CALCIFICATION, IDIOPATHIC, 4
c0393590
1,152
omim
https://www.omim.org/entry/615007
2019-09-22T15:53:29
{"doid": ["0060230"], "omim": ["615007"], "orphanet": ["1980"], "genereviews": ["NBK1421"]}
Lethal polymalformative syndrome, Boissel type is a rare, genetic, lethal, multiple congenital anomalies/dysmorphic syndrome characterized by failure to thrive, severe developmental delay, severe postanatal microcephaly, frequent congenital cardiac defects and characteristic facial dysmorphysm (including coarse face ...
Lethal polymalformative syndrome, Boissel type
c2752001
1,153
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=210144
2021-01-23T17:58:03
{"mesh": ["C567856"], "omim": ["612938"], "umls": ["C2752001"], "icd-10": ["Q87.8"]}
Lateral pontine syndrome Pons SpecialtyNeurology A lateral pontine syndrome is a lesion which is similar to the lateral medullary syndrome, but because it occurs in the pons, it also involves the cranial nerve nuclei of the pons. ## Contents * 1 Symptoms * 2 Causes * 3 Diagnosis * 4 Treatment * 5...
Lateral pontine syndrome
None
1,154
wikipedia
https://en.wikipedia.org/wiki/Lateral_pontine_syndrome
2021-01-18T18:38:21
{"wikidata": ["Q17125280"]}
For the equine form of the disease, see Pituitary pars intermedia dysfunction. Cushing's disease Other namesCushing disease, tertiary or secondary hypercortisolism, tertiary or secondary hypercorticism, Itsenko-Cushing disease[1][2] SpecialtyEndocrinology Cushing's disease is one cause of Cushing's synd...
Cushing's disease
c0010481
1,155
wikipedia
https://en.wikipedia.org/wiki/Cushing%27s_disease
2021-01-18T18:40:47
{"mesh": ["D003480"], "icd-10": ["E24.0"], "orphanet": ["96253"], "wikidata": ["Q1947304"]}
Langer–Giedion syndrome Other namesDeletion 8q24.1, monosomy 8q24.1, trichorhinophalangeal syndrome type II (TRPS2), Langer-Giedion chromosome region (LGCR)[1][2] A person showing the typical features of Langer-Giedion syndrome SpecialtyMedical genetics Langer–Giedion syndrome (LGS) is a very uncommon ...
Langer–Giedion syndrome
c0023003
1,156
wikipedia
https://en.wikipedia.org/wiki/Langer%E2%80%93Giedion_syndrome
2021-01-18T18:30:25
{"gard": ["7801"], "mesh": ["D015826"], "umls": ["C2931237"], "icd-9": ["755.8"], "icd-10": ["Q87.8"], "orphanet": ["502"], "wikidata": ["Q3508795"]}
"CCVI" redirects here. For other uses, see CCVI (disambiguation). Chronic cerebrospinal venous insufficiency Veins of the neck. V.jugularis interna is proposed to be stenosed or have a malformed valve in CCSVI cases. SpecialtyCardiology Chronic cerebrospinal venous insufficiency (CCSVI or CCVI) is a ter...
Chronic cerebrospinal venous insufficiency controversy
None
1,157
wikipedia
https://en.wikipedia.org/wiki/Chronic_cerebrospinal_venous_insufficiency_controversy
2021-01-18T18:56:59
{"umls": ["CL529180"], "icd-10": ["I87.8"], "wikidata": ["Q1088054"]}
This article has multiple issues. Please help improve it or discuss these issues on the talk page. (Learn how and when to remove these template messages) This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be c...
HIV/AIDS in South African townships
None
1,158
wikipedia
https://en.wikipedia.org/wiki/HIV/AIDS_in_South_African_townships
2021-01-18T18:34:37
{"wikidata": ["Q5629880"]}
Pyoderma gangrenosum (PG) is a primarily sterile inflammatory neutrophilic dermatosis characterized by recurrent cutaneous ulcerations with a mucopurulent or hemorrhagic exudate. ## Epidemiology The exact prevalence of PG is unknown. The incidence has been estimated to range between 1 and 3.3 in 330,000. The incide...
