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This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Contagious disease" – news · newspapers · books · scholar · JSTOR (September 2016) (Learn how and when to remove this t...
Contagious disease
c0009450
1,200
wikipedia
https://en.wikipedia.org/wiki/Contagious_disease
2021-01-18T19:05:39
{"mesh": ["D003141"], "wikidata": ["Q2995419"]}
Osteopetrosis refers to a group of rare, inherited skeletal disorders characterized by increased bone density and abnormal bone growth. Symptoms and severity can vary greatly, ranging from neonatal onset with life-threatening complications (such as bone marrow failure) to the incidental finding of osteopetrosis o...
Osteopetrosis autosomal recessive 6
c1969093
1,201
gard
https://rarediseases.info.nih.gov/diseases/4156/osteopetrosis-autosomal-recessive-6
2021-01-18T17:58:31
{"mesh": ["C566931"], "omim": ["611497"], "umls": ["C1969093"], "synonyms": ["OPTB6", "Autosomal recessive osteopetrosis type 6", "Osteopetrosis autosomal recessive intermediate form"]}
The leg of this Pisaster ochraceus sea star in Oregon is disintegrating as a result of sea star wasting syndrome Sea star wasting disease or starfish wasting syndrome is a disease of starfish and several other echinoderms that appears sporadically, causing mass mortality of those affected.[1] There are around 40 dif...
Sea star wasting disease
None
1,202
wikipedia
https://en.wikipedia.org/wiki/Sea_star_wasting_disease
2021-01-18T18:36:22
{"wikidata": ["Q15241744"]}
A rare, genetic, paroxysmal dystonia disorder characterized by childhood to adolescent-onset of episodic paroxysmal choreoathetosis, triggered mainly by sudden movements, prolonged exercise, anxiety and emotional stress, in association with progressive spastic paraparesis (onest in adulthood), gait ataxia, mild to mo...
Paroxysmal dystonic choreathetosis with episodic ataxia and spasticity
c1832855
1,203
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=53583
2021-01-23T18:41:07
{"mesh": ["C563401"], "omim": ["601042"], "umls": ["C1832855"], "icd-10": ["G24.8"], "synonyms": ["DYT9", "Episodic choreoathetosis/spasticity"]}
Idiopathic acute eosinophilic pneumonia (IAEP) is characterized by the rapid accumulation of eosinophils in the lungs. Eosinophils are a type of white blood cell and are part of the immune system. IAEP can occur at any age but most commonly affects otherwise healthy individuals between 20 and 40 years of age. Signs a...
Idiopathic acute eosinophilic pneumonia
c4518469
1,204
gard
https://rarediseases.info.nih.gov/diseases/519/idiopathic-acute-eosinophilic-pneumonia
2021-01-18T17:59:50
{"orphanet": ["724"], "synonyms": ["IAEP"]}
A number sign (#) is used with this entry because Leber congenital amaurosis-15 and juvenile retinitis pigmentosa are caused by homozygous or compound heterozygous mutation in the TULP1 gene (602280) on chromosome 6p21.3. Description Autosomal recessive childhood-onset severe retinal dystrophy is a heterogeneous gr...
LEBER CONGENITAL AMAUROSIS 15
c0339527
1,205
omim
https://www.omim.org/entry/613843
2019-09-22T15:57:16
{"doid": ["0110189"], "mesh": ["D057130"], "omim": ["613843"], "orphanet": ["65"], "genereviews": ["NBK531510"]}
## Clinical Features Reid et al. (1998) reported 4 individuals from 2 generations of a family who had recurrent episodes of parotitis beginning in childhood and, in the only adult at the time of report, remitting at the age of 14 years. In this individual, however, the episodes recurred during each of 2 pregnancies...
PAROTITIS, JUVENILE RECURRENT
c1863691
1,206
omim
https://www.omim.org/entry/603588
2019-09-22T16:12:50
{"mesh": ["C566359"], "omim": ["603588"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Microcoria" – news · newspapers · books · scholar · JSTOR (December 2009) (Learn how and when to remove this template m...
Microcoria
c1303009
1,207
wikipedia
https://en.wikipedia.org/wiki/Microcoria
2021-01-18T18:38:29
{"gard": ["3635"], "mesh": ["C537550"], "umls": ["C1303009"], "orphanet": ["566"], "wikidata": ["Q720101"]}
Protein–energy malnutrition Other namesProtein–calorie malnutrition, PEM, PCM SpecialtyEndocrinology Protein–energy malnutrition (PEM), sometimes called protein-energy undernutrition (PEU), is a form of malnutrition that is defined as a range of pathological conditions arising from coincident lack of die...
Protein–energy malnutrition
c0033677
1,208
wikipedia
https://en.wikipedia.org/wiki/Protein%E2%80%93energy_malnutrition
2021-01-18T18:51:12
{"mesh": ["D011502"], "umls": ["C0033677"], "wikidata": ["Q4082071"]}
Morahan et al. (1996) mapped an insulin-dependent diabetes mellitus gene, designated IDDM13, to chromosome 2q34 on the basis of analysis of 98 affected sib pairs. The maximum lod score with D2S164 was 3.345. Using the MAP-MAKER/Sibs program, which allows multipoint linkage analysis to be performed on data collect...
DIABETES MELLITUS, INSULIN-DEPENDENT, 13
c1832474
1,209
omim
https://www.omim.org/entry/601318
2019-09-22T16:15:11
{"mesh": ["C563352"], "omim": ["601318"], "synonyms": ["Alternative titles", "INSULIN-DEPENDENT DIABETES MELLITUS 13"]}
A Pierre Robin syndrome associated with bone disease characterized by severe short-limbed dwarfism, joint dislocations, club feet along with distinctive facies and radiographic findings. ## Epidemiology Atelosteogenesis I (AOI) is a very rare infrequently described disorder. ## Clinical description Affected neona...
Atelosteogenesis type I
c0265283
1,210
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1190
2021-01-23T18:39:19
{"gard": ["9287"], "mesh": ["C535396"], "omim": ["108720"], "umls": ["C0265283"], "icd-10": ["Q78.8"], "synonyms": ["AO1", "AOI", "Atelosteogenesis type 1", "Giant cell chondrodysplasia", "Spondylo-humero-femoral dysplasia"]}
For a phenotypic description of gout and a discussion of genetic heterogeneity of serum uric acid concentration quantitative trait loci, see UAQTL1 (138900). Mapping Sulem et al. (2011) tested 16 million SNPs, identified through whole-genome sequencing of 457 Icelanders, for association with gout and serum uric aci...
URIC ACID CONCENTRATION, SERUM, QUANTITATIVE TRAIT LOCUS 6
c3553635
1,211
omim
https://www.omim.org/entry/614747
2019-09-22T15:54:19
{"omim": ["614747"]}
This article is an orphan, as no other articles link to it. Please introduce links to this page from related articles; try the Find link tool for suggestions. (January 2018) Allomnesia or memory illusion is a memory disorder, which involves distorted memories of a past situation. It is generally a physiological ...
Allomnesia
None
1,212
wikipedia
https://en.wikipedia.org/wiki/Allomnesia
2021-01-18T18:35:16
{"icd-9": ["780.93"], "icd-10": ["R41.3"], "wikidata": ["Q3612627"]}
See Immune Response to Synthetic Polypeptide--IRPHEGAL (146810) and Chan et al. (1984). *[v]: View this template *[t]: Discuss this template *[e]: Edit this template *[c.]: circa *[AA]: Adrenergic agonist *[AD]: Acetaldehyde dehydrogenase *[HAART]: highly active antiretroviral therapy *[Ki]: Inhi...