Pyoderma gangrenosum
c0085652
1,159
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=48104
2021-01-23T16:53:03
{"gard": ["7510"], "mesh": ["D017511"], "umls": ["C0085652"], "icd-10": ["L88"]}
Elastofibroma dorsi is a rare, acquired, dermis elastic tissue disorder characterized by a benign, slowly progressive, often bilateral, non-encapsulated lesion, usually presenting as an ill-defined mass under the inferior angle of the scapula (but other locations have been reported), which adheres to the deep layers ...
Elastofibroma dorsi
c0334460
1,160
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=228243
2021-01-23T18:51:26
{}
Yuan-Harel-Lupski (YUHAL) syndrome is a rare neurological condition that has a combination of features of two other disorders, Potocki-Lupski syndrome and type 1A Charcot-Marie-Tooth disease. The first signs and symptoms of YUHAL syndrome begin in infancy. Infants with YUHAL syndrome usually have weak muscle tone (h...
Yuan-Harel-Lupski syndrome
c4225255
1,161
medlineplus
https://medlineplus.gov/genetics/condition/yuan-harel-lupski-syndrome/
2021-01-27T08:24:33
{"omim": ["616652"], "synonyms": []}
Not to be confused with sarcoma. Sarcoidosis Other namesSarcoïdosis, sarcoid, Besnier-Boeck-Schaumann disease[1] Chest X-ray showing the typical nodularity of sarcoidosis, predominantly in the bases of the lungs. Pronunciation * sar-koy-DO-sis SpecialtyRheumatology SymptomsDepends on the organ inv...
Sarcoidosis
c0036202
1,162
wikipedia
https://en.wikipedia.org/wiki/Sarcoidosis
2021-01-18T18:43:36
{"gard": ["7607"], "mesh": ["D012507"], "umls": ["C0036202"], "orphanet": ["797"], "wikidata": ["Q193894"]}
Neurolymphomatosis is a rare syndrome of peripheral and cranial nerve dysfunction in patients with hematologic malignancies, mostly non-Hodgkin's lymphoma or acute leukemia, characterized by painful or painless involvement of peripheral or cranial nerves or nerve roots. The clinical presentation is diverse depend...
Neurolymphomatosis
c0024793
1,163
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=206586
2021-01-23T18:02:27
{"mesh": ["D008380"]}
Neonatal hepatitis SpecialtyNeonatology Neonatal hepatitis refers to many forms of liver dysfunction that affects fetuses and neonates.[1] It is most often caused by viruses or metabolic diseases, and many cases are of an unknown cause.[2] ## Contents * 1 Signs and symptoms * 2 Causes * 3 Diagnosis ...
Neonatal hepatitis
c0027613
1,164
wikipedia
https://en.wikipedia.org/wiki/Neonatal_hepatitis
2021-01-18T19:10:31
{"icd-9": ["774.4"], "icd-10": ["P59.2"], "wikidata": ["Q6993479"]}
A number sign (#) is used with this entry because porphyria cutanea tarda type II, or familial PCT, is caused by heterozygous mutation in the gene encoding uroporphyrinogen decarboxylase (UROD; 613521). Hepatoerythropoietic porphyria (HEP) is caused by homozygous or compound heterozygous mutation in the UROD gene...
PORPHYRIA CUTANEA TARDA
c0162566
1,165
omim
https://www.omim.org/entry/176100
2019-09-22T16:35:55
{"doid": ["3132"], "mesh": ["D017119"], "omim": ["176100"], "icd-10": ["E80.1"], "orphanet": ["443062", "101330", "95159"], "synonyms": ["UROD DEFICIENCY", "PORPHYRIA CUTANEA TARDA, TYPE II", "PORPHYRIA, HEPATOCUTANEOUS TYPE", "Alternative titles", "UROPORPHYRINOGEN DECARBOXYLASE DEFICIENCY", "PCT", "Porphyria cutanea ...
Dermatological condition Atrophodermia vermiculata Other namesAcne vermoulante, Acne vermoulanti, Atrophoderma reticulata symmetrica faciei, Atrophoderma reticulatum, Atrophoderma vermiculata, Atrophoderma vermiculatum, Atrophodermia reticulata symmetrica faciei, Atrophodermia ulerythematosa, Atrophodermie vermicu...
Atrophodermia vermiculata
c0263429
1,166
wikipedia
https://en.wikipedia.org/wiki/Atrophodermia_vermiculata
2021-01-18T18:51:00
{"gard": ["9744"], "mesh": ["C537412"], "umls": ["C0263429"], "icd-10": ["L66.4"], "orphanet": ["79100"], "wikidata": ["Q16835166"]}
## Summary ### Clinical characteristics. Autosomal dominant epilepsy with auditory features (ADEAF) is a focal epilepsy syndrome with auditory symptoms and/or receptive aphasia as prominent ictal manifestations. The most common auditory symptoms are simple unformed sounds including humming, buzzing, or ringing;...
Autosomal Dominant Epilepsy with Auditory Features
None
1,167
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1537/
2021-01-18T21:41:39
{"synonyms": ["ADEAF", "Autosomal Dominant Lateral Temporal Epilepsy (ADLTE)"]}
A rare hereditary sensory and autonomic neuropathy characterized by anhidrosis, insensitivity to pain, self-mutilating behavior and episodes of fever. ## Epidemiology Whilst several hundred cases have been reported worldwide, the exact prevalence is unknown. Most of the cases described were from the Israeli Bedouin...
Hereditary sensory and autonomic neuropathy type 4
c0020074
1,168
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=642
2021-01-23T17:49:03
{"gard": ["3006"], "mesh": ["D009477"], "omim": ["256800"], "umls": ["C0020074"], "icd-10": ["G60.8"], "synonyms": ["CIPA", "Congenital insensitivity to pain with anhidrosis", "HSAN4", "Hereditary sensory and autonomic neuropathy type IV"]}
A number sign (#) is used with this entry because 4 known genetic mechanisms can cause Angelman syndrome (AS). Approximately 70% of AS cases result from de novo maternal deletions involving chromosome 15q11.2-q13; approximately 2% result from paternal uniparental disomy of 15q11.2-q13; and 2 to 3% result from imprint...
ANGELMAN SYNDROME
c0162635
1,169
omim
https://www.omim.org/entry/105830
2019-09-22T16:45:10
{"doid": ["1932"], "mesh": ["D017204"], "omim": ["105830"], "icd-10": ["Q93.51"], "orphanet": ["72"], "synonyms": ["Alternative titles", "HAPPY PUPPET SYNDROME, FORMERLY"], "genereviews": ["NBK1144"]}
A number sign (#) is used with this entry because vitelliform macular dystrophy-2 (VMD2), also known as Best disease, is caused by heterozygous mutation in the bestrophin gene (BEST1; 607854) on chromosome 11q12. Description Best vitelliform macular dystrophy is an early-onset autosomal dominant disorder characteri...
MACULAR DYSTROPHY, VITELLIFORM, 2
c0339510
1,170
omim
https://www.omim.org/entry/153700
2019-09-22T16:38:44
{"doid": ["0050661"], "mesh": ["D057826"], "omim": ["153700"], "orphanet": ["1243"], "synonyms": ["Alternative titles", "VITELLIFORM MACULAR DYSTROPHY, EARLY-ONSET", "VITELLIFORM MACULAR DYSTROPHY, JUVENILE-ONSET", "BEST MACULAR DYSTROPHY", "MACULAR DEGENERATION, POLYMORPHIC VITELLINE", "BEST VITELLIFORM MACULAR DYSTRO...
Cyclosporiasis Other namescyclosporosis Cyclospora cayetanensis SpecialtyInfectious disease Cyclosporiasis is a disease caused by infection with Cyclospora cayetanensis, a pathogenic protozoan transmitted by feces or feces-contaminated food and water.[1] Outbreaks have been reported due to contaminated fru...
Cyclosporiasis
c0343398
1,171
wikipedia
https://en.wikipedia.org/wiki/Cyclosporiasis
2021-01-18T18:47:38
{"gard": ["9528"], "mesh": ["D021866"], "umls": ["C0343398"], "orphanet": ["210"], "wikidata": ["Q3008595"]}
Dihydropteridine reductase deficiency (DHPR) is a severe form of hyperphenylalaninemia (high levels of the amino acid phenylalanine in the blood) due to impaired renewal of a substance known as tetrahydrobiopterin (BH4). Tetrahydrobiopterin normally helps process several amino acids, including phenylalanine, and ...