IMMUNE RESPONSE TO SYNTHETIC POLYPEPTIDE--IRGAT
c1840267
1,213
omim
https://www.omim.org/entry/146820
2019-09-22T16:39:37
{"omim": ["146820"]}
Congenital hyperinsulinism is a disease where there are abnormally high levels of insulin, a hormone produced by the beta cells of the pancreas that helps control blood sugar levels. Because of the high levels of insulin, people with this disease have frequent episodes of low blood sugar (hypoglycemia) that can even ...
Congenital hyperinsulinism
c3888018
1,214
gard
https://rarediseases.info.nih.gov/diseases/3947/congenital-hyperinsulinism
2021-01-18T18:01:09
{"mesh": ["D044903"], "orphanet": ["657"], "synonyms": ["Persistent hyperinsulinemic hypoglycemia of infancy", "PHHI", "Hyperinsulinemic hypoglycemia familial", "Hypoglycemia hyperinsulinemic of infancy", "Hyperinsulinism familial with pancreatic nesidioblastosis", "Nesidioblastosis of pancreas", "Hyperinsulinism conge...
For a phenotypic description and a discussion of genetic heterogeneity of malignant hyperthermia, see MHS1 (145600). Mapping In 3 unrelated families, Levitt et al. (1991) excluded linkage of the MHS phenotype to loci on 19q13.1, thus indicating genetic heterogeneity. Levitt et al. (1992) extended these studies to 1...
MALIGNANT HYPERTHERMIA, SUSCEPTIBILITY TO, 2
c0024591
1,215
omim
https://www.omim.org/entry/154275
2019-09-22T16:38:34
{"mesh": ["D008305"], "omim": ["154275"], "orphanet": ["423"], "synonyms": ["Alternative titles", "MHS2"], "genereviews": ["NBK1146"]}
A rare form of chronic cutaneous lupus erythematosus characterized by extreme photosensitivity with intermittent formation of erythematous, edematous, urticarial-like, smooth plaques on sun-exposed skin areas. The lesions heal without scarring. The course of the disease is benign, and development of systemic lupus er...
Lupus erythematosus tumidus
c0406636
1,216
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=90283
2021-01-23T17:37:24
{"gard": ["13003"], "umls": ["C0406636"], "icd-10": ["L93.2"], "synonyms": ["Intermittent cutaneous lupus"]}
## Description Ebstein anomaly is characterized by downward displacement of variable severity of the tricuspid valve into the right ventricle. The valve leaflets may be dysplastic, and a variable portion of the proximal part of the right ventricle is in continuity with the right atrium ('atrialized'), because of th...
EBSTEIN ANOMALY
c0013481
1,217
omim
https://www.omim.org/entry/224700
2019-09-22T16:28:28
{"doid": ["14289"], "mesh": ["D004437"], "omim": ["224700"], "icd-9": ["746.2"], "icd-10": ["Q22.5"], "orphanet": ["1880"]}
## Clinical Features Arias et al. (1976) described a seemingly new form of skeletal dysplasia among the Irapa Indians of Venezuela. Features included short spine from platyspondyly, short metacarpals and metatarsals, and striking changes in the proximal femoral and distal humeral epiphyses. Hernandez et al. (1980)...
SPONDYLOEPIMETAPHYSEAL DYSPLASIA, IRAPA TYPE
c0432213
1,218
omim
https://www.omim.org/entry/271650
2019-09-22T16:22:02
{"mesh": ["C562958"], "omim": ["271650"], "orphanet": ["93351"]}
Remnants of the pupillary membrane persist as strands and other irregular tissue in the region of the pupil. Cassady and Light (1957) described a family in which 11 persons in 4 generations showed remnants of the pupillary membrane. Four of these also had congenital cataract and 3 had increased corneal diameter. Poss...
PUPILLARY MEMBRANE, PERSISTENCE OF
c0271130
1,219
omim
https://www.omim.org/entry/178900
2019-09-22T16:35:22
{"mesh": ["C562700"], "omim": ["178900"]}
A number sign (#) is used with this entry because of evidence that early infantile epileptic encephalopathy-30 (EIEE30) is caused by heterozygous mutation in the SIK1 gene (605705) on chromosome 21q22. For a general phenotypic description and a discussion of genetic heterogeneity of EIEE, see 308350. Clinical Featu...
EPILEPTIC ENCEPHALOPATHY, EARLY INFANTILE, 30
c0270855
1,220
omim
https://www.omim.org/entry/616341
2019-09-22T15:49:11
{"doid": ["0080465"], "mesh": ["C562695"], "omim": ["616341"], "orphanet": ["1935", "3451", "1934"]}
Medium-chain acyl-coenzyme A dehydrogenase deficiency (MCADD) is an inherited metabolic disorder that prevents the body from converting certain fats to energy, particularly during periods without food (fasting). People with MCADD do not have enough of an enzyme needed to metabolize a group of fats called medium-chain...
Medium-chain acyl-coenzyme A dehydrogenase deficiency
c0220710
1,221
gard
https://rarediseases.info.nih.gov/diseases/540/medium-chain-acyl-coenzyme-a-dehydrogenase-deficiency
2021-01-18T17:59:12
{"mesh": ["C536038"], "omim": ["201450"], "umls": ["C0220710"], "orphanet": ["42"], "synonyms": ["MCAD deficiency", "Acyl-CoA dehydrogenase medium chain deficiency of", "MCADH deficiency", "ACADM deficiency", "MCADD", "Medium chain acyl CoA dehydrogenase deficiency", "Medium-chain acyl-CoA dehydrogenase deficiency"]}
## Summary The purpose of this overview is to increase the awareness of clinicians regarding the causes of Bardet-Biedl syndrome and related genetic counseling issues. The following are the goals of this overview: ### Goal 1. Describe the clinical characteristics of Bardet-Biedl syndrome. ### Goal 2. Review the...
Bardet-Biedl Syndrome Overview
None
1,222
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1363/
2021-01-18T21:40:16
{"synonyms": []}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Sesamoiditis" – news · newspapers · books · scholar · JSTOR (January 2015) (Learn how and when to remove this template ...
Sesamoiditis
c0264076
1,223
wikipedia
https://en.wikipedia.org/wiki/Sesamoiditis
2021-01-18T18:54:12
{"icd-9": ["733.99"], "icd-10": ["M89.37"], "wikidata": ["Q4411017"]}
Noncompaction cardiomyopathy Other namesSpongiform cardiomyopathy Noncompaction cardiomyopathy is inherited in an autosomal dominant manner SpecialtyCardiology Non-compaction cardiomyopathy (NCC), is a rare congenital cardiomyopathy that affects both children and adults.[1] It results from the failure ...
Noncompaction cardiomyopathy
c1858725
1,224
wikipedia
https://en.wikipedia.org/wiki/Noncompaction_cardiomyopathy
2021-01-18T18:42:20
{"gard": ["10985"], "mesh": ["C565821", "D056830"], "umls": ["C1858725"], "icd-10": ["I42.8"], "orphanet": ["54260"], "wikidata": ["Q1725245"]}
Aase syndrome Other namesHydrocephalus-cleft palate-joint contractures syndrome, Aase-Smith syndrome Aase syndrome or Aase–Smith syndrome is a rare inherited disorder characterized by anemia with some joint and skeletal deformities. Aase syndrome is thought to be an autosomal dominant inherited disorder.[1...