Dihydropteridine reductase deficiency
c0268465
1,172
gard
https://rarediseases.info.nih.gov/diseases/4319/dihydropteridine-reductase-deficiency
2021-01-18T18:00:51
{"mesh": ["D010661"], "omim": ["261630"], "orphanet": ["226"], "synonyms": ["DHPR deficiency", "Hyperphenylalaninemia, BH-4-deficient, C", "Hyperphenylalaninemia due to dihydropteridine reductase deficiency", "Phenylketonuria type 2", "Quinoid dihydropteridine reductase deficiency", "QDPR deficiency", "PKU type 2"]}
A number sign (#) is used with this entry because spinocerebellar ataxia-7 (SCA7) is caused by a heterozygous expanded trinucleotide repeat in the gene encoding ataxin-7 (ATXN7; 607640) on chromosome 3p14. Description Spinocerebellar ataxia-7 (SCA7) is an autosomal dominant neurodegenerative disorder characterized ...
SPINOCEREBELLAR ATAXIA 7
c0752125
1,173
omim
https://www.omim.org/entry/164500
2019-09-22T16:37:10
{"doid": ["0050958"], "mesh": ["D020754"], "omim": ["164500"], "orphanet": ["94147"], "synonyms": ["Alternative titles", "OLIVOPONTOCEREBELLAR ATROPHY III", "OPCA III", "OPCA WITH RETINAL DEGENERATION", "OPCA WITH MACULAR DEGENERATION AND EXTERNAL OPHTHALMOPLEGIA", "AUTOSOMAL DOMINANT CEREBELLAR ATAXIA, TYPE II", "ADCA...
A popliteal artery aneurysm is a bulging (aneurysm) of the popliteal artery.[1] A PAA is diagnosed when a focal dilation greater than 50% of the normal vessel diameter is found (the normal diameter of a popliteal artery is 0.7-1.1 cm). PAAs are the most common aneurysm of peripheral vasculature, accounting for 85% of...
Popliteal artery aneurysm
c0264964
1,174
wikipedia
https://en.wikipedia.org/wiki/Popliteal_artery_aneurysm
2021-01-18T19:01:22
{"umls": ["C0264964"], "icd-10": ["I72.4"], "wikidata": ["Q18343639"]}
Lujo hemorrhagic fever, caused by the Lujo virus (a newly discovered Old World arenavirus) is a zoonotic disease from Zambia, Africa, whose reservoir is unknown and is characterized by fever and hemorrhagic manifestations with an extremely high fatality rate of 80% (in the 5 reported cases to date) and a moderate...
Lujo hemorrhagic fever
c4274433
1,175
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=319213
2021-01-23T17:30:57
{"icd-10": ["A96.8"], "synonyms": ["Zambian hemorrhagic fever"]}
CYLD cutaneous syndrome causes the growth of several types of non-cancerous (benign) skin tumors. Tumors mainly grow on the scalp and face, but can also grow on the torso, genitals and armpits. Tumors usually first appear in the teens or early adulthood. The types of tumors that occur in CYLD cutaneous syndrome may i...
CYLD cutaneous syndrome
c1857941
1,176
gard
https://rarediseases.info.nih.gov/diseases/10179/cyld-cutaneous-syndrome
2021-01-18T18:01:00
{"mesh": ["C536611"], "omim": ["605041"], "orphanet": ["79493"], "synonyms": ["BRSS", "Spiegler-Brooke syndrome", "SBS", "Ancell-Spiegler cylindromas", "Brooke-Spiegler syndrome", "Familial cylindromatosis", "Multiple familial trichoepitheliomas"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Fibrillary astrocytoma" – news · newspapers · books · scholar · JSTOR (April 2010) (Learn how and when to remove this t...
Fibrillary astrocytoma
c0334582
1,177
wikipedia
https://en.wikipedia.org/wiki/Fibrillary_astrocytoma
2021-01-18T19:08:07
{"mesh": ["D001254"], "umls": ["C0334582"], "orphanet": ["251601"], "wikidata": ["Q953330"]}
A rare syndrome with combined immunodeficiency characterized by intrauterine and postnatal growth retardation, chronic neutropenia, and natural killer (NK) cell deficiency due a defect in DNA replication leading to blockade of immune cell differentiation in the bone marrow, particularly affecting NK cells. Other ...
Combined immunodeficiency due to GINS1 deficiency
c4693356
1,178
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=505227
2021-01-23T17:44:03
{"omim": ["617827"], "synonyms": ["CID due to GINS1 deficiency", "Combined immunodeficiency with intrauterine growth retardation-NK cell deficiency-neutropenia", "Combined immunodeficiency with intrauterine growth retardation-natural killer cell deficiency-neutropenia"]}
A number sign (#) is used with this entry because of evidence that hypochromic microcytic anemia with iron overload-2 (AHMIO2) is caused by heterozygous mutation in the STEAP3 gene (609671) on chromosome 2q14. One such family has been reported. For a discussion of genetic heterogeneity of hypochromic microcytic anem...