Aase syndrome
c0220686
1,225
wikipedia
https://en.wikipedia.org/wiki/Aase_syndrome
2021-01-18T18:45:28
{"gard": ["5642"], "mesh": ["C535332"], "umls": ["C0220686"], "orphanet": ["916"], "wikidata": ["Q303400"]}
A number sign (#) is used with this entry because of evidence that isolated microphthalmia-4 (MCOP4) is caused by mutation in the GDF6 gene (601147) on chromosome 8q22. For a phenotypic description and a discussion of genetic heterogeneity of isolated microphthalmia, see MCOP1 (251600). Molecular Genetics Asai...
MICROPHTHALMIA, ISOLATED 4
c2751307
1,226
omim
https://www.omim.org/entry/613094
2019-09-22T15:59:41
{"doid": ["0060836"], "mesh": ["C567757"], "omim": ["613094", "251600"], "orphanet": ["2542"], "synonyms": ["Isolated anophthalmia-microphthalmia syndrome", "MAC spectrum", "Microphthalmia-anophthalmia-coloboma spectrum"], "genereviews": ["NBK1378"]}
Maroteaux et al. (1978) proposed this term for a type of oligosaccharidosis in which a glomerular nephropathy develops early and causes death at a young age. The clinical and radiologic features are dysmorphic facies, visceral storage disease, early and severe mental retardation, and skeletal abnormalities of a type ...
NEPHROSIALIDOSIS
c0268228
1,227
omim
https://www.omim.org/entry/256150
2019-09-22T16:24:25
{"mesh": ["C537366"], "omim": ["256150"], "orphanet": ["87876"]}
Neonatal onset multisystem inflammatory disease (NOMID) is a disorder that causes persistent inflammation and tissue damage primarily affecting the nervous system, skin, and joints. Recurrent episodes of mild fever may also occur in this disorder. People with NOMID have a skin rash that is usually present from birth...
Neonatal onset multisystem inflammatory disease
c0409818
1,228
medlineplus
https://medlineplus.gov/genetics/condition/neonatal-onset-multisystem-inflammatory-disease/
2021-01-27T08:25:08
{"gard": ["1356"], "mesh": ["D056587"], "omim": ["607115"], "synonyms": []}
Jejunal atresia is a birth defect in a newborn characterized by partial or complete absence of the membrane connecting the small intestines to the abdominal wall (the mesentery). It causes a portion of the small intestines (the jejunum) to twist around an artery that supplies blood to the colon (the marginal artery)....
Jejunal atresia
c0266175
1,229
gard
https://rarediseases.info.nih.gov/diseases/6799/jejunal-atresia
2021-01-18T17:59:41
{"mesh": ["D007409"], "omim": ["243600"], "synonyms": ["Apple peel syndrome", "Apple peel small bowel syndrome", "APSB", "Apple-peel intestinal atresia", "Familial apple peel jejunal atresia", "Atresia of small intestine", "Intestinal atresia type IIIb", "Jejunoileal atresia", "Small intestinal atresia"]}
Prolidase deficiency is an inherited disorder of peptide metabolism characterized by severe skin lesions, recurrent infections (involving mainly the skin and respiratory system), dysmorphic facial features, variable cognitive impairment, and splenomegaly. ## Epidemiology The exact prevalence is unknown but a preval...
Prolidase deficiency
c0268532
1,230
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=742
2021-01-23T17:21:11
{"gard": ["7473"], "mesh": ["D056732"], "omim": ["170100"], "umls": ["C0268532", "C1534653"], "icd-10": ["E72.8"], "synonyms": ["Hyperimidodipeptiduria"]}
## Summary ### Clinical characteristics. The autosomal dominant TRPV4 disorders (previously considered to be clinically distinct phenotypes before their molecular basis was discovered) are now grouped into neuromuscular disorders and skeletal dysplasias; however, the overlap within each group is considerable. Affec...
Autosomal Dominant TRPV4 Disorders
None
1,231
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK201366/
2021-01-18T21:41:27
{"synonyms": []}
A rare, syndromic intellectual disability characterized by developmental delay, speech apraxia, autism with stereotypies, intellectual disability and unspecific dysmorphic facial features. Seizures or isolated EEG abnormalities may also be associated. *[v]: View this template *[t]: Discuss this template *[e]: ...
Intellectual disability-autism-speech apraxia-craniofacial dysmorphism syndrome
c4540131
1,232
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=529965
2021-01-23T17:41:43
{"omim": ["617682"], "synonyms": ["Pilarowski-Bjornsson syndrome"]}
## Summary ### Clinical characteristics. Dysferlinopathy includes a spectrum of muscle disease characterized by two main phenotypes: Miyoshi myopathy with primarily distal weakness and limb-girdle muscular dystrophy type 2B (LGMD2B) with primarily proximal weakness. Miyoshi myopathy (median age of onset 19 years) i...
Dysferlinopathy
c2931687
1,233
gene_reviews
https://www.ncbi.nlm.nih.gov/books/NBK1303/
2021-01-18T21:29:54
{"mesh": ["C537995"], "synonyms": []}
## Description Otosclerosis is a hearing disorder that is associated with disordered bone remodeling in the otic capsule. The bone remodeling can result in conductive, mixed, or sensorineural hearing loss as a result of stapes footplate fixation or cochlear involvement (summary by Schrauwen et al., 2011). Clinical...
OTOSCLEROSIS 10
c3888339
1,234
omim
https://www.omim.org/entry/615589
2019-09-22T15:51:33
{"omim": ["615589"]}
Form of dysgammaglobulinemia IgG deficiency Other namesSelective deficiency of immunoglobulin G Immunoglobulin G SpecialtyHematology IgG deficiency is a form of dysgammaglobulinemia where the proportional levels of the IgG isotype are reduced relative to other immunoglobulin isotypes. IgG deficiency is of...
IgG deficiency
c0162539
1,235
wikipedia
https://en.wikipedia.org/wiki/IgG_deficiency
2021-01-18T18:46:20
{"gard": ["10371"], "mesh": ["D017099"], "umls": ["C0162539"], "wikidata": ["Q17094243"]}
A number sign (#) is used with this entry because of evidence that multiple epiphyseal dysplasia-3 (EDM3) is caused by heterozygous mutation in the COL9A3 gene (120270) on chromosome 20q13. Description Multiple epiphyseal dysplasia is characterized by early-onset short stature, waddling gait, and stiffness and/...
EPIPHYSEAL DYSPLASIA, MULTIPLE, 3
c1832998
1,236
omim
https://www.omim.org/entry/600969
2019-09-22T16:15:40
{"doid": ["0070304"], "mesh": ["C535503"], "omim": ["600969"], "orphanet": ["166002"], "synonyms": [], "genereviews": ["NBK1123"]}
A rare autoimmune bullous skin disease characterized by acquired, subepidermal tense bullae occurring on normal of inflamed skin and that is typically widespread (occurring in the flexor regions of the proximal arms and legs, in the armpits, groin and the abdomen) and often associated with pruritus. The evolution is ...
Bullous pemphigoid
c0030805
1,237
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=703
2021-01-23T18:27:37
{"gard": ["5972"], "mesh": ["D010391"], "umls": ["C0030805"], "icd-10": ["L12.0"]}
## Description Vesicoureteral reflux (VUR) is characterized by the reflux of urine from the bladder into the ureters and sometimes into the kidneys. It is a risk factor for urinary tract infections. Primary VUR results from a developmental defect of the ureterovesical junction (UVJ). In combination with intrarenal ...
VESICOURETERAL REFLUX 1
c4551858
1,238
omim
https://www.omim.org/entry/193000
2019-09-22T16:32:00
{"doid": ["9620"], "mesh": ["D014718"], "omim": ["193000"], "orphanet": ["289365"], "synonyms": ["VUR", "Alternative titles", "Familial VUR"]}
A rare subtype of kyphoscoliotic Ehlers-Danlos syndrome characterized by congenital muscle hypotonia, congenital or early-onset kyphoscoliosis (progressive or non-progressive), and generalized joint hypermobility with dislocations/subluxations (in particular of the shoulders, hips, and knees). Additional common featu...
Kyphoscoliotic Ehlers-Danlos syndrome due to FKBP22 deficiency
c3281160
1,239
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=300179
2021-01-23T18:53:50
{"omim": ["614557"], "icd-10": ["Q79.6"], "synonyms": ["Ehlers-Danlos syndrome with kyphoscoliosis, myopathy, and deafness", "Ehlers-Danlos syndrome with kyphoscoliosis, myopathy, and hearing loss", "FKBP14-related EDS", "FKBP22-deficient EDS", "Kyphoscoliotic EDS due to FKBP22 deficiency", "kEDS-FKBP14"]}
A number sign (#) is used with this entry because hemoglobin H disease is caused by contiguous gene deletion of the hemoglobin alpha-1 (HBA1; 141800) and alpha-2 (HBA2; 141850) genes on one chromosome 16, and a defect, deletional or nondeletional, in either HBA1 or HBA2 on the other. Description Hemoglobin H diseas...
HEMOGLOBIN H DISEASE
c1260396
1,240
omim
https://www.omim.org/entry/613978
2019-09-22T15:56:53
{"doid": ["0110031"], "omim": ["613978"], "orphanet": ["93616"], "synonyms": ["Alternative titles", "ALPHA-THALASSEMIA, HEMOGLOBIN H TYPE", "HEMOGLOBIN H DISEASE, DELETIONAL"]}
A rare group of inherited congenital malformation disorders characterized by craniosynostosis and fusion or webbing of the fingers or toes, often with other associated manifestations. ## Epidemiology The exact prevalence and birth incidence of ACS syndromes are not known. Overall incidence of all forms of craniosyn...
Acrocephalosyndactyly
c1510455
1,241
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=946
2021-01-23T18:46:03
{"mesh": ["D000168"], "umls": ["C1510455"], "icd-10": ["Q87.0"], "synonyms": ["ACS", "Acrocephalosyndactylia"]}
Amnion nodosum are nodules found on the amnion, and is frequently present in oligohydramnios.[1] The nodules are composed of squamous cell aggregates derived from the vernix caseosa on the fetal skin. Amnion nodosum is caused by the unexpected abrasion of amnion with depositions of the fetal surface cells and acellul...
Amnion nodosum
c0269802
1,242
wikipedia
https://en.wikipedia.org/wiki/Amnion_nodosum
2021-01-18T18:29:53
{"umls": ["C0269802"], "icd-9": ["658.8"], "wikidata": ["Q4747401"]}
Ring chromosome 13 is a chromosomal anomaly of chromosome 13 characterized by a widely variable phenotype (ranging from mild to severe) principally characterized by intrauterine growth retardation, developmental delay, short stature, moderate to severe intellectual deficit, microcephaly, facial dysmorphism (i.e. ...
Ring chromosome 13 syndrome
c2931808
1,243
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=96176
2021-01-23T17:10:27
{"gard": ["6069"], "mesh": ["C538303"], "umls": ["C2931808"], "icd-10": ["Q93.2"], "synonyms": ["Ring 13", "Ring chromosome 13"]}
A complex form of hereditary spastic paraplegia, characterized by an onset in childhood or adulthood of progressive spastic paraplegia (with spastic gait, spasticity, lower limb weakness, pes cavus and urinary urgency) associated with the additional manifestation of peripheral sensorimotor neuropathy. *[v]: View t...
Autosomal dominant spastic paraplegia type 36
c2936879
1,244
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=320365
2021-01-23T17:03:28
{"mesh": ["C567930"], "omim": ["613096"], "umls": ["C2936879"], "icd-10": ["G11.4"], "synonyms": ["SPG36"]}
Mastocytosis occurs when too many mast cells accumulate in the skin and/or internal organs such as the liver, spleen, bone marrow, and small intestines. Mast cells are a type of white blood cell in the immune system. Mast cells are responsible for protecting the body from infection and releasing chemicals to create i...
Mastocytosis
c0024899
1,245
gard
https://rarediseases.info.nih.gov/diseases/6987/mastocytosis
2021-01-18T17:59:14
{"mesh": ["D008415"], "omim": ["154800"], "orphanet": ["98292"], "synonyms": ["Mast cell disease"]}
Synesthesia that associates numbers or letters with colors How someone with grapheme–color synesthesia might perceive (not "see") certain letters and numbers Grapheme–color synaesthesia or colored grapheme synesthesia is a form of synesthesia in which an individual's perception of numerals and letters is associated...
Grapheme–color synesthesia
None
1,246
wikipedia
https://en.wikipedia.org/wiki/Grapheme%E2%80%93color_synesthesia
2021-01-18T18:43:47
{"wikidata": ["Q287285"]}
Congenital respiratory-biliary fistula (RBF) is a rare developmental defect characterized by an anomalous connection of trachea or bronchus with left hepatic duct presenting with respiratory distress, recurrent respiratory infections and biliary expectoration or vomitus. *[v]: View this template *[t]: Discuss th...
Congenital respiratory-biliary fistula
None
1,247
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2040
2021-01-23T17:00:32
{"gard": ["1475"], "icd-10": ["Q32.4"]}
A number sign (#) is used with this entry because neurofibromatosis type II (NF2) is caused by heterozygous mutation in the gene encoding neurofibromin-2 (NF2; 607379), which is also called merlin, on chromosome 22q12. Description The central or type II form of neurofibromatosis (NF2) is an autosomal dominant multi...
NEUROFIBROMATOSIS, TYPE II
c0027832
1,248
omim
https://www.omim.org/entry/101000
2019-09-22T16:45:31
{"doid": ["0111252"], "mesh": ["D016518"], "omim": ["101000"], "icd-9": ["237.72"], "icd-10": ["Q85.02"], "orphanet": ["637"], "synonyms": ["Alternative titles", "NEUROFIBROMATOSIS, CENTRAL TYPE", "ACOUSTIC SCHWANNOMAS, BILATERAL", "BILATERAL ACOUSTIC NEUROFIBROMATOSIS", "ACOUSTIC NEURINOMA, BILATERAL"], "genereviews":...
A rare peeling skin syndrome characterized by superficial peeling of the skin predominantly affecting the dorsa of the hands and feet. ## Epidemiology Acral PSS is rare, with approximately 40 cases described in the literature to date. ## Clinical description The disease manifests shortly after birth or in early c...