ANEMIA, HYPOCHROMIC MICROCYTIC, WITH IRON OVERLOAD 2
c3808920
1,179
omim
https://www.omim.org/entry/615234
2019-09-22T15:52:46
{"doid": ["0050642"], "omim": ["615234"], "orphanet": ["300298"], "synonyms": ["Severe congenital hypochromic sideroblastic anemia"]}
Carpenter syndrome is a condition characterized by premature fusion of skull bones (craniosynostosis); finger and toe abnormalities; and other developmental problems. The features in affected people vary. Craniosynostosis can give the head a pointed appearance; cause asymmetry of the head and face; affect the develop...
Carpenter syndrome
c1275078
1,180
gard
https://rarediseases.info.nih.gov/diseases/6003/carpenter-syndrome
2021-01-18T18:01:36
{"mesh": ["C563187"], "omim": ["201000"], "orphanet": ["65759"], "synonyms": ["Acrocephalopolysyndactyly type 2", "ACPS 2", "Acrocephalosyndactyly, type II", "Carpenter syndrome 1", "CRPT1"]}
Kisch and Nasuhoglu (1953) described a mediosternal, longitudinally directed streak of hypopigmentation in 5 blacks. I have observed this, but no systematic family studies have been done. See Futcher line (137000) and raindrop depigmentation (179500) for other pigment peculiarities in blacks. Inheritance \- Autos...
MEDIOSTERNAL DEPIGMENTATION LINE
c1835085
1,181
omim
https://www.omim.org/entry/155200
2019-09-22T16:38:30
{"omim": ["155200"]}
A mitochondrially inherited degeneration of retinal cells in human Leber's hereditary optic neuropathy Other namesLeber hereditary optic atrophy Leber’s hereditary optic neuropathy has a mitochondrial inheritance pattern. SpecialtyOphthalmology Frequency1:30,000 to 1:50,000 Leber's hereditary optic neur...
Leber's hereditary optic neuropathy
c0917796
1,182
wikipedia
https://en.wikipedia.org/wiki/Leber%27s_hereditary_optic_neuropathy
2021-01-18T18:45:59
{"gard": ["6870"], "mesh": ["D029242"], "umls": ["C0917796"], "icd-9": ["377.16"], "orphanet": ["104"], "wikidata": ["Q1262161"]}
Pregnancy-associated malaria (PAM) or placental malaria is a presentation of the common illness that is particularly life-threatening to both mother and developing fetus.[1] PAM is caused primarily by infection with Plasmodium falciparum,[1][2] the most dangerous of the four species of malaria-causing parasites t...
Pregnancy-associated malaria
c0156799
1,183
wikipedia
https://en.wikipedia.org/wiki/Pregnancy-associated_malaria
2021-01-18T18:35:15
{"umls": ["C0156799", "C0404795"], "icd-9": ["647.4"], "icd-10": ["O98.6"], "wikidata": ["Q7239883"]}
Spinocerebellar ataxia type 6 Other namesDiseasesDB = 12339 This condition is inherited in an autosomal dominant manner SpecialtyNeurology Spinocerebellar ataxia type 6 (SCA6) is a rare, late-onset, autosomal dominant disorder, which, like other types of SCA, is characterized by dysarthria, oculomotor ...
Spinocerebellar ataxia type 6
c0752124
1,184
wikipedia
https://en.wikipedia.org/wiki/Spinocerebellar_ataxia_type_6
2021-01-18T19:01:40
{"gard": ["10351"], "mesh": ["D020754"], "umls": ["C0752124"], "icd-9": ["334.9"], "icd-10": ["G11.2"], "orphanet": ["98758"], "wikidata": ["Q2868788"]}
High-grade neuroendocrine carcinoma of the corpus uteri is an extremely rare, aggressive, primary uterine neoplasm, originating from neuroendocrine cells scattered within the endometrium, characterized, macroscopically, by a bulky, frequently polypoid, mass with abundant necrosis located in the uterus and, histol...