Acral peeling skin syndrome
c1853354
1,249
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=263534
2021-01-23T18:49:05
{"gard": ["12863"], "mesh": ["C536316"], "omim": ["609796"], "umls": ["C1853354"], "icd-10": ["Q80.8"], "synonyms": ["Acral PSS", "Acral deciduous skin", "Localized PSS", "Localized deciduous skin"]}
## Clinical Features Crome and Williams (1960) observed multilocular encephalomalacia in an infant who died at 1 month of age. A sib was living at age 6 years but may have had the same abnormality manifested by microcephaly, spastic diplegia, and mental retardation. It is not certain that this is a distinct entity....
ENCEPHALOMALACIA, MULTILOCULAR
c1856991
1,250
omim
https://www.omim.org/entry/225700
2019-09-22T16:28:21
{"mesh": ["C565597"], "omim": ["225700"]}
Citrullinemia type I is a rare autosomal recessive urea cycle defect characterized biologically by hyperammonemia and clinically by progressive lethargy, poor feeding and vomiting in the neonatal form (Acute neonatal citrullinemia type I, see this term) and by variable hyperammonemia in the later-onset form (Adult-on...
Citrullinemia type I
c0751751
1,251
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=247525
2021-01-23T17:43:33
{"mesh": ["D020159"], "omim": ["215700"], "umls": ["C0751751"], "icd-10": ["E72.2"], "synonyms": ["ASS deficiency", "Argininosuccinate synthase deficiency", "Argininosuccinate synthetase deficiency", "Argininosuccinic acid synthase deficiency", "Argininosuccinic acid synthetase deficiency", "CTLN1", "Citrullinemia type...
Huang et al. (1999) described a brother and sister, in a sibship of 4, with multiple congenital anomalies, including Hirschsprung disease. The boy was born with bilateral complete cleft lip and palate, telecanthus, duplication of the great toes, and postaxial polydactyly of the right foot. Echocardiogram showed atria...
HIRSCHSPRUNG DISEASE WITH HEART DEFECTS, LARYNGEAL ANOMALIES, AND PREAXIAL POLYDACTYLY
c1858696
1,252
omim
https://www.omim.org/entry/604211
2019-09-22T16:12:27
{"mesh": ["C565817"], "omim": ["604211"]}
Leber congenital amaurosis is an eye disorder that primarily affects the retina, which is the specialized tissue at the back of the eye that detects light and color. People with this disorder typically have severe visual impairment beginning in infancy. The visual impairment tends to be stable, although it may worsen...
Leber congenital amaurosis
c2931258
1,253
medlineplus
https://medlineplus.gov/genetics/condition/leber-congenital-amaurosis/
2021-01-27T08:25:08
{"gard": ["634"], "mesh": ["C536600"], "omim": ["204000", "611755", "610612", "612712", "613341", "204100", "604232", "604393", "604537", "608553"], "synonyms": []}
Not to be confused with Pneumococcal pneumonia. Pneumocystis pneumonia Other namesPneumocystis jirovecii pneumonia, pneumocystis carinii pneumonia Pneumocystis jirovecii cysts from bronchoalveolar lavage, stained with Toluidine blue O stain SpecialtyInfectious disease, Pulmonology CausesPneumocystis jiroveci...
Pneumocystis pneumonia
c1535939
1,254
wikipedia
https://en.wikipedia.org/wiki/Pneumocystis_pneumonia
2021-01-18T18:43:20
{"mesh": ["D011020"], "wikidata": ["Q15401586"]}
Chromosome 6p duplication is a chromosome abnormality that occurs when there is an extra copy of genetic material on the short arm (p) of chromosome 6. The severity of the condition and the signs and symptoms depend on the size and location of the duplication and which genes are involved. Features that often occu...
Chromosome 6p duplication
c2931621
1,255
gard
https://rarediseases.info.nih.gov/diseases/5352/chromosome-6p-duplication
2021-01-18T18:01:20
{"mesh": ["C537811"], "umls": ["C2931621"], "synonyms": ["Duplication 6p", "Trisomy 6p", "6p duplication", "6p trisomy", "Partial trisomy 6p"]}
A rare, syndromic intellectual disability characterized by global developmental delay including severely delayed or absent speech, moderate to severe intellectual disability, behavioral issues, stereotypic behavior, febrile seizures and epilepsy, abnormal gait, vision defects, and characteristic facial features. Intr...
DYRK1A-related intellectual disability syndrome due to 21q22.13q22.2 microdeletion
None
1,256
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=268261
2021-01-23T19:09:55
{"icd-10": ["Q93.5"], "synonyms": ["21q22.13q22.2 microdeletion syndrome", "Del(21)(q22.13q22.2)", "Monosomy 21q22.13q22.2"]}
Prothrombin G20210A Other namesProthrombin thrombophilia,[1] factor II mutation, prothrombin mutation, rs1799963, factor II G20210A SymptomsBlood clots[1] Frequency2% (Caucasians)[1] Prothrombin G20210A is a genetic condition that increases the risk of blood clots including from deep vein thrombosis, and o...
Prothrombin G20210A
c2584409
1,257
wikipedia
https://en.wikipedia.org/wiki/Prothrombin_G20210A
2021-01-18T18:35:24
{"umls": ["C2584409"], "wikidata": ["Q2113626"]}
Medical condition A flail limb (also flail arm or flail leg) is a medical term which refers to an extremity in which the primary nerve has been severed or ceased to function, resulting in complete lack of mobility and sensation. Although blood typically continues to flow through the limb, it is completely useles...
Flail limb
c0231446
1,258
wikipedia
https://en.wikipedia.org/wiki/Flail_limb
2021-01-18T18:32:04
{"umls": ["C0231446"], "wikidata": ["Q5457051"]}
Pressure of speech Other namesPressured speech SpecialtyPsychiatry Pressure of speech is a tendency to speak rapidly and frenziedly. Pressured speech is motivated by an urgency that may not be apparent to the listener. The speech produced is difficult to interrupt. Such speech may be too fast, erratic, ...
Pressure of speech
c0233718
1,259
wikipedia
https://en.wikipedia.org/wiki/Pressure_of_speech
2021-01-18T18:29:17
{"umls": ["C0233718"], "wikidata": ["Q7241734"]}
A number sign (#) is used with this entry because Wolff-Parkinson-White syndrome can be caused by mutation in the gamma-2 regulatory subunit of AMP-activated protein kinase (PRKAG2; 602743). Mutation in the PRKAG2 gene can also cause a form of hypertrophic cardiomyopathy in which some patients exhibit WPW (CMH6;...
WOLFF-PARKINSON-WHITE SYNDROME
c0043202
1,260
omim
https://www.omim.org/entry/194200
2019-09-22T16:31:45
{"doid": ["384"], "mesh": ["D014927"], "omim": ["194200"], "icd-10": ["I45.6"], "synonyms": ["Alternative titles", "WPW SYNDROME"]}
A number sign (#) is used with this entry because of evidence that metatropic dysplasia is caused by heterozygous mutation in the TRPV4 gene (605427) on chromosome 12q24.1. Description Metatropic dysplasia (MD) is characterized by short limbs with limitation and enlargement of joints and usually severe kyphoscolios...
METATROPIC DYSPLASIA
c0265281
1,261
omim
https://www.omim.org/entry/156530
2019-09-22T16:38:15
{"mesh": ["C537356"], "omim": ["156530"], "orphanet": ["2635"], "synonyms": ["Alternative titles", "METATROPIC DWARFISM"], "genereviews": ["NBK201366"]}
This article does not cite any sources. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Hemotympanum" – news · newspapers · books · scholar · JSTOR (June 2020) (Learn how and when to remove this template message) Tympani...