High-grade neuroendocrine carcinoma of the corpus uteri
None
1,185
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=213731
2021-01-23T17:40:42
{"icd-10": ["C54.0", "C54.1", "C54.2", "C54.3", "C54.8"], "synonyms": ["High-grade neuroendocrine carcinoma of the uterine corpus", "Poorly differentiated neuroendocrine carcinoma of the corpus uteri", "Poorly differentiated neuroendocrine carcinoma of the endometrium"]}
Sulfatidosis SpecialtyEndocrinology Sulfatidosis is a form of lysosomal storage disease resulting in a proliferation of sulfatide. ## Contents * 1 Causes * 2 Diagnosis * 2.1 Types * 3 Treatment * 4 See also * 5 References * 6 External links ## Causes[edit] It is caused by a genetic insuffic...
Sulfatidosis
c1706192
1,186
wikipedia
https://en.wikipedia.org/wiki/Sulfatidosis
2021-01-18T18:40:32
{"mesh": ["D052516"], "wikidata": ["Q7636192"]}
Infectious bacterial disease Scanning electron microphotograph depicting a mass of Yersinia pestis bacteria (the cause of bubonic plague) in the foregutte of the flea vector Sylvatic plague is an infectious bacterial disease caused by the plague bacterium (Yersinia pestis) that primarily affects rodents, such a...
Sylvatic plague
None
1,187
wikipedia
https://en.wikipedia.org/wiki/Sylvatic_plague
2021-01-18T18:51:04
{"wikidata": ["Q16992883"]}
A disorder of carnitine cycle and carnitine transport that is characterized classically by early childhood onset cardiomyopathy often with weakness and hypotonia, failure to thrive and recurrent hypoglycemic hypoketotic seizures and/or coma. ## Epidemiology Systemic primary carnitine deficiency (SPCD) exact pre...
Systemic primary carnitine deficiency
c0342788
1,188
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=158
2021-01-23T18:58:16
{"gard": ["5104"], "mesh": ["C536778"], "omim": ["212140"], "umls": ["C0342788"], "icd-10": ["E71.3"], "synonyms": ["CDSP", "CUD", "Carnitine transporter defect", "Carnitine uptake deficiency", "Deficiency of plasma-membrane carnitine transporter", "SPCD"]}
Human jaw cyst Glandular odontogenic cyst Other namesSialo-Odontogenic cyst Relative incidence of odontogenic cysts.[1] Glandular odontogenic cyst is labeled at bottom. SymptomsJaw expansion, swelling, impairment to the tooth, root and cortical plate [2][3] CausesCellular mutation, cyst maturation at glandul...
Glandular odontogenic cyst
c0399558
1,189
wikipedia
https://en.wikipedia.org/wiki/Glandular_odontogenic_cyst
2021-01-18T18:49:22
{"wikidata": ["Q5566618"]}
Patulous Eustachian tube Other namesPatent Eustachian tube SpecialtyENT surgery Patulous Eustachian tube (PET) is the name of a physical disorder where the Eustachian tube, which is normally closed, instead stays intermittently open. When this occurs, the person experiences autophony, the hearing of self...
Patulous Eustachian tube
c0155434
1,190
wikipedia
https://en.wikipedia.org/wiki/Patulous_Eustachian_tube
2021-01-18T18:41:02
{"gard": ["10812"], "umls": ["C0155434"], "wikidata": ["Q1361850"]}
A number sign (#) is used with this entry because heterozygous mutation in the PALB2 gene (610355) on chromosome 16p12 confers susceptibility to pancreatic cancer. For background, phenotypic description, and a discussion of genetic heterogeneity of pancreatic carcinoma, see 260350. Molecular Genetics To explor...
PANCREATIC CANCER, SUSCEPTIBILITY TO, 3
c2931038
1,191
omim
https://www.omim.org/entry/613348
2019-09-22T15:58:53
{"mesh": ["C535837"], "omim": ["613348"], "orphanet": ["1333"], "synonyms": ["Alternative titles", "PNCA3"]}
A number sign (#) is used with this entry because of evidence that bradyopsia is caused by mutations in RGS9 (604067) or its anchor protein R9AP (607814). Clinical Features Kooijman et al. (1991) described 3 unrelated Dutch patients with prolonged electroretinal response suppression (PERRS) and stationary subnormal...