Hemotympanum
c0019125
1,262
wikipedia
https://en.wikipedia.org/wiki/Hemotympanum
2021-01-18T19:04:06
{"umls": ["C0019125"], "wikidata": ["Q1642058"]}
Intellectual disability-developmental delay-contractures syndrome, formerly known as Wieacker-Wolff syndrome, is a severe X-linked recessive neurodevelopmental disorder characterized by severe contractures (arthrogryposis; see this term) and intellectual disability. ## Epidemiology Prevalence and incidence rate...
Intellectual disability-developmental delay-contractures syndrome
c0796200
1,263
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=3454
2021-01-23T18:11:00
{"gard": ["7890"], "mesh": ["C536703"], "omim": ["314580"], "umls": ["C0796200"], "icd-10": ["G71.8"], "synonyms": ["Foot contractures-muscle atrophy-oculomotor apraxia syndrome", "Wieacker-Wolff syndrome"]}
North American Indian childhood cirrhosis (NAIC) is a disease in humans that can affect Ojibway-Cree children in northwestern Quebec, Canada.[1] The disease is due to an autosomal recessive abnormality of the CIRH1A gene, which codes for cirhin.[2] NAIC is a ribosomopathy.[3][4] An R565W mutation of CIRH1A[2][5] lea...
North American Indian childhood cirrhosis
c1858051
1,264
wikipedia
https://en.wikipedia.org/wiki/North_American_Indian_childhood_cirrhosis
2021-01-18T19:01:25
{"mesh": ["C565737"], "umls": ["C1858051"], "orphanet": ["168583"], "wikidata": ["Q25324164"]}
A very rare lysosomal storage disease that is clinically and pathologically heterogeneous and is characterized by deficient NAGA activity. ## Epidemiology Exact prevalence of NAGA deficiency is unknown but fewer than 20 cases have been reported to date in patients of German, Dutch, Spanish, Japanese, French and Mor...
Alpha-N-acetylgalactosaminidase deficiency
c1836544
1,265
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=3137
2021-01-23T18:30:09
{"mesh": ["C536631"], "omim": ["609241", "609242"], "umls": ["C0342850", "C1836544"], "icd-10": ["E77.1"], "synonyms": ["NAGA deficiency", "Schindler disease"]}
A number sign (#) is used with this entry because of evidence that cranioectodermal dysplasia-4 (CED4) is caused by compound heterozygous mutation in the WDR19 gene (608151) on chromosome 4p14. One such family has been reported. Description Cranioectodermal dysplasia (CED), also known as Sensenbrenner syndrome, is ...
CRANIOECTODERMAL DYSPLASIA 4
c0432235
1,266
omim
https://www.omim.org/entry/614378
2019-09-22T15:55:28
{"doid": ["0080033"], "mesh": ["C562966"], "omim": ["614378"], "orphanet": ["1515"], "genereviews": ["NBK154653"]}
Large, right lower lobe pneumatocele is shown, compromising ventilation in a premature infant with RDS and superimposed RSV pneumonitis. A pneumatocele is a cavity in the lung parenchyma filled with air that may result from pulmonary trauma during mechanical ventilation.[1] Gas-filled, or air-filled lesions in bone...
Pneumatocele
c0333160
1,267
wikipedia
https://en.wikipedia.org/wiki/Pneumatocele
2021-01-18T19:01:47
{"umls": ["C0333160"], "icd-10": ["G93.88"], "wikidata": ["Q7205984"]}
Thousand cankers disease A walnut tree in Denver, Colorado affected by Thousand cankers disease. Common namesTCD Causal agentsGeosmithia morbida HostsWalnut trees (Juglans sp.) Vectorswalnut twig beetle (Pityophthorus juglandis) EPPO CodeGEOHMO Thousand cankers disease (TCD) is a recently r...
Thousand cankers disease
None
1,268
wikipedia
https://en.wikipedia.org/wiki/Thousand_cankers_disease
2021-01-18T18:55:43
{"wikidata": ["Q17119323"]}
Megacystis (fetal) SpecialtyUrology Fetal megacystis[1] is a rare disease that is identified by an abnormally large or distended bladder. ## Contents * 1 Cause * 2 Diagnosis * 3 Treatment * 4 See also * 5 References * 6 External links ## Cause[edit] Megacystis is associated with Berdon syndrome...
Megacystis (fetal)
c1855311
1,269
wikipedia
https://en.wikipedia.org/wiki/Megacystis_(fetal)
2021-01-18T18:35:42
{"mesh": ["C536139"], "umls": ["C1855311"], "wikidata": ["Q6808346"]}
A number sign (#) is used with this entry because of evidence that osteogenesis imperfecta type VI (OI6) is caused by homozygous mutation in the SERPINF1 gene (172860) on chromosome 17p13.3. Description Osteogenesis imperfecta (OI) comprises a group of connective tissue disorders characterized by bone fragility and...
OSTEOGENESIS IMPERFECTA, TYPE VI
c0268362
1,270
omim
https://www.omim.org/entry/613982
2019-09-22T15:56:57
{"doid": ["0110350"], "mesh": ["C536044"], "omim": ["613982"], "orphanet": ["216812", "216820", "666"]}
X-linked infantile nystagmus is a condition characterized by abnormal eye movements. Nystagmus is a term that refers to involuntary side-to-side movements of the eyes. In people with this condition, nystagmus is present at birth or develops within the first six months of life. The abnormal eye movements may worsen wh...
X-linked infantile nystagmus
c1839580
1,271
medlineplus
https://medlineplus.gov/genetics/condition/x-linked-infantile-nystagmus/
2021-01-27T08:25:15
{"gard": ["2969"], "mesh": ["C537853"], "omim": ["310700"], "synonyms": []}
Constitutional mismatch repair deficiency syndrome is a rare, inherited cancer-predisposing syndrome characterized by the development of a broad spectrum of malignancies during childhood, including mainly brain, hematological and gastrointestinal cancers, although embryonic and other tumors have also been occasionall...
Constitutional mismatch repair deficiency syndrome
c0265325
1,272
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=252202
2021-01-23T17:30:31
{"mesh": ["C536928"], "omim": ["276300"], "synonyms": ["CMMR-D syndrome"]}
Nutcracker syndrome Other namesNutcracker phenomenon, renal vein entrapment syndrome, mesoaortic compression of the left renal vein The nutcracker syndrome results from compression of the left renal vein between the aorta and the superior mesenteric artery. The nutcracker syndrome (NCS) results most commonly...
Nutcracker syndrome
c3178770
1,273
wikipedia
https://en.wikipedia.org/wiki/Nutcracker_syndrome
2021-01-18T18:32:30
{"gard": ["11971"], "mesh": ["D059228"], "umls": ["C3178770"], "orphanet": ["71273"], "wikidata": ["Q1504516"]}
A number sign (#) is used with this entry because of evidence that band heterotopia (BH) is caused by homozygous or compound heterozygous mutation in the EML1 gene (602033) on chromosome 14q32. Clinical Features Kielar et al. (2014) reported a French family in which 3 brothers had severe developmental delay wit...
BAND HETEROTOPIA
c1848201
1,274
omim
https://www.omim.org/entry/600348
2019-09-22T16:16:16
{"doid": ["0111169"], "mesh": ["D054221"], "omim": ["600348"], "orphanet": ["99796"]}
A rare urogenital tumor characterized by stromal and epithelial components forming cysts lined by hyperplastic epithelium in a cellular or sarcomatoid stroma. The tumors may be clinically benign or malignant and tend to recur after transurethral resection. Metastatic spread is to lungs, bone, and liver. Patients may ...
Phyllodes tumor of the prostate
c1334615
1,275
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=498228
2021-01-23T17:08:32
{"mesh": ["C549759"], "synonyms": ["Cystic epithelial-stromal tumors of the prostate", "Cystosarcoma phyllodes of the prostate", "Phyllodes type of atypical prostatic hyperplasia"]}
A number sign (#) is used with this entry because of evidence that autosomal dominant congenital deafness with onychodystrophy (DDOD) is caused by heterozygous mutation in the ATP6V1B2 gene (606939) on chromosome 8p21. Description The DDOD syndrome is characterized by autosomal dominant inheritance of congenital de...
DEAFNESS, CONGENITAL, WITH ONYCHODYSTROPHY, AUTOSOMAL DOMINANT
c2675730
1,276
omim
https://www.omim.org/entry/124480
2019-09-22T16:42:34
{"mesh": ["C567274"], "omim": ["124480"], "orphanet": ["3231", "79499"], "synonyms": ["DDOD SYNDROME", "Alternative titles"]}
Keratosis follicularis spinulosa decalvans Other namesSiemens-1 syndrome Keratosis follicularis spinulosa decalvans is a rare X-linked disorder described by Siemens in 1926, a disease that begins in infancy with keratosis pilaris localized on the face, then evolves to more diffuse involvement.[1]:580,762[2]:64...
Keratosis follicularis spinulosa decalvans
c0343057
1,277
wikipedia
https://en.wikipedia.org/wiki/Keratosis_follicularis_spinulosa_decalvans
2021-01-18T18:29:38
{"gard": ["6829"], "mesh": ["C536159"], "umls": ["C0343057"], "orphanet": ["2340"], "wikidata": ["Q6393653"]}
A rare genetic multiple congenital anomalies/dysmorphic syndrome characterized by global developmental delay, intellectual disability, hypotonia, craniofacial dysmorphism (such as ridged metopic sutures, long palpebral fissures, broad nasal bridge, hypoplastic alae nasi, low-set, prominent ears, prominent midline...
Neurodevelopmental disorder-craniofacial dysmorphism-cardiac defect-skeletal anomalies syndrome
c4225274
1,278
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=453499
2021-01-23T18:08:23
{"omim": ["616580"], "synonyms": ["Au-Kline syndrome"]}
Capra-DeMarco syndrome is characterized by sagittal craniosynostosis, hydrocephalus, Chiari I malformation and radioulnar synostosis. Other clinical findings include blepharophimosis, small low-set ears, hypoplastic philtrum, kidney malformation, and hypogenitalism. ## Epidemiology The syndrome was described in two...
Craniosynostosis-hydrocephalus-Arnold-Chiari malformation type I-radioulnar synostosis syndrome
c3267187
1,279
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=171839
2021-01-23T19:01:21
{"umls": ["C3267187"], "icd-10": ["Q87.8"], "synonyms": ["Berant syndrome", "Capra-DeMarco syndrome", "Familial scaphocephaly-radioulnar synostosis syndrome"]}
Hypocalcemic rickets is a group of genetic diseases characterized by hypocalcemia and rickets. It comprises hypocalcemic vitamin D dependent rickets (VDDR-I) and hypocalcemic vitamin D resistant rickets (HVDRR) (see these terms). ## Clinical description Characteristic clinical features include slow growth, bone pai...
Hypocalcemic rickets
c4302195
1,280
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=289103
2021-01-23T17:17:01
{}
## Description Human personality traits that can be reliably measured by rating scales show a considerable heritable component. One such instrument is the tridimensional personality questionnaire (TPQ), which was designed by Cloninger et al. (1993) to measure 4 distinct domains of temperament--novelty seeking, harm...
NOVELTY SEEKING PERSONALITY TRAIT
c1866430
1,281
omim
https://www.omim.org/entry/601696
2019-09-22T16:14:25
{"omim": ["601696"]}
Germ-cell tumor Micrograph of a seminoma, a common germ cell tumor. SpecialtyOncology Germ cell tumor (GCT) is a neoplasm derived from germ cells. Germ-cell tumors can be cancerous or benign. Germ cells normally occur inside the gonads (ovary[1] and testis). GCTs that originate outside the gonads may be birt...
Germ cell tumor
c0205851
1,282
wikipedia
https://en.wikipedia.org/wiki/Germ_cell_tumor
2021-01-18T18:49:27
{"mesh": ["D009373"], "umls": ["C0205851"], "icd-9": ["183", "220", "186", "222.0"], "icd-10": ["C62", "C56", "D27", "D29.2"], "orphanet": ["3399"], "wikidata": ["Q1737977"]}
Okamoto syndrome is characterised by congenital hydronephrosis, intellectual deficit, growth retardation, cleft palate, generalised hypotonia and a characteristic face. Cardiac anomalies have also been reported. To date, 6 cases have been reported. *[v]: View this template *[t]: Discuss this template *[e]:...
Okamoto syndrome
c1858043
1,283
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=2729
2021-01-23T18:13:07
{"gard": ["4064"], "mesh": ["C565736"], "omim": ["604916"], "icd-10": ["Q87.8"]}
"Miner's lung" redirects here. For the book, see Miners' Lung (book). Pneumoconiosis Micrograph of asbestosis (with ferruginous bodies), a type of pneumoconiosis. H&E stain. SpecialtyPulmonology Pneumoconiosis is the general term for a class of interstitial lung diseases where inhalation of dust has caused ...
Pneumoconiosis
c0032273
1,284
wikipedia
https://en.wikipedia.org/wiki/Pneumoconiosis
2021-01-18T18:55:03
{"mesh": ["D011009"], "umls": ["C0032273"], "orphanet": ["182098"], "wikidata": ["Q651223"]}
For a discussion of genetic heterogeneity of quantitative trait loci for stature (STQTL), see STQTL1 (606255). Mapping By analyzing a sample of 1,816 individuals from 79 pedigrees, Liu et al. (2004) found linkage evidence suggesting a quantitative trait locus underlying height on chromosome 9q22.32 (maximum mul...
STATURE QUANTITATIVE TRAIT LOCUS 8
c1864691
1,285
omim
https://www.omim.org/entry/610114
2019-09-22T16:05:12
{"omim": ["610114"]}
Charlie M syndrome is a rare bone developmental disorder which belongs to a group of oromandibular limb hypogenesis syndromes that includes hypoglossia-hypodactyly and glossopalatine ankylosis (see these terms). The major anomalies which occur commonly in this group are hypoplasia of the mandible, syndactyly and ectr...
Charlie M syndrome
c4518555
1,286
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=1406
2021-01-23T18:07:08
{"gard": ["1261"], "icd-10": ["Q87.0"]}
This article needs additional citations for verification. Please help improve this article by adding citations to reliable sources. Unsourced material may be challenged and removed. Find sources: "Depigmentation" – news · newspapers · books · scholar · JSTOR (December 2006) (Learn how and when to remove this templa...