PROLONGED ELECTRORETINAL RESPONSE SUPPRESSION
c1842073
1,192
omim
https://www.omim.org/entry/608415
2019-09-22T16:07:54
{"doid": ["0050335"], "mesh": ["C564243"], "omim": ["608415"], "orphanet": ["75374"], "synonyms": ["PERRS", "Alternative titles", "BRADYOPSIA", "Prolonged electroretinal response suppression"]}
## Summary ### Clinical characteristics. Hemophilia B is characterized by deficiency in factor IX clotting activity that results in prolonged oozing after injuries, tooth extractions, or surgery, and delayed or recurrent bleeding prior to complete wound healing. The age of diagnosis and frequency of bleeding episod...
Hemophilia B
c0008533
1,193
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1495/
2021-01-18T21:22:03
{"mesh": ["D002836"], "synonyms": ["Christmas Disease", "Factor IX Deficiency"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Pinta" disease – news · newspapers · books · scholar · JSTOR (May 2018) (Learn how and when to remove this template mes...
Pinta (disease)
c0031946
1,194
wikipedia
https://en.wikipedia.org/wiki/Pinta_(disease)
2021-01-18T19:01:37
{"gard": ["7397"], "mesh": ["D010874"], "umls": ["C0153242", "C0153243", "C0153244", "C0031946", "C0153241"], "wikidata": ["Q922029"]}
Kelley-Seegmiller syndrome (KSS) is the mildest form of hypoxanthine-guanine phosphoribosyltransferase (HPRT) deficiency (see this term), a hereditary disorder of purine metabolism, and is associated with uric acid overproduction (UAO) leading to urolithiasis, and early-onset gout. ## Epidemiology The exact pre...
Hypoxanthine guanine phosphoribosyltransferase partial deficiency
c0268117
1,195
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=79233
2021-01-23T18:34:33
{"mesh": ["C562583"], "omim": ["300323"], "umls": ["C0268117"], "icd-10": ["E79.8"], "synonyms": ["HPRT deficiency, grade I", "HPRT partial deficiency", "HPRT-related gout", "HPRT-related hyperuricemia", "HPRT1 partial deficiency", "Hypoxanthine guanine phosphoribosyltransferase 1 partial deficiency", "Hypoxanthine gua...
Periorbital dermatitis Other namesPeriocular dermatitis[1] Periorbital dermatitis SpecialtyDermatology Periorbital dermatitis is a skin condition, a variant of perioral dermatitis, occurring on the lower eyelids and skin adjacent to the upper and lower eyelids.[2] ## See also[edit] * Granulomatous peri...
Periorbital dermatitis
None
1,196
wikipedia
https://en.wikipedia.org/wiki/Periorbital_dermatitis
2021-01-18T18:58:23
{"wikidata": ["Q7168677"]}
A number sign (#) is used with this entry because transient neonatal cyanosis is caused by heterozygous mutation in the HBG2 gene (142250) on chromosome 11p15.5. Description Neonatal cyanosis is characterized by symptoms in the fetus and neonate that gradually abate by 5 to 6 months of age. The disorder is caus...
CYANOSIS, TRANSIENT NEONATAL
c3151421
1,197
omim
https://www.omim.org/entry/613977
2019-09-22T15:56:58
{"omim": ["613977"], "orphanet": ["280615"], "synonyms": ["Transient neonatal cyanosis and anemia due to Toms River Hemoglobin"]}
Congenital hepatic fibrosis is a rare disease of the liver that is present at birth. Symptoms include the following: a large liver, a large spleen, gastrointestinal bleeding caused by varices, increased pressure in the blood vessels that carry blood to the liver (portal hypertension), and scar tissue in the liver (fi...
Congenital hepatic fibrosis
c0009714
1,198
gard
https://rarediseases.info.nih.gov/diseases/6168/congenital-hepatic-fibrosis
2021-01-18T18:01:08
{"mesh": ["C562378"], "synonyms": []}
For a general phenotypic description and a discussion of genetic heterogeneity of kala-azar, which is also known as visceral leishmaniasis, see 608207. Mapping A major susceptibility gene for kala-azar has been identified on chromosome 22q12 (KAZA1; 608207) in the Aringa ethnic group in eastern Sudan. Miller et al....
KALA-AZAR, SUSCEPTIBILITY TO, 3
c1969648
1,199
omim
https://www.omim.org/entry/611382
2019-09-22T16:03:21
{"omim": ["611382"], "synonyms": ["Alternative titles", "LEISHMANIASIS, VISCERAL, SUSCEPTIBILITY TO, 3"]}