Depigmentation
c0162835
1,287
wikipedia
https://en.wikipedia.org/wiki/Depigmentation
2021-01-18T18:40:52
{"mesh": ["D017496"], "wikidata": ["Q3705665"]}
Cylindroma SpecialtyOncology, dermatology A variant of eccrine spiradenoma which can be multiple on the scalp and can coalesce to form a 'Turban' tumour. In pathology, a cylindroma is a tumour with nests of cells that resemble a cylinder in cross section. Types include: * Dermal eccrine cylindroma, a b...
Cylindroma
c1305968
1,288
wikipedia
https://en.wikipedia.org/wiki/Cylindroma
2021-01-18T18:51:49
{"gard": ["12346"], "mesh": ["C536611"], "umls": ["C1305968"], "icd-10": ["D23"], "wikidata": ["Q245711"]}
Spondyloepiphyseal dysplasia (SED) is a group of rare genetic conditions that affect bone growth in the spine, arms, and legs. Other features include problems with vision and hearing, clubfeet, cleft palate, arthritis, and difficulty with breathing as curvature of the spine progresses. There are two main types of...
Spondyloepiphyseal dysplasia
c0038015
1,289
gard
https://rarediseases.info.nih.gov/diseases/7687/spondyloepiphyseal-dysplasia
2021-01-18T17:57:32
{"mesh": ["D010009"], "orphanet": ["253"], "synonyms": []}
## Description An X-linked recessive inhibitor (XS) of the Lutheran blood group system (111200) has been reported. For a discussion of Lutheran blood group phenotypes, see 247420. Clinical Features Norman et al. (1985, 1986) studied a family in which 5 males showed the Lu(a-b-) phenotype. The red cells of these ...
LUTHERAN SUPPRESSOR, X-LINKED
c3887995
1,290
omim
https://www.omim.org/entry/309050
2019-09-22T16:18:15
{"omim": ["309050"], "synonyms": ["Alternative titles", "LUXS"]}
A rare congenital limb malformation characterized by duplication of the fifth digit in a hand or foot, with an extra, well-formed, functional digit at the metacarpophalangeal/metatarsophalangeal or carpometacarpal/tarsometatarsal joint. The malformation can be an isolated finding or be associated with a large number ...
Postaxial polydactyly type A
c3887487
1,291
orphanet
https://www.orpha.net/consor/cgi-bin/OC_Exp.php?lng=EN&Expert=93334
2021-01-23T17:02:19
{"mesh": ["C562429"], "omim": ["174200", "263450", "602085", "607324", "608562", "615226", "618219", "618498"], "umls": ["C3887487"], "icd-10": ["Q69.0"]}
Stercoral perforation Play media Axial CT cine clip showing loculated fluid, free intraperitoneal fluid, extraluminal gas, and focal discontinuity of the wall of the sigmoid colon with stool in the defect consistent with stercoral perforation. The person was a heavy opioid user Stercoral perforation is...
Stercoral perforation
None
1,292
wikipedia
https://en.wikipedia.org/wiki/Stercoral_perforation
2021-01-18T18:46:17
{"wikidata": ["Q7611182"]}
Eosinophilic fasciitis Other namesShulman syndrome[1] SpecialtyRheumatology Eosinophilic fasciitis (/ˌiːəˌsɪnəˈfɪlɪk ˌfæʃiˈaɪtɪs, ˌiːoʊ-, -ˌfæsi-/[2][3]), also known as "Shulman's syndrome",[4] is a form of fasciitis, the inflammatory diseases that affect the fascia, the connective tissues surrounding mu...
Eosinophilic fasciitis
c0264005
1,293
wikipedia
https://en.wikipedia.org/wiki/Eosinophilic_fasciitis
2021-01-18T18:41:28
{"gard": ["6351"], "mesh": ["C562487"], "umls": ["C0264005"], "icd-9": ["728.89"], "icd-10": ["M35.4"], "orphanet": ["3165"], "wikidata": ["Q2325206"]}
Clay-shoveler fracture C7 spinous process. SpecialtyNeurosurgery Clay-shoveler's fracture is a stable fracture through the spinous process of a vertebra occurring at any of the lower cervical or upper thoracic vertebrae, classically at C6 or C7.[1] In Australia in the 1930s, men digging deep ditches toss...
Clay-shoveler fracture
None
1,294
wikipedia
https://en.wikipedia.org/wiki/Clay-shoveler_fracture
2021-01-18T18:54:34
{"wikidata": ["Q5129816"]}
Main article: Myocardial infarction Myocardial infarction complications may occur immediately following a heart attack (in the acute phase), or may need time to develop (a chronic problem). After an infarction, an obvious complication is a second infarction, which may occur in the domain of another atherosclerot...
Myocardial infarction complications
None
1,295
wikipedia
https://en.wikipedia.org/wiki/Myocardial_infarction_complications
2021-01-18T18:42:42
{"icd-10": ["I23"], "wikidata": ["Q6947903"]}
A number sign (#) is used with this entry because some evidence has suggested that susceptibility to idiopathic generalized epilepsy-11 (EIG11), juvenile myoclonic epilepsy-8 (EJM8), and juvenile absence epilepsy-2 (EJA2) may be conferred by variation in the chloride channel-2 gene (CLCN2; 600570) on chromosome 3...
EPILEPSY, IDIOPATHIC GENERALIZED, SUSCEPTIBILITY TO, 11
c0270853
1,296
omim
https://www.omim.org/entry/607628
2019-09-22T16:08:59
{"doid": ["0111312"], "mesh": ["D020190"], "omim": ["607628"], "orphanet": ["307"]}
Type of congenital heart defect Not to be confused with Teratology. Tetralogy of Fallot Other namesFallot’s syndrome, Fallot’s tetrad, Steno-Fallot tetralogy[1] Diagram of a healthy heart and one with tetralogy of Fallot SpecialtyCardiac surgery, pediatrics SymptomsEpisodes of bluish color to the skin, diff...
Tetralogy of Fallot
c0039685
1,297
wikipedia
https://en.wikipedia.org/wiki/Tetralogy_of_Fallot
2021-01-18T18:54:21
{"gard": ["2245"], "mesh": ["D013771"], "umls": ["C0039685"], "orphanet": ["3303"], "wikidata": ["Q1126831"]}
"Hepatite" redirects here. For the mineral of that name, see Baryte. An inflammation of the liver. Hepatitis Alcoholic hepatitis as seen with a microscope, showing fatty changes (white circles), remnants of dead liver cells, and Mallory bodies (twisted-rope shaped inclusions within some liver cells). (H&E sta...
Hepatitis
c0019158
1,298
wikipedia
https://en.wikipedia.org/wiki/Hepatitis
2021-01-18T18:38:18
{"mesh": ["D006505"], "umls": ["C0019158"], "wikidata": ["Q131742"]}
A number sign (#) is used with this entry because of evidence that slow-channel congenital myasthenic syndrome-1A (CMS1A) is caused by heterozygous mutation in the CHRNA1 gene (100690) on chromosome 2q31. There are rare reports of recessive inheritance. Mutation in the CHRNA1 gene can also cause fast-channel CMS...
MYASTHENIC SYNDROME, CONGENITAL, 1A, SLOW-CHANNEL
c0751882
1,299
omim
https://www.omim.org/entry/601462
2019-09-22T16:14:42
{"doid": ["0110663"], "mesh": ["D020294"], "omim": ["601462"], "orphanet": ["98913", "590"], "synonyms": ["CMS IIa, FORMERLY", "Alternative titles", "MYASTHENIC SYNDROME, CONGENITAL, TYPE IIa, FORMERLY"], "genereviews": ["NBK1168"]